Trial Outcomes & Findings for Impact of Statin Therapy on Muscle Mitochondrial Function and Aerobic Capacity (NCT NCT03351998)

NCT ID: NCT03351998

Last Updated: 2024-12-18

Results Overview

Recruitment status

COMPLETED

Study phase

PHASE4

Target enrollment

68 participants

Primary outcome timeframe

value at 12 months minus value at baseline

Results posted on

2024-12-18

Participant Flow

All 68 participants that were officially enrolled were randomized.

Participant milestones

Participant milestones
Measure
Placebo
Participants receiving matching placebo oral tablet. Placebo Oral Tablet: Matching placebo pill.
Low Dose Statin
Participants will receive Lipitor 20Mg Tablet to take daily. Lipitor 20Mg Tablet: 20 mg/day pills.
High Dose Statin
Participants will receive Lipitor 80Mg Tablet to take daily. Lipitor 80Mg Tablet: 80 mg/day pills.
Overall Study
STARTED
23
24
21
Overall Study
COMPLETED
16
19
17
Overall Study
NOT COMPLETED
7
5
4

Reasons for withdrawal

Withdrawal data not reported

Baseline Characteristics

Impact of Statin Therapy on Muscle Mitochondrial Function and Aerobic Capacity

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Placebo
n=23 Participants
Participants receiving matching placebo oral tablet. Placebo Oral Tablet: Matching placebo pill.
Low Dose Statin
n=24 Participants
Participants will receive Lipitor 20Mg Tablet to take daily. Lipitor 20Mg Tablet: 20 mg/day pills.
High Dose Statin
n=21 Participants
Participants will receive Lipitor 80Mg Tablet to take daily. Lipitor 80Mg Tablet: 80 mg/day pills.
Total
n=68 Participants
Total of all reporting groups
Age, Continuous
52.98 years
STANDARD_DEVIATION 8.28 • n=5 Participants
54.53 years
STANDARD_DEVIATION 7.66 • n=7 Participants
54.10 years
STANDARD_DEVIATION 7.14 • n=5 Participants
53.87 years
STANDARD_DEVIATION 7.64 • n=4 Participants
Sex: Female, Male
Female
16 Participants
n=5 Participants
17 Participants
n=7 Participants
16 Participants
n=5 Participants
49 Participants
n=4 Participants
Sex: Female, Male
Male
7 Participants
n=5 Participants
7 Participants
n=7 Participants
5 Participants
n=5 Participants
19 Participants
n=4 Participants
Race (NIH/OMB)
American Indian or Alaska Native
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
0 Participants
n=4 Participants
Race (NIH/OMB)
Asian
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
0 Participants
n=4 Participants
Race (NIH/OMB)
Native Hawaiian or Other Pacific Islander
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
0 Participants
n=4 Participants
Race (NIH/OMB)
Black or African American
2 Participants
n=5 Participants
1 Participants
n=7 Participants
3 Participants
n=5 Participants
6 Participants
n=4 Participants
Race (NIH/OMB)
White
20 Participants
n=5 Participants
23 Participants
n=7 Participants
16 Participants
n=5 Participants
59 Participants
n=4 Participants
Race (NIH/OMB)
More than one race
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
0 Participants
n=4 Participants
Race (NIH/OMB)
Unknown or Not Reported
1 Participants
n=5 Participants
0 Participants
n=7 Participants
2 Participants
n=5 Participants
3 Participants
n=4 Participants
Region of Enrollment
United States
23 participants
n=5 Participants
24 participants
n=7 Participants
21 participants
n=5 Participants
68 participants
n=4 Participants
Total Cholesterol
199.65 mg/dL
STANDARD_DEVIATION 38.82 • n=5 Participants
211.75 mg/dL
STANDARD_DEVIATION 41.68 • n=7 Participants
214.33 mg/dL
STANDARD_DEVIATION 33.53 • n=5 Participants
208 mg/dL
STANDARD_DEVIATION 38.32 • n=4 Participants
Weight
93.79 kg
STANDARD_DEVIATION 13.89 • n=5 Participants
90.60 kg
STANDARD_DEVIATION 15.87 • n=7 Participants
89.28 kg
STANDARD_DEVIATION 15.22 • n=5 Participants
91.27 kg
STANDARD_DEVIATION 14.92 • n=4 Participants
BMI
32.96 kg/m^2
STANDARD_DEVIATION 4.55 • n=5 Participants
31.14 kg/m^2
STANDARD_DEVIATION 3.74 • n=7 Participants
32.31 kg/m^2
STANDARD_DEVIATION 4.98 • n=5 Participants
32.12 kg/m^2
STANDARD_DEVIATION 4.43 • n=4 Participants
Relative Peak VO2 Max
24.12 mL/kg/min
STANDARD_DEVIATION 5.7 • n=5 Participants
25.53 mL/kg/min
STANDARD_DEVIATION 6.97 • n=7 Participants
24.92 mL/kg/min
STANDARD_DEVIATION 5.12 • n=5 Participants
24.87 mL/kg/min
STANDARD_DEVIATION 5.96 • n=4 Participants

