Trial Outcomes & Findings for Controlled Trial Evaluating Avacopan in C3 Glomerulopathy (NCT NCT03301467)

NCT ID: NCT03301467

Last Updated: 2025-03-13

Results Overview

Change from baseline to Week 26 in the biopsy-based C3G Histologic Index for disease activity - Subjects with Elevated C5b-9 (\> 244 ng/mL) in the Intent-to-Treat Population. C3G Histological Index for Disease Activity Scores can range from 0 to 21. A decrease indicates improvement. C3G=C3 glomerulopathy

Recruitment status

COMPLETED

Study phase

PHASE2

Target enrollment

57 participants

Primary outcome timeframe

Week 26

Results posted on

2025-03-13

Participant Flow

Participant milestones

Participant milestones
Measure
Placebo Group
Avacopan-matching placebo capsules x 3 administered twice daily during the 26 week blinded treatment period period Avacopan-matching placebo: Orally administered
Avacopan Group
Avacopan (formerly CCX168) 10 mg capsules x 3 administered twice daily during the blinded 26 week blinded treatment period Avacopan: Orally administered
Overall Study
STARTED
29
28
Overall Study
COMPLETED
25
25
Overall Study
NOT COMPLETED
4
3

Reasons for withdrawal

Withdrawal data not reported

Baseline Characteristics

2 patients missed baseline Urinary MCP-1 data.

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Placebo Group
n=29 Participants
Avacopan-matching placebo capsules x 3 administered twice daily during the 26 week blinded treatment period period Avacopan-matching placebo: Orally administered
Avacopan Group
n=28 Participants
Avacopan (formerly CCX168) 10 mg capsules x 3 administered twice daily during the blinded 26 week blinded treatment period Avacopan: Orally administered
Total
n=57 Participants
Total of all reporting groups
Age, Continuous
37.2 years
STANDARD_DEVIATION 17.53 • n=29 Participants
32.2 years
STANDARD_DEVIATION 15.03 • n=28 Participants
34.7 years
STANDARD_DEVIATION 16.39 • n=57 Participants
Age, Customized
12-17 years
2 Participants
n=29 Participants
0 Participants
n=28 Participants
2 Participants
n=57 Participants
Age, Customized
18-50 years
20 Participants
n=29 Participants
23 Participants
n=28 Participants
43 Participants
n=57 Participants
Age, Customized
51-65 years
4 Participants
n=29 Participants
4 Participants
n=28 Participants
8 Participants
n=57 Participants
Age, Customized
>65 years
3 Participants
n=29 Participants
1 Participants
n=28 Participants
4 Participants
n=57 Participants
Sex: Female, Male
Female
13 Participants
n=29 Participants
9 Participants
n=28 Participants
22 Participants
n=57 Participants
Sex: Female, Male
Male
16 Participants
n=29 Participants
19 Participants
n=28 Participants
35 Participants
n=57 Participants
Ethnicity (NIH/OMB)
Hispanic or Latino
4 Participants
n=29 Participants
2 Participants
n=28 Participants
6 Participants
n=57 Participants
Ethnicity (NIH/OMB)
Not Hispanic or Latino
25 Participants
n=29 Participants
26 Participants
n=28 Participants
51 Participants
n=57 Participants
Ethnicity (NIH/OMB)
Unknown or Not Reported
0 Participants
n=29 Participants
0 Participants
n=28 Participants
0 Participants
n=57 Participants
Race (NIH/OMB)
American Indian or Alaska Native
0 Participants
n=29 Participants
0 Participants
n=28 Participants
0 Participants
n=57 Participants
Race (NIH/OMB)
Asian
3 Participants
n=29 Participants
2 Participants
n=28 Participants
5 Participants
n=57 Participants
Race (NIH/OMB)
Native Hawaiian or Other Pacific Islander
0 Participants
n=29 Participants
0 Participants
n=28 Participants
0 Participants
n=57 Participants
Race (NIH/OMB)
Black or African American
0 Participants
n=29 Participants
1 Participants
n=28 Participants
1 Participants
n=57 Participants
Race (NIH/OMB)
White
25 Participants
n=29 Participants
24 Participants
n=28 Participants
49 Participants
n=57 Participants
Race (NIH/OMB)
More than one race
0 Participants
n=29 Participants
0 Participants
n=28 Participants
0 Participants
n=57 Participants
Race (NIH/OMB)
Unknown or Not Reported
1 Participants
n=29 Participants
1 Participants
n=28 Participants
2 Participants
n=57 Participants
Region of Enrollment
Canada
2 participants
n=29 Participants
3 participants
n=28 Participants
5 participants
n=57 Participants
Region of Enrollment
Netherlands
5 participants
n=29 Participants
1 participants
n=28 Participants
6 participants
n=57 Participants
Region of Enrollment
Belgium
1 participants
n=29 Participants
2 participants
n=28 Participants
3 participants
n=57 Participants
Region of Enrollment
United States
10 participants
n=29 Participants
11 participants
n=28 Participants
21 participants
n=57 Participants
Region of Enrollment
Ireland
3 participants
n=29 Participants
3 participants
n=28 Participants
6 participants
n=57 Participants
Region of Enrollment
Denmark
1 participants
n=29 Participants
1 participants
n=28 Participants
2 participants
n=57 Participants
Region of Enrollment
Italy
1 participants
n=29 Participants
0 participants
n=28 Participants
1 participants
n=57 Participants
Region of Enrollment
United Kingdom
2 participants
n=29 Participants
2 participants
n=28 Participants
4 participants
n=57 Participants
Region of Enrollment
Germany
2 participants
n=29 Participants
1 participants
n=28 Participants
3 participants
n=57 Participants
Region of Enrollment
Spain
2 participants
n=29 Participants
4 participants
n=28 Participants
6 participants
n=57 Participants
Geographic Region
North America
12 Participants
n=29 Participants
14 Participants
n=28 Participants
26 Participants
n=57 Participants
Geographic Region
Rest of World
17 Participants
n=29 Participants
14 Participants
n=28 Participants
31 Participants
n=57 Participants
Age at Diagnosis of C3G
33.3 years
STANDARD_DEVIATION 17.95 • n=29 Participants
28.2 years
STANDARD_DEVIATION 17.08 • n=28 Participants
30.8 years
STANDARD_DEVIATION 17.56 • n=57 Participants
C3GN or DDD
C3GN
25 Participants
n=29 Participants
23 Participants
n=28 Participants
48 Participants
n=57 Participants
C3GN or DDD
DDD
4 Participants
n=29 Participants
4 Participants
n=28 Participants
8 Participants
n=57 Participants
C3GN or DDD
Missing
0 Participants
n=29 Participants
1 Participants
n=28 Participants
1 Participants
n=57 Participants
History of Kidney Transplant
Yes
2 Participants
n=29 Participants
1 Participants
n=28 Participants
3 Participants
n=57 Participants
History of Kidney Transplant
No
27 Participants
n=29 Participants
26 Participants
n=28 Participants
53 Participants
n=57 Participants
History of Kidney Transplant
Missing
0 Participants
n=29 Participants
1 Participants
n=28 Participants
1 Participants
n=57 Participants
C5b-9 Stratum
> 244 ng/mL
22 Participants
n=29 Participants
21 Participants
n=28 Participants
43 Participants
n=57 Participants
C5b-9 Stratum
<= 244 ng/mL
7 Participants
n=29 Participants
7 Participants
n=28 Participants
14 Participants
n=57 Participants
Duration of C3G
46.7 months
STANDARD_DEVIATION 43.78 • n=29 Participants
48.2 months
STANDARD_DEVIATION 46.38 • n=28 Participants
47.4 months
STANDARD_DEVIATION 44.68 • n=57 Participants
eGFR
72.34 mL/min/1.73m²
STANDARD_DEVIATION 43.509 • n=29 Participants
79.29 mL/min/1.73m²
STANDARD_DEVIATION 39.751 • n=28 Participants
75.75 mL/min/1.73m²
STANDARD_DEVIATION 41.480 • n=57 Participants
UPCR
2.80 g/g
STANDARD_DEVIATION 2.435 • n=29 Participants
4.11 g/g
STANDARD_DEVIATION 3.380 • n=28 Participants
3.44 g/g
STANDARD_DEVIATION 2.985 • n=57 Participants
UPCR (g/g)
> 1 g/g
21 Participants
n=29 Participants
22 Participants
n=28 Participants
43 Participants
n=57 Participants
UPCR (g/g)
<= 1 g/g
8 Participants
n=29 Participants
6 Participants
n=28 Participants
14 Participants
n=57 Participants
Urinary MCP-1:Creatinine Ratio
750.29 pg/mg Creatinine
STANDARD_DEVIATION 492.542 • n=28 Participants • 2 patients missed baseline Urinary MCP-1 data.
1215.88 pg/mg Creatinine
STANDARD_DEVIATION 1303.359 • n=27 Participants • 2 patients missed baseline Urinary MCP-1 data.
978.85 pg/mg Creatinine
STANDARD_DEVIATION 997.191 • n=55 Participants • 2 patients missed baseline Urinary MCP-1 data.
Body Weight
72.65 kilogram(s)
STANDARD_DEVIATION 12.631 • n=29 Participants
78.33 kilogram(s)
STANDARD_DEVIATION 19.229 • n=28 Participants
75.44 kilogram(s)
STANDARD_DEVIATION 16.317 • n=57 Participants
Height
171.41 centimeter(s)
STANDARD_DEVIATION 8.773 • n=29 Participants
173.82 centimeter(s)
STANDARD_DEVIATION 10.805 • n=28 Participants
172.60 centimeter(s)
STANDARD_DEVIATION 9.810 • n=57 Participants
BMI
24.65 kilogram(s)/square meter
STANDARD_DEVIATION 3.410 • n=29 Participants
26.05 kilogram(s)/square meter
STANDARD_DEVIATION 6.375 • n=28 Participants
25.34 kilogram(s)/square meter
STANDARD_DEVIATION 5.090 • n=57 Participants
EQ-5D-5L Index Score
0.88 units on a scale
STANDARD_DEVIATION 0.145 • n=29 Participants
0.87 units on a scale
STANDARD_DEVIATION 0.116 • n=28 Participants
0.88 units on a scale
STANDARD_DEVIATION 0.130 • n=57 Participants
EQ-5D-5L VAS Score
78.83 units on a scale
STANDARD_DEVIATION 20.604 • n=29 Participants
73.61 units on a scale
STANDARD_DEVIATION 19.070 • n=28 Participants
76.26 units on a scale
STANDARD_DEVIATION 19.862 • n=57 Participants
Viral Test Results HIV-1/2 Antibody
Reactive
0 Participants
n=29 Participants
0 Participants
n=28 Participants
0 Participants
n=57 Participants
Viral Test Results HIV-1/2 Antibody
Non-reactive
29 Participants
n=29 Participants
28 Participants
n=28 Participants
57 Participants
n=57 Participants
Viral Test Results - Hepatitis B Virus Surface Antigen
Reactive
0 Participants
n=29 Participants
0 Participants
n=28 Participants
0 Participants
n=57 Participants
Viral Test Results - Hepatitis B Virus Surface Antigen
Non-reactive
29 Participants
n=29 Participants
28 Participants
n=28 Participants
57 Participants
n=57 Participants
Viral Test Results - Hepatitis C Virus Antibody
Reactive
0 Participants
n=29 Participants
1 Participants
n=28 Participants
1 Participants
n=57 Participants
Viral Test Results - Hepatitis C Virus Antibody
Non-reactive
29 Participants
n=29 Participants
27 Participants
n=28 Participants
56 Participants
n=57 Participants

