Study of Romiplostim for Chemotherapy-induced Thrombocytopenia in Adult Subjects With Gastrointestinal, Pancreatic, or Colorectal Cancer

NCT ID: NCT03362177

Last Updated: 2025-01-20

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

165 participants

Study Classification

INTERVENTIONAL

Study Start Date

2019-09-30

Study Completion Date

2025-01-09

Brief Summary

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Study of Romiplostim for Chemotherapy-induced Thrombocytopenia in Adult Subjects with Gastrointestinal, Pancreatic, or Colorectal Cancer

Detailed Description

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RECITE: A phase 3 Randomized Placebo-controlled Double-blind Study of Romiplostim for the Treatment of Chemotherapy-induced Thrombocytopenia in Patients Receiving Oxaliplatin-based Chemotherapy for Treatment of Gastrointestinal, Pancreatic, or Colorectal Cancer

Conditions

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Chemotherapy-induced Thrombocytopenia

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Investigators

Study Groups

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Romiplostim

Participants will be enrolled to the study in a 2:1 randomization ratio. Amgen investigational product (romiplostim or placebo) will be administered in the clinic by a qualified healthcare provider as a subcutaneous injection.

Group Type EXPERIMENTAL

Romiplostim

Intervention Type BIOLOGICAL

This study is designed to study Romiplostim for the treatment of chemotherapy-induced thrombocytopenia (CIT) in patients receiving chemotherapy for the treatment of gastrointestinal/colorectal/pancreatic cancer.

Placebo

Participants will be enrolled to the study in a 2:1 randomization ratio. Amgen investigational product (romiplostim or placebo) will be administered in the clinic by a qualified healthcare provider as a subcutaneous injection.

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type OTHER

Placebo Comparator

Interventions

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Romiplostim

This study is designed to study Romiplostim for the treatment of chemotherapy-induced thrombocytopenia (CIT) in patients receiving chemotherapy for the treatment of gastrointestinal/colorectal/pancreatic cancer.

Intervention Type BIOLOGICAL

Placebo

Placebo Comparator

Intervention Type OTHER

Eligibility Criteria

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Inclusion Criteria

* Subject has provided informed consent prior to initiation of any study specific activities/procedures or subject's legally acceptable representative has provided informed consent prior to any study-specific activities/procedures being initiated when the subject has any kind of condition that, in the opinion of the investigator, may compromise the ability of the subject to give written informed consent.
* Males or females greater than or equal to 18 years of age at signing of the informed consent.
* Histologically or cytologically confirmed diagnosis of gastrointestinal, pancreatic, or colorectal adenocarcinoma, defined as cancers of the esophagus (including esophagogastric junction \[EGJ\] cancer), stomach, pancreas, colon, or rectum. Tumor stage will not affect eligibility.
* Subjects must be receiving 1 of the following regimens: An oxaliplatin-based chemotherapy regimen, containing 5 FU or capecitabine plus oxaliplatin (irinotecan may be added for FOLFIRINOX or FOLFOXIRI) on a 14- or 21 day schedule, respectively; OR, subjects must have chemotherapy-induced thrombocytopenia from a non-protocol chemotherapy regimen, planning to start treatment with one of the protocol chemotherapy regimens which has been delayed greater than or equal to one week due to chemotherapy-induced thrombocytopenia. Note: Use of these regimens are permitted with (1) anti angiogenic agents (such as bevacizumab) or (2) targeted therapy (such as anti epidermal growth factor receptor agents);
* Subjects must have a local platelet count ≤ 85 x 10\^9/L on study day 1.
* Subjects must be at least 14 days removed from the start of the chemotherapy cycle immediately prior to study day 1 if they received FOLFOX, FOLFIRINOX or FOLFOXIRI, and 21 days removed if they received CAPEOX.
* Subjects must have at least 3 remaining planned cycles of chemotherapy at study enrollment.
* Eastern Cooperative Oncology Group (ECOG) performance status of 0, 1, or 2.

