A Study of Pembrolizumab Plus Epacadostat With Platinum-based Chemotherapy Versus Pembrolizumab Plus Platinum-based Chemotherapy Plus Placebo in Metastatic Non-Small Cell Lung Cancer (KEYNOTE-715-06/ECHO-306-06)

NCT ID: NCT03322566

Last Updated: 2022-01-24

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

233 participants

Study Classification

INTERVENTIONAL

Study Start Date

2018-01-09

Study Completion Date

2020-10-16

Brief Summary

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The purpose of this study was to evaluate the efficacy and safety of pembrolizumab plus epacadostat with platinum-based chemotherapy versus pembrolizumab plus platinum-based chemotherapy plus placebo as first-line therapy in participants with metastatic non-small cell lung cancer (NSCLC).

Detailed Description

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Conditions

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Lung Cancer

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Pembrolizumab + Chemotherapy + Epacadostat

Participant received pembrolizumab 200 mg intravenous (IV) infusion, every 3 weeks (Q3W) on Day 1 of each 21 day cycle for up to 35 cycles + epacadostat 100 mg tablets, orally, twice daily (BID) in each 21 day cycle for up to 35 cycles + platinum-doublet chemotherapy (pemetrexed 500 mg/m\^2 IV infusion, Q3W + cisplatin 75 mg/m\^2 IV infusion, Q3W or carboplatin 5-6 mg/mL/min IV infusion Q3W for 4 cycles followed by pemetrexed maintenance; or paclitaxel 200 mg /m\^2 IV infusion, Q3W + carboplatin 5-6 mg/mL/min IV infusion Q3W for 4 cycles).

Group Type EXPERIMENTAL

Pembrolizumab

Intervention Type DRUG

Pembrolizumab administered intravenously every 3 weeks.

Epacadostat

Intervention Type DRUG

Epacadostat administered orally twice daily.

Platinum-based chemotherapy

Intervention Type DRUG

Investigator selected one of the following regimens: pemetrexed + cisplatin, pemetrexed + carboplatin, or paclitaxel + carboplatin, depending on histology.

Pembrolizumab + Chemotherapy + Placebo

Participant received pembrolizumab 200 mg IV infusion, Q3W on Day 1 of each 21 day cycle for up to 35 cycles + epacadostat matching placebo tablets, orally, BID in each 21 day cycle for up to 35 cycles + platinum-doublet chemotherapy (pemetrexed 500 mg/m\^2 IV infusion, Q3W + cisplatin 75 mg/m\^2 IV infusion, Q3W or carboplatin 5-6 mg/mL/min IV infusion Q3W for 4 cycles followed by pemetrexed maintenance; or paclitaxel 200 mg /m\^2 IV infusion, Q3W + carboplatin 5-6 mg/mL/min IV infusion Q3W for 4 cycles).

Group Type EXPERIMENTAL

Pembrolizumab

Intervention Type DRUG

Pembrolizumab administered intravenously every 3 weeks.

Platinum-based chemotherapy

Intervention Type DRUG

Investigator selected one of the following regimens: pemetrexed + cisplatin, pemetrexed + carboplatin, or paclitaxel + carboplatin, depending on histology.

Placebo

Intervention Type DRUG

Matching placebo administered orally twice daily.

Pembrolizumab + Epacadostat

Participant received pembrolizumab 200 mg IV infusion, Q3W on Day 1 of each 21 day cycle for up to 35 cycles + epacadostat 100 mg tablets, orally, BID in each 21 day cycle for up to 35 cycles.

Group Type EXPERIMENTAL

Pembrolizumab

Intervention Type DRUG

Pembrolizumab administered intravenously every 3 weeks.

Epacadostat

Intervention Type DRUG

Epacadostat administered orally twice daily.

Interventions

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Pembrolizumab

Pembrolizumab administered intravenously every 3 weeks.

Intervention Type DRUG

Epacadostat

Epacadostat administered orally twice daily.