PRIMARY outcome

Timeframe: Week 26

Population: Subjects with Elevated C5b-9 (\> 244 ng/mL) in the Intent-to-Treat (ITT) Population. The number of subjects with data at baseline and the specified visit is reported. ITT Population: The ITT Population included all randomized subjects who received at least one dose of study medication; subjects with a histologic activity score of 0 at baseline or who were ongoing and had not completed the Week 26 visit were not included in the ITT population.

Change from baseline to Week 26 in the biopsy-based C3G Histologic Index for disease activity - Subjects with Elevated C5b-9 (\> 244 ng/mL) in the Intent-to-Treat Population. C3G Histological Index for Disease Activity Scores can range from 0 to 21. A decrease indicates improvement. C3G=C3 glomerulopathy

Outcome measures

Outcome measures
Measure
Placebo Group
n=21 Participants
Avacopan-matching placebo capsules x 3 administered twice daily during the 26 week blinded treatment period period Avacopan-matching placebo: Orally administered
Avacopan Group
n=19 Participants
Avacopan (formerly CCX168) 10 mg capsules x 3 administered twice daily during the blinded 26 week blinded treatment period Avacopan: Orally administered
Change From Baseline to Week 26 in the C3G Histologic Index for Disease Activity - Subjects With Elevated C5b-9
-0.9 score on a scale
Interval -2.2 to 0.4
-1.0 score on a scale
Interval -2.3 to 0.4

PRIMARY outcome

Timeframe: Week 26

Population: Combined C5b-9 Strata (elevated \[\> 244 ng/mL\] and non-elevated C5b-9) in the Intent-to-Treat (ITT) Population ITT Population: The ITT Population included all randomized subjects who received at least one dose of study medication; subjects with a histologic activity score of 0 at baseline or who were ongoing and had not completed the Week 26 visit were not included in the ITT population.

Percent change from baseline to Week 26 in the biopsy-based C3G Histologic Index for disease activity - Combined C5b-9 Strata (elevated \[\> 244 ng/mL\] and non-elevated C5b-9) in the Intent-to-Treat Population. C3G Histological Index for Disease Activity Scores can range from 0 to 21. A decrease indicates improvement. C3G=C3 glomerulopathy \* Multiple Imputation: Missing Week 26 values are imputed using the regression method to create 100 complete datasets.

Outcome measures

Outcome measures
Measure
Placebo Group
n=26 Participants
Avacopan-matching placebo capsules x 3 administered twice daily during the 26 week blinded treatment period period Avacopan-matching placebo: Orally administered
Avacopan Group
n=26 Participants
Avacopan (formerly CCX168) 10 mg capsules x 3 administered twice daily during the blinded 26 week blinded treatment period Avacopan: Orally administered
Percent Change From Baseline to Week 26 in the C3G Histologic Index for Disease Activity - Combined C5b-9 Strata
26.20 Percentage change
Standard Error 47.302
-5.77 Percentage change
Standard Error 5.904

SECONDARY outcome

Timeframe: Week 26

Population: Subjects with Elevated C5b-9 (\> 244 ng/mL) in the Intent-to-Treat (ITT) Population. The number of subjects with C3G Histological Index of Disease Activity Percent Change at Week 26 is reported. ITT Population: The ITT Population included all randomized subjects who received at least one dose of study medication; subjects with a histologic activity score of 0 at baseline or who were ongoing and had not completed the Week 26 visit were not included in the ITT population.

Proportion of subjects who have a histologic response defined as a decrease (improvement) in the biopsy-based C3G Histologic Index for activity of at least 35% from baseline to 26 weeks - Subjects with Elevated C5b-9 (\> 244 ng/mL) in the Intent-to-Treat Population. C3G Histological Index for Disease Activity Scores can range from 0 to 21. A decrease indicates improvement. C3G=C3 glomerulopathy

Outcome measures

Outcome measures
Measure
Placebo Group
n=20 Participants
Avacopan-matching placebo capsules x 3 administered twice daily during the 26 week blinded treatment period period Avacopan-matching placebo: Orally administered
Avacopan Group
n=18 Participants
Avacopan (formerly CCX168) 10 mg capsules x 3 administered twice daily during the blinded 26 week blinded treatment period Avacopan: Orally administered
Proportion of Subjects Who Have a Histologic Response Defined as a Decrease (Improvement) in the Biopsy-based C3G Histologic Index for Activity of at Least 35% From Baseline to 26 Weeks - Subjects With Elevated C5b-9
Responder
4 Participants
2 Participants
Proportion of Subjects Who Have a Histologic Response Defined as a Decrease (Improvement) in the Biopsy-based C3G Histologic Index for Activity of at Least 35% From Baseline to 26 Weeks - Subjects With Elevated C5b-9
Non-Responder
16 Participants
16 Participants

SECONDARY outcome

Timeframe: Week 26

Population: Combined C5b-9 Strata (elevated \[\> 244 ng/mL\] and non-elevated C5b-9) in the Intent-to-Treat (ITT) Population. The number of subjects with C3G Histological Index of Disease Activity Percent Change at Week 26 is reported. The ITT Population included all randomized subjects who received at least one dose of study medication; subjects with a histologic activity score of 0 at baseline or who were ongoing and had not completed the Week 26 visit were not included in the ITT population.

Proportion of subjects who have a histologic response defined as a decrease (improvement) in the biopsy-based C3G Histologic Index for activity of at least 35% from baseline to 26 weeks - Combined C5b-9 Strata (elevated \[\> 244 ng/mL\] and non-elevated C5b-9) in the Intent-to-Treat Population. C3G Histological Index for Disease Activity Scores can range from 0 to 21. A decrease indicates improvement. C3G=C3 glomerulopathy

Outcome measures

Outcome measures
Measure
Placebo Group
n=25 Participants
Avacopan-matching placebo capsules x 3 administered twice daily during the 26 week blinded treatment period period Avacopan-matching placebo: Orally administered
Avacopan Group
n=25 Participants
Avacopan (formerly CCX168) 10 mg capsules x 3 administered twice daily during the blinded 26 week blinded treatment period Avacopan: Orally administered
Proportion of Subjects Who Have a Histologic Response Defined as a Decrease (Improvement) in the Biopsy-based C3G Histologic Index for Activity of at Least 35% From Baseline to 26 Weeks - Combined C5b-9 Strata
Responder
7 Participants
4 Participants
Proportion of Subjects Who Have a Histologic Response Defined as a Decrease (Improvement) in the Biopsy-based C3G Histologic Index for Activity of at Least 35% From Baseline to 26 Weeks - Combined C5b-9 Strata
Non-Responder
18 Participants
21 Participants

SECONDARY outcome

Timeframe: Week 26

Population: Subjects with Elevated C5b-9 (\> 244 ng/mL) in the Intent-to-Treat (ITT) Population. The number of subjects with data at baseline and the specified visit is reported. ITT Population: The ITT Population included all randomized subjects who received at least one dose of study medication; subjects with a histologic activity score of 0 at baseline or who were ongoing and had not completed the Week 26 visit were not included in the ITT population.