PRIMARY outcome

Timeframe: value at 12 months minus value at baseline

Outcome measures

Outcome measures
Measure
Placebo
n=16 Participants
Participants receiving matching placebo oral tablet. Placebo Oral Tablet: Matching placebo pill.
Low Dose Statin
n=17 Participants
Participants will receive Lipitor 20Mg Tablet to take daily. Lipitor 20Mg Tablet: 20 mg/day pills.
High Dose Statin
n=16 Participants
Participants will receive Lipitor 80Mg Tablet to take daily. Lipitor 80Mg Tablet: 80 mg/day pills.
Difference in Mitochondrial Respiratory Function
36 pmols/s/mg
Standard Deviation 366
32 pmols/s/mg
Standard Deviation 213
-3 pmols/s/mg
Standard Deviation 180

SECONDARY outcome

Timeframe: value at 12 months minus value at baseline

Outcome measures

Outcome measures
Measure
Placebo
n=15 Participants
Participants receiving matching placebo oral tablet. Placebo Oral Tablet: Matching placebo pill.
Low Dose Statin
n=18 Participants
Participants will receive Lipitor 20Mg Tablet to take daily. Lipitor 20Mg Tablet: 20 mg/day pills.
High Dose Statin
n=17 Participants
Participants will receive Lipitor 80Mg Tablet to take daily. Lipitor 80Mg Tablet: 80 mg/day pills.
Change in VO2 Max
-0.2 L/min
Standard Deviation 0.23
0.03 L/min
Standard Deviation 0.16
-0.06 L/min
Standard Deviation 0.18

Adverse Events

Placebo

Serious events: 1 serious events
Other events: 15 other events
Deaths: 0 deaths

Low Dose Statin

Serious events: 0 serious events
Other events: 17 other events
Deaths: 0 deaths

High Dose Statin

Serious events: 0 serious events
Other events: 14 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
Placebo
n=23 participants at risk
Participants receiving matching placebo oral tablet. Placebo Oral Tablet: Matching placebo pill.
Low Dose Statin
n=24 participants at risk
Participants will receive Lipitor 20Mg Tablet to take daily. Lipitor 20Mg Tablet: 20 mg/day pills.
High Dose Statin
n=21 participants at risk
Participants will receive Lipitor 80Mg Tablet to take daily. Lipitor 80Mg Tablet: 80 mg/day pills.
Cardiac disorders
Cardiovascular event (SVT) unrelated to intervention
4.3%
1/23 • Number of events 1 • Participants were contacted weekly by phone or email and prompted to disclose any adverse events. Additional adverse events could be reported if participant contacted study team outside of the usual weekly check in. Adverse events were monitored until symptoms subsided or adverse event ended or until the end of the 12 month intervention period.
The definitions used for adverse events and/or serious adverse events are the same as clinicaltrials.gov definitions
0.00%
0/24 • Participants were contacted weekly by phone or email and prompted to disclose any adverse events. Additional adverse events could be reported if participant contacted study team outside of the usual weekly check in. Adverse events were monitored until symptoms subsided or adverse event ended or until the end of the 12 month intervention period.
The definitions used for adverse events and/or serious adverse events are the same as clinicaltrials.gov definitions
0.00%
0/21 • Participants were contacted weekly by phone or email and prompted to disclose any adverse events. Additional adverse events could be reported if participant contacted study team outside of the usual weekly check in. Adverse events were monitored until symptoms subsided or adverse event ended or until the end of the 12 month intervention period.
The definitions used for adverse events and/or serious adverse events are the same as clinicaltrials.gov definitions