Exclusion Criteria

Previous or Current Medical Conditions

* Acute lymphoblastic leukemia.
* Acute myeloid leukemia.
* Any myeloid malignancy.
* Myelodysplastic syndrome. Baseline bone marrow biopsy is not required to rule out MDS. However, if a bone marrow biopsy and cytogenetics were performed as part of diagnostic or staging work-up, these results will be collected to confirm.
* Myeloproliferative disease.
* Multiple myeloma.
* Within 4 months prior to enrollment, any history of active congestive heart failure (New York Heart Association \[NYHA\] Class III to IV), symptomatic ischemia, uncontrolled arrhythmias, clinically significant electrocardiogram (ECG) abnormalities, screening ECG with corrected QT (QTc) interval of \> 470 msec, pericardial disease, or myocardial infarction.
* Major surgery ≤ 28 days or minor surgery ≤ 3 days prior to enrollment.
* New or uncontrolled venous thromboembolism or thrombotic events within 3 months prior to screening. To be eligible, subjects must have received at least 14 days of anticoagulation for a new thrombotic event and considered to be both stable and suitable for continued therapeutic anticoagulation during trial participation.
* History of arterial thrombosis (eg, stroke or transient ischemic attack) within 6 months of screening.
* Evidence of active infection within 2 weeks prior to first dose of study treatment.
* Known human immunodeficiency virus infection. Subjects without a documented diagnosis in their medical history will require a local laboratory assessment at screening. If local laboratory results are not available, use central laboratory results.
* Known active chronic hepatitis B or C infection. Subjects without a documented diagnosis in their medical history will require a local laboratory assessment at screening. If local laboratory results are not available, use central laboratory results. Hepatitis B and C infection is based on the following results:
* Positive for hepatitis B surface antigen (HBsAg) (indicative of chronic hepatitis B or recent acute hepatitis B).
* Negative HBsAg and positive for hepatitis B core antibody: hepatitis B virus DNA by polymerase chain reaction (PCR) is necessary. Detectable hepatitis B virus DNA suggests occult hepatitis B.
* Positive Hepatitis C virus antibody (HCVAb): hepatitis C virus RNA by PCR is necessary. Detectable hepatitis C virus RNA suggests chronic hepatitis C.
* Secondary malignancy within the past 5 years except:
* Adequately treated non-melanoma skin cancer or lentigo maligna without evidence of disease.
* Adequately treated cervical carcinoma in situ without evidence of disease.
* Adequately treated breast ductal carcinoma in situ without evidence of disease.
* Prostatic intraepithelial neoplasia without evidence of prostate cancer.
* Adequately treated urothelial papillary noninvasive carcinoma or carcinoma in situ.
* Malignancy treated with curative intent and with no known active disease present for at least 3 years before enrollment and felt to be at low risk for recurrence by the treating physician
* Thrombocytopenia due to another etiology other than CIT (eg, chronic liver disease, prior history of immune thrombocytopenia purpura).

Prior/Concomitant Therapy

• Previous use of romiplostim, pegylated recombinant human megakaryocyte growth and development factor, eltrombopag, recombinant human TPO, any other TPO receptor agonist, or any investigational platelet producing agent.

Prior/Concurrent Clinical Study Experience • Currently receiving treatment in another investigational device or drug study, or less than 28 days since ending treatment on another investigational device or drug study(ies). Other investigational procedures while participating in this study are excluded.

Diagnostic Assessments

* Anemia (hemoglobin \<80 g/L \[8 g/dL\]) on the day of initiation of investigational product as assessed by local labs. Use of red cell transfusions and erythropoietic stimulating agents is permitted throughout the study as per institutional guidelines.
* Neutropenia (absolute neutrophil count 1 x 10\^9/L) on the day of initiation of investigational product as assessed by local labs. Use of granulocyte-colony stimulating factor is permitted throughout the study as per institutional guidelines.
* Abnormal renal function with creatinine clearance \< 30 mL/min using the Cockcroft-Gault estimated creatinine clearance as assessed by local laboratory during screening. If local laboratory results are not available, use central laboratory results.
* Abnormal liver function (total bilirubin \> 3 X ULN; alanine aminotransferase \[ALT\] or aspartate aminotransferase \[AST\] \> 3 X ULN for subjects without liver metastases or ≥ 5 X ULN for subjects with liver metastases) as assessed by local laboratory during screening. If local laboratory results are not available, use central laboratory results.

Other Exclusions

* Females who are pregnant or breastfeeding or planning to become pregnant or breastfeed during treatment and for an additional 6 months after treatment (and chemotherapy) discontinuation (females of childbearing potential should only be included after a confirmed menstrual period and a negative highly sensitive urine or serum pregnancy test.)
* Females of childbearing potential unwilling to use a highly effective method of contraception during treatment and for an additional 6 months after treatment (and chemotherapy) discontinuation.
* Males unwilling to use contraception\* (male condom or sexual abstinence) or their female partner(s) of childbearing potential who are unwilling to use a highly effective method of contraception during treatment (and chemotherapy) and for an additional 6 months after treatment (and chemotherapy) discontinuation.