Change from baseline to Week 26 in the biopsy-based C3G Histologic Index for disease chronicity over the placebo-controlled treatment period - Subjects with Elevated C5b-9 (\> 244 ng/mL) in the Intent-to-Treat Population. C3G Histological Index for Disease Chronicity Scores can range from 0 to 10. A decrease indicates improvement. C3G=C3 glomerulopathy

Outcome measures

Outcome measures
Measure
Placebo Group
n=21 Participants
Avacopan-matching placebo capsules x 3 administered twice daily during the 26 week blinded treatment period period Avacopan-matching placebo: Orally administered
Avacopan Group
n=19 Participants
Avacopan (formerly CCX168) 10 mg capsules x 3 administered twice daily during the blinded 26 week blinded treatment period Avacopan: Orally administered
Change From Baseline to Week 26 in the C3G Histologic Index for Disease Chronicity - Subjects With Elevated C5b-9
1.5 score on a scale
Interval 0.9 to 2.2
1.1 score on a scale
Interval 0.3 to 1.8

SECONDARY outcome

Timeframe: Week 26

Population: Combined C5b-9 Strata (elevated \[\> 244 ng/mL\] and non-elevated C5b-9) in the Intent-to-Treat (ITT) Population. The number of subjects with data at baseline and the specified visit is reported. ITT Population: The ITT Population included all randomized subjects who received at least one dose of study medication; subjects with a histologic activity score of 0 at baseline or who were ongoing and had not completed the Week 26 visit were not included in the ITT population.

Change from baseline to Week 26 in the biopsy-based C3G Histologic Index for disease chronicity over the placebo-controlled treatment period - Combined C5b-9 Strata (elevated \[\> 244 ng/mL\] and non-elevated C5b-9) in the Intent-to-Treat Population. C3G Histological Index for Disease Chronicity Scores can range from 0 to 10. A decrease indicates improvement. C3G=C3 glomerulopathy

Outcome measures

Outcome measures
Measure
Placebo Group
n=26 Participants
Avacopan-matching placebo capsules x 3 administered twice daily during the 26 week blinded treatment period period Avacopan-matching placebo: Orally administered
Avacopan Group
n=26 Participants
Avacopan (formerly CCX168) 10 mg capsules x 3 administered twice daily during the blinded 26 week blinded treatment period Avacopan: Orally administered
Change From Baseline to Week 26 in the C3G Histologic Index for Disease Chronicity - Combined C5b-9 Strata
1.6 score on a scale
Interval 1.1 to 2.2
0.8 score on a scale
Interval 0.2 to 1.4

SECONDARY outcome

Timeframe: Week 26

Population: Subjects with Elevated C5b-9 (\> 244 ng/mL) in the Intent-to-Treat (ITT) Population. The number of subjects with data at baseline and the specified visit is reported. ITT Population: The ITT Population included all randomized subjects who received at least one dose of study medication; subjects with a histologic activity score of 0 at baseline or who were ongoing and had not completed the Week 26 visit were not included in the ITT population.

The percent change from baseline over 26 weeks in estimated Glomerular Filtration Rate (eGFR) - Subjects with Elevated C5b-9 (\> 244 ng/mL) in the Intent-to-Treat Population.

Outcome measures

Outcome measures
Measure
Placebo Group
n=20 Participants
Avacopan-matching placebo capsules x 3 administered twice daily during the 26 week blinded treatment period period Avacopan-matching placebo: Orally administered
Avacopan Group
n=18 Participants
Avacopan (formerly CCX168) 10 mg capsules x 3 administered twice daily during the blinded 26 week blinded treatment period Avacopan: Orally administered
Renal Function as Assessed by Percent Change From Baseline Over 26 Weeks in eGFR - Subjects With Elevated C5b-9
-4.73 Percentage change
Interval -12.29 to 2.83
6.11 Percentage change
Interval -1.86 to 14.08

SECONDARY outcome

Timeframe: Week 26

Population: Combined C5b-9 Strata (elevated \[\> 244 ng/mL\] and non-elevated C5b-9) in the Intent-to-Treat (ITT) Population. The number of subjects with data at baseline and the specified visit is reported. ITT Population: The ITT Population included all randomized subjects who received at least one dose of study medication; subjects with a histologic activity score of 0 at baseline or who were ongoing and had not completed the Week 26 visit were not included in the ITT population.

The percent change from baseline over 26 weeks in estimated Glomerular Filtration Rate (eGFR) - Combined C5b-9 Strata (elevated \[\> 244 ng/mL\] and non-elevated C5b-9) in the Intent-to-Treat Population.

Outcome measures

Outcome measures
Measure
Placebo Group
n=25 Participants
Avacopan-matching placebo capsules x 3 administered twice daily during the 26 week blinded treatment period period Avacopan-matching placebo: Orally administered
Avacopan Group
n=25 Participants
Avacopan (formerly CCX168) 10 mg capsules x 3 administered twice daily during the blinded 26 week blinded treatment period Avacopan: Orally administered
Renal Function as Assessed by Percent Change From Baseline Over 26 Weeks in eGFR - Combined C5b-9 Strata
-5.88 Percentage change
Interval -12.32 to 0.56
4.79 Percentage change
Interval -1.66 to 11.23

SECONDARY outcome

Timeframe: Week 26

Population: Subjects with Elevated C5b-9 (\> 244 ng/mL) in the Intent-to-Treat (ITT) Population. The number of subjects with data at baseline and the specified visit is reported. ITT Population: The ITT Population included all randomized subjects who received at least one dose of study medication; subjects with a histologic activity score of 0 at baseline or who were ongoing and had not completed the Week 26 visit were not included in the ITT population.

The change from baseline over 26 weeks in estimated Glomerular Filtration Rate (eGFR) - Subjects with Elevated C5b-9 (\> 244 ng/mL) in the Intent-to-Treat Population.

Outcome measures

Outcome measures
Measure
Placebo Group
n=20 Participants
Avacopan-matching placebo capsules x 3 administered twice daily during the 26 week blinded treatment period period Avacopan-matching placebo: Orally administered
Avacopan Group
n=18 Participants
Avacopan (formerly CCX168) 10 mg capsules x 3 administered twice daily during the blinded 26 week blinded treatment period Avacopan: Orally administered
Renal Function as Assessed by Change From Baseline Over 26 Weeks in eGFR - Subjects With Elevated C5b-9
-3.57 mL/min/1.73m^2
Interval -8.43 to 1.29
0.44 mL/min/1.73m^2
Interval -4.69 to 5.56

SECONDARY outcome

Timeframe: Week 26

Population: Combined C5b-9 Strata (elevated \[\> 244 ng/mL\] and non-elevated C5b-9) in the Intent-to-Treat (ITT) Population. The number of subjects with data at baseline and the specified visit is reported. ITT Population: The ITT Population included all randomized subjects who received at least one dose of study medication; subjects with a histologic activity score of 0 at baseline or who were ongoing and had not completed the Week 26 visit were not included in the ITT population.

The change from baseline over 26 weeks in estimated Glomerular Filtration Rate (eGFR) - Combined C5b-9 Strata (elevated \[\> 244 ng/mL\] and non-elevated C5b-9) in the Intent-to-Treat Population.

Outcome measures

Outcome measures
Measure
Placebo Group
n=25 Participants
Avacopan-matching placebo capsules x 3 administered twice daily during the 26 week blinded treatment period period Avacopan-matching placebo: Orally administered
Avacopan Group
n=25 Participants
Avacopan (formerly CCX168) 10 mg capsules x 3 administered twice daily during the blinded 26 week blinded treatment period Avacopan: Orally administered
Renal Function as Assessed by Change From Baseline Over 26 Weeks in eGFR - Combined C5b-9 Strata
-3.35 mL/min/1.73m^2
Interval -7.56 to 0.85
0.47 mL/min/1.73m^2
Interval -3.75 to 4.68

SECONDARY outcome

Timeframe: Week 26

Population: Subjects with Elevated C5b-9 (\> 244 ng/mL) in the Intent-to-Treat (ITT) Population. The number of subjects with data at baseline and the specified visit is reported. ITT Population: The ITT Population included all randomized subjects who received at least one dose of study medication; subjects with a histologic activity score of 0 at baseline or who were ongoing and had not completed the Week 26 visit were not included in the ITT population.

