A Study of Paliperidone Palmitate 6-Month Formulation

NCT ID: NCT03345342

Last Updated: 2025-04-29

Study Results

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

841 participants

Study Classification

INTERVENTIONAL

Study Start Date

2017-11-20

Study Completion Date

2020-05-08

Brief Summary

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The purpose of this study is to demonstrate that injection cycles consisting of a single administration of paliperidone palmitate 6-month (PP6M) are not less effective than 2 sequentially administered injections of paliperidone palmitate 3-month PP3M) (350 or 525 mg eq.) for the prevention of relapse in participants with schizophrenia previously stabilized on corresponding doses of paliperidone palmitate 1-month (PP1M) (100 or 150 mg eq.) or PP3M (350 or 525 mg eq.).

Detailed Description

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The primary hypothesis of this study is that the efficacy of PP6M is non-inferior to PP3M for preventing relapse in participants with schizophrenia who were previously stabilized on corresponding doses of PP1M or PP3M. The study consists of mainly 3 phases: a screening phase (up to 28 days), a maintenance phase (of 1 or 3 months), and a double-blind phase (of 12 months \[neither the researchers nor the participants know what treatment the participant is receiving\]). Additional/conditional phases include a transition phase (before maintenance phase). Study evaluations include efficacy, pharmacokinetics, pharmacodynamics, and safety. The study duration will vary from approximately 13 months to 19 months.

Conditions

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Schizophrenia

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Investigators

Study Groups

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PP1M: Transition Phase

Participants who previously have not achieved stability with moderate to higher doses of Paliperidone palmitate 1-month (PP1M) or Paliperidone palmitate 3-month (PP3M) will enter into a transition period of up to 4 months. During transition period participants will receive 1 to 5 injections of PP1M 50 to 100 milligrams equivalent (mg eq.). The participants who achieved stability (stability is defined as at least 3 months of injections with the last 2 doses being the same strength) with PP1M 100 mg eq. will precede from transition phase to maintenance phase.

Group Type EXPERIMENTAL

PP1M

Intervention Type DRUG

Participants will receive intramuscular injection of PP1M 50 to 150 mg eq.

PP1M/PP3M: Maintenance Phase

All the participants will receive only 1 dose of PP1M 100 or 150 mg eq. or PP3M 350 or 525 mg eq. The participants will precede from maintenance phase to double-blind phase.

Group Type EXPERIMENTAL

PP3M 350 mg eq.

Intervention Type DRUG

Participants will receive intramuscular injection of PP3M 350 mg eq.

PP3M 525 mg eq.

Intervention Type DRUG

Participants will receive intramuscular injection of PP3M 525 mg eq.

PP1M

Intervention Type DRUG

Participants will receive intramuscular injection of PP1M 50 to 150 mg eq.

PP6M or Placebo: Double-Blind Phase

Participants will receive intramuscular injection of PP6M in left gluteal muscle on Day 1 and right gluteal muscle on Day 183 with alternating placebo in right gluteal muscle on Day 92 and left gluteal muscle on Day 274.

Group Type EXPERIMENTAL

PP6M

Intervention Type DRUG

Participants will receive intramuscular injection of PP6M.

Placebo

Intervention Type OTHER

Participants will receive matching placebo.

PP3M: Double-Blind Phase

Participants will receive intramuscular injections of PP3M at dose of 350 mg eq. or 525 mg eq. in left gluteal muscle on Day 1 and 274 and right gluteal muscle on Day 92 and 183.

Group Type EXPERIMENTAL

PP3M 350 mg eq.

Intervention Type DRUG

Participants will receive intramuscular injection of PP3M 350 mg eq.

PP3M 525 mg eq.

Intervention Type DRUG

Participants will receive intramuscular injection of PP3M 525 mg eq.

Interventions

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PP6M

Participants will receive intramuscular injection of PP6M.

Intervention Type DRUG

PP3M 350 mg eq.

Participants will receive intramuscular injection of PP3M 350 mg eq.

Intervention Type DRUG

PP3M 525 mg eq.

Participants will receive intramuscular injection of PP3M 525 mg eq.

Intervention Type DRUG

PP1M

Participants will receive intramuscular injection of PP1M 50 to 150 mg eq.

Intervention Type DRUG

Placebo

Participants will receive matching placebo.

