Study to Evaluate Efficacy and Safety of PF-04965842 in Subjects Aged 12 Years And Older With Moderate to Severe Atopic Dermatitis

NCT ID: NCT03349060

Last Updated: 2019-12-10

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

387 participants

Study Classification

INTERVENTIONAL

Study Start Date

2017-12-07

Study Completion Date

2019-03-26

Brief Summary

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B7451012 is a Phase 3 study to evaluate PF-04965842 in patients aged 12 years and older with a minimum body weight of 40 kg who have moderate to severe atopic dermatitis. The efficacy and safety of two dosage strengths of PF-04965842, 100 mg and 200 mg taken orally once daily, will be evaluated relative to placebo over 12 weeks of study participation. Eligible patients will have an option to enter a long-term extension study after completing 12 weeks of treatment.

Detailed Description

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Conditions

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Dermatitis, Atopic

Keywords

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atopic dermatitis atopic eczema eczema JAK janus kinase

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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PF-04965842 100 mg

Group Type EXPERIMENTAL

PF-04965842 100 mg

Intervention Type DRUG

PF-04965842 100 mg, administered as two tablets to be taken orally once daily for 12 weeks

PF-04965842 200 mg

Group Type EXPERIMENTAL

PF-04965842 200 mg

Intervention Type DRUG

PF-04965842 200 mg, administered as two tablets to be taken orally once daily for 12 weeks

Placebo

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Placebo, administered as two tablets to be taken orally once daily for 12 weeks

Interventions

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PF-04965842 100 mg

PF-04965842 100 mg, administered as two tablets to be taken orally once daily for 12 weeks

Intervention Type DRUG

PF-04965842 200 mg

PF-04965842 200 mg, administered as two tablets to be taken orally once daily for 12 weeks

Intervention Type DRUG

Placebo

Placebo, administered as two tablets to be taken orally once daily for 12 weeks

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* 12 years of age or older with a minimum body weight of 40 kg
* Diagnosis of atopic dermatitis (AD) for at least 1 year and current status of moderate to severe disease (\>= the following scores: BSA 10%, IGA 3, EASI 16, Pruritus NRS 4)
* Recent history of inadequate response or inability to tolerate topical AD treatments or require systemic treatments for AD control

Exclusion Criteria

* Unwilling to discontinue current AD medications prior to the study or require treatment with prohibited medications during the study
* Prior treatment with JAK inhibitors
* Other active nonAD inflammatory skin diseases or conditions affecting skin
* Medical history including thrombocytopenia, coagulopathy or platelet dysfunction, Q wave interval abnormalities, current or history of certain infections, cancer, lymphoproliferative disorders and other medical conditions at the discretion of the investigator
* Pregnant or breastfeeding women, or women of childbearing potential who are unwilling to use contraception
Minimum Eligible Age

12 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Pfizer

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Pfizer CT.gov Call Center

Role: STUDY_DIRECTOR

Pfizer

Locations

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Clinical Research Center of Alabama, LLC

Birmingham, Alabama, United States

Site Status

California Dermatology & Clinical Research Institute

Encinitas, California, United States

Site Status

Rady Children's Hospital - San Diego/University of California, San Diego

San Diego, California, United States

Site Status

TCR Medical Corporation

San Diego, California, United States

Site Status

Clinical Science Institute

Santa Monica, California, United States

Site Status

Florida Academic Centers Research and Education, LLC

Coral Gables, Florida, United States

Site Status

Olympian Clinical Research

Largo, Florida, United States

Site Status

Forward Clinical Trials, Inc.

Tampa, Florida, United States

Site Status

Meridian Clinical Research, LLC

Savannah, Georgia, United States

Site Status

NorthShore University HealthSystem Dermatology Clinical Trials Unit

Skokie, Illinois, United States

Site Status

Dawes Fretzin Clinical Research Group, LLC

Indianapolis, Indiana, United States

Site Status

Dawes Fretzin Dermatology Group, LLC

Indianapolis, Indiana, United States

Site Status

Tufts Medical Center

Boston, Massachusetts, United States

Site Status

Henry Ford Medical Center, New Center One

Detroit, Michigan, United States

Site Status

Somerset Skin Centre

Troy, Michigan, United States

Site Status

MediSearch Clinical Trials

Saint Joseph, Missouri, United States

Site Status

Lynn Health Science Institute

Oklahoma City, Oklahoma, United States

Site Status

Vital Prospects Clinical Research Institute, P.C.

Tulsa, Oklahoma, United States

Site Status

Oregon Health & Science University

Portland, Oregon, United States

Site Status

Medical University of South Carolina Investigational Drug Services

Charleston, South Carolina, United States

Site Status

MUSC SCTR Research Nexus Clinic and Laboratory

Charleston, South Carolina, United States

Site Status

Arlington Research Center, Inc.