Percent change from baseline Over 26 Weeks in UPCR in patients with Abnormal UPCR at Baseline (\>= 0.15 g/g) - Subjects with Elevated C5b-9 (\> 244 ng/mL) in the Intent-to-Treat Population. LSM=Least Squares Mean; UPCR = Urine Protein : Creatinine Ratio

Outcome measures

Outcome measures
Measure
Placebo Group
n=20 Participants
Avacopan-matching placebo capsules x 3 administered twice daily during the 26 week blinded treatment period period Avacopan-matching placebo: Orally administered
Avacopan Group
n=18 Participants
Avacopan (formerly CCX168) 10 mg capsules x 3 administered twice daily during the blinded 26 week blinded treatment period Avacopan: Orally administered
Percent Change From Baseline Over 26 Weeks in UPCR in Patients With Abnormal UPCR at Baseline - Subjects With Elevated C5b-9
-14 Percentage change
Interval -34.0 to 12.0
-16 Percentage change
Interval -36.0 to 12.0

SECONDARY outcome

Timeframe: Week 26

Population: Combined C5b-9 Strata (elevated \[\> 244 ng/mL\] and non-elevated C5b-9) in the Intent-to-Treat (ITT) Population. The number of subjects with data at baseline and the specified visit is reported. ITT Population: The ITT Population included all randomized subjects who received at least one dose of study medication; subjects with a histologic activity score of 0 at baseline or who were ongoing and had not completed the Week 26 visit were not included in the ITT population.

Percent change from baseline Over 26 Weeks in UPCR in patients with Abnormal UPCR at Baseline (\>= 0.15 g/g) - Combined C5b-9 Strata (elevated \[\> 244 ng/mL\] and non-elevated C5b-9) in the Intent-to-Treat Population. LSM=Least Squares Mean; UPCR = Urine Protein : Creatinine Ratio

Outcome measures

Outcome measures
Measure
Placebo Group
n=25 Participants
Avacopan-matching placebo capsules x 3 administered twice daily during the 26 week blinded treatment period period Avacopan-matching placebo: Orally administered
Avacopan Group
n=24 Participants
Avacopan (formerly CCX168) 10 mg capsules x 3 administered twice daily during the blinded 26 week blinded treatment period Avacopan: Orally administered
Percent Change From Baseline Over 26 Weeks in UPCR in Patients With Abnormal UPCR at Baseline - Combined C5b-9 Strata
-14 Percentage change
Interval -33.0 to 10.0
-26 Percentage change
Interval -42.0 to -6.0

SECONDARY outcome

Timeframe: Week 26

Population: Subjects with Elevated C5b-9 (\> 244 ng/mL) in the Intent-to-Treat (ITT) Population. The number of subjects with data at baseline and the specified visit is reported. ITT Population: The ITT Population included all randomized subjects who received at least one dose of study medication; subjects with a histologic activity score of 0 at baseline or who were ongoing and had not completed the Week 26 visit were not included in the ITT population.

Percent change from baseline over 26 weeks in urinary MCP-1: creatinine ratio - Subjects with Elevated C5b-9 (\> 244 ng/mL) in the Intent-to-Treat Population. LSM=Least Squares Mean; MCP-1=Monocyte Chemoattractant Protein-1

Outcome measures

Outcome measures
Measure
Placebo Group
n=19 Participants
Avacopan-matching placebo capsules x 3 administered twice daily during the 26 week blinded treatment period period Avacopan-matching placebo: Orally administered
Avacopan Group
n=17 Participants
Avacopan (formerly CCX168) 10 mg capsules x 3 administered twice daily during the blinded 26 week blinded treatment period Avacopan: Orally administered
Percent Change From Baseline Over 26 Weeks in Urinary MCP-1 - Subjects With Elevated C5b-9
1 Percentage change
Interval -18.0 to 25.0
-23 Percentage change
Interval -39.0 to -4.0

SECONDARY outcome

Timeframe: Week 26

Population: Combined C5b-9 Strata (elevated \[\> 244 ng/mL\] and non-elevated C5b-9) in the Intent-to-Treat (ITT) Population. The number of subjects with data at baseline and the specified visit is reported. ITT Population: The ITT Population included all randomized subjects who received at least one dose of study medication; subjects with a histologic activity score of 0 at baseline or who were ongoing and had not completed the Week 26 visit were not included in the ITT population.

Percent change from baseline over 26 weeks in urinary MCP-1: creatinine ratio - Combined C5b-9 Strata (elevated \[\> 244 ng/mL\] and non-elevated C5b-9) in the Intent-to-Treat Population. LSM=Least Squares Mean; MCP-1=Monocyte Chemoattractant Protein-1

Outcome measures

Outcome measures
Measure
Placebo Group
n=24 Participants
Avacopan-matching placebo capsules x 3 administered twice daily during the 26 week blinded treatment period period Avacopan-matching placebo: Orally administered
Avacopan Group
n=23 Participants
Avacopan (formerly CCX168) 10 mg capsules x 3 administered twice daily during the blinded 26 week blinded treatment period Avacopan: Orally administered
Percent Change From Baseline Over 26 Weeks in Urinary MCP-1 - Combined C5b-9 Strata
1 Percentage change
Interval -17.0 to 23.0
-12 Percentage change
Interval -28.0 to 7.0

SECONDARY outcome

Timeframe: Week 26

Population: Subjects with Elevated C5b-9 (\> 244 ng/mL) in the Intent-to-Treat (ITT) Population. The number of subjects with data at baseline and the specified visit is reported. ITT Population: The ITT Population included all randomized subjects who received at least one dose of study medication; subjects with a histologic activity score of 0 at baseline or who were ongoing and had not completed the Week 26 visit were not included in the ITT population.

Change from baseline over 26 weeks in EQ-5D-5L Health Scale VAS and Index Score - Subjects with Elevated C5b-9 (\> 244 ng/mL) in the Intent-to-Treat Population. EQ-5D-5L: EuroQuality of Life-5 Domains-5 Levels. The EQ-5D-5L consists of 2 pages: the EQ-5D descriptive system and the EQ visual analogue scale (EQ VAS). The descriptive system comprises five dimensions: mobility, self-care, usual activities, pain/discomfort and anxiety/depression. Each dimension has 5 levels: no problems, slight problems, moderate problems, severe problems and extreme problems. The answers given can be converted into an Index Score ranging from 0 for death to 1 for perfect health. The EQ-5D questionnaire also includes a Visual Analog Scale (VAS), by which respondents can report their perceived health status with a grade ranging from 0 (the worst imaginable health) to 100 (the best imaginable health).

Outcome measures

Outcome measures
Measure
Placebo Group
n=20 Participants
Avacopan-matching placebo capsules x 3 administered twice daily during the 26 week blinded treatment period period Avacopan-matching placebo: Orally administered
Avacopan Group
n=18 Participants
Avacopan (formerly CCX168) 10 mg capsules x 3 administered twice daily during the blinded 26 week blinded treatment period Avacopan: Orally administered
Change From Baseline Over 26 Weeks in EQ-5D-5L Health Scale VAS and Index Score - Subjects With Elevated C5b-9
EQ-5D-5L Index Score
0.0220 score on a scale
Interval -0.0206 to 0.0647
-0.0202 score on a scale
Interval -0.0653 to 0.0249
Change From Baseline Over 26 Weeks in EQ-5D-5L Health Scale VAS and Index Score - Subjects With Elevated C5b-9
EQ-5D-5L VAS Score
-3.5 score on a scale
Interval -7.8 to 0.8
-1.9 score on a scale
Interval -6.4 to 2.7

SECONDARY outcome

Timeframe: Week 26

Population: Combined C5b-9 Strata (elevated \[\> 244 ng/mL\] and non-elevated C5b-9) in the Intent-to-Treat (ITT) Population. The number of subjects with data at baseline and the specified visit is reported. ITT Population: The ITT Population included all randomized subjects who received at least one dose of study medication; subjects with a histologic activity score of 0 at baseline or who were ongoing and had not completed the Week 26 visit were not included in the ITT population.

Change from baseline over 26 weeks in EQ-5D-5L Health Scale VAS and Index Score - Combined C5b-9 Strata (elevated \[\> 244 ng/mL\] and non-elevated C5b-9) in the Intent-to-Treat Population. EQ-5D-5L: EuroQuality of Life-5 Domains-5 Levels. The EQ-5D-5L consists of 2 pages: the EQ-5D descriptive system and the EQ visual analogue scale (EQ VAS). The descriptive system comprises five dimensions: mobility, self-care, usual activities, pain/discomfort and anxiety/depression. Each dimension has 5 levels: no problems, slight problems, moderate problems, severe problems and extreme problems. The answers given can be converted into an Index Score ranging from 0 for death to 1 for perfect health. The EQ-5D questionnaire also includes a Visual Analog Scale (VAS), by which respondents can report their perceived health status with a grade ranging from 0 (the worst imaginable health) to 100 (the best imaginable health).

Outcome measures

Outcome measures
Measure
Placebo Group
n=25 Participants
Avacopan-matching placebo capsules x 3 administered twice daily during the 26 week blinded treatment period period Avacopan-matching placebo: Orally administered
Avacopan Group
n=25 Participants
Avacopan (formerly CCX168) 10 mg capsules x 3 administered twice daily during the blinded 26 week blinded treatment period Avacopan: Orally administered
Change From Baseline Over 26 Weeks in EQ-5D-5L Health Scale VAS and Index Score - Combined C5b-9 Strata
EQ-5D-5L VAS Score
0.1 score on a scale
Interval -3.9 to 4.2
-1.9 score on a scale
Interval -6.0 to 2.2
Change From Baseline Over 26 Weeks in EQ-5D-5L Health Scale VAS and Index Score - Combined C5b-9 Strata
EQ-5D-5L Index Score
0.0060 score on a scale
Interval -0.0334 to 0.0454
-0.0138 score on a scale
Interval -0.0533 to 0.0256

SECONDARY outcome

Timeframe: Week 26

Population: Subjects with Elevated C5b-9 (\> 244 ng/mL) in the Intent-to-Treat (ITT) Population. The number of subjects with data at baseline and the specified visit is reported. ITT Population: The ITT Population included all randomized subjects who received at least one dose of study medication; subjects with a histologic activity score of 0 at baseline or who were ongoing and had not completed the Week 26 visit were not included in the ITT population.