\*If the male's sole partner is of non-childbearing potential, he is not required to use additional forms of contraception during the study.
* Subject has known sensitivity to any of the products to be administered during dosing.
* Subject likely to not be available to complete all protocol-required study visits or procedures, and/or to comply with all required study procedures (eg, COAs) to the best of the subject and investigator's knowledge.
* History or evidence of any other clinically significant disorder, condition or disease (with the exception of those outlined above) that, in the opinion of the investigator or Amgen physician, if consulted, would pose a risk to subject safety or interfere with the study evaluation, procedures or completion.
* Male subjects with a pregnant partner who are unwilling to practice abstinence or use a condom during treatment (and chemotherapy) and for an additional period of 6 months after treatment (and chemotherapy) discontinuation.
* Male subjects unwilling to abstain from donating sperm during treatment (and chemotherapy) and for an additional 6 months after treatment (and chemotherapy) discontinuation.
Minimum Eligible Age

18 Years

Maximum Eligible Age

100 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Amgen

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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MD

Role: STUDY_DIRECTOR

Amgen

Locations

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Saint Bernards Medical Center

Jonesboro, Arkansas, United States

Site Status

Pacific Cancer Medical Center Inc

Anaheim, California, United States

Site Status

University of California Irvine

Orange, California, United States

Site Status

Colorado West Healthcare System dba Grand Valley Oncology

Grand Junction, Colorado, United States

Site Status

Mid Florida Hematology and Oncology Centers PA

Orange City, Florida, United States

Site Status

Oncology and Hematology Associates of West Broward, PA

Tamarac, Florida, United States

Site Status

Cleveland Clinic Florida

Weston, Florida, United States

Site Status

Orchard Healthcare Research Inc

Skokie, Illinois, United States

Site Status

Christus Saint Frances Cabrini Hospital

Alexandria, Louisiana, United States

Site Status

University Medical Center New Orleans

New Orleans, Louisiana, United States

Site Status

Christus Highland Cancer Treatment Center

Shreveport, Louisiana, United States

Site Status

Mercy Medical Center

Baltimore, Maryland, United States

Site Status

American Oncology Partners, PA

Bethesda, Maryland, United States

Site Status

Massachusetts General Hospital Cancer Center

Boston, Massachusetts, United States

Site Status

Beth Israel Deaconess Medical Center

Boston, Massachusetts, United States

Site Status

Hattiesburg Clinic Hematology/Oncology

Hattiesburg, Mississippi, United States

Site Status

Oncology Hematology Associates

Springfield, Missouri, United States

Site Status

Morristown Medical Center

Morristown, New Jersey, United States

Site Status

Regional Cancer Care Associates

Sparta, New Jersey, United States

Site Status

The Center for Cancer and Blood Disorders

Fort Worth, Texas, United States

Site Status

Medical Oncology Associates PS

Spokane, Washington, United States

Site Status

Yakima Valley Memorial Hospital

Yakima, Washington, United States

Site Status

Hospital Universitario Fundacion Favaloro

Ciudad Autonoma de Buenos Aires, Buenos Aires, Argentina

Site Status

Instituto Oncologico Cordoba

Córdoba, Córdoba Province, Argentina

Site Status

Centro de Investigaciones Clínicas Clínica Viedma

Viedma, Río Negro Province, Argentina

Site Status

Centro de Diagnostico Investigacion y Tratamiento

Salta, , Argentina

Site Status

Landeskrankenhaus Steyr

Steyr, , Austria

Site Status

Universitaetsklinikum Allgemeines Krankenhaus Wien

Vienna, , Austria

Site Status

Instituto de Oncologia do Parana

Curitiba, Paraná, Brazil

Site Status

Vencer e Oncoclinica

Teresina, Piauí, Brazil

Site Status

Centro de Pesquisa da Serra Gaucha - Cepesg

Caxias do Sul, Rio Grande do Sul, Brazil

Site Status

Catarina Pesquisa Clinica

Itajaí, Santa Catarina, Brazil

Site Status

