Effect of Radiotherapy on ATTR Cardiac Amyloidosis : a Proof of Concept Study

NCT ID: NCT03397810

Last Updated: 2021-05-11

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

Get a concise snapshot of the trial, including recruitment status, study phase, enrollment targets, and key timeline milestones.

Recruitment Status

RECRUITING

Clinical Phase

NA

Total Enrollment

36 participants

Study Classification

INTERVENTIONAL

Study Start Date

2019-03-15

Study Completion Date

2026-02-28

Brief Summary

Review the sponsor-provided synopsis that highlights what the study is about and why it is being conducted.

Cardiac amyloidosis is responsible for significant morbidity associated with heart failure, and carries a poor prognosis. Currently there are very limited treatment options for this condition. Radiotherapy has been used successfully to treat amyloidosis elsewhere in the body, however has not been tried in cardiac amyloidosis. Therefore this study aims to assess the effect of radiotherapy on cardiac amyloidosis, to evaluate whether it can successfully reduce the burden of amyloid deposits in the myocardium as assessed by 18F-Amyloid PET.

Detailed Description

Dive into the extended narrative that explains the scientific background, objectives, and procedures in greater depth.

The intervention will involve administration of external beam radiotherapy (5 fractions of 2Gy) focused to the heart.

Measurements of effect will be assessed at 12 weeks by:

Amyloid PET Cardiac MRI with administration of gadolinium and ultrasound A blood venous sample (cardiac biomarkers) Quality of life assessments

Conditions

See the medical conditions and disease areas that this research is targeting or investigating.

Amyloid Cardiomyopathy

Study Design

Understand how the trial is structured, including allocation methods, masking strategies, primary purpose, and other design elements.

Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

Review each arm or cohort in the study, along with the interventions and objectives associated with them.

Singe arm

Subjects will receive a low dose radiotherapy focused to the heart

Group Type EXPERIMENTAL

low dose radiotherapy

Intervention Type RADIATION

10 Gy in 5 fractions of 2 Gy on 5 consecutive days

Interventions

Learn about the drugs, procedures, or behavioral strategies being tested and how they are applied within this trial.

low dose radiotherapy

10 Gy in 5 fractions of 2 Gy on 5 consecutive days

Intervention Type RADIATION

Eligibility Criteria

Check the participation requirements, including inclusion and exclusion rules, age limits, and whether healthy volunteers are accepted.

Inclusion Criteria

* Age \>65 y.o.
* Dyspnoea on exertion (NYHA II or more).
* Stable elevated cardiac enzymes (ultra sensitive Troponin T \> 14 ng/L on consecutive sampling or BNP \> 100pg/mL)
* A positive 99mTc-DPD cardiac scintigraphy (Grade 2 and 3) suggesting an ATTR or wt amyloidosis.
* Additional imaging also compatible with cardiac amyloidosis (cardiac ultrasound showing basal to apical longitudinal strain gradient and magnetic resonance imaging with elevated T1 value or extracellular volume).
* Compliance with the informed consent as attested by its signature.
* Positive baseline 18F-Florbetapir imaging, as assessed visually and quantitatively by a Tissue to Background Ratio \> 1.45

Exclusion Criteria

* Positive serum protein immunoelectrophoresis with monoclonal gammapathy.
* Previous external beam radiotherapy including the chest.
* Claustrophobia
* Presence of internal non-MR compatible devices
* Creatinine glomerular filtration rate \< 30 ml/min
* Oncologic disease (excluding skin cancer) active or in remission from less than 5 years
Minimum Eligible Age

65 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

Meet the organizations funding or collaborating on the study and learn about their roles.

Philippe Meyer

OTHER

Sponsor Role lead

Responsible Party

Identify the individual or organization who holds primary responsibility for the study information submitted to regulators.

Philippe Meyer

Principal Investigator

Responsibility Role SPONSOR_INVESTIGATOR

Locations

Explore where the study is taking place and check the recruitment status at each participating site.

Geneva University Hospital

Geneva, , Switzerland

Site Status RECRUITING

Countries

Review the countries where the study has at least one active or historical site.

Switzerland

Central Contacts

Reach out to these primary contacts for questions about participation or study logistics.

René Nkoulou, Dr.

Role: CONTACT

+41 22 37 27 196

Philippe Meyer, Dr.

Role: CONTACT

+41 22 37 27 225

Facility Contacts

Find local site contact details for specific facilities participating in the trial.

René Nkoulou, Dr.

Role: primary

Other Identifiers

Review additional registry numbers or institutional identifiers associated with this trial.

2017-00640

Identifier Type: -

Identifier Source: org_study_id

More Related Trials

Additional clinical trials that may be relevant based on similarity analysis.

Thailand ATTR-CM Registry
NCT06338696 RECRUITING
Ultrasound Therapy In Cardiac Amyloidosis
NCT04667494 RECRUITING PHASE4
Clinical Study of ATTR-CM
NCT04935021 RECRUITING PHASE4
Cardiac Amyloidosis Discovery Trial
NCT06469372 COMPLETED NA