Change from baseline over 26 weeks in SF-36 v2 - Subjects with Elevated C5b-9 (\> 244 ng/mL) in the Intent-to-Treat Population. SF-36v2: Medical Outcomes Survey Short Form-36 version 2. SF-36v2 measures each of the following eight health domains: Physical Functioning, Role-Physical, Bodily Pain, General Health, Vitality, Social Functioning, Role-Emotional, and Mental Health. Scores on each item are summed and averaged. The SF-36v2 component domain scores range from 0 (worst health) to 100 (best health).

Outcome measures

Outcome measures
Measure
Placebo Group
n=21 Participants
Avacopan-matching placebo capsules x 3 administered twice daily during the 26 week blinded treatment period period Avacopan-matching placebo: Orally administered
Avacopan Group
n=19 Participants
Avacopan (formerly CCX168) 10 mg capsules x 3 administered twice daily during the blinded 26 week blinded treatment period Avacopan: Orally administered
Change From Baseline Over 26 Weeks in SF-36 v2 - Subjects With Elevated C5b-9
SF-36v2: Physical Functioning
2.8518 score on a scale
Interval -3.2409 to 8.9446
3.2197 score on a scale
Interval -3.3108 to 9.7502
Change From Baseline Over 26 Weeks in SF-36 v2 - Subjects With Elevated C5b-9
SF-36v2: Role-Physical
-4.2592 score on a scale
Interval -11.5984 to 3.0801
3.5162 score on a scale
Interval -4.2634 to 11.2958
Change From Baseline Over 26 Weeks in SF-36 v2 - Subjects With Elevated C5b-9
SF-36v2: Bodily Pain
3.6 score on a scale
Interval -4.2 to 11.4
-3.5 score on a scale
Interval -12.0 to 4.9
Change From Baseline Over 26 Weeks in SF-36 v2 - Subjects With Elevated C5b-9
SF-36v2: General Health Perceptions
-0.9 score on a scale
Interval -7.0 to 5.2
1.6 score on a scale
Interval -4.8 to 8.0
Change From Baseline Over 26 Weeks in SF-36 v2 - Subjects With Elevated C5b-9
SF-36v2: Vitality
-2.472 score on a scale
Interval -8.906 to 3.963
3.898 score on a scale
Interval -2.978 to 10.774
Change From Baseline Over 26 Weeks in SF-36 v2 - Subjects With Elevated C5b-9
SF-36v2: Social Functioning
4.58 score on a scale
Interval -2.3 to 11.47
0.34 score on a scale
Interval -7.2 to 7.88
Change From Baseline Over 26 Weeks in SF-36 v2 - Subjects With Elevated C5b-9
SF-36v2: Role-Emotional
0.6859 score on a scale
Interval -6.8507 to 8.2225
3.2461 score on a scale
Interval -4.6899 to 11.1821
Change From Baseline Over 26 Weeks in SF-36 v2 - Subjects With Elevated C5b-9
SF-36v2: Mental Health
2.423 score on a scale
Interval -3.684 to 8.53
2.730 score on a scale
Interval -3.791 to 9.251
Change From Baseline Over 26 Weeks in SF-36 v2 - Subjects With Elevated C5b-9
SF-36v2: Physical Component
-0.3257 score on a scale
Interval -2.609 to 1.9576
0.0762 score on a scale
Interval -2.4423 to 2.5947
Change From Baseline Over 26 Weeks in SF-36 v2 - Subjects With Elevated C5b-9
SF-36v2: Mental Component
0.7556 score on a scale
Interval -2.356 to 3.8672
0.7608 score on a scale
Interval -2.6341 to 4.1558

SECONDARY outcome

Timeframe: Week 26

Population: Combined C5b-9 Strata (elevated \[\> 244 ng/mL\] and non-elevated C5b-9) in the Intent-to-Treat (ITT) Population. The number of subjects with data at baseline and the specified visit is reported. ITT Population: The ITT Population included all randomized subjects who received at least one dose of study medication; subjects with a histologic activity score of 0 at baseline or who were ongoing and had not completed the Week 26 visit were not included in the ITT population.

Change from baseline over 26 weeks in SF-36 v2 - Combined C5b-9 Strata (elevated \[\> 244 ng/mL\] and non-elevated C5b-9) in the Intent-to-Treat Population. SF-36v2: Medical Outcomes Survey Short Form-36 version 2. SF-36v2 measures each of the following eight health domains: Physical Functioning, Role-Physical, Bodily Pain, General Health, Vitality, Social Functioning, Role-Emotional, and Mental Health. Scores on each item are summed and averaged. The SF-36v2 component domain scores range from 0 (worst health) to 100 (best health).

Outcome measures

Outcome measures
Measure
Placebo Group
n=26 Participants
Avacopan-matching placebo capsules x 3 administered twice daily during the 26 week blinded treatment period period Avacopan-matching placebo: Orally administered
Avacopan Group
n=26 Participants
Avacopan (formerly CCX168) 10 mg capsules x 3 administered twice daily during the blinded 26 week blinded treatment period Avacopan: Orally administered
Change From Baseline Over 26 Weeks in SF-36 v2 - Combined C5b-9 Strata
SF-36v2: Physical Functioning
2.9619 score on a scale
Interval -2.715 to 8.6389
4.6532 score on a scale
Interval -1.1123 to 10.4187
Change From Baseline Over 26 Weeks in SF-36 v2 - Combined C5b-9 Strata
SF-36v2: Role-Physical
-2.4712 score on a scale
Interval -9.6179 to 4.6755
1.2077 score on a scale
Interval -5.9734 to 8.3887
Change From Baseline Over 26 Weeks in SF-36 v2 - Combined C5b-9 Strata
SF-36v2: Bodily Pain
1.5 score on a scale
Interval -5.7 to 8.7
-2.0 score on a scale
Interval -9.3 to 5.4
Change From Baseline Over 26 Weeks in SF-36 v2 - Combined C5b-9 Strata
SF-36v2: General Health Perceptions
-1.0 score on a scale
Interval -6.6 to 4.6
0.7 score on a scale
Interval -4.9 to 6.2
Change From Baseline Over 26 Weeks in SF-36 v2 - Combined C5b-9 Strata
SF-36v2: Vitality
-0.468 score on a scale
Interval -6.283 to 5.348
4.085 score on a scale
Interval -1.782 to 9.952
Change From Baseline Over 26 Weeks in SF-36 v2 - Combined C5b-9 Strata
SF-36v2: Social Functioning
4.66 score on a scale
Interval -1.41 to 10.73
1.55 score on a scale
Interval -4.66 to 7.76
Change From Baseline Over 26 Weeks in SF-36 v2 - Combined C5b-9 Strata
SF-36v2: Role-Emotional
4.3024 score on a scale
Interval -3.3147 to 11.9195
7.8375 score on a scale
Interval 0.2129 to 15.462
Change From Baseline Over 26 Weeks in SF-36 v2 - Combined C5b-9 Strata
SF-36v2: Mental Health
1.503 score on a scale
Interval -3.911 to 6.917
3.914 score on a scale
Interval -1.543 to 9.37
Change From Baseline Over 26 Weeks in SF-36 v2 - Combined C5b-9 Strata
SF-36v2: Physical Component
-0.3578 score on a scale
Interval -2.5452 to 1.8296
-0.5096 score on a scale
Interval -2.768 to 1.7489
Change From Baseline Over 26 Weeks in SF-36 v2 - Combined C5b-9 Strata
SF-36v2: Mental Component
1.3591 score on a scale
Interval -1.797 to 4.5153
2.3874 score on a scale
Interval -0.8529 to 5.6277

SECONDARY outcome

Timeframe: From day 1 throughout the study period (day 182/week 26)

Population: Safety Population: The safety population included all subjects who were randomized and had received at least one dose of study drug.

Number of Subjects with Treatment-emergent SAEs, AEs, relatedness to study medication and Withdrawals Due to AEs AEs=Adverse events SAEs=Serious adverse events TEAE=Treatment-emergent adverse events 'Possibly related' refers to the Investigators' causality assessment

Outcome measures

Outcome measures
Measure
Placebo Group
n=29 Participants
Avacopan-matching placebo capsules x 3 administered twice daily during the 26 week blinded treatment period period Avacopan-matching placebo: Orally administered
Avacopan Group
n=28 Participants
Avacopan (formerly CCX168) 10 mg capsules x 3 administered twice daily during the blinded 26 week blinded treatment period Avacopan: Orally administered
Number of Subjects With Treatment-emergent SAEs, AEs, Relatedness to Study Medication and Withdrawals Due to AEs
Number of subjects with at least one TEAE
24 participants
25 participants
Number of Subjects With Treatment-emergent SAEs, AEs, Relatedness to Study Medication and Withdrawals Due to AEs
Number of subjects with SAEs
3 participants
3 participants
Number of Subjects With Treatment-emergent SAEs, AEs, Relatedness to Study Medication and Withdrawals Due to AEs
Number of subjects with TEAEs possibly related to Study Medication
11 participants
10 participants
Number of Subjects With Treatment-emergent SAEs, AEs, Relatedness to Study Medication and Withdrawals Due to AEs
Number of subjects with TEAEs leading to discontinuation
1 participants
1 participants

SECONDARY outcome

Timeframe: From day 1 throughout the study period (day 182/week 26)

Population: Safety Population: The safety population included all subjects who were randomized and had received at least one dose of study drug.

