Assess Safety and Efficacy of Vilaprisan in Subjects With Uterine Fibroids (ASTEROID 3)

NCT ID: NCT03400943

Last Updated: 2023-05-03

Study Results

Results available

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Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE3

Total Enrollment

93 participants

Study Classification

INTERVENTIONAL

Study Start Date

2018-01-17

Study Completion Date

2022-04-06

Brief Summary

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The primary objective of this study was to show superiority in the treatment of HMB of vilaprisan in subjects with uterine fibroids compared to placebo.

The secondary objectives of this study were to additionally evaluate the efficacy and safety of vilaprisan in subjects with uterine fibroids.

Detailed Description

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Conditions

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Uterine Fibroids

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors
Blinding will be applied to Treatment Groups A1, B1, and B2; Treatment Group A2 will be open-label

Study Groups

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Vilaprisan (A1)

Vilaprisan (2 mg) in treatment period 1 for 12 weeks and in treatment period 2 for 12 weeks, separated by 1 bleeding episode.

Group Type EXPERIMENTAL

Vilaprisan (BAY1002670)

Intervention Type DRUG

2 mg of Vilaprisan once daily up to 2 x 12 weeks

Placebo

Intervention Type DRUG

Matching placebo was administered to group B1 and B2.

Vilaprisan (A2)

Vilaprisan (2 mg) in treatment period 1 for 12 weeks and in treatment period 2 for 12 weeks without a break.

Group Type EXPERIMENTAL

Vilaprisan (BAY1002670)

Intervention Type DRUG

2 mg of Vilaprisan once daily up to 2 x 12 weeks

Placebo+Vilaprisan (B1)

Placebo in treatment period 1 for 12 weeks, and vilaprisan (2 mg) in treatment period 2 for 12 weeks, separated by 1 bleeding episode.

Group Type EXPERIMENTAL

Vilaprisan (BAY1002670)

Intervention Type DRUG

2 mg of Vilaprisan once daily up to 2 x 12 weeks

Placebo

Intervention Type DRUG

Matching placebo was administered to group B1 and B2.

Vilaprisan+Placebo (B2)

Vilaprisan (2 mg) in treatment period 1 for 12 weeks and placebo in treatment period 2 for 12 weeks, separated by 1 bleeding episode.

Group Type EXPERIMENTAL

Vilaprisan (BAY1002670)

Intervention Type DRUG

2 mg of Vilaprisan once daily up to 2 x 12 weeks

Placebo

Intervention Type DRUG

Matching placebo was administered to group B1 and B2.

Interventions

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Vilaprisan (BAY1002670)

2 mg of Vilaprisan once daily up to 2 x 12 weeks

Intervention Type DRUG

Placebo

Matching placebo was administered to group B1 and B2.

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Women, 18 years or older in good General health
* Diagnosis of uterine fibroid(s) documented by ultrasound at screening with at least 1 fibroid with largest Diameter ≥ 30 mm and \< 120 mm
* Heavy menstrual bleeding (HMB) in at least 2 bleeding periods during the Screening period each with blood loss volume of \>80.00 mL documented by alkaline hematin (AH) method
* An endometrial biopsy performed during the Screening period without significant histological disorder such as endometrial hyperplasia (including simple hyperplasia) or other significant endometrial pathology
* Use of an acceptable non-hormonal method of contraception (ie, either male condom, cap, diaphragm or sponge, each in combination with spermicide) starting at Visit 1 until the end of the study

Exclusion Criteria

* Pregnancy or lactation (less than 3 month since delivery, abortion, or lactation before start of Treatment)
* Hypersensitivity to any ingredient of the study drug
* Any condition requiring immediate blood transfusion
* Laboratory values outside inclusion range before randomization and considered as clinically relevant.
* Any diseases, conditions, or medications that can compromise the function of the body systems and could result in altered absorption, excessive accumulation, impaired metabolism, or altered excretion of the study drug
* Any diseases or conditions that might interfere with the conduct of the study or the interpretation of the results
* Abuse of alcohol, drugs, or medicines (eg, laxatives)
* Use of other treatments that might interfere with the conduct of the study or the interpretation of the results
* Undiagnosed abnormal genital bleeding
Minimum Eligible Age

18 Years

Eligible Sex

FEMALE

Accepts Healthy Volunteers

No

Sponsors

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Bayer

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Bayer Study Director

Role: STUDY_DIRECTOR

Bayer

Locations

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University of Alabama at Birmingham

Birmingham, Alabama, United States

Site Status

California Center for Clinical Research

Arcadia, California, United States

Site Status

Core Healthcare Group

Cerritos, California, United States

Site Status

AVIVA Research

Escondido, California, United States

Site Status

National Research Institute - Los Angeles

Los Angeles, California, United States

Site Status

Harbor - UCLA Medical Center

Torrance, California, United States

Site Status

Ideal Clinical Research

Aventura, Florida, United States

Site Status

South Florida Medical Research

Aventura, Florida, United States

Site Status

Helix Biomedics, LLC

Boynton Beach, Florida, United States

Site Status

Dr. Victoria Garcia & Associates, LLC Doral Medical Research

Doral, Florida, United States

Site Status

Sweet Hope Research Specialty, Inc. - Hialeah

Hialeah, Florida, United States

Site Status

Clinical Neurosciences Solutions, Inc. DBA CNS Healthcare

Jacksonville, Florida, United States

Site Status

Altus Research

Lake Worth, Florida, United States

Site Status

Axcess Medical Research, LLC

Loxahatchee Groves, Florida, United States

Site Status

Ocean Blue Medical Research Center, Inc.