Arlington, Texas, United States

Site Status

The University of Texas Health Science Center Houston

Houston, Texas, United States

Site Status

Texas Dermatology and Laser Specialists

San Antonio, Texas, United States

Site Status

Virginia Clinical Research, Inc.

Norfolk, Virginia, United States

Site Status

Pace Dermatology Associates

Lakewood, Washington, United States

Site Status

MultiCare Allenmore Hospital

Tacoma, Washington, United States

Site Status

MultiCare Institute for Research and Innovation

Tacoma, Washington, United States

Site Status

Pace Dermatology Associates

Tacoma, Washington, United States

Site Status

Australian Clinical Research Network (ACRN)

Maroubra, New South Wales, Australia

Site Status

Spectrum Medical Imaging

Maroubra, New South Wales, Australia

Site Status

Queensland X-Ray

Upper Mount Gravatt, Queensland, Australia

Site Status

Veracity Clinical Research Pty Ltd

Woolloongabba, Queensland, Australia

Site Status

Emeritus Research

Camberwell, Victoria, Australia

Site Status

Skin and Cancer Foundation Inc

Carlton, Victoria, Australia

Site Status

Melbourne Radiology Clinic

East Melbourne, Victoria, Australia

Site Status

Sinclair Dermatology

East Melbourne, Victoria, Australia

Site Status

The Royal Children's Hospital

Parkville, Victoria, Australia

Site Status

Bridge Road Imaging

Richmond, Victoria, Australia

Site Status

Kirk Barber Research

Calgary, Alberta, Canada

Site Status

Institute for Skin Advancement

Calgary, Alberta, Canada

Site Status

Dr. Chih-ho Hong Medical Inc

Surrey, British Columbia, Canada

Site Status

University of British Columbia Department of Dermatology and Skin Science

Vancouver, British Columbia, Canada

Site Status

Wiseman Dermatology Research Inc.

Winnipeg, Manitoba, Canada

Site Status

Lynderm Research Inc

Markham, Ontario, Canada

Site Status

SKiN Centre for Dermatology

Peterborough, Ontario, Canada

Site Status

The Centre for Dermatology

Richmond Hill, Ontario, Canada

Site Status

York Dermatology Center

Richmond Hill, Ontario, Canada

Site Status

Research Toronto

Toronto, Ontario, Canada

Site Status

Innovaderm Research Inc.

Montreal, Quebec, Canada

Site Status

Diex Research Sherbrooke Inc.

Sherbrooke, Quebec, Canada

Site Status

Lekarna Na Vaclavskem namesti

Kutná Hora, , Czechia

Site Status

Kozni ambulance Kutna Hora, s.r.o.

Kutná Hora, , Czechia

Site Status

Lekarna Fakultni Nemocnice Ostrava

Ostrava - Poruba, , Czechia

Site Status

Fakultni Nemocnice Ostrava, Kozni oddeleni

Ostrava - Poruba, , Czechia

Site Status

Sanatorium profesora Arenbergera

Prague, , Czechia

Site Status

Lekarna U sv. Ignace

Prague, , Czechia

Site Status

Krajska zdravotni a.s.,Masarykova nemocnice o.z.

Ústí nad Labem, , Czechia

Site Status

Lekarna Masarykovy nemocnice v Usti nad Labem, o.z.

Ústí nad Labem, , Czechia

Site Status

Universitaetsklinikum Schleswig-Holstein/Campus Luebeck

Lübeck, Schleswig-Holstein, Germany

Site Status

Fachklinik Bad Bentheim

Bad Bentheim, , Germany

Site Status

Charité - Universitaetsmedizin Berlin, CCM

Berlin, , Germany

Site Status

ISA - Interdisciplinary Study Association GmbH

Berlin, , Germany

Site Status

Universitaetsklinikum Carl Gustav Carus der Technischen Universitaet Dresden

Dresden, , Germany

Site Status

Universitätsklinikum Erlangen, Hautklinik

Erlangen, , Germany

Site Status

Universitaetsklinikum Schleswig-Holstein, Campus Kiel

Kiel, , Germany

Site Status

Ludwig-Maximilians-University Munich

Munich, , Germany

Site Status

Universitätsklinikum Münster

Münster, , Germany

Site Status

Klinische Forschung Schwerin GmbH

Schwerin, , Germany

Site Status

Bács-Kiskun Megyei Kórház, Bőr-és nemibeteg Szakrendelés

Kecskemét, Bács-Kiskun county, Hungary

Site Status

Debreceni Egyetem Klinikai Kozpont Borgyogyaszati Klinika

Debrecen, , Hungary

Site Status

Bacs-Kiskun Megyei Korhaz Kozponti Radiologiai Osztaly

Kecskemét, , Hungary

Site Status

CRU Hungary Ltd.