Other adverse events

Other adverse events
Measure
Placebo
n=23 participants at risk
Participants receiving matching placebo oral tablet. Placebo Oral Tablet: Matching placebo pill.
Low Dose Statin
n=24 participants at risk
Participants will receive Lipitor 20Mg Tablet to take daily. Lipitor 20Mg Tablet: 20 mg/day pills.
High Dose Statin
n=21 participants at risk
Participants will receive Lipitor 80Mg Tablet to take daily. Lipitor 80Mg Tablet: 80 mg/day pills.
Respiratory, thoracic and mediastinal disorders
COVID-19
13.0%
3/23 • Number of events 4 • Participants were contacted weekly by phone or email and prompted to disclose any adverse events. Additional adverse events could be reported if participant contacted study team outside of the usual weekly check in. Adverse events were monitored until symptoms subsided or adverse event ended or until the end of the 12 month intervention period.
The definitions used for adverse events and/or serious adverse events are the same as clinicaltrials.gov definitions
12.5%
3/24 • Number of events 3 • Participants were contacted weekly by phone or email and prompted to disclose any adverse events. Additional adverse events could be reported if participant contacted study team outside of the usual weekly check in. Adverse events were monitored until symptoms subsided or adverse event ended or until the end of the 12 month intervention period.
The definitions used for adverse events and/or serious adverse events are the same as clinicaltrials.gov definitions
0.00%
0/21 • Participants were contacted weekly by phone or email and prompted to disclose any adverse events. Additional adverse events could be reported if participant contacted study team outside of the usual weekly check in. Adverse events were monitored until symptoms subsided or adverse event ended or until the end of the 12 month intervention period.
The definitions used for adverse events and/or serious adverse events are the same as clinicaltrials.gov definitions
Renal and urinary disorders
UTI
8.7%
2/23 • Number of events 2 • Participants were contacted weekly by phone or email and prompted to disclose any adverse events. Additional adverse events could be reported if participant contacted study team outside of the usual weekly check in. Adverse events were monitored until symptoms subsided or adverse event ended or until the end of the 12 month intervention period.
The definitions used for adverse events and/or serious adverse events are the same as clinicaltrials.gov definitions
0.00%
0/24 • Participants were contacted weekly by phone or email and prompted to disclose any adverse events. Additional adverse events could be reported if participant contacted study team outside of the usual weekly check in. Adverse events were monitored until symptoms subsided or adverse event ended or until the end of the 12 month intervention period.
The definitions used for adverse events and/or serious adverse events are the same as clinicaltrials.gov definitions
0.00%
0/21 • Participants were contacted weekly by phone or email and prompted to disclose any adverse events. Additional adverse events could be reported if participant contacted study team outside of the usual weekly check in. Adverse events were monitored until symptoms subsided or adverse event ended or until the end of the 12 month intervention period.
The definitions used for adverse events and/or serious adverse events are the same as clinicaltrials.gov definitions
Gastrointestinal disorders
GI Upset
8.7%
2/23 • Number of events 2 • Participants were contacted weekly by phone or email and prompted to disclose any adverse events. Additional adverse events could be reported if participant contacted study team outside of the usual weekly check in. Adverse events were monitored until symptoms subsided or adverse event ended or until the end of the 12 month intervention period.
The definitions used for adverse events and/or serious adverse events are the same as clinicaltrials.gov definitions
12.5%
3/24 • Number of events 3 • Participants were contacted weekly by phone or email and prompted to disclose any adverse events. Additional adverse events could be reported if participant contacted study team outside of the usual weekly check in. Adverse events were monitored until symptoms subsided or adverse event ended or until the end of the 12 month intervention period.
The definitions used for adverse events and/or serious adverse events are the same as clinicaltrials.gov definitions
14.3%
3/21 • Number of events 3 • Participants were contacted weekly by phone or email and prompted to disclose any adverse events. Additional adverse events could be reported if participant contacted study team outside of the usual weekly check in. Adverse events were monitored until symptoms subsided or adverse event ended or until the end of the 12 month intervention period.