Intervention Type DRUG

Platinum-based chemotherapy

Investigator selected one of the following regimens: pemetrexed + cisplatin, pemetrexed + carboplatin, or paclitaxel + carboplatin, depending on histology.

Intervention Type DRUG

Placebo

Matching placebo administered orally twice daily.

Intervention Type DRUG

Other Intervention Names

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MK-3475 INCB024360

Eligibility Criteria

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Inclusion Criteria

* Histologically or cytologically confirmed diagnosis of stage IV NSCLC without epidermal growth factor receptor (EGFR)-sensitizing mutation, ROS1 and/or anaplastic lymphoma kinase (ALK) translocation
* Measurable disease based on RECIST 1.1
* Life expectancy of at least 3 months.
* Eastern Cooperative Oncology Group (ECOG) performance status of 0 or 1.
* Adequate organ function per protocol-defined criteria.
* Provide tumor tissue sample.

Exclusion Criteria

* Known untreated central nervous system metastases and/or carcinomatous meningitis
* History of (non-infectious) pneumonitis that required systemic steroids or current pneumonitis/interstitial lung disease.
* Symptomatic ascites or pleural effusion.
* Known history of an additional malignancy, except if the participant has undergone potentially curative therapy with no evidence of that disease recurrence for 5 years since initiation of that therapy.
* Active autoimmune disease that has required systemic treatment in past 2 years.
* Has had an allogeneic tissue/solid organ transplant.
* Has a known history of human immunodeficiency virus (HIV) infection. HIV testing is not required unless mandated by the local health authority.
* Has known history of or is positive for active Hepatitis B (HBsAg reactive) or has active Hepatitis C (HCV RNA). Note: Testing must be performed to determine eligibility.
* History or presence of an abnormal electrocardiogram (ECG) that, in the Investigator's opinion, is clinically meaningful.
* Use of protocol-defined prior/concomitant therapy.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Merck Sharp & Dohme LLC

INDUSTRY

Sponsor Role collaborator

Incyte Corporation

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Lance Leopold, MD

Role: STUDY_DIRECTOR

Incyte Corporation

Locations

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Southern Cancer Center, PC

Daphne, Alabama, United States

Site Status

Western Regional Medical Center, Inc.

Goodyear, Arizona, United States

Site Status

Arizona Oncology Associates PC- HOPE

Tucson, Arizona, United States

Site Status

Lynn Cancer Institute

Boca Raton, Florida, United States

Site Status

Florida Cancer Specialists (South Region)

Fort Myers, Florida, United States

Site Status

Florida Cancer Specialists (North Region)

St. Petersburg, Florida, United States

Site Status

PPG-Oncology

Fort Wayne, Indiana, United States

Site Status

University of Michigan

Ann Arbor, Michigan, United States

Site Status

MMCORC

Saint Louis Park, Minnesota, United States

Site Status

St. Vincent Healthcare Frontier Cancer Center

Billings, Montana, United States

Site Status

New York Oncology Hematology P.C

Albany, New York, United States

Site Status

Oncology Hematology Care, Inc.

Cincinnati, Ohio, United States

Site Status

Southwestern Regional Medical Center, Inc.