Number of Treatment-emergent SAEs, AEs, relatedness to study medication and Withdrawals Due to AEs AEs=Adverse events SAEs=Serious adverse events TEAE=Treatment-emergent adverse events 'Possibly related' refers to the Investigators' causality assessment

Outcome measures

Outcome measures
Measure
Placebo Group
n=29 Participants
Avacopan-matching placebo capsules x 3 administered twice daily during the 26 week blinded treatment period period Avacopan-matching placebo: Orally administered
Avacopan Group
n=28 Participants
Avacopan (formerly CCX168) 10 mg capsules x 3 administered twice daily during the blinded 26 week blinded treatment period Avacopan: Orally administered
Number of Treatment-emergent SAEs, AEs, Relatedness to Study Medication and Withdrawals Due to AEs
Number of TEAEs
107 Adverse events
149 Adverse events
Number of Treatment-emergent SAEs, AEs, Relatedness to Study Medication and Withdrawals Due to AEs
Number of SAEs
4 Adverse events
6 Adverse events
Number of Treatment-emergent SAEs, AEs, Relatedness to Study Medication and Withdrawals Due to AEs
Number of TEAEs possibly related to Study Medication
24 Adverse events
38 Adverse events
Number of Treatment-emergent SAEs, AEs, Relatedness to Study Medication and Withdrawals Due to AEs
Number of TEAEs leading to discontinuation
2 Adverse events
2 Adverse events

Adverse Events

Placebo Group

Serious events: 3 serious events
Other events: 24 other events
Deaths: 0 deaths

Avacopan Group

Serious events: 3 serious events
Other events: 25 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
Placebo Group
n=29 participants at risk
Avacopan-matching placebo capsules x 3 administered twice daily during the 26 week blinded treatment period period Avacopan-matching placebo: Orally administered The safety population included all subjects who were randomized and had received at least one dose of study drug.
Avacopan Group
n=28 participants at risk
Avacopan (formerly CCX168) 10 mg capsules x 3 administered twice daily during the blinded 26 week blinded treatment period Avacopan: Orally administered The safety population included all subjects who were randomized and had received at least one dose of study drug.
Infections and infestations
Gastroenteritis salmonella
0.00%
0/29 • From day 1 throughout the study period (day 182/week 26)
An adverse event is considered treatment-emergent if the start date/time of the event is on or after the date/time of first study drug treatment up to the final observation in the double-blind treatment period (week 26).
3.6%
1/28 • Number of events 1 • From day 1 throughout the study period (day 182/week 26)
An adverse event is considered treatment-emergent if the start date/time of the event is on or after the date/time of first study drug treatment up to the final observation in the double-blind treatment period (week 26).
Infections and infestations
Neutropenic sepsis
0.00%
0/29 • From day 1 throughout the study period (day 182/week 26)
An adverse event is considered treatment-emergent if the start date/time of the event is on or after the date/time of first study drug treatment up to the final observation in the double-blind treatment period (week 26).
3.6%
1/28 • Number of events 1 • From day 1 throughout the study period (day 182/week 26)
An adverse event is considered treatment-emergent if the start date/time of the event is on or after the date/time of first study drug treatment up to the final observation in the double-blind treatment period (week 26).
Infections and infestations
Pneumonia
3.4%
1/29 • Number of events 1 • From day 1 throughout the study period (day 182/week 26)
An adverse event is considered treatment-emergent if the start date/time of the event is on or after the date/time of first study drug treatment up to the final observation in the double-blind treatment period (week 26).
3.6%
1/28 • Number of events 1 • From day 1 throughout the study period (day 182/week 26)
An adverse event is considered treatment-emergent if the start date/time of the event is on or after the date/time of first study drug treatment up to the final observation in the double-blind treatment period (week 26).
Infections and infestations
Bacterial parotitis
3.4%
1/29 • Number of events 1 • From day 1 throughout the study period (day 182/week 26)
An adverse event is considered treatment-emergent if the start date/time of the event is on or after the date/time of first study drug treatment up to the final observation in the double-blind treatment period (week 26).
0.00%
0/28 • From day 1 throughout the study period (day 182/week 26)
An adverse event is considered treatment-emergent if the start date/time of the event is on or after the date/time of first study drug treatment up to the final observation in the double-blind treatment period (week 26).
Infections and infestations
Bronchitis
3.4%
1/29 • Number of events 1 • From day 1 throughout the study period (day 182/week 26)
An adverse event is considered treatment-emergent if the start date/time of the event is on or after the date/time of first study drug treatment up to the final observation in the double-blind treatment period (week 26).
0.00%
0/28 • From day 1 throughout the study period (day 182/week 26)
An adverse event is considered treatment-emergent if the start date/time of the event is on or after the date/time of first study drug treatment up to the final observation in the double-blind treatment period (week 26).
Investigations
Neutrophil count decreased
0.00%
0/29 • From day 1 throughout the study period (day 182/week 26)
An adverse event is considered treatment-emergent if the start date/time of the event is on or after the date/time of first study drug treatment up to the final observation in the double-blind treatment period (week 26).
3.6%
1/28 • Number of events 1 • From day 1 throughout the study period (day 182/week 26)
An adverse event is considered treatment-emergent if the start date/time of the event is on or after the date/time of first study drug treatment up to the final observation in the double-blind treatment period (week 26).
Musculoskeletal and connective tissue disorders
Sjogren's syndrome
0.00%
0/29 • From day 1 throughout the study period (day 182/week 26)
An adverse event is considered treatment-emergent if the start date/time of the event is on or after the date/time of first study drug treatment up to the final observation in the double-blind treatment period (week 26).
3.6%
1/28 • Number of events 1 • From day 1 throughout the study period (day 182/week 26)
An adverse event is considered treatment-emergent if the start date/time of the event is on or after the date/time of first study drug treatment up to the final observation in the double-blind treatment period (week 26).
Renal and urinary disorders
Acute kidney injury
0.00%
0/29 • From day 1 throughout the study period (day 182/week 26)
An adverse event is considered treatment-emergent if the start date/time of the event is on or after the date/time of first study drug treatment up to the final observation in the double-blind treatment period (week 26).
3.6%
1/28 • Number of events 1 • From day 1 throughout the study period (day 182/week 26)
An adverse event is considered treatment-emergent if the start date/time of the event is on or after the date/time of first study drug treatment up to the final observation in the double-blind treatment period (week 26).
Psychiatric disorders
Alcohol withdrawal syndrome
3.4%
1/29 • Number of events 1 • From day 1 throughout the study period (day 182/week 26)
An adverse event is considered treatment-emergent if the start date/time of the event is on or after the date/time of first study drug treatment up to the final observation in the double-blind treatment period (week 26).
0.00%
0/28 • From day 1 throughout the study period (day 182/week 26)
An adverse event is considered treatment-emergent if the start date/time of the event is on or after the date/time of first study drug treatment up to the final observation in the double-blind treatment period (week 26).

