A Study of Trifluridine/Tipiracil (Also Known as S 95005 or TAS-102) in Patients With a Pretreated Colorectal Cancer That Has Spread (Metastatic).

NCT ID: NCT03306394

Last Updated: 2024-07-25

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

907 participants

Study Classification

INTERVENTIONAL

Study Start Date

2016-10-18

Study Completion Date

2020-11-30

Brief Summary

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The purpose of this study is to collect additional safety and efficacy data during treatment with trifluridine / tipiracil in patients with a pretreated metastatic colorectal cancer (mCRC).

Eligible patients may receive an early access to trifluridine / tipiracil through this clinical study until progression of disease, unacceptable toxicity, investigator decision, patient refusal or until market authorization or reimbursement has been granted by the relevant Authority of the country where that patient is treated or until trifluridine / tipiracil is available by a doctor's prescription or can be accessed from another source or Sponsor decision.

Detailed Description

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Conditions

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Metastatic Colorectal Cancer

Study Design

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Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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S95005

Film-coated tablet containing 15 mg of trifluridine and 7.065 mg of tipiracil hydrochloride, or 20 mg of trifluridine and 9.42 mg of tipiracil hydrochloride, taken orally twice a day at the dose of 35 mg/m²/dose. The treatment is given until progression of disease, unacceptable toxicity, investigator decision, patient refusal or until market authorization or reimbursement has been granted by the relevant Authority of the country where that patient is treated or until trifluridine / tipiracil is available by a doctor's prescription or can be accessed from another source or Sponsor decision.

Group Type EXPERIMENTAL

Trifluridine/Tipiracil hydrochloride (S95005)

Intervention Type DRUG

Interventions

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Trifluridine/Tipiracil hydrochloride (S95005)

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Male or Female participant aged ≥18 years old.
* Has definitive histologically confirmed adenocarcinoma of the colon or rectum.
* Has metastatic lesion(s).
* Has received at least 2 prior regimens of standard chemotherapies (including fluoropyrimidines, irinotecan, oxaliplatin, an anti-VEGF monoclonal antibody and at least one of the anti-EGFR monoclonal antibodies for RAS wild-type patients) for mCRC and is refractory or intolerant to those chemotherapies or is not candidate for those chemotherapies.
* Has Eastern Cooperative Oncology Group (ECOG) performance status of 0 or 1 during the screening period.
* Is able to take medications orally (i.e., no feeding tube).
* Has adequate organ function.
* Women of childbearing potential must have been tested negative in a serum pregnancy test within 7 days prior to first day of test drug administration. Female participants of childbearing potential and male participants with partners of childbearing potential must agree to use a highly effective method of birth control during the study and for 6 months after the discontinuation of study medication. Women and female partners using hormonal contraceptive must also use a barrier method.

Exclusion Criteria

* Pregnancy, breastfeeding or possibility of becoming pregnant during the study.
* Eligible for enrolment into another available ongoing clinical study of trifluridine / tipiracil.
* Has previously received trifluridine / tipiracil or hypersensitivity to the active substances or to any of the excipients of trifluridine / tipiracil.
* Has rare hereditary problems of galactose intolerance, the Lapp lactase deficiency, or glucose-galactose malabsorption.
* Has certain serious illness or medical condition(s) described in the protocol.
* Has had certain other recent treatment e.g. major surgery, anticancer therapy, radiation therapy, participation in another interventional study, within the specified time frames prior to first day of study drug administration.
* Has unresolved toxicity of greater than or equal to Common Terminology Criteria for Adverse Events (CTCAE) Grade 2 attributed to any prior therapies (excluding anemia, alopecia, skin pigmentation, and platinum-induced neurotoxicity).
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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ADIR, a Servier Group company

INDUSTRY

Sponsor Role collaborator

Institut de Recherches Internationales Servier

OTHER

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Chris O'Brien Lifehouse Oncology

Camperdown, , Australia

Site Status

St Vincent's Hospital The Kinghorn Cancer Centre

Darlinghurst, , Australia

Site Status

St Vincent's Hospital (Melbourne) Cancer Centre

Fitzroy, , Australia

Site Status

The Canberra Hospital Cancer,Ambulatory & Community Health Service (CACHS) Bldg 19