Tulsa, Oklahoma, United States

Site Status

St. Luke's Hospital - Anderson Campus

Easton, Pennsylvania, United States

Site Status

Allegheny General Hospital

Pittsburgh, Pennsylvania, United States

Site Status

Tennessee Oncology, PLLC/The Sarah Cannon Research Institute

Chattanooga, Tennessee, United States

Site Status

Tennessee Oncology, PLLC/The Sarah Cannon Research Institute

Nashville, Tennessee, United States

Site Status

Texas Oncology-Denton South

Denton, Texas, United States

Site Status

Oncology & Hematology Assoc. SW Virginia, Inc., DBA Blue Ridge Cancer Care

Blacksburg, Virginia, United States

Site Status

Emily Couric Clinical Cancer Center

Charlottesville, Virginia, United States

Site Status

Seattle Cancer Care Alliance

Seattle, Washington, United States

Site Status

Blacktown Hospital

Blacktown, New South Wales, Australia

Site Status

Chris OBrien Lifehouse

Camperdown, New South Wales, Australia

Site Status

The Crown Princess Mary Cancer Centre Westmead

Westmead, New South Wales, Australia

Site Status

Southern Medical Day Care Centre

Wollongong, New South Wales, Australia

Site Status

MNCCI Port Macquarie Base Hospital

Port Macquarie, New South Wales (Australia), Australia

Site Status

Cairns Base Hospital

Cairns, Queensland, Australia

Site Status

BCCA-Cancer Centre of the Southern Interior

Kelowna, British Columbia, Canada

Site Status

Lions Gate Hospital

North Vancouver, British Columbia, Canada

Site Status

CISSS de la Monteregie-Centre

Greenfield Park, Quebec, Canada

Site Status

CSSS de Laval- Hopital de la Cite de la Sante

Laval, Quebec, Canada

Site Status

CIUSSS Ouest de l'Ile - St-Mary's Hospital

Montreal, Quebec, Canada

Site Status

CIUSSS du Nord-de-l'ILe-de-Montreal Hopital du Sacre-Coeur de Montreal

Montreal, Quebec, Canada

Site Status

CHU de Quebec - Hotel-Dieu de Quebec

Québec, Quebec, Canada

Site Status

CIUSSS de la Mauricie-et-du-Centre-du-Quebec

Trois-Rivières, Quebec, Canada

Site Status

Zala Megyei Korhaz Pozvai Telephely

Pózva, Zalaegerszeg, Hungary

Site Status

Orszagos Koranyi TBC es Pulmonologiai Intezet

Budapest, , Hungary

Site Status

Veszprem Megyei Tudogyogyintezet

Farkasgyepű, , Hungary

Site Status

Bekes Megyei Pandy Kalman Korhaz

Gyula, , Hungary

Site Status

CRU Hungary Kft.

Miskolc, , Hungary

Site Status

Jasz Nagykun Szolnok Megyei Hetenyi Geza Korhaz Rendelointezet

Szolnok, , Hungary

Site Status

St Vincents University Hospital

Dublin, , Ireland

Site Status

Ha Emek Medical Center

Afula, , Israel

Site Status

Soroka Medical Center

Beersheba, , Israel

Site Status

Rambam Medical Center

Haifa, , Israel

Site Status

Meir Medical Center

Kfar Saba, , Israel

Site Status

Rabin Medical Center

Petah Tikva, , Israel

Site Status

Chaim Sheba Medcal Center

Ramat Gan, , Israel

Site Status

Centro Di Riferimento Oncologico

Aviano, , Italy

Site Status

A.O.U. Policlinico Vittorio Emanuele - Presidio Gaspare Rodolico

Catania, , Italy

Site Status

Fondazione IRCCS Istituto Nazionale dei Tumori

Milan, , Italy

Site Status

Istituto Europeo di Oncologia

Milan, , Italy

Site Status

Ospedale San Gerardo - ASST Monza

Monza, , Italy

Site Status

Medical Care Research S.A. de C.V.

Mérida, Yucatán, Mexico

Site Status

Oaxaca Site Management Organization S.C.