Miami Springs, Florida, United States

Site Status

Accelerated Enrollment Solutions a business of PPD

Orlando, Florida, United States

Site Status

Discovery Clinical Research

Plantation, Florida, United States

Site Status

ONCOVA Clinical Research, Inc.

Saint Cloud, Florida, United States

Site Status

Georgia Center For Women

Atlanta, Georgia, United States

Site Status

Agile Clinical Research Trials, LLC

Atlanta, Georgia, United States

Site Status

Atlanta Women's Research Institute, Inc. - Alpharetta

Atlanta, Georgia, United States

Site Status

Medisense, Inc.

Atlanta, Georgia, United States

Site Status

Paramount Research Solutions-College Park

College Park, Georgia, United States

Site Status

One Health Research Clinic

Norcross, Georgia, United States

Site Status

Fellows Research Alliance - Savannah

Savannah, Georgia, United States

Site Status

GTC Research

Shawnee Mission, Kansas, United States

Site Status

Omni Fertility and Laser Institute

Shreveport, Louisiana, United States

Site Status

PharmaSite Research, Inc.

Baltimore, Maryland, United States

Site Status

Simmonds, Martin and Helmbrecht

Gaithersburg, Maryland, United States

Site Status

Advantia Health, LLC Obstetrics & Gynecology Assoc.

Silver Spring, Maryland, United States

Site Status

SUNY Downstate Medical Center

Brooklyn, New York, United States

Site Status

Carolinas Healthcare System

Charlotte, North Carolina, United States

Site Status

Unified Women's Clinical Research - Morehead City

Morehead City, North Carolina, United States

Site Status

Eastern Carolina Women's Center

New Bern, North Carolina, United States

Site Status

Wake Research, Inc.

Raleigh, North Carolina, United States

Site Status

Main Line Fertility Center

Bryn Mawr, Pennsylvania, United States

Site Status

Clinical Research of Philadelphia, LLC

Philadelphia, Pennsylvania, United States

Site Status

Fellows Research Alliance, Inc.

Bluffton, South Carolina, United States

Site Status

Medical University of South Carolina

Charleston, South Carolina, United States

Site Status

Fusion Clinical Research of Spartanburg, LLC

Spartanburg, South Carolina, United States

Site Status

Chattanooga Medical Research, LLC

Chattanooga, Tennessee, United States

Site Status

Clinical Neurosciences Solutions, Inc DBA CNS Healthcare

Memphis, Tennessee, United States

Site Status

Paramount Research Solutions-Nashville

Nashville, Tennessee, United States

Site Status

Texas Health Care, PLLC

Fort Worth, Texas, United States

Site Status

Willowbend Health & Wellness Associates

Frisco, Texas, United States

Site Status

Family Medicine Clinic

Georgetown, Texas, United States

Site Status

Biopharma Informatic, Inc.

Houston, Texas, United States

Site Status

Centex Studies, Inc.

Houston, Texas, United States

Site Status

The Center for Clinical Trials, Inc.