Miskolc, , Hungary

Site Status

Pecsi Tudomanyegyetem Klinikai Kozpont, Bor-,Nemikortani es Onkodermatologiai Klinika

Pécs, , Hungary

Site Status

Pecsi Tudomanyegyetem Klinikai Kozpont

Pécs, , Hungary

Site Status

MULTIKLINIKA Salute Sp. z o.o.

Katowice, , Poland

Site Status

Silmedic Sp. z o.o., Oddzial w Katowicach

Katowice, , Poland

Site Status

Centrum Medyczne Angelius Provita

Katowice, , Poland

Site Status

Pro Familia Altera Sp. z o.o.

Katowice, , Poland

Site Status

NZOZ "DERMED" Centrum Medyczne Sp. z o.o. - Oddzial w Lodzi

Lodz, , Poland

Site Status

Dermoklinika Centrum Medyczne s.c., M. Kierstan, J. Narbutt, A. Lesiak

Lodz, , Poland

Site Status

Dermedic Jacek Zdybski

Ostrowiec Świętokrzyski, , Poland

Site Status

Wojskowy Instytut Medyczny, Klinika Dermatologiczna

Warsaw, , Poland

Site Status

Derriford Hospital, Plymouth Hospitals NHS Trust

Plymouth, Devon, United Kingdom

Site Status

Royal Free London NHS Foundation Trust

London, Greater London, United Kingdom

Site Status

Sheffield Teaching Hospitals NHS Foundation Trust

Sheffield, South Yorkshire, England, United Kingdom

Site Status

Sheffield Children's Hospital NHS Foundation Trust

Sheffield, South Yorkshire, United Kingdom

Site Status

The Dudley Group NHS Foundation Trust

Dudley, , United Kingdom

Site Status

Countries

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United States Australia Canada Czechia Germany Hungary Poland United Kingdom

References

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Paller AS, Eichenfield LF, Irvine AD, Flohr C, Wollenberg A, Barbarot S, Bangert C, Spergel JM, Selfridge A, Biswas P, Fan H, Alderfer J, Watkins M, Koppensteiner H. Integrated Efficacy and Safety Analysis of Abrocitinib in Adolescents With Moderate-to-Severe Atopic Dermatitis. Allergy. 2025 Aug;80(8):2213-2224. doi: 10.1111/all.16512. Epub 2025 Mar 3.

Reference Type DERIVED
PMID: 40028832 (View on PubMed)

Silverberg JI, Thyssen JP, Lazariciu I, Myers DE, Guler E, Chovatiya R. Abrocitinib may improve itch and quality of life in patients with itch-dominant atopic dermatitis. Skin Health Dis. 2024 May 5;4(4):e382. doi: 10.1002/ski2.382. eCollection 2024 Aug.

Reference Type DERIVED
PMID: 39104653 (View on PubMed)

Armstrong AW, Alexis AF, Blauvelt A, Silverberg JI, Feeney C, Levenberg M, Chan G, Zhang F, Fostvedt L. Predicting Abrocitinib Efficacy at Week 12 Based on Clinical Response at Week 4: A Post Hoc Analysis of Four Randomized Studies in Moderate-to-Severe Atopic Dermatitis. Dermatol Ther (Heidelb). 2024 Jul;14(7):1849-1861. doi: 10.1007/s13555-024-01183-3. Epub 2024 Jun 19.

Reference Type DERIVED
PMID: 38896380 (View on PubMed)

Schmid-Grendelmeier P, Gooderham MJ, Hartmann K, Konstantinou GN, Fellmann M, Koulias C, Clibborn C, Biswas P, Brunner PM. Efficacy and safety of abrocitinib in patients with moderate-to-severe atopic dermatitis and comorbid allergies. Allergy. 2024 Jan;79(1):174-183. doi: 10.1111/all.15952. Epub 2023 Nov 21.

Reference Type DERIVED
PMID: 37988255 (View on PubMed)

Alexis AF, Silverberg JI, Rice ZP, Armstrong AW, Desai SR, Fonacier L, Kabashima K, Biswas P, Cella RR, Chan GL, Levenberg M. Abrocitinib efficacy and safety in moderate-to-severe atopic dermatitis by race, ethnicity, and Fitzpatrick skin type. Ann Allergy Asthma Immunol. 2024 Mar;132(3):383-389.e3. doi: 10.1016/j.anai.2023.11.002. Epub 2023 Nov 10.

Reference Type DERIVED
PMID: 37949351 (View on PubMed)

Blauvelt A, Boguniewicz M, Brunner PM, Luna PC, Biswas P, DiBonaventura M, Farooqui SA, Rojo R, Cameron MC. Abrocitinib monotherapy in Investigator's Global Assessment nonresponders: improvement in signs and symptoms of atopic dermatitis and quality of life. J Dermatolog Treat. 2022 Aug;33(5):2605-2613. doi: 10.1080/09546634.2022.2059053. Epub 2022 Jul 6.