Intervention Type OTHER

Other Intervention Names

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R092670 R092670 R092670 R092670

Eligibility Criteria

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Inclusion Criteria

* Must meet the diagnostic criteria for schizophrenia according to Diagnostic and Statistical Manual of Mental Disorders, Fifth Edition (DSM 5) for at least 6 months before screening
* Must be receiving treatment with paliperidone palmitate (as either the paliperidone palmitate 1-month (PP1M) or paliperidone palmitate 3-month (PP3M) formulation), or injectable risperidone, or any oral antipsychotic
* Must be able, in the opinion of the investigator, to discontinue any antipsychotic medication other than PP1M) or PP3M during the Screening Phase
* Must have a full Positive and Negative Syndrome Scale (PANSS) score of less than (\<) 70 points at screening
* Must have a body mass index (BMI) between 17 and 40 kilogram (kg)/meter (m)\^2 (inclusive) and must have a body weight of at least 47 kg at screening
* Must be willing to receive gluteal injections of medication during the Double-blind Phase

Exclusion Criteria

* Must not be receiving any form of involuntary treatment, such as involuntary psychiatric hospitalization, parole-mandated treatment, or court-mandated treatment
* Must not have attempted suicide within 12 months before screening and must not be at imminent risk of suicide or violent behavior, as clinically assessed by the investigator at the time of screening
* Must not have a DSM-5 diagnosis of moderate or severe substance use disorder (except for nicotine and caffeine) within 6 months of screening; however, acute or intermittent substance use prior to screening is not exclusionary, depending upon the clinical judgment of the investigator
* Must not have a history of neuroleptic malignant syndrome or tardive dyskinesia
* Must not have a history of intolerability or severe reactions to moderate or higher doses of antipsychotic medications and must not have any other factors that would, in the judgment of the investigator, indicate that treatment with moderate or higher doses of paliperidone palmitate would be intolerable or unsafe
Minimum Eligible Age

18 Years

Maximum Eligible Age

70 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Janssen Research & Development, LLC

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Janssen Research & Development, LLC Clinical Trial

Role: STUDY_DIRECTOR

Janssen Research & Development, LLC

Locations

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Woodland Research Northwest

Rogers, Arkansas, United States

Site Status

California Pharmaceutical Research Institute, Inc.

Anaheim, California, United States

Site Status

ATP Clinical Research

Costa Mesa, California, United States

Site Status

Collaborative NeuroScience Network

Garden Grove, California, United States

Site Status

Synergy East

Lemon Grove, California, United States

Site Status

Pacific Research Partners

Oakland, California, United States

Site Status

SF-Care, Inc

San Rafael, California, United States

Site Status

New Life Medical Research Center, Inc.

Hialeah, Florida, United States

Site Status

Clintex Research Group

Miami, Florida, United States

Site Status

Florida Research Center Inc.

Miami, Florida, United States

Site Status

Olympian Clinical Research

Tampa, Florida, United States

Site Status

Atlanta Center for Medical Research

Atlanta, Georgia, United States

Site Status

Uptown Research Institute

Chicago, Illinois, United States

Site Status

Alexian Behavioral Health Hospital

Hoffman Estates, Illinois, United States

Site Status

Ascension via Christi Research

Wichita, Kansas, United States

Site Status

Massachusetts General Hospital

Boston, Massachusetts, United States

Site Status

Cherry Street Services, Inc.