Loema Instituto de Pesquisa Clinica e Consultores Ltda

Campinas, São Paulo, Brazil

Site Status

Casa de Saude Santa Marcelina

São Paulo, São Paulo, Brazil

Site Status

Complex Oncology Center - Ruse EOOD

Rousse, , Bulgaria

Site Status

Medical Center Nadezhda Clinical EOOD

Sofia, , Bulgaria

Site Status

Specialized Hospital for Active Treatment of Oncology EAD

Sofia, , Bulgaria

Site Status

Cape Breton Cancer Centre, Nova Scotia Health Authority

Sydney, Nova Scotia, Canada

Site Status

Grand River Regional Cancer Centre at Grand River Hospital

Kitchener, Ontario, Canada

Site Status

Fundacion Colombiana de Cancerologia Clinica Vida

Medellín, Antioquia, Colombia

Site Status

Oncomedica Imat

Montería, Departamento de Córdoba, Colombia

Site Status

Centro Medico Imbanaco

Cali, Valle del Cauca Department, Colombia

Site Status

Centre Hospitalier Universitaire de Brest

Brest, , France

Site Status

Hôpital Européen Georges Pompidou

Paris, , France

Site Status

Hopital Foch

Suresnes, , France

Site Status

Institut Gustave Roussy

Villejuif, , France

Site Status

General Hospital of Athens Laiko

Athens, , Greece

Site Status

Aretaieio Hospital

Athens, , Greece

Site Status

Evgenidio Hospital I Agia Trias

Athens, , Greece

Site Status

Attikon University Hospital

Athens, , Greece

Site Status

General Oncology Hospital of Kifissia Agioi Anargyroi

Athens, , Greece

Site Status

University Hospital of Patras

Pátrai, , Greece

Site Status

Agios Loukas Clinic

Thessaloniki, , Greece

Site Status

Del-pesti Centrumkorhaz - Orszagos Hematologiai es Infektologiai Intezet

Budapest, , Hungary

Site Status

Debreceni Egyetem Klinikai Kozpont

Debrecen, , Hungary

Site Status

Gyor-Moson-Sopron Varmegyei Petz Aladar Egyetemi Oktatokorhaz

Győr, , Hungary

Site Status

Szegedi Tudomanyegyetem Szent-Gyorgyi Albert Klinikai Kozpont Altalanos Orvostudomanyi Kar

Szeged, , Hungary

Site Status

Azienda Socio Sanitaria Territoriale di Cremona

Cremona, , Italy

Site Status

Azienda Socio Sanitaria Territoriale Grande Ospedale Metropolitano Niguarda

Milan, , Italy

Site Status

Azienda Ospedaliera Citta della Salute e della Scienza di Torino Ospedale Molinette

Torino, , Italy

Site Status

Oncotech

La Paz, Baja California Sur, Mexico

Site Status

Centro de Atencion e Investigacion Cardiovascular del Potosi Sc

San Luis Potosí City, San Luis Potosí, Mexico

Site Status

Centro Medico Nacional Siglo XXI

México, , Mexico

Site Status

Oaxaca Site Management Organization SC

Oaxaca City, , Mexico

Site Status

Hospital Goyeneche

Arequipa, , Peru

Site Status

Oncosalud

Lima, , Peru

Site Status

Wojewodzki Szpital Specjalistyczny w Bialej Podlaskiej

Biała Podlaska, , Poland

Site Status

Powiatowe Centrum Zdrowia w Brzezinach Sp Z o o

Brzeziny, , Poland

Site Status

Uniwersytecki Szpital Kliniczny w Poznaniu

Poznan, , Poland

Site Status

Uniwersytecki Szpital Kliniczny w Poznaniu

Poznan, , Poland

Site Status

Centro Hospitalar Universitario de Lisboa Norte, EPE - Hospital de Santa Maria

Lisbon, , Portugal

Site Status

Unidade Local de Saude de Matosinhos, EPE - Hospital Pedro Hispano

Matosinhos Municipality, , Portugal

Site Status

Centro Hospitalar Universitario do Porto, EPE - Hospital de Santo Antonio

Porto, , Portugal

Site Status

Centro Hospitalar Universitario de Sao Joao, EPE - Hospital Sao Joao

Porto, , Portugal

Site Status

Centro Hospitalar Tras-os-Montes e Alto Douro EPE - Unidade de Vila Real

Vila Real, , Portugal

Site Status

Policlinica de Diagnostic Rapid

Brasov, , Romania

Site Status

Fundeni Clinical Institute for Digestive Disorders and Liver Transplantation

Bucharest, , Romania

Site Status

Spitalul Clinic al Cailor Ferate Cluj Napoca

Cluj-Napoca, , Romania

Site Status

SC Medisprof SRL

Cluj-Napoca, , Romania

Site Status

Centrul de Oncologie Sf Nectarie SRL

Craiova, , Romania

Site Status

Institutul Regional de Oncologie Iasi

Iași, , Romania

Site Status

SC Oncomed SRL

Timișoara, , Romania

Site Status

SBHI of Arkhangelsk region Arkhangelsk clinical oncology dispensary

Arkhangelsk, , Russia

Site Status

Autonomic SHI Republican clinical oncology dispensary of MoH of the Republic of Tatarstan