Reference Type DERIVED
PMID: 35763326 (View on PubMed)

Stander S, Bhatia N, Gooderham MJ, Silverberg JI, Thyssen JP, Biswas P, DiBonaventura M, Romero W, Farooqui SA. High threshold efficacy responses in moderate-to-severe atopic dermatitis are associated with additional quality of life benefits: pooled analyses of abrocitinib monotherapy studies in adults and adolescents. J Eur Acad Dermatol Venereol. 2022 Aug;36(8):1308-1317. doi: 10.1111/jdv.18170. Epub 2022 May 6.

Reference Type DERIVED
PMID: 35462428 (View on PubMed)

Wojciechowski J, Malhotra BK, Wang X, Fostvedt L, Valdez H, Nicholas T. Population pharmacokinetic-pharmacodynamic modelling of platelet time-courses following administration of abrocitinib. Br J Clin Pharmacol. 2022 Aug;88(8):3856-3871. doi: 10.1111/bcp.15334. Epub 2022 Apr 11.

Reference Type DERIVED
PMID: 35342978 (View on PubMed)

Wojciechowski J, Malhotra BK, Wang X, Fostvedt L, Valdez H, Nicholas T. Population Pharmacokinetics of Abrocitinib in Healthy Individuals and Patients with Psoriasis or Atopic Dermatitis. Clin Pharmacokinet. 2022 May;61(5):709-723. doi: 10.1007/s40262-021-01104-z. Epub 2022 Jan 21.

Reference Type DERIVED
PMID: 35061234 (View on PubMed)

Cork MJ, McMichael A, Teng J, Valdez H, Rojo R, Chan G, Zhang F, Myers DE, DiBonaventura M. Impact of oral abrocitinib on signs, symptoms and quality of life among adolescents with moderate-to-severe atopic dermatitis: an analysis of patient-reported outcomes. J Eur Acad Dermatol Venereol. 2022 Mar;36(3):422-433. doi: 10.1111/jdv.17792. Epub 2021 Dec 4.

Reference Type DERIVED
PMID: 34743361 (View on PubMed)

Simpson EL, Silverberg JI, Nosbaum A, Winthrop KL, Guttman-Yassky E, Hoffmeister KM, Egeberg A, Valdez H, Zhang M, Farooqui SA, Romero W, Thorpe AJ, Rojo R, Johnson S. Integrated Safety Analysis of Abrocitinib for the Treatment of Moderate-to-Severe Atopic Dermatitis From the Phase II and Phase III Clinical Trial Program. Am J Clin Dermatol. 2021 Sep;22(5):693-707. doi: 10.1007/s40257-021-00618-3. Epub 2021 Aug 18.

Reference Type DERIVED
PMID: 34406619 (View on PubMed)

Silverberg JI, Thyssen JP, Simpson EL, Yosipovitch G, Stander S, Valdez H, Rojo R, Biswas P, Myers DE, Feeney C, DiBonaventura M. Impact of Oral Abrocitinib Monotherapy on Patient-Reported Symptoms and Quality of Life in Adolescents and Adults with Moderate-to-Severe Atopic Dermatitis: A Pooled Analysis of Patient-Reported Outcomes. Am J Clin Dermatol. 2021 Jul;22(4):541-554. doi: 10.1007/s40257-021-00604-9. Epub 2021 May 5.

Reference Type DERIVED
PMID: 33954933 (View on PubMed)

Simpson EL, Sinclair R, Forman S, Wollenberg A, Aschoff R, Cork M, Bieber T, Thyssen JP, Yosipovitch G, Flohr C, Magnolo N, Maari C, Feeney C, Biswas P, Tatulych S, Valdez H, Rojo R. Efficacy and safety of abrocitinib in adults and adolescents with moderate-to-severe atopic dermatitis (JADE MONO-1): a multicentre, double-blind, randomised, placebo-controlled, phase 3 trial. Lancet. 2020 Jul 25;396(10246):255-266. doi: 10.1016/S0140-6736(20)30732-7.

Reference Type DERIVED
PMID: 32711801 (View on PubMed)

Provided Documents

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Document Type: Statistical Analysis Plan

View Document

Document Type: Study Protocol

View Document

Related Links

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https://pmiform.com/clinical-trial-info-request?StudyID=B7451012

To obtain contact information for a study center near you, click here.

Other Identifiers

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2017-003651-29

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

MONO-1

Identifier Type: OTHER

Identifier Source: secondary_id

JADE MONO-1

Identifier Type: OTHER

Identifier Source: secondary_id

B7451012

Identifier Type: -

Identifier Source: org_study_id