Garran, , Australia

Site Status

Royal Brisbane & Women's Hospital Clinical Research Unit

Herston, , Australia

Site Status

Cabrini Hospital Cabrini Haematology and Oncology Centre

Malvern, , Australia

Site Status

Perth Oncology - Mount Hospital

Perth, , Australia

Site Status

The Queen Elizabeth Hospital Haematology and Oncology Unit

Woodville, , Australia

Site Status

Hôpital Universitaire Erasme Gastro-Entérologie

Brussels, , Belgium

Site Status

Cliniques Universitaires St. Luc Oncologie médicale

Brussels, , Belgium

Site Status

Universitair Ziekenhuis Antwerpen Oncologie

Edegem, , Belgium

Site Status

U.Z. Gent Digestieve Oncologie

Ghent, , Belgium

Site Status

UZ Leuven Campus Gasthuisberg Digestieve Oncologie

Leuven, , Belgium

Site Status

Hospital Mãe de Deus Centro Intergrado de Pesquisa

Porto Alegre, , Brazil

Site Status

Clinicas Oncológicas Integradas (COI)

Rio de Janeiro, , Brazil

Site Status

AMO Assistencia Multidisciplinar em Oncologia GEM Assistencia Medica Especializada

Salvador, , Brazil

Site Status

Instituto do Cancer do Estado de Sao Paulo - ICESP Núcleo de Pesquisa

São Paulo, , Brazil

Site Status

Hospital A C Camargo Unidade de Pesquisa Clínica

São Paulo, , Brazil

Site Status

Instituto Brasileiro de Controle do Câncer Unidadde de Pesquisa Clínica

São Paulo, , Brazil

Site Status

Complex oncology center - Plovdiv

Plovdiv, , Bulgaria

Site Status

Military Medical Academy - MHAT Oncology clinic

Sofia, , Bulgaria

Site Status

Specialized hospital for active treatment in oncology

Sofia, , Bulgaria

Site Status

SHAT of oncology diseases

Varna, , Bulgaria

Site Status

Klinicki bolnicki centar Rijeka Klinika za radioterapiju i onkologiju

Rijeka, , Croatia

Site Status

Klinicki bolnicki centar Zagreb Klinika za onkologiju

Zagreb, , Croatia

Site Status

Hopital Privé Les Bonnettes Pharmacie centrale

Arras, , France

Site Status

Institut Sainte Catherine Institut Sainte Catherine

Avignon, , France

Site Status

Centre de lutte contre le cancer Francois Baclesse UCP Digestif

Caen, , France

Site Status

Hôpital Trousseau Hépato-gastroentérologie et cancérologie digestive

Chambray-lès-Tours, , France

Site Status

CHU Hôpital du Bocage/ François Mitterrand Hépato-gastroentérologie

Dijon, , France

Site Status

CHU de Grenoble Oncologie médicale Hépato-gastroentérologie - 7D

Grenoble, , France

Site Status

CHD - Les Oudairies service d'hepato-gastroenterologie

La Roche-sur-Yon, , France

Site Status

Franco-British Institue Department of Medical Oncology

Levallois-Perret, , France

Site Status

Hopital Privé Jean Mermoz Service de Gastro entérologie et d'Oncologie médicale

Lyon, , France

Site Status

CRLCC Léon Bérard Service d'Oncologie

Lyon, , France

Site Status

CHU de la Timone Hépato-Gastro-Entérologie

Marseille, , France

Site Status

Hôpital Nord Franche-Comté - Site du Mittan Service d'oncologie médicale

Montbéliard, , France

Site Status

CRLCC Val d'Aurelle Oncologie Médicale

Montpellier, , France

Site Status

Centre Antoine Lacassagne Dpt d'Oncologie Médicale

Nice, , France

Site Status

Hôpital Saint-Antoine Service d'Oncologie Médicale

Paris, , France

Site Status

Hôpital Européen Georges Pompidou Oncologie Hépatogastroenterologie-oncologie digestive

Paris, , France

Site Status

Groupe Hospitalier Pitié Salpêtrière Service d'hépato-gastro-entérologie

Paris, , France

Site Status

Hôpital Haut-Lévèque Hépato-gastroentérologie et oncologie digestive

Pessac, , France

Site Status

CHU de Poitiers Pole Régional de Cancérologie

Poitiers, , France

Site Status

CHU Robert DEBRE service d'hepato-gastroenterologie / Cancérologie Digestive

Reims, , France

Site Status

Centre Eugène Marquis Service d'Oncologie Médicale

Rennes, , France

Site Status

Hôpital Nord Pôle Digestif Urologie-Andrologie

Saint-Etienne, , France

Site Status

CHU Toulouse Rangueil Oncologie médicale digestive

Toulouse, , France

Site Status

Bon Secours Hospital

Cork, , Ireland

Site Status

The Adelaide and Meath Hospital

Dublin, , Ireland

Site Status

Ist.Tumori "Giovanni Paolo II" IRCCS Osp.Oncologico di Bari U.O.C. di Oncologia Medica