Oaxaca City, , Mexico

Site Status

FAICIC Clinical Research

Veracruz, , Mexico

Site Status

Belgorod Regional Oncology Dispensary

Belgorod, , Russia

Site Status

Udmurtia Republic Regional Clinical Oncology Dispensary

Izhevsk, , Russia

Site Status

Republican Clinical Oncology Dispensary of Tatarstan MoH

Kazan', , Russia

Site Status

Central Clinical Hospital with polyclinic

Moscow, , Russia

Site Status

Moscow Research Oncology Institute

Moscow, , Russia

Site Status

SBI of Stavropol region Pyatigorskiy Oncologic dispensary

Pyatigorsk, , Russia

Site Status

SBHI Leningrad Regional Clinical Hospital

Saint Petersburg, , Russia

Site Status

SBHI Samara Regional Clinical Oncology Dispensary

Samara, , Russia

Site Status

Oncological Dispensary #2 of Ministry of Health of Krasnodar region

Sochi, , Russia

Site Status

Tomsk Scientific Research Institute of Oncology

Tomsk, , Russia

Site Status

National Cancer Center

Goyang-si, , South Korea

Site Status

Severance Hospital Yonsei University Health System

Seoul, , South Korea

Site Status

Asan Medical Center

Seoul, , South Korea

Site Status

Samsung Medical Center

Seoul, , South Korea

Site Status

Hospital Universitario Insular de Gran Canaria

Las Palmas de Gran Canaria, Gran Canaria, Spain

Site Status

Hospital Juan Ramón Jimenez

Huelva, , Spain

Site Status

Institut Catala Oncologia de Bellvitge - ICO

L'Hospitalet de Llobregat, , Spain

Site Status

Hospital Universitario La Paz

Madrid, , Spain

Site Status

Hospital Universitario La Fe

Valencia, , Spain

Site Status

Hospital Clinico Universitario Lozano Blesa

Zaragoza, , Spain

Site Status

Chang Gung Medical Foundation, Kaohsiung Branch

Kaohsiung City, , Taiwan

Site Status

China Medical University Hospital

Taichung, , Taiwan

Site Status

National Cheng Kung University Hospital

Tainan City, , Taiwan

Site Status

National Taiwan University Hospital

Taipei, , Taiwan

Site Status

Chang Gung Medical Foundation, Linkou Branch

Taoyuan District, , Taiwan

Site Status

Ege Universitesi Tip Fakultesi Hastanesi

Izmir, Bornova, Turkey (Türkiye)

Site Status

Baskent Universitesi Adana Uygulama ve Arastirma Hastanesi

Adana, , Turkey (Türkiye)

Site Status

Cukurova Universitesi Tıp Fakultesi Balcalı Hastanesi

Adana, , Turkey (Türkiye)

Site Status

Hacettepe Universitesi Tip Fakultesi Hastanesi

Ankara, , Turkey (Türkiye)

Site Status

Uludag Universitesi Tip Fakultesi

Bursa, , Turkey (Türkiye)

Site Status

Pamukkale Unv. Tip Fak

Denizli, , Turkey (Türkiye)

Site Status

Istanbul Universitesi Cerrahpasa Tip Fakultesi

Istanbul, , Turkey (Türkiye)

Site Status

Samsun Medical Park Hastanesi

Samsun, , Turkey (Türkiye)

Site Status

Namık Kemal University Medical Faculty

Tekirdağ, , Turkey (Türkiye)

Site Status

Mount Vernon Cancer Centre

Northwood, Middlesex, United Kingdom

Site Status

Western General Hospital

Edinburgh, , United Kingdom

Site Status

North Middlesex Hospital

London, , United Kingdom

Site Status

Freeman Hospital Newcastle upon Tyne Foundation NHS Trust

Newcastle upon Tyne, , United Kingdom

Site Status

Countries

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United States Australia Canada Hungary Ireland Israel Italy Mexico Russia South Korea Spain Taiwan Turkey (Türkiye) United Kingdom

References

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Boyer M, Hui R, Urban D, Clingan P, Su WC, Devaux C, Gadgeel S, Garassino M, Leopold L, Daniel J, Munteanu MC, Samkari A, Luo Y, Abreu DR. Pembrolizumab with platinum-based chemotherapy with or without epacadostat as first-line treatment for metastatic non-small cell lung cancer: a randomized, partially double-blind, placebo-controlled phase II study. BMC Cancer. 2024 Jul 25;23(Suppl 1):1250. doi: 10.1186/s12885-022-10427-4.

Reference Type DERIVED
PMID: 39054462 (View on PubMed)

Provided Documents

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Document Type: Study Protocol and Statistical Analysis Plan

View Document

Other Identifiers

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2017-001810-27

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

KEYNOTE-715-06/ECHO-306-06

Identifier Type: -

Identifier Source: org_study_id

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