Low-Dose Atropine for Treatment of Myopia

NCT ID: NCT03334253

Last Updated: 2023-09-05

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

View full results

Basic Information

Get a concise snapshot of the trial, including recruitment status, study phase, enrollment targets, and key timeline milestones.

Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

200 participants

Study Classification

INTERVENTIONAL

Study Start Date

2018-06-01

Study Completion Date

2022-09-12

Brief Summary

Review the sponsor-provided synopsis that highlights what the study is about and why it is being conducted.

Study Objectives

The objectives for this randomized trial are:

1. To determine the efficacy of daily low-dose atropine (0.01%) for slowing myopia progression over a two-year treatment period in children aged 5 to less than 13 years (Primary Outcome On-Treatment).
2. To determine the efficacy of atropine treatment on myopia progression 6 months following cessation of low-dose atropine treatment (Secondary Outcome Off-Treatment).

Synopsis of Study Design The current study is designed as an efficacy study, making effort to maximize adherence to treatment group assignments. After a run-in phase during which all participants are treated with daily artificial tear eyedrops for 2-4 weeks (and glasses are updated if required) to assess their ability to adhere to daily eye drops, participants are randomly assigned to daily atropine or placebo for 24 months, followed by 6 months off treatment.

Detailed Description

Dive into the extended narrative that explains the scientific background, objectives, and procedures in greater depth.

Study Objectives

The objectives for this randomized trial are:

1. To determine the efficacy of daily low-dose atropine (0.01%) for slowing myopia progression over a two-year treatment period in children aged 5 to less than 13 years with myopia -1.00 to -6.00D at the time of enrollment (Primary Outcome On-Treatment).
2. To determine the efficacy of atropine treatment on myopia progression 6 months following cessation of low-dose atropine treatment (Secondary Outcome Off-Treatment).

Synopsis of Study Design The current study is designed as an efficacy study, making effort to maximize adherence to treatment group assignments. After a run-in phase during which all participants are treated with daily artificial tear eyedrops for 2-4 weeks (and glasses are updated if required) to assess their ability to adhere to daily eye drops, participants are randomly assigned to daily atropine or placebo for 24 months, followed by 6 months off treatment.

Conditions

See the medical conditions and disease areas that this research is targeting or investigating.

Myopia

Study Design

Understand how the trial is structured, including allocation methods, masking strategies, primary purpose, and other design elements.

Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

The current study is designed as an efficacy study, making effort to maximize adherence to treatment group assignments. After a run-in phase during which all participants are treated with daily artificial tear eyedrops for 2-4 weeks (and glasses are updated if required) to assess their ability to adhere to daily eye drops, participants are randomly assigned to daily atropine or placebo for 24 months, followed by 6 months off treatment.
Primary Study Purpose

TREATMENT

Blinding Strategy

TRIPLE

Participants Investigators Outcome Assessors
Cycloplegic autorefraction, axial length, and additional biometry will be measured by a masked examiner at all follow-up visits using the same instrumentation on the participant throughout the study. Masking will be accomplished by having site personnel administer cyclopentolate to both eyes of each participant and wait 30 minutes before he/she sees the masked examiner. The masked examiner may be a technician or an investigator and must be certified to complete these measurements. Parents, patients, and investigators are also masked to treatment.

Study Groups

Review each arm or cohort in the study, along with the interventions and objectives associated with them.

Atropine Group

0.01% atropine eyedrops administered 1 drop to each eye daily in each eye for 24 months, followed by 6 months off atropine eyedrops

Group Type EXPERIMENTAL

Atropine

Intervention Type DRUG

Daily 0.01% atropine eyedrops

Placebo Group

Placebo eyedrops administered 1 drop to each eye daily in each eye for 24 months, followed by 6 months off placebo eyedrops

Group Type PLACEBO_COMPARATOR

Placebo Eyedrops

Intervention Type OTHER

Daily placebo eyedrops

Interventions

Learn about the drugs, procedures, or behavioral strategies being tested and how they are applied within this trial.

Atropine

Daily 0.01% atropine eyedrops

Intervention Type DRUG

Placebo Eyedrops

Daily placebo eyedrops

Intervention Type OTHER

Other Intervention Names

Discover alternative or legacy names that may be used to describe the listed interventions across different sources.

Low-Dose Atropine

Eligibility Criteria

Check the participation requirements, including inclusion and exclusion rules, age limits, and whether healthy volunteers are accepted.

Inclusion Criteria

* Age 5 years to \<13 years at time of enrollment. Children within 4 weeks of their 13th birthday are not eligible.
* Refractive error meeting the following by cycloplegic autorefraction:

* Myopia -1.00D to -6.00D spherical equivalent (SE) in both eyes
* Astigmatism \<=1.50D in both eyes
* Anisometropia \<1.00D SE
* Gestational age ≥ 32 weeks.
* Birth weight \>1500g.
* Parent understands the protocol and is willing to accept randomization to atropine or placebo.
* Is willing to participate in a 2 to 4 week run-in phase using daily artificial tear eyedrops.
* Able to return in 2 to 4 weeks for possible randomization.
* Parent has a phone (or access to phone) and is willing to be contacted by Investigator's site staff.
* Relocation outside of the area of an active PEDIG site within next 32 months is not anticipated.