Bari, , Italy

Site Status

Fondazione Poliambulanza Istituto Ospedaliero Clinical Oncology

Brescia, , Italy

Site Status

ARNAS - Azienda Ospedaliera Garibaldi - Nesima Struttura Complessa di Oncologia Medica

Catania, , Italy

Site Status

Azienda Ospedaliero-Universitaria Careggi Struttura Complessa Oncologia Medica

Florence, , Italy

Site Status

Ist.Scientifico Romagnolo per lo Studio e la Cura dei Tumori Department of Clinical Oncology

Meldola, , Italy

Site Status

Fondazione IRCCS Istituto Nazionale dei Tumori S.S. Oncologia Medica Gastrenterologia

Milan, , Italy

Site Status

A.O.U. Seconda Università degli Studi di Napoli U.O.C. di Oncologia Medica e di Ematologia

Napoli, , Italy

Site Status

Istituto Oncologico Veneto IOV - IRCCS Unità Operativa Complessa Oncologia Medica 1

Padua, , Italy

Site Status

Azienda Ospedaliera "Civico-Di Cristina" - Ospedale Civico Oncologia Medica

Palermo, , Italy

Site Status

Ospedale Civile Santo Spirito Struttura Complessa di Oncologia Medica

Pescara, , Italy

Site Status

A.O.U. Pisana-Ospedale Santa Chiara U.O. di Oncologia Medica 2

Pisa, , Italy

Site Status

Arcispedale Santa Maria Nuova Unità di Oncologia

Reggio Emilia, , Italy

Site Status

Ospedale INFERMI Reparto di Oncologia

Rimini, , Italy

Site Status

Policlinico Universitario Campus Biomedico UOC di Oncologia Medica

Roma, , Italy

Site Status

Policlinico Universitario Agostino Gemelli U.O.C. di Oncologia Medica

Roma, , Italy

Site Status

Istituto Clinico Humanitas I.R.C.C.S Dipartimento di Oncologia Medica ed Ematologia

Rozzano (MI), , Italy

Site Status

IRCSS Casa Sollievo della Sofferenza Dipartimento Onco-Ematologia

San Giovanni Rotondo, , Italy

Site Status

A.O.U. Città della Salute e della Scienza di Torino S.C. Oncologia Medica 1 - Colo-Rectal Cancer Unit

Torino, , Italy

Site Status

Centro Hemato-Oncologico de Panama

Panama City, , Panama

Site Status

Bialostockie Centrum Onkologii im Marii Curie-Sklodowskiej Oddzial Onkologii Klinicznej im Dr Ewy Pileckiej z pododdzialem Chemioterapii Dziennej

Bialystok, , Poland

Site Status

Uniwersyteckie Centrum Kliniczne Klinika Onkologii i Radioterapii

Gdansk, , Poland

Site Status

Opolskie Centrum Onkologii im. Tadeusza Koszarowskiego Oddzial Onkologii Klinicznej

Opole, , Poland

Site Status

Wielkopolskie Centrum Onkologii im Marii Sklodowskiej-Curie Oddzial Chemioterapii

Poznan, , Poland

Site Status

Centrum Onkologii - Instytut im. Marii Sklodowskiej-Curie Klinika Gastroenterologii Onkologicznej

Warsaw, , Poland

Site Status

Magodent Sp. z o.o.

Warsaw, , Poland

Site Status

Hospital Garcia de Orta Serviço de Oncologia Médica

Almada, , Portugal

Site Status

Centro Hospitalar e Universitário de Comibra E.P.E. Serviço de Oncologia Médica

Coimbra, , Portugal

Site Status

Instituto Português de Oncologia de Coimbra Serviço de Oncologia Médica

Coimbra, , Portugal

Site Status

Centro Hospitalar de Lisboa Norte E.P.E. - H. Santa Maria Serviço de Oncologia Médica

