Study of BGB-A317 in Participants With Previously Treated Unresectable HCC

NCT ID: NCT03419897

Last Updated: 2024-10-26

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

249 participants

Study Classification

INTERVENTIONAL

Study Start Date

2018-04-09

Study Completion Date

2022-07-06

Brief Summary

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This study investigated the efficacy, safety, and pharmacokinetics of the anti-PD-1 monoclonal antibody BGB-A317 in participants with previously treated hepatocellular unresectable carcinoma.

Detailed Description

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Conditions

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Hepatocellular Carcinoma (HCC)

Study Design

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Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Tislelizumab

200 milligrams once every 3 weeks

Group Type EXPERIMENTAL

Tislelizumab

Intervention Type DRUG

Administered intravenously

Interventions

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Tislelizumab

Administered intravenously

Intervention Type DRUG

Other Intervention Names

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BGB-A317

Eligibility Criteria

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Inclusion Criteria

1. Histologically confirmed HCC
2. Participants with Barcelona Clinic Liver Cancer (BCLC) Stage C, or BCLC stage B not amenable to locoregional therapy or relapsed after locoregional therapy, and not amenable to a curative treatment approach
3. Has received at least 1 line of systemic therapy for unresectable HCC
4. Has at least 1 measurable lesion as defined per RECIST v1.1
5. Child-Pugh score A
6. Easter Cooperative Oncology Group (ECOG) Performance Status ≤ 1
7. Adequate organ function

Exclusion Criteria

1. Known fibrolamellar HCC, sarcomatoid HCC, or mixed cholangiocarcinoma and HCC histology
2. Prior therapies targeting PD-1 or PD-L1
3. Has known brain or leptomeningeal metastasis
4. Tumor thrombus involving main trunk of portal vein or inferior vena cava
5. Loco-regional therapy to the liver within 4 weeks before enrollment
6. Medical history of interstitial lung disease, non-infectious pneumonitis or uncontrolled systemic diseases, including diabetes, hypertension, pulmonary fibrosis, or acute lung diseases
7. Has received:

1. Within 28 days or 5 half-lives (whichever is shorter) of the first study drug administration: any chemotherapy, immunotherapy (eg, interleukin, interferon, thymoxin) or any investigational therapies
2. Within 14 days of the first study drug administration: sorafenib, regorafenib, or any Chinese herbal medicine or Chinese patent medicines used to control cancer
8. Active autoimmune diseases or history of autoimmune diseases that may relapse
9. Participant with any condition requiring systemic treatment with either corticosteroids (\> 10 mg daily of prednisone or equivalent) or other immunosuppressive medication within 14 days before study drug administration
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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BeiGene

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Study Director

Role: STUDY_DIRECTOR

BeiGene

Locations

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Anhui Provincial Hospital

Hefei, Anhui, China

Site Status

The Second Hospital of Anhui Medical University

Hefei, Anhui, China

Site Status

Military Hospital of China

Beijing, Beijing Municipality, China

Site Status

Beijing Cancer Hospital

Beijing, Beijing Municipality, China

Site Status

Chinese Pla General Hospital

Beijing, Beijing Municipality, China

Site Status

Sun Yat Sen Memorial Hospital, Sun Yat Sen University (South)

Guangzhou, Guangdong, China

Site Status

Nanfang Hospital of Southern Medical University

Guangzhou, Guangdong, China

Site Status

Peking University Shenzhen Hospital

Shenzhen, Guangdong, China

Site Status

Harbin Medical University Cancer Hospital

Harbin, Heilongjiang, China

Site Status

Henan Cancer Hospital

Zhengzhou, Henan, China

Site Status

Union Hospital of Tongji Medical College, Huazhong University of Science and Technology