Houston, Texas, United States

Site Status

Houston Center for Clinical Research, LLC

Sugar Land, Texas, United States

Site Status

Millennium Clinical Trials, LLC

Arlington, Virginia, United States

Site Status

Synexus Research, LLC

Richmond, Virginia, United States

Site Status

Multiprofile Hospital for Active Treatment-Dr. T. Venkova AD

Gabrovo, , Bulgaria

Site Status

Hospital for Active Treatment - Prof.Paraskev Stoyanov AD

Lovech, , Bulgaria

Site Status

MHAT Dr. Bratan Shukerov AD

Smolyan, , Bulgaria

Site Status

MHAT for Women's Health - Nadezhda OOD

Sofia, , Bulgaria

Site Status

900th Hospital of Joint Logistics Support Force

Fuzhou, Fujian, China

Site Status

Guangzhou Women and Children's Medical Center

Guangzhou, Guangdong, China

Site Status

The Third Affiliated Hospital, Sun Yat-Sen University

Guangzhou, Guangdong, China

Site Status

Boai Hospital of Zhongshan

Zhongshan, Guangdong, China

Site Status

Hainan General Hospital

Haikou, Hainan, China

Site Status

Wuhan Tongji Reproductive Medicine Hospital

Wuhan, Hubei, China

Site Status

Nanjing Maternity and Child Health Care Hospital

Nanjing, Jiangsu, China

Site Status

NJ Drum Tower Hospital, the Affil Hos of NJ Univ Med School

Nanjing, Jiangsu, China

Site Status

Zhongda Hospital Southeast University

Nanjing, Jiangsu, China

Site Status

1st Affiliated hospital of Soochow University

Suzhou, Jiangsu, China

Site Status

Jiangxi Maternal and Child Health Hospital

Nanchang, Jiangxi, China

Site Status

The Second Affiliated Hospital of Nanchang University

Nanchang, Jiangxi, China

Site Status

The First Hospital of Jilin University

Changchun, Jilin, China

Site Status

The First Affiliated Hospital of Dalian Medical University

Dalian, Liaoning, China

Site Status

Shengjing Hospital of China Medical University

Shenyang, Liaoning, China

Site Status

General Hospital of Ningxia Medical University

Yinchuan, Ningxia, China

Site Status

Second Affiliated Hospital of Xi'an Jiaotong University

Xi'an, Shaanxi, China

Site Status

The First Affiliated Hospital of Xi'an Jiaotong University

Xi'an, Shaanxi, China

Site Status

The Second Affiliated Hospital of Shanxi Medical University

Taiyuan, Shanxi, China

Site Status

The First Affiliated Hospital of Xinjiang Medical University

Ürümqi, Xinjiang, China

Site Status

Women's Hospital School of Medicine Zhejiang University

Hangzhou, Zhejiang, China

Site Status

Sir Run Run Shaw Hospital, Zhejiang University School of Med

Hangzhou, Zhejiang, China

Site Status

The Second Affliated Hospital of Wenzhou Medicial University

Wenzhou, Zhejiang, China

Site Status

Beijing Hospital of Traditional Chinese Medicine

Beijing, , China

Site Status

Peking University First Hospital

Beijing, , China

Site Status

Beijing Friendship Hospital, Capital Medical University

Beijing, , China

Site Status

Beijing Tiantan Hospital, Captial Medical University

Beijing, , China

Site Status

Shanghai East Hospital Affiated to Tongji University

Shanghai, , China

Site Status

Tianjin Medical University General Hospital

Tianjin, , China

Site Status

Gynekologie MEDA s.r.o.

Brno, , Czechia

Site Status

Soukroma gynekologicka ambulance

Fulnek, , Czechia

Site Status

Gynekologie Studentsky dum s.r.o.

Prague, , Czechia

Site Status

MUDr. Ivana Salamonova s.r.o.

Vysoké Mýto, , Czechia

Site Status

Clalit Health Services through HaEmek Medical Center

Afula, , Israel

Site Status

Hillel Yaffe Medical Center

Hadera, , Israel

Site Status

Lady Davis Carmel Medical Center

Haifa, , Israel

Site Status

Meir Medical Center

Kfar Saba, , Israel

Site Status

University Hospital Kebangsaan Malaysia

Kuala Lumpur, , Malaysia

Site Status

Hospital Wanita dan Kanak-Kanak Sabah

Sabak Bernam, , Malaysia

Site Status

Sarawak General Hospital

Sarawak, , Malaysia

Site Status

P3 Research Ltd Hawkes Bay

Hawkes Bay, , New Zealand

Site Status

P3 Research

Tauranga, , New Zealand

Site Status

KK Women's and Children's Hospital

Singapore, , Singapore

Site Status

Dr L Reynders Practice

Lyttelton Manor, Gauteng, South Africa

Site Status

Wilgeheuwel Hospital

Roodepoort, Gauteng, South Africa

Site Status

Umhlanga Medical Centre

Durban, KwaZulu-Natal, South Africa

Site Status

Ethekwini Hospital & Heart Centre

Durban, KwaZulu-Natal, South Africa

Site Status

Countries

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United States Bulgaria China Czechia Israel Malaysia New Zealand Singapore South Africa

References

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Al-Hendy A, Zhou YF, Faustmann T, Groettrup-Wolfers E, Laapas K, Parke S, Seitz C. Efficacy and safety of vilaprisan in women with uterine fibroids: data from the ASTEROID 3 randomized controlled trial. F S Sci. 2023 Nov;4(4):317-326. doi: 10.1016/j.xfss.2023.06.003. Epub 2023 Jul 10.

Reference Type DERIVED
PMID: 37437885 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Related Links

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https://clinicaltrials.bayer.com/

Click here to find information for studies related to Bayer products. To find this study enter the ClinicalTrials.gov identifier (NCT) number or Bayer Study Identifier (ID) in the search field.

http://www.clinicaltrialsregister.eu/

Click here to find information about studies related to Bayer Healthcare products conducted in Europe

Other Identifiers

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2017-002997-38

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

15787

Identifier Type: -

Identifier Source: org_study_id

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