Lisbon, , Portugal

Site Status

Instituto Português de Oncologia do Porto Serviço de Oncologia Médica

Porto, , Portugal

Site Status

Centro Hospitalar de São João E.P.E. Serviço de Oncologia

Porto, , Portugal

Site Status

Spitalul Clinic "Fundeni" Departament Oncologie Medicala - Gastroenterologie

Bucharest, , Romania

Site Status

Institutul Oncologic "Prof. Dr. I. Chiricuta" Cluj Napoca Oncologie Medicala

Cluj-Napoca, , Romania

Site Status

Institutul Regional de Oncologie Iasi Clinica de Oncologie Medicala

Iași, , Romania

Site Status

Onkologicky ustav sv. Alzbety,s.r.o. Interna Klinika VSZ a SP a OUSA

Bratislava, , Slovakia

Site Status

Vychodoslovensky onkologicky ustav Oddelenie klinickej onkologie

Košice, , Slovakia

Site Status

Onkoloski Institut Ljubljana

Ljubljana, , Slovenia

Site Status

Gazi University Faculty of Medicine Medical Oncology Department

Ankara, , Turkey (Türkiye)

Site Status

Hacettepe University Faculty of Medicine

Ankara, , Turkey (Türkiye)

Site Status

Uludag University Faculty of Medicine

Bursa, , Turkey (Türkiye)

Site Status

Trakya University Faculty of Medicine

Edirne, , Turkey (Türkiye)

Site Status

Istanbul University

Istanbul, , Turkey (Türkiye)

Site Status

Marmara University Pendik Training and Research Hospital

Istanbul, , Turkey (Türkiye)

Site Status

Ege University Faculty of Medicine Medical Oncology Department

Izmir, , Turkey (Türkiye)

Site Status

Erciyes University Mehmet Kemal Dedeman Hematology Oncology

Kayseri, , Turkey (Türkiye)

Site Status

Kharkiv Regional Oncology Center

Kharkiv, , Ukraine

Site Status

Kyiv City Clinical Oncological Centre Day care facility

Kiev, , Ukraine

Site Status

Clinical and diagn.Centre of Medics-rey Inter. Group LLC - Hospital of Israeli Oncology "LISOD

Kyiv, , Ukraine

Site Status

Treatment-diagnostic Centre PJSC "House of medicine"

Odesa, , Ukraine

Site Status

Countries

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Australia Belgium Brazil Bulgaria Croatia France Ireland Italy Panama Poland Portugal Romania Slovakia Slovenia Turkey (Türkiye) Ukraine

References

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Bachet JB, Wyrwicz L, Price T, Cremolini C, Phelip JM, Portales F, Ozet A, Cicin I, Atlan D, Becquart M, Vidot L, Mounedji N, Van Cutsem E, Taieb J, Falcone A. Safety, efficacy and patient-reported outcomes with trifluridine/tipiracil in pretreated metastatic colorectal cancer: results of the PRECONNECT study. ESMO Open. 2020 Jun;5(3):e000698. doi: 10.1136/esmoopen-2020-000698.

Reference Type BACKGROUND
PMID: 32487542 (View on PubMed)

Taieb J, Price T, Vidot L, Chevallier B, Wyrwicz L, Bachet JB. Safety and efficacy of trifluridine/tipiracil in previously treated metastatic colorectal cancer: final results from the phase IIIb single-arm PRECONNECT study by duration of therapy. BMC Cancer. 2023 Jan 27;23(1):94. doi: 10.1186/s12885-022-10489-4.

Reference Type DERIVED
PMID: 36707808 (View on PubMed)

Ozet A, Dane F, Aykan NF, Yalcin S, Evrensel T, Ozkan M, Karabulut B, Ormeci MN, Atasev O, Vidot L, Cicin I. Safety and efficacy of trifluridine/tipiracil in previously treated metastatic colorectal cancer: PRECONNECT Turkey. Future Oncol. 2022 Sep;18(29):3267-3276. doi: 10.2217/fon-2022-0455. Epub 2022 Aug 30.

Reference Type DERIVED
PMID: 36040321 (View on PubMed)

Zaniboni A, Barone CA, Banzi MC, Bergamo F, Blasi L, Bordonaro R, Bartolomeo MD, Costanzo FD, Frassineti GL, Garufi C, Giuliani F, Latiano TP, Martinelli E, Personeni N, Racca P, Tamburini E, Tonini G, Besse MG, Spione M, Falcone A. Italian results of the PRECONNECT study: safety and efficacy of trifluridine/tipiracil in metastatic colorectal cancer. Future Oncol. 2021 Jun;17(18):2315-2324. doi: 10.2217/fon-2020-1278. Epub 2021 Mar 5.

Reference Type DERIVED
PMID: 33663264 (View on PubMed)

Study Documents

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Document Type: Individual Participant Data Set

View Document

Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Document Type: Informed Consent Form

View Document

Document Type: Clinical Study Report

View Document

Document Type: study-level clinical trial data

View Document

Other Identifiers

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2016-002311-18

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

CL3-95005-004

Identifier Type: -

Identifier Source: org_study_id

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