Kazan', , Russia

Site Status

Clinical hospital 2, Group of companies medsi

Moscow, , Russia

Site Status

Medsi Group

Moscow Region, , Russia

Site Status

LLC Tonus

Nizhny Novgorod, , Russia

Site Status

Omsk Regional Clinical Oncology Dispensary

Omsk, , Russia

Site Status

State budget institution of public health Pyatigorsk oncology dispensary

Pyatigorsk, , Russia

Site Status

State Institution of Public Health

Ryazan, , Russia

Site Status

Leningrad Regional Oncology Dispensary na L D Roman

Saint Petersburg, , Russia

Site Status

FSBI Scientific and Research Oncology Institute named after N N Petrov

Saint Petersburg, , Russia

Site Status

State Institution of Public Health Oncology Dispensary 2 of Public Health Krasnodar Region

Sochi, , Russia

Site Status

State Institution of Public Health Tambov Regional Oncology Dispensary

Tambov, , Russia

Site Status

Respublican clinical oncology dispensary Minzdrava of Republic of Bashkortostan

Ufa, , Russia

Site Status

Hospital Clinico Universitario San Cecilio

Granada, Andalusia, Spain

Site Status

Hospital Clinico Universitario de Salamanca

Salamanca, Castille and León, Spain

Site Status

Hospital Universitario Arnau de Vilanova Lleida

Lleida, Catalonia, Spain

Site Status

Hospital Universitari Sant Joan de Reus

Reus, Catalonia, Spain

Site Status

Complexo Hospitalario Universitario de Ourense

Ourense, Galicia, Spain

Site Status

Hospital Universitario Madrid Sanchinarro

Madrid, , Spain

Site Status

Baskent Universitesi Adana Doktor Turgut Noyan Uygulama ve Arastirma Merkezi

Adana, , Turkey (Türkiye)

Site Status

Doktor Abdurrahman Yurtaslan Ankara Onkoloji Egitim ve Arastirma Hastanesi

Ankara, , Turkey (Türkiye)

Site Status

Hacettepe Universitesi Tip Fakultesi

Ankara, , Turkey (Türkiye)

Site Status

Gazi Universitesi Saglik Arastirma ve Uygulama Merkezi Gazi Hastanesi

Ankara, , Turkey (Türkiye)

Site Status

Ankara Bilkent Sehir Hastanesi

Ankara, , Turkey (Türkiye)

Site Status

Trakya Universitesi Saglik Arastirma ve Uygulama Merkezi

Edirne, , Turkey (Türkiye)

Site Status

Istanbul Universitesi Onkoloji Enstitusu

Istanbul, , Turkey (Türkiye)

Site Status

Prof Dr Cemil Tascioglu Sehir Hastanesi

Istanbul, , Turkey (Türkiye)

Site Status

Goztepe Prof Dr Suleyman Yalcin Sehir Hastanesi

Istanbul, , Turkey (Türkiye)

Site Status

Ege Universitesi Tip Fakultesi

Izmir, , Turkey (Türkiye)

Site Status

Izmir Ekonomi Universitesi Medical Point Hastanesi

Izmir, , Turkey (Türkiye)

Site Status

Kocaeli Universitesi Arastirma ve Uygulama Hastanesi

Kocaeli, , Turkey (Türkiye)

Site Status

VM Medical Park Samsun Hastanesi

Samsun, , Turkey (Türkiye)

Site Status

Communal Institution Chernivtsi Regional Clinical Oncological Dispensary

Chernivtsi, , Ukraine

Site Status

Prykarpatskyy Clinical Oncology Centre

Ivano-Frankivsk, , Ukraine

Site Status

Transcarpathian Regional Clinical Oncological Dispensary

Uzhhorod, , Ukraine

Site Status

Countries

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United States Argentina Austria Brazil Bulgaria Canada Colombia France Greece Hungary Italy Mexico Peru Poland Portugal Romania Russia Spain Turkey (Türkiye) Ukraine

Related Links

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http://www.amgentrials.com

AmgenTrials clinical trials website

Other Identifiers

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2017-002992-25

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

20140346

Identifier Type: -

Identifier Source: org_study_id

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