Exclusion Criteria

* Current or previous myopia treatment with atropine, pirenzepine or other anti-muscarinic agent.
* Current or previous use of bifocals, progressive-addition lenses, or multi-focal contact lenses.
* Current or previous use of orthoK, rigid gas permeable, or other contact lenses being used to reduce myopia progression.
* Known atropine allergy.
* Abnormality of the cornea, lens, central retina, iris or ciliary body.
* Current or prior history of manifest strabismus, amblyopia, or nystagmus.
* Prior eyelid, strabismus, intraocular, or refractive surgery.
* Down syndrome or cerebral palsy.
* Females who are pregnant, lactating, or intending to become pregnant within the next 30 months.

* A negative urine pregnancy test will be required for all females who have experienced menarche.
Minimum Eligible Age

5 Years

Maximum Eligible Age

12 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

Meet the organizations funding or collaborating on the study and learn about their roles.

Pediatric Eye Disease Investigator Group

NETWORK

Sponsor Role collaborator

National Eye Institute (NEI)

NIH

Sponsor Role collaborator

Jaeb Center for Health Research

OTHER

Sponsor Role lead

Responsible Party

Identify the individual or organization who holds primary responsibility for the study information submitted to regulators.

Responsibility Role SPONSOR

Principal Investigators

Learn about the lead researchers overseeing the trial and their institutional affiliations.

Michael X Repka, MD, MBA

Role: STUDY_CHAIR

Wilmer Eye Institute

Katherine K Weise, OD, MBA

Role: STUDY_CHAIR

University of Alabama Birmingham Pediatric Eye Care, Birmingham Health Care

Locations

Explore where the study is taking place and check the recruitment status at each participating site.

University of Alabama at Birmingham

Birmingham, Alabama, United States

Site Status

The Emory Eye Center Dept of Ophthalmology

Atlanta, Georgia, United States

Site Status

St Luke's Hospital

Boise, Idaho, United States

Site Status

Illinois College of Optometry

Chicago, Illinois, United States

Site Status

Ticho Eye Associates

Chicago Ridge, Illinois, United States

Site Status

Boston Children's Hospital Waltham

Boston, Massachusetts, United States

Site Status

Pediatric Ophthalmology Associates, Inc.

Columbus, Ohio, United States

Site Status

Eye Care Associates, Inc.

Poland, Ohio, United States

Site Status

Dean A. McGee Eye Institute, University of Oklahoma

Oklahoma City, Oklahoma, United States

Site Status

Casey Eye Institute

Portland, Oregon, United States

Site Status

Vanderbilt University Medical Center - Vanderbilt Eye Institute

Nashville, Tennessee, United States

Site Status

University of Houston College of Optometry

Houston, Texas, United States

Site Status

Rocky Mountain Eye Care Associates

Salt Lake City, Utah, United States

Site Status

Countries

Review the countries where the study has at least one active or historical site.

United States

References

Explore related publications, articles, or registry entries linked to this study.

Repka MX, Weise KK, Chandler DL, Wu R, Melia BM, Manny RE, Kehler LAF, Jordan CO, Raghuram A, Summers AI, Lee KA, Petersen DB, Erzurum SA, Pang Y, Lenhart PD, Ticho BH, Beck RW, Kraker RT, Holmes JM, Cotter SA; Pediatric Eye Disease Investigator Group. Low-Dose 0.01% Atropine Eye Drops vs Placebo for Myopia Control: A Randomized Clinical Trial. JAMA Ophthalmol. 2023 Aug 1;141(8):756-765. doi: 10.1001/jamaophthalmol.2023.2855.

Reference Type RESULT
PMID: 37440213 (View on PubMed)

Weise KK, Repka MX, Zhu Y, Manny RE, Raghuram A, Chandler DL, Summers AI, Lee KA, Kehler LAF, Pang Y, Allen MS, Anderson HA, Erzurum SA, Golden RP, Koutnik CA, Kuo AF, Lenhart PD, Mokka PL, Petersen DB, Ticho BH, Wiecek EK, Yin H, Beaulieu WT, Kraker RT, Holmes JM, Cotter SA; Pediatric Eye Disease Investigator Group. Baseline factors associated with myopia progression and axial elongation over 30 months in children 5 to 12 years of age. Optom Vis Sci. 2024 Oct 1;101(10):619-626. doi: 10.1097/OPX.0000000000002187.

Reference Type DERIVED
PMID: 39480129 (View on PubMed)

Provided Documents

Download supplemental materials such as informed consent forms, study protocols, or participant manuals.

Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Document Type: Informed Consent Form

View Document

Other Identifiers

Review additional registry numbers or institutional identifiers associated with this trial.

2U10EY011751

Identifier Type: NIH

Identifier Source: secondary_id

View Link

MTS1

Identifier Type: -

Identifier Source: org_study_id

More Related Trials

Additional clinical trials that may be relevant based on similarity analysis.

Study of OT-101 in Treating Myopia
NCT04770610 ACTIVE_NOT_RECRUITING PHASE3