The definitions used for adverse events and/or serious adverse events are the same as clinicaltrials.gov definitions
Musculoskeletal and connective tissue disorders
Muscle or Joint Pain
26.1%
6/23 • Number of events 6 • Participants were contacted weekly by phone or email and prompted to disclose any adverse events. Additional adverse events could be reported if participant contacted study team outside of the usual weekly check in. Adverse events were monitored until symptoms subsided or adverse event ended or until the end of the 12 month intervention period.
The definitions used for adverse events and/or serious adverse events are the same as clinicaltrials.gov definitions
33.3%
8/24 • Number of events 9 • Participants were contacted weekly by phone or email and prompted to disclose any adverse events. Additional adverse events could be reported if participant contacted study team outside of the usual weekly check in. Adverse events were monitored until symptoms subsided or adverse event ended or until the end of the 12 month intervention period.
The definitions used for adverse events and/or serious adverse events are the same as clinicaltrials.gov definitions
28.6%
6/21 • Number of events 7 • Participants were contacted weekly by phone or email and prompted to disclose any adverse events. Additional adverse events could be reported if participant contacted study team outside of the usual weekly check in. Adverse events were monitored until symptoms subsided or adverse event ended or until the end of the 12 month intervention period.
The definitions used for adverse events and/or serious adverse events are the same as clinicaltrials.gov definitions
Investigations
Adverse event related to testing for study
8.7%
2/23 • Number of events 2 • Participants were contacted weekly by phone or email and prompted to disclose any adverse events. Additional adverse events could be reported if participant contacted study team outside of the usual weekly check in. Adverse events were monitored until symptoms subsided or adverse event ended or until the end of the 12 month intervention period.
The definitions used for adverse events and/or serious adverse events are the same as clinicaltrials.gov definitions
20.8%
5/24 • Number of events 6 • Participants were contacted weekly by phone or email and prompted to disclose any adverse events. Additional adverse events could be reported if participant contacted study team outside of the usual weekly check in. Adverse events were monitored until symptoms subsided or adverse event ended or until the end of the 12 month intervention period.
The definitions used for adverse events and/or serious adverse events are the same as clinicaltrials.gov definitions
9.5%
2/21 • Number of events 2 • Participants were contacted weekly by phone or email and prompted to disclose any adverse events. Additional adverse events could be reported if participant contacted study team outside of the usual weekly check in. Adverse events were monitored until symptoms subsided or adverse event ended or until the end of the 12 month intervention period.
The definitions used for adverse events and/or serious adverse events are the same as clinicaltrials.gov definitions
Respiratory, thoracic and mediastinal disorders
Sinus Infection/Flu Symptoms
0.00%
0/23 • Participants were contacted weekly by phone or email and prompted to disclose any adverse events. Additional adverse events could be reported if participant contacted study team outside of the usual weekly check in. Adverse events were monitored until symptoms subsided or adverse event ended or until the end of the 12 month intervention period.
The definitions used for adverse events and/or serious adverse events are the same as clinicaltrials.gov definitions
12.5%
3/24 • Number of events 3 • Participants were contacted weekly by phone or email and prompted to disclose any adverse events. Additional adverse events could be reported if participant contacted study team outside of the usual weekly check in. Adverse events were monitored until symptoms subsided or adverse event ended or until the end of the 12 month intervention period.
The definitions used for adverse events and/or serious adverse events are the same as clinicaltrials.gov definitions
14.3%
3/21 • Number of events 3 • Participants were contacted weekly by phone or email and prompted to disclose any adverse events. Additional adverse events could be reported if participant contacted study team outside of the usual weekly check in. Adverse events were monitored until symptoms subsided or adverse event ended or until the end of the 12 month intervention period.
The definitions used for adverse events and/or serious adverse events are the same as clinicaltrials.gov definitions

Additional Information

John P. Thyfault

University of Kansas Medical Center

Phone: 913-588-1790

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place