Grand Rapids, Michigan, United States

Site Status

St. Louis Clinical Trials

St Louis, Missouri, United States

Site Status

The Zucker Hillside Hospital

Glen Oaks, New York, United States

Site Status

Clinical Trials of America Inc

Hickory, North Carolina, United States

Site Status

Wexner Medical Center at the Ohio State University

Columbus, Ohio, United States

Site Status

Midwest Clinical Research Center

Dayton, Ohio, United States

Site Status

University of Pennsylvania Medical Center

Philadelphia, Pennsylvania, United States

Site Status

Future Search Trials of Dallas

Dallas, Texas, United States

Site Status

Psychiatric and Behavioral Solutions

Salt Lake City, Utah, United States

Site Status

Fundacion para el Estudio y Tratamiento de las Enfermedades Mentales

Buenos Aires, , Argentina

Site Status

CEN

Córdoba, , Argentina

Site Status

Sanatorio Prof. Leon S. Morra

Córdoba, , Argentina

Site Status

Instituto de Neurociencias San Agustin

La Plata, , Argentina

Site Status

Clinica Privada de Salud Mental Santa Teresa de Ávila

La Plata, , Argentina

Site Status

C I A P Centro de investigacion y Asistencia en Psiquiatria

Rosario, , Argentina

Site Status

The Lyell McEwin Hospital

Elizabeth Vale, , Australia

Site Status

Neuro Trials Victoria

Noble Park, , Australia

Site Status

Trial Tech Tecnologia em Pesquisas com Medicamentos

Curitiba, , Brazil

Site Status

Instituto Bairral de Psiquiatria

Itapira, , Brazil

Site Status

Hospital das Clinicas de Porto Alegre

Porto Alegre, , Brazil

Site Status

Ruschel Medicina e Pesquisa Clínica Ltda

Rio de Janeiro, , Brazil

Site Status

CPQuali Pesquisa Clinica LTDA ME

São Paulo, , Brazil

Site Status

SPDM - Associacao Paulista para o Desenvolvimento da Medicina - Hospital Sao Paulo

São Paulo, , Brazil

Site Status

Hospital Das Clinicas Da Faculdade De Medicina Da USP

São Paulo, , Brazil

Site Status

Mental Health Center Prof. Dr. Ivan Temkov

Burgas, , Bulgaria

Site Status

State Psychiatric Hospital Pazardzhik

Pazardzhik, , Bulgaria

Site Status

UMHAT 'Sveti Georgi'-Plovdiv

Plovdiv, , Bulgaria

Site Status

State Psychiatric HospitalDr.Georgi Kissiov

Radnevo, , Bulgaria

Site Status

Centre for Mental Health Prof.N.Shipkovenski EOOD

Sofia, , Bulgaria

Site Status

Medical Center Intermedica, OOD

Sofia, , Bulgaria

Site Status

Psychiatricka ambulance, MUDr. Marta Holanova

Brno, , Czechia

Site Status

NeuropsychiatrieHK, s.r.o.

Hradec Kralove-Vekose, , Czechia

Site Status

A Shine S R O

Pilsen, , Czechia

Site Status

Pragtis S R O

Prague, , Czechia

Site Status

Institut Neuropsychiatricke pece

Prague, , Czechia

Site Status

Psychiatricka ambulance MUDr. Simona Papezova

Prague, , Czechia

Site Status

C.H.S. Charles Perrens

Bordeaux, , France

Site Status

CHRU La Colombière

Montpellier, , France

Site Status

CHU Caremeau

Nîmes, , France

Site Status

Hopital Sainte Anne

Paris, , France

Site Status

Hopital Sainte Musse

Toulon, , France

Site Status

Kwai Chung Hospital

Hong Kong, , Hong Kong

Site Status

Queen Mary Hospital

Hong Kong, , Hong Kong

Site Status

Józsefvarosi Szent Kozma Egészségügyi Központ

Budapest, , Hungary

Site Status

Petz Aladar Megyei Oktato Korhaz

Győr, , Hungary

Site Status

Bács-Kiskun Megyei Kórház a Szegedi Tudományegyetem Általános Orvostudományi Kar Oktató Kórháza

Kalocsa, , Hungary

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CRU Hungary Kft.

Miskolc, , Hungary

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Ratandeep Multispeciality Hospital

Ahmedabad, , India

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Sri Ramachandra Medical Centre

Chennai, , India

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Asha hospital

Hyderabad, , India

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Ahana Hospitals

Madurai, , India

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Vinaya Hospital and Research Center

Mangalore, , India

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Kasturba Medical College Hospital

