Myelodysplastic Syndrome--CDA-2 Hematological Improvement National Affirmation Study

NCT ID: NCT03335943

Last Updated: 2017-11-08

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

UNKNOWN

Clinical Phase

PHASE4

Total Enrollment

800 participants

Study Classification

INTERVENTIONAL

Study Start Date

2017-12-01

Study Completion Date

2020-12-01

Brief Summary

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This Study aims to evaluate the efficacy and safety of CDA-2 in the treatment of International Prognostic Scoring System (IPSS) Lower/Intermediate-risk myelodysplastic syndrome (MDS) in Chinese patients.

Detailed Description

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Patients with lower/intermediate-risk myelodysplastic syndrome (MDS) have rare therapeutic options other than supportive care. In pilot studies, CDA-2 showed promising results of hematological improvement in these patients.

To date, the optimal regimen for CDA-2 treatment is not well established. The researchers are going to make a multi-centered clinical trial to evaluate the efficacy and safety of CDA-2 in 800 patients with International Prognostic Scoring System(IPSS) Lower/Intermediate-risk myelodysplastic syndrome (MDS).

Eligible patients will be given CDA-2 intravenously, with 200 ml each day for 14 consecutive days in every four weeks (one cycle). The treatment will be repeated at least for 3 cycles. The patients will be followed up to 24 weeks.

The primary endpoint is hematological improvement (HI) at 12 weeks according to IWG criteria. Full blood counts will be done on all patients every week. Change in bone marrow function as measured by changes in bone marrow morphology and cytogenetics will be assessed before and after 3 cycles of the treatment.

The secondary endpoint is the therapy response. Complete remission (CR), partial remission (PR) and response duration, side effects, evaluation of QOL will be evaluated at the end of the treatment in every cycle.

Adverse events of the treatment will be recorded for evaluation of the safety.

Conditions

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Myelodysplastic Syndrome (MDS)

Keywords

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CDA-2, MDS

Study Design

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Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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CDA-2 (Cell Differentiation Agent 2)

Patients will be given CDA-2 therapy.

Group Type EXPERIMENTAL

CDA-2 (Cell Differentiation Agent 2)

Intervention Type DRUG

CDA-2 will be given intravenously, with 200 ml each day for 14 consecutive days in every four weeks (one cycle). The treatment will be repeated at least for 3 cycles.

Interventions

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CDA-2 (Cell Differentiation Agent 2)

CDA-2 will be given intravenously, with 200 ml each day for 14 consecutive days in every four weeks (one cycle). The treatment will be repeated at least for 3 cycles.

Intervention Type DRUG

Other Intervention Names

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Uroacitides (a compound mixed of peptides and organic acids)

Eligibility Criteria

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Inclusion Criteria

* Documented diagnosis of MDS according to World Health Organization (WHO)/French American British (FAB) classification that meets IPSS-R classification of low, or intermediate-1 risk disease.
* Subject is 18 to 85years of age the time of signing the informed consent form (ICF).
* Able to adhere to the study visit schedule and other protocol requirements
* Eastern Cooperative Oncology Group (ECOG) score of 0, 1, or 2.
* Laboratory test results within these ranges: Serum creatinine \</=1.5 mg/dL x Upper limit of the normal (ULN),Blood urine nitrogen (BUN)\</=1.5 mg/dL x Upper limit of the normal (ULN),Total bilirubin \</=1.5 mg/dL x Upper limit of the normal (ULN),Serum glutamic oxaloacetic transaminase/aspartate transaminase (SGOT/AST) and Serum glutamic pyruvic transaminase/alanine transaminase (SGPT/ALT)\</=2 x Upper limit of the normal (ULN).
* No prior intensive combination chemotherapy or dose Azacitidine,Decitabine,and Lenalidomide,etc.
* Capable of understanding the investigational nature, potential risks and benefits of the study, and able to provide valid informed consent.

Exclusion Criteria

* IPSS risk group intermediate-2 or high risk
* breast feeding and pregnant women
* MDS associated with del 5q cytogenetic abnormality
* Patients with history of hepatitis B, C, HIV(+), alcoholic liver disease or evidence of hepatopathy will be excluded.
* Any significant concurrent disease, illness, or psychiatric disorder that would compromise patient safety or compliance, interfere with consent, study participation, follow up, or interpretation of study results.
Minimum Eligible Age

18 Years

Maximum Eligible Age

85 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Harbin Institute of Hematology & Oncology

UNKNOWN

Sponsor Role collaborator

Chinese Society of Hematology

OTHER

Sponsor Role lead

Responsible Party

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Wu Depei

Professor

Responsibility Role PRINCIPAL_INVESTIGATOR

References

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Ma X. Epidemiology of myelodysplastic syndromes. Am J Med. 2012 Jul;125(7 Suppl):S2-5. doi: 10.1016/j.amjmed.2012.04.014.

Reference Type BACKGROUND
PMID: 22735748 (View on PubMed)

Fenaux P, Haase D, Sanz GF, Santini V, Buske C; ESMO Guidelines Working Group. Myelodysplastic syndromes: ESMO Clinical Practice Guidelines for diagnosis, treatment and follow-up. Ann Oncol. 2014 Sep;25 Suppl 3:iii57-69. doi: 10.1093/annonc/mdu180. Epub 2014 Jul 25. No abstract available.

Reference Type BACKGROUND
PMID: 25185242 (View on PubMed)

Other Identifiers

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CDA-2 MDS-2017

Identifier Type: -

Identifier Source: org_study_id