Wuhan, Hubei, China

Site Status

Hubei Cancer Hospital

Wuhan, Hubei, China

Site Status

Xuzhou Central Hospital

Xuzhou, Jiangsu, China

Site Status

The First Affiliated Hospital of Nanchang University Branch Donghu

Nanchang, Jiangxi, China

Site Status

The Second Affiliated Hospital of Nanchang University

Nanchang, Jiangxi, China

Site Status

Jilin Cancer Hospital

Changchun, Jilin, China

Site Status

Weifang Peoples Hospital

Weifang, Shandong, China

Site Status

Fudan University Shanghai Cancer Center

Shanghai, Shanghai Municipality, China

Site Status

Affiliated Zhongshan Hospital of Fudan University

Shanghai, Shanghai Municipality, China

Site Status

Tianjin Medical University Cancer Institute and Hospital

Tianjin, Tianjin Municipality, China

Site Status

The First Affiliated Hospital, Zhejiang University School of Medicine

Hangzhou, Zhejiang, China

Site Status

Zhejiang University College of Medicine Second Affiliated Hospital

Hangzhou, Zhejiang, China

Site Status

Sir Run Run Shaw Hospital, Zhejiang University School of Medicine

Hangzhou, Zhejiang, China

Site Status

Zhejiang Cancer Hospital

Hangzhou, Zhejiang, China

Site Status

The First Affiliated Hospital of Wenzhou Medical University

Wenzhou, Zhejiang, China

Site Status

Hopital Beaujon

Clichy, , France

Site Status

Hopital de La Croix Rousse

Lyon, , France

Site Status

Chu Montpellier Hopital Saint Eloi

Montpellier, , France

Site Status

Centre Hospitalier Universitaire Nantes Hotel Dieu

Nantes, , France

Site Status

Hopital Larchet Chu Nice

Nice, , France

Site Status

Groupe Hospitalier Du Haut Leveque

Pessac, , France

Site Status

Chu de Poitiers Site de La Mileterie

Poitiers, , France

Site Status

Centre Eugene Marquis

Rennes, , France

Site Status

Institut Gustave Roussy

Villejuif, , France

Site Status

Kliniken Essen Mitte Evang Huyssens Stiftung

Essen, , Germany

Site Status

Universitatsklinikum Hamburg Eppendorf

Hamburg, , Germany

Site Status

Klinikum Johannes Gutenberg Universitaet Mainz

Mainz, , Germany

Site Status

Azienda Ospedaliero Universitaria Pisana

Pisa, , Italy

Site Status

Istituto Clinico Humanitas

Rozzano, , Italy

Site Status

Narodowy Instytut Onkologii Im Marii Skodowskiej Curie Pastwowy Instytut Badawczy

Warsaw, , Poland

Site Status

Hospital Universitario Vall Dhebron

Barcelona, , Spain

Site Status

Ico Lhospitalet Hospital Duran I Reynals

Barcelona, , Spain

Site Status

Hospital Universitario La Paz

Madrid, , Spain

Site Status

Hospital Universitario Hm Madrid Sanchinarro

Madrid, , Spain

Site Status

E Da Hospital Kaohsiung

Kaohsiung City, , Taiwan

Site Status

National Cheng Kung University Hospital

Tainan City, , Taiwan

Site Status

National Taiwan University Hospital

Taipei, , Taiwan

Site Status

Taipei Veterans General Hospital

Taipei, , Taiwan

Site Status

Linkou Chang Gung Memorial Hospital

Taoyuan District, , Taiwan

Site Status

Queen Elizabeth Hospital

Birmingham, , United Kingdom

Site Status

The Christie Hospital

Greater Manchester, , United Kingdom

Site Status

Royal Free Hospital London Nhs Trust

London, , United Kingdom

Site Status

Kings College

London, , United Kingdom

Site Status

Freeman Hospital

Newcastle upon Tyne, , United Kingdom

Site Status

Countries

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China France Germany Italy Poland Spain Taiwan United Kingdom

References

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Ren Z, Ducreux M, Abou-Alfa GK, Merle P, Fang W, Edeline J, Li Z, Wu L, Assenat E, Hu S, Rimassa L, Zhang T, Blanc JF, Pan H, Ross P, Yen CJ, Tran A, Shao G, Bouattour M, Chen Y, Meyer T, Hou J, Tougeron D, Bai Y, Hou MM, Meng Z, Wu J, Li V, Chica-Duque S, Cheng AL. Tislelizumab in Patients with Previously Treated Advanced Hepatocellular Carcinoma (RATIONALE-208): A Multicenter, Non-Randomized, Open-Label, Phase 2 Trial. Liver Cancer. 2022 Oct 4;12(1):72-84. doi: 10.1159/000527175. eCollection 2023 Feb.

Reference Type BACKGROUND
PMID: 36872927 (View on PubMed)

Serrano D, Podger L, Barnes G, Song J, Tang B. Psychometric validation of the EORTC QLQ-HCC18 in patients with previously treated unresectable hepatocellular carcinoma. Qual Life Res. 2022 Mar;31(3):937-950. doi: 10.1007/s11136-021-02992-1. Epub 2021 Sep 13.

Reference Type BACKGROUND
PMID: 34518988 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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2017-003983-10

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

CTR20171257

Identifier Type: REGISTRY

Identifier Source: secondary_id

BGB-A317-208

Identifier Type: -

Identifier Source: org_study_id

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