Manipal, , India

Site Status

Jehangir Clinical Development Center Pvt Ltd

Pune, , India

Site Status

Deva Institute of Health Care and Research Pvt Ltd

Varanasi, , India

Site Status

Clinica Psichiatrica - Università di Cagliari

Cagliari, , Italy

Site Status

Dipartimento di Salute Mentale

Lecce, , Italy

Site Status

Seconda Universita degli Studi di Napoli - Azienda Ospedaliera Universitaria

Napoli, , Italy

Site Status

Universita degli Studi di Roma 'La Sapienza' - Azienda Ospedaliera Sant Andrea

Roma, , Italy

Site Status

Hospital Bahagia Ulu Kinta

Ipoh, , Malaysia

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Hospital Kuala Lumpur

Kuala Lumpur, , Malaysia

Site Status

University Malaya Medical Centre

Kuala Lumpur, , Malaysia

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Sarawak General Hospital

Kuching, , Malaysia

Site Status

Gabipros SC

Mexico City, , Mexico

Site Status

Instituto Neuropsique

Monterrey, , Mexico

Site Status

Centro de Estudios Clinicos y Especialidades Medicas S C

Monterrey, , Mexico

Site Status

Infosame/Research

Monterrey, , Mexico

Site Status

Centro de Atencion e Investigacion Cardiovascular del Potosi S C

San Luis Potosí City, , Mexico

Site Status

Mlynowamed Specjalistyczny Psychiatryczny Gabinet Lekarski Joanna Lazarczyk

Bialystok, , Poland

Site Status

Wlokiennicza MED Specjalistyczna Praktyka Lekarska dr n.med. Tomasz Markowski

Bialystok, , Poland

Site Status

Zespol Opieki Zdrowotnej w Chelmnie

Chełmno, , Poland

Site Status

Centrum Badan Klinicznych PI House sp z o o

Gdansk, , Poland

Site Status

Szpital Specjalistyczny im H Klimontowicza Oddzial Psychiatryczny

Gorlice, , Poland

Site Status

Niepubliczny Zaklad Opieki Psychiatrycznej MENTIS

Leszno, , Poland

Site Status

Centrum Medyczne Luxmed Sp z o o

Lublin, , Poland

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Poradnia Zdrowia Psychicznego 'Syntonia' w Pruszczu Gdanskim

Pruszcz Gdański, , Poland

Site Status

Mazowieckie Specjalistyczne Centrum Zdrowia im. Prof. Jana Mazurkiewicza w Pruszkowie

Pruszków, , Poland

Site Status

Wojewodzki Szpital Zespolony im L Rydygiera w Toruniu

Torun, , Poland

Site Status

Clinical Psychiatric Hospital #3 Named After V.A. Gilyarovsky

Moscow, , Russia

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Psychiatric Clinical hospital 1 named after N.A. Alekseev

Moscow, , Russia

Site Status

Nizny Novgorod clinical psychiatric hospital 1

Nizny Novgorod, , Russia

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Psychoneurological Dispensary of Frunzensky District

Saint Petersburg, , Russia

Site Status

Psychoneurological dispensary 10

Saint Petersburg, , Russia

Site Status

St-Petersburg Bekhterev Psychoneurological Research Institute

Saint Petersburg, , Russia

Site Status

Psychoneurological dispensary 1

Saint Petersburg, , Russia

Site Status

SHI 'Saratov City Clinical Hospital 2 n.a V.I. Razumovsky

Saratov, , Russia

Site Status

Saratov Regional Psychiatric hospital named after St. Sofia

Saratov, , Russia

Site Status

Psychoneurological Dispensary #4

St.Peterburg, , Russia

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Research Institute of Mental Health

Tomsk, , Russia

Site Status

Sverdlovsk Regional Clinical Psychiatric Hospital

Yekaterinburg, , Russia

Site Status

Flexivest 14 Research

Cape Town, , South Africa

Site Status

Gert Bosch Pretoria South Africa

Pretoria, , South Africa

Site Status

Juan Schrönen - Western Cape South Africa

Welgemoed, , South Africa

Site Status

Chonnam National University Hospital

Gwangju, , South Korea

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CHA Bundang Medical Center, CHA University

Gyeonggi-do, , South Korea

Site Status

Chonbuk National Univ Hospital

Jeonju, , South Korea

Site Status

Seoul National University Hospital

Seoul, , South Korea

Site Status

Hosp Univ Vall D Hebron

Barcelona, , Spain

Site Status

Inst. Internac. Neurociencias Aplicadas

Barcelona, , Spain

Site Status

Hosp. Univ. de Basurto

Bilbao, , Spain

Site Status

Centro Salud Mental La Corredoria

Oviedo, , Spain

Site Status

Hosp. El Bierzo

Ponferrada, , Spain

Site Status

Hosp. Clinico Univ. de Valencia

Valencia, , Spain

Site Status

Hosp. Prov. de Zamora

Zamora, , Spain

Site Status

National Cheng Kung University Hospital

Tainan City, , Taiwan

Site Status

Mackay Memorial Hospital

Taipei, , Taiwan

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Taipei Veterans General Hospital