Other adverse events

Other adverse events
Measure
Placebo Group
n=29 participants at risk
Avacopan-matching placebo capsules x 3 administered twice daily during the 26 week blinded treatment period period Avacopan-matching placebo: Orally administered The safety population included all subjects who were randomized and had received at least one dose of study drug.
Avacopan Group
n=28 participants at risk
Avacopan (formerly CCX168) 10 mg capsules x 3 administered twice daily during the blinded 26 week blinded treatment period Avacopan: Orally administered The safety population included all subjects who were randomized and had received at least one dose of study drug.
General disorders
Oedema peripheral
3.4%
1/29 • Number of events 1 • From day 1 throughout the study period (day 182/week 26)
An adverse event is considered treatment-emergent if the start date/time of the event is on or after the date/time of first study drug treatment up to the final observation in the double-blind treatment period (week 26).
17.9%
5/28 • Number of events 6 • From day 1 throughout the study period (day 182/week 26)
An adverse event is considered treatment-emergent if the start date/time of the event is on or after the date/time of first study drug treatment up to the final observation in the double-blind treatment period (week 26).
General disorders
Fatigue
0.00%
0/29 • From day 1 throughout the study period (day 182/week 26)
An adverse event is considered treatment-emergent if the start date/time of the event is on or after the date/time of first study drug treatment up to the final observation in the double-blind treatment period (week 26).
10.7%
3/28 • Number of events 3 • From day 1 throughout the study period (day 182/week 26)
An adverse event is considered treatment-emergent if the start date/time of the event is on or after the date/time of first study drug treatment up to the final observation in the double-blind treatment period (week 26).
General disorders
Pyrexia
6.9%
2/29 • Number of events 4 • From day 1 throughout the study period (day 182/week 26)
An adverse event is considered treatment-emergent if the start date/time of the event is on or after the date/time of first study drug treatment up to the final observation in the double-blind treatment period (week 26).
0.00%
0/28 • From day 1 throughout the study period (day 182/week 26)
An adverse event is considered treatment-emergent if the start date/time of the event is on or after the date/time of first study drug treatment up to the final observation in the double-blind treatment period (week 26).
Infections and infestations
Influenza
3.4%
1/29 • Number of events 1 • From day 1 throughout the study period (day 182/week 26)
An adverse event is considered treatment-emergent if the start date/time of the event is on or after the date/time of first study drug treatment up to the final observation in the double-blind treatment period (week 26).
7.1%
2/28 • Number of events 2 • From day 1 throughout the study period (day 182/week 26)
An adverse event is considered treatment-emergent if the start date/time of the event is on or after the date/time of first study drug treatment up to the final observation in the double-blind treatment period (week 26).
Infections and infestations
Lower respiratory tract infection
0.00%
0/29 • From day 1 throughout the study period (day 182/week 26)
An adverse event is considered treatment-emergent if the start date/time of the event is on or after the date/time of first study drug treatment up to the final observation in the double-blind treatment period (week 26).
7.1%
2/28 • Number of events 2 • From day 1 throughout the study period (day 182/week 26)
An adverse event is considered treatment-emergent if the start date/time of the event is on or after the date/time of first study drug treatment up to the final observation in the double-blind treatment period (week 26).
Infections and infestations
Upper respiratory tract infection
10.3%
3/29 • Number of events 3 • From day 1 throughout the study period (day 182/week 26)
An adverse event is considered treatment-emergent if the start date/time of the event is on or after the date/time of first study drug treatment up to the final observation in the double-blind treatment period (week 26).
7.1%
2/28 • Number of events 3 • From day 1 throughout the study period (day 182/week 26)
An adverse event is considered treatment-emergent if the start date/time of the event is on or after the date/time of first study drug treatment up to the final observation in the double-blind treatment period (week 26).
Infections and infestations
Nasopharyngitis
10.3%
3/29 • Number of events 4 • From day 1 throughout the study period (day 182/week 26)
An adverse event is considered treatment-emergent if the start date/time of the event is on or after the date/time of first study drug treatment up to the final observation in the double-blind treatment period (week 26).
3.6%
1/28 • Number of events 1 • From day 1 throughout the study period (day 182/week 26)
An adverse event is considered treatment-emergent if the start date/time of the event is on or after the date/time of first study drug treatment up to the final observation in the double-blind treatment period (week 26).
Gastrointestinal disorders
Vomiting
3.4%
1/29 • Number of events 1 • From day 1 throughout the study period (day 182/week 26)
An adverse event is considered treatment-emergent if the start date/time of the event is on or after the date/time of first study drug treatment up to the final observation in the double-blind treatment period (week 26).
14.3%
4/28 • Number of events 4 • From day 1 throughout the study period (day 182/week 26)
An adverse event is considered treatment-emergent if the start date/time of the event is on or after the date/time of first study drug treatment up to the final observation in the double-blind treatment period (week 26).
Gastrointestinal disorders
Diarrhoea
10.3%
3/29 • Number of events 4 • From day 1 throughout the study period (day 182/week 26)
An adverse event is considered treatment-emergent if the start date/time of the event is on or after the date/time of first study drug treatment up to the final observation in the double-blind treatment period (week 26).
7.1%
2/28 • Number of events 2 • From day 1 throughout the study period (day 182/week 26)
An adverse event is considered treatment-emergent if the start date/time of the event is on or after the date/time of first study drug treatment up to the final observation in the double-blind treatment period (week 26).
Gastrointestinal disorders
Abdominal pain
10.3%
3/29 • Number of events 3 • From day 1 throughout the study period (day 182/week 26)
An adverse event is considered treatment-emergent if the start date/time of the event is on or after the date/time of first study drug treatment up to the final observation in the double-blind treatment period (week 26).
3.6%
1/28 • Number of events 1 • From day 1 throughout the study period (day 182/week 26)
An adverse event is considered treatment-emergent if the start date/time of the event is on or after the date/time of first study drug treatment up to the final observation in the double-blind treatment period (week 26).
Gastrointestinal disorders
Nausea
10.3%
3/29 • Number of events 3 • From day 1 throughout the study period (day 182/week 26)
An adverse event is considered treatment-emergent if the start date/time of the event is on or after the date/time of first study drug treatment up to the final observation in the double-blind treatment period (week 26).
3.6%
1/28 • Number of events 1 • From day 1 throughout the study period (day 182/week 26)
An adverse event is considered treatment-emergent if the start date/time of the event is on or after the date/time of first study drug treatment up to the final observation in the double-blind treatment period (week 26).
Gastrointestinal disorders
Dyspepsia
6.9%
2/29 • Number of events 2 • From day 1 throughout the study period (day 182/week 26)
An adverse event is considered treatment-emergent if the start date/time of the event is on or after the date/time of first study drug treatment up to the final observation in the double-blind treatment period (week 26).
0.00%
0/28 • From day 1 throughout the study period (day 182/week 26)
An adverse event is considered treatment-emergent if the start date/time of the event is on or after the date/time of first study drug treatment up to the final observation in the double-blind treatment period (week 26).
Gastrointestinal disorders
Mouth ulceration
6.9%
2/29 • Number of events 2 • From day 1 throughout the study period (day 182/week 26)
An adverse event is considered treatment-emergent if the start date/time of the event is on or after the date/time of first study drug treatment up to the final observation in the double-blind treatment period (week 26).
0.00%
0/28 • From day 1 throughout the study period (day 182/week 26)
An adverse event is considered treatment-emergent if the start date/time of the event is on or after the date/time of first study drug treatment up to the final observation in the double-blind treatment period (week 26).
Investigations
Blood creatine phosphokinase increased
3.4%
1/29 • Number of events 1 • From day 1 throughout the study period (day 182/week 26)
An adverse event is considered treatment-emergent if the start date/time of the event is on or after the date/time of first study drug treatment up to the final observation in the double-blind treatment period (week 26).
10.7%
3/28 • Number of events 4 • From day 1 throughout the study period (day 182/week 26)
An adverse event is considered treatment-emergent if the start date/time of the event is on or after the date/time of first study drug treatment up to the final observation in the double-blind treatment period (week 26).
Investigations
Blood creatinine increased
0.00%
0/29 • From day 1 throughout the study period (day 182/week 26)
An adverse event is considered treatment-emergent if the start date/time of the event is on or after the date/time of first study drug treatment up to the final observation in the double-blind treatment period (week 26).
10.7%
3/28 • Number of events 3 • From day 1 throughout the study period (day 182/week 26)
An adverse event is considered treatment-emergent if the start date/time of the event is on or after the date/time of first study drug treatment up to the final observation in the double-blind treatment period (week 26).
Investigations
Weight decreased
0.00%
0/29 • From day 1 throughout the study period (day 182/week 26)
An adverse event is considered treatment-emergent if the start date/time of the event is on or after the date/time of first study drug treatment up to the final observation in the double-blind treatment period (week 26).
10.7%
3/28 • Number of events 3 • From day 1 throughout the study period (day 182/week 26)
An adverse event is considered treatment-emergent if the start date/time of the event is on or after the date/time of first study drug treatment up to the final observation in the double-blind treatment period (week 26).
Investigations
Lipase increased
0.00%
0/29 • From day 1 throughout the study period (day 182/week 26)
An adverse event is considered treatment-emergent if the start date/time of the event is on or after the date/time of first study drug treatment up to the final observation in the double-blind treatment period (week 26).
7.1%
2/28 • Number of events 2 • From day 1 throughout the study period (day 182/week 26)
An adverse event is considered treatment-emergent if the start date/time of the event is on or after the date/time of first study drug treatment up to the final observation in the double-blind treatment period (week 26).
Investigations
Aspartate aminotransferase increased
6.9%
2/29 • Number of events 2 • From day 1 throughout the study period (day 182/week 26)
An adverse event is considered treatment-emergent if the start date/time of the event is on or after the date/time of first study drug treatment up to the final observation in the double-blind treatment period (week 26).
3.6%
1/28 • Number of events 1 • From day 1 throughout the study period (day 182/week 26)
An adverse event is considered treatment-emergent if the start date/time of the event is on or after the date/time of first study drug treatment up to the final observation in the double-blind treatment period (week 26).
Blood and lymphatic system disorders
Anaemia
10.3%
3/29 • Number of events 3 • From day 1 throughout the study period (day 182/week 26)
An adverse event is considered treatment-emergent if the start date/time of the event is on or after the date/time of first study drug treatment up to the final observation in the double-blind treatment period (week 26).
10.7%
3/28 • Number of events 3 • From day 1 throughout the study period (day 182/week 26)
An adverse event is considered treatment-emergent if the start date/time of the event is on or after the date/time of first study drug treatment up to the final observation in the double-blind treatment period (week 26).
Blood and lymphatic system disorders
Lymphopenia
0.00%
0/29 • From day 1 throughout the study period (day 182/week 26)
An adverse event is considered treatment-emergent if the start date/time of the event is on or after the date/time of first study drug treatment up to the final observation in the double-blind treatment period (week 26).
10.7%
3/28 • Number of events 3 • From day 1 throughout the study period (day 182/week 26)
An adverse event is considered treatment-emergent if the start date/time of the event is on or after the date/time of first study drug treatment up to the final observation in the double-blind treatment period (week 26).
Injury, poisoning and procedural complications
Hand fracture
0.00%
0/29 • From day 1 throughout the study period (day 182/week 26)
An adverse event is considered treatment-emergent if the start date/time of the event is on or after the date/time of first study drug treatment up to the final observation in the double-blind treatment period (week 26).
7.1%
2/28 • Number of events 2 • From day 1 throughout the study period (day 182/week 26)
An adverse event is considered treatment-emergent if the start date/time of the event is on or after the date/time of first study drug treatment up to the final observation in the double-blind treatment period (week 26).
Musculoskeletal and connective tissue disorders
Pain in extremity
0.00%
0/29 • From day 1 throughout the study period (day 182/week 26)
An adverse event is considered treatment-emergent if the start date/time of the event is on or after the date/time of first study drug treatment up to the final observation in the double-blind treatment period (week 26).
7.1%
2/28 • Number of events 2 • From day 1 throughout the study period (day 182/week 26)
An adverse event is considered treatment-emergent if the start date/time of the event is on or after the date/time of first study drug treatment up to the final observation in the double-blind treatment period (week 26).
Musculoskeletal and connective tissue disorders
Back pain
10.3%
3/29 • Number of events 3 • From day 1 throughout the study period (day 182/week 26)
An adverse event is considered treatment-emergent if the start date/time of the event is on or after the date/time of first study drug treatment up to the final observation in the double-blind treatment period (week 26).
3.6%
1/28 • Number of events 1 • From day 1 throughout the study period (day 182/week 26)
An adverse event is considered treatment-emergent if the start date/time of the event is on or after the date/time of first study drug treatment up to the final observation in the double-blind treatment period (week 26).
Musculoskeletal and connective tissue disorders
Muscle spasms
10.3%
3/29 • Number of events 3 • From day 1 throughout the study period (day 182/week 26)
An adverse event is considered treatment-emergent if the start date/time of the event is on or after the date/time of first study drug treatment up to the final observation in the double-blind treatment period (week 26).
0.00%
0/28 • From day 1 throughout the study period (day 182/week 26)
An adverse event is considered treatment-emergent if the start date/time of the event is on or after the date/time of first study drug treatment up to the final observation in the double-blind treatment period (week 26).
Nervous system disorders
Headache
6.9%
2/29 • Number of events 4 • From day 1 throughout the study period (day 182/week 26)
An adverse event is considered treatment-emergent if the start date/time of the event is on or after the date/time of first study drug treatment up to the final observation in the double-blind treatment period (week 26).
17.9%
5/28 • Number of events 5 • From day 1 throughout the study period (day 182/week 26)
An adverse event is considered treatment-emergent if the start date/time of the event is on or after the date/time of first study drug treatment up to the final observation in the double-blind treatment period (week 26).
Nervous system disorders
Tremor
6.9%
2/29 • Number of events 2 • From day 1 throughout the study period (day 182/week 26)
An adverse event is considered treatment-emergent if the start date/time of the event is on or after the date/time of first study drug treatment up to the final observation in the double-blind treatment period (week 26).
0.00%
0/28 • From day 1 throughout the study period (day 182/week 26)
An adverse event is considered treatment-emergent if the start date/time of the event is on or after the date/time of first study drug treatment up to the final observation in the double-blind treatment period (week 26).
Metabolism and nutrition disorders
Decreased appetite
0.00%
0/29 • From day 1 throughout the study period (day 182/week 26)
An adverse event is considered treatment-emergent if the start date/time of the event is on or after the date/time of first study drug treatment up to the final observation in the double-blind treatment period (week 26).
10.7%
3/28 • Number of events 3 • From day 1 throughout the study period (day 182/week 26)
An adverse event is considered treatment-emergent if the start date/time of the event is on or after the date/time of first study drug treatment up to the final observation in the double-blind treatment period (week 26).
Metabolism and nutrition disorders
Hypokalaemia
0.00%
0/29 • From day 1 throughout the study period (day 182/week 26)
An adverse event is considered treatment-emergent if the start date/time of the event is on or after the date/time of first study drug treatment up to the final observation in the double-blind treatment period (week 26).
7.1%
2/28 • Number of events 2 • From day 1 throughout the study period (day 182/week 26)
An adverse event is considered treatment-emergent if the start date/time of the event is on or after the date/time of first study drug treatment up to the final observation in the double-blind treatment period (week 26).
Metabolism and nutrition disorders
Hyperkalaemia
6.9%
2/29 • Number of events 2 • From day 1 throughout the study period (day 182/week 26)
An adverse event is considered treatment-emergent if the start date/time of the event is on or after the date/time of first study drug treatment up to the final observation in the double-blind treatment period (week 26).
3.6%
1/28 • Number of events 2 • From day 1 throughout the study period (day 182/week 26)
An adverse event is considered treatment-emergent if the start date/time of the event is on or after the date/time of first study drug treatment up to the final observation in the double-blind treatment period (week 26).
Respiratory, thoracic and mediastinal disorders
Cough
6.9%
2/29 • Number of events 2 • From day 1 throughout the study period (day 182/week 26)
An adverse event is considered treatment-emergent if the start date/time of the event is on or after the date/time of first study drug treatment up to the final observation in the double-blind treatment period (week 26).
3.6%
1/28 • Number of events 1 • From day 1 throughout the study period (day 182/week 26)
An adverse event is considered treatment-emergent if the start date/time of the event is on or after the date/time of first study drug treatment up to the final observation in the double-blind treatment period (week 26).
Respiratory, thoracic and mediastinal disorders
Oropharyngeal pain
6.9%
2/29 • Number of events 2 • From day 1 throughout the study period (day 182/week 26)
An adverse event is considered treatment-emergent if the start date/time of the event is on or after the date/time of first study drug treatment up to the final observation in the double-blind treatment period (week 26).
3.6%
1/28 • Number of events 1 • From day 1 throughout the study period (day 182/week 26)
An adverse event is considered treatment-emergent if the start date/time of the event is on or after the date/time of first study drug treatment up to the final observation in the double-blind treatment period (week 26).
Skin and subcutaneous tissue disorders
Acne
3.4%
1/29 • Number of events 1 • From day 1 throughout the study period (day 182/week 26)
An adverse event is considered treatment-emergent if the start date/time of the event is on or after the date/time of first study drug treatment up to the final observation in the double-blind treatment period (week 26).
7.1%
2/28 • Number of events 2 • From day 1 throughout the study period (day 182/week 26)
An adverse event is considered treatment-emergent if the start date/time of the event is on or after the date/time of first study drug treatment up to the final observation in the double-blind treatment period (week 26).
Psychiatric disorders
Depression
0.00%
0/29 • From day 1 throughout the study period (day 182/week 26)
An adverse event is considered treatment-emergent if the start date/time of the event is on or after the date/time of first study drug treatment up to the final observation in the double-blind treatment period (week 26).
7.1%
2/28 • Number of events 2 • From day 1 throughout the study period (day 182/week 26)
An adverse event is considered treatment-emergent if the start date/time of the event is on or after the date/time of first study drug treatment up to the final observation in the double-blind treatment period (week 26).
Vascular disorders
Hypertension
10.3%
3/29 • Number of events 3 • From day 1 throughout the study period (day 182/week 26)
An adverse event is considered treatment-emergent if the start date/time of the event is on or after the date/time of first study drug treatment up to the final observation in the double-blind treatment period (week 26).
10.7%
3/28 • Number of events 4 • From day 1 throughout the study period (day 182/week 26)
An adverse event is considered treatment-emergent if the start date/time of the event is on or after the date/time of first study drug treatment up to the final observation in the double-blind treatment period (week 26).
Vascular disorders
Orthostatic hypotension
6.9%
2/29 • Number of events 2 • From day 1 throughout the study period (day 182/week 26)
An adverse event is considered treatment-emergent if the start date/time of the event is on or after the date/time of first study drug treatment up to the final observation in the double-blind treatment period (week 26).
0.00%
0/28 • From day 1 throughout the study period (day 182/week 26)
An adverse event is considered treatment-emergent if the start date/time of the event is on or after the date/time of first study drug treatment up to the final observation in the double-blind treatment period (week 26).

Additional Information

Clinical trial disclosure

ChemoCentryx, Inc.

Phone: 650.210.2900

Results disclosure agreements

  • Principal investigator is a sponsor employee The PI shall provide Sponsor with an advance copy of any proposed publication or oral presentation at least 60 days prior to the planned date of submission or presentation and Sponsor shall have 60 days to review the proposed publication. Sponsor may request in writing, and the PI shall agree to, (a) the deletion of any Confidential Information, (b) any reasonable changes requested by Sponsor, or (c) a delay of such proposed submission for an additional period, not to exceed 90 days.
  • Publication restrictions are in place

Restriction type: OTHER