Taipei, , Taiwan

Site Status

Chang Gung Memorial Hospital

Taoyuan District, , Taiwan

Site Status

Abdurrah Yurtarslan Training and Research Hospital

Ankara, , Turkey (Türkiye)

Site Status

Ankara Numune Research and Training Hospital

Ankara, , Turkey (Türkiye)

Site Status

Erenkoy Mental Health Hospital

Istanbul, , Turkey (Türkiye)

Site Status

Selcuk University, Medical School, Department of Psychiatry

Konya, , Turkey (Türkiye)

Site Status

Sakarya University Medical Faculty Psychiatry Department

Sakarya, , Turkey (Türkiye)

Site Status

MNCE of Kyiv RC Regional Psychiatric and Narcological Medical Association

Hlevakha, , Ukraine

Site Status

Mnpe of Kharkiv Regional Council 'Regional Clinical Psychiatric Hospital #3'

Kharkiv, , Ukraine

Site Status

CNPE'Kherson Regional Institution of Mental Care'of Kherson Regional Council

Kherson, , Ukraine

Site Status

Kyiv Territorial Medical Incorporation 'Psychiatry'

Kyiv, , Ukraine

Site Status

Municipal Institution 'Lviv Regional Clinical Psycho-Neurological Dispensary'

Lviv, , Ukraine

Site Status

CNCE of the Lviv Regional Council 'Lviv Regional Clinical Psychiatric Hospital'

Lviv, , Ukraine

Site Status

CNCE Odesa regional psychiatric hospital #2 Odesa regional council

Oleksandrivka, , Ukraine

Site Status

CNCE 'Cherkasy Regional Psychiatric Hospital of Cherkasy Regional Council'

Smila, , Ukraine

Site Status

CNCE 'Vinnytsya RC Psychoneurological Hospital n.a. O.I. Yushchenko Vinnytsya RC'

Vinnytsia, , Ukraine

Site Status

Countries

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United States Argentina Australia Brazil Bulgaria Czechia France Hong Kong Hungary India Italy Malaysia Mexico Poland Russia South Africa South Korea Spain Taiwan Turkey (Türkiye) Ukraine

References

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Richarz U, Han J, Bai YM, Yu-Hai Chen E, Chung YC, Jhanwar VG, Kim SW, Sulaiman AH, Knight K, Gopal S. Efficacy and safety of paliperidone palmitate 6-monthly long-acting injectable in reduction of relapses in patients with schizophrenia: An Asian subgroup analysis of phase 3, randomized study. Medicine (Baltimore). 2023 Aug 25;102(34):e34623. doi: 10.1097/MD.0000000000034623.

Reference Type DERIVED
PMID: 37653768 (View on PubMed)

Najarian D, Turkoz I, Knight RK, Galderisi S, Lamaison HF, Zalitacz P, Aravind S, Richarz U. Long-Term Efficacy and Safety of Paliperidone 6-Month Formulation: An Open-Label 2-Year Extension of a 1-Year Double-Blind Study in Adult Participants With Schizophrenia. Int J Neuropsychopharmacol. 2023 Aug 29;26(8):537-544. doi: 10.1093/ijnp/pyad028.

Reference Type DERIVED
PMID: 37480362 (View on PubMed)

Najarian D, Sanga P, Wang S, Lim P, Singh A, Robertson MJ, Cohen K, Schotte A, Milz R, Venkatasubramanian R, T'Jollyn H, Walling DP, Galderisi S, Gopal S. A Randomized, Double-Blind, Multicenter, Noninferiority Study Comparing Paliperidone Palmitate 6-Month Versus the 3-Month Long-Acting Injectable in Patients With Schizophrenia. Int J Neuropsychopharmacol. 2022 Mar 17;25(3):238-251. doi: 10.1093/ijnp/pyab071.

Reference Type DERIVED
PMID: 34791283 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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R092670PSY3015

Identifier Type: OTHER

Identifier Source: secondary_id

2017-001941-28

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

CR108390

Identifier Type: -

Identifier Source: org_study_id

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