Trial Outcomes & Findings for Dose Ranging Study of the Safety and Efficacy of Orally Administered Lyophilized Fecal Microbiota Product (PRIM-DJ2727) for the Treatment of Recurrent Clostridium Difficile Infection (CDI) (NCT NCT03298048)

NCT ID: NCT03298048

Last Updated: 2020-03-06

Results Overview

Recruitment status

TERMINATED

Study phase

PHASE2

Target enrollment

17 participants

Primary outcome timeframe

180 days

Results posted on

2020-03-06

Participant Flow

2 of the 17 enrolled did not start treatment: one did not start treatment due to physician's concerns about patient taking bowel prep, and the second did not start treatment because of hospitalization.

Participant milestones

Participant milestones
Measure
Low Fecal Microbiota Dose
receiving healthy microbiota (PRIM-DJ2727) collected from 50g stool for 2 consecutive days Low fecal microbiota dose: receiving healthy microbiota (PRIM-DJ2727) collected from 50g stool for 2 consecutive days
Mid Fecal Microbiota Dose
receiving healthy microbiota (PRIM-DJ2727) collected from 100g stool on the 1st day of treatment and from 50g stool on the 2nd day of the treatment Mid fecal microbiota dose: receiving healthy microbiota (PRIM-DJ2727) collected from 100g stool on the 1st day of treatment and from 50g stool on the 2nd day of the treatment
High Fecal Microbiota Dose
receiving healthy microbiota (PRIM-DJ2727) collected from 100g stool for 2 consecutive days High fecal microbiota dose: receiving healthy microbiota (PRIM-DJ2727) collected from 100g stool for 2 consecutive days
Overall Study
STARTED
4
3
8
Overall Study
COMPLETED
4
3
8
Overall Study
NOT COMPLETED
0
0
0

Reasons for withdrawal

Withdrawal data not reported

Baseline Characteristics

Dose Ranging Study of the Safety and Efficacy of Orally Administered Lyophilized Fecal Microbiota Product (PRIM-DJ2727) for the Treatment of Recurrent Clostridium Difficile Infection (CDI)

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Low Fecal Microbiota Dose
n=4 Participants
receiving healthy microbiota (PRIM-DJ2727) collected from 50g stool for 2 consecutive days Low fecal microbiota dose: receiving healthy microbiota (PRIM-DJ2727) collected from 50g stool for 2 consecutive days
Mid Fecal Microbiota Dose
n=3 Participants
receiving healthy microbiota (PRIM-DJ2727) collected from 100g stool on the 1st day of treatment and from 50g stool on the 2nd day of the treatment Mid fecal microbiota dose: receiving healthy microbiota (PRIM-DJ2727) collected from 100g stool on the 1st day of treatment and from 50g stool on the 2nd day of the treatment
High Fecal Microbiota Dose
n=8 Participants
receiving healthy microbiota (PRIM-DJ2727) collected from 100g stool for 2 consecutive days High fecal microbiota dose: receiving healthy microbiota (PRIM-DJ2727) collected from 100g stool for 2 consecutive days
Total
n=15 Participants
Total of all reporting groups
Age, Continuous
49 years
n=5 Participants
52 years
n=7 Participants
72.5 years
n=5 Participants
68 years
n=4 Participants
Sex: Female, Male
Female
3 Participants
n=5 Participants
2 Participants
n=7 Participants
7 Participants
n=5 Participants
12 Participants
n=4 Participants
Sex: Female, Male
Male
1 Participants
n=5 Participants
1 Participants
n=7 Participants
1 Participants
n=5 Participants
3 Participants
n=4 Participants
Ethnicity (NIH/OMB)
Hispanic or Latino
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
0 Participants
n=4 Participants
Ethnicity (NIH/OMB)
Not Hispanic or Latino
4 Participants
n=5 Participants
3 Participants
n=7 Participants
8 Participants
n=5 Participants
15 Participants
n=4 Participants
Ethnicity (NIH/OMB)
Unknown or Not Reported
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
0 Participants
n=4 Participants
Race (NIH/OMB)
American Indian or Alaska Native
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
0 Participants
n=4 Participants
Race (NIH/OMB)
Asian
0 Participants
n=5 Participants
0 Participants
n=7 Participants
1 Participants
n=5 Participants
1 Participants
n=4 Participants
Race (NIH/OMB)
Native Hawaiian or Other Pacific Islander
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
0 Participants
n=4 Participants
Race (NIH/OMB)
Black or African American
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
0 Participants
n=4 Participants
Race (NIH/OMB)
White
4 Participants
n=5 Participants
2 Participants
n=7 Participants
7 Participants
n=5 Participants
13 Participants
n=4 Participants
Race (NIH/OMB)
More than one race
0 Participants
n=5 Participants
1 Participants
n=7 Participants
0 Participants
n=5 Participants
1 Participants
n=4 Participants
Race (NIH/OMB)
Unknown or Not Reported
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
0 Participants
n=4 Participants
Number of Patients with Inflammatory bowel disease
2 Participants
n=5 Participants
1 Participants
n=7 Participants
1 Participants
n=5 Participants
4 Participants
n=4 Participants

PRIMARY outcome

Timeframe: 180 days

Outcome measures

Outcome measures
Measure
Low Fecal Microbiota Dose
n=4 Participants
receiving healthy microbiota (PRIM-DJ2727) collected from 50g stool for 2 consecutive days Low fecal microbiota dose: receiving healthy microbiota (PRIM-DJ2727) collected from 50g stool for 2 consecutive days
Mid Fecal Microbiota Dose
n=3 Participants
receiving healthy microbiota (PRIM-DJ2727) collected from 100g stool on the 1st day of treatment and from 50g stool on the 2nd day of the treatment Mid fecal microbiota dose: receiving healthy microbiota (PRIM-DJ2727) collected from 100g stool on the 1st day of treatment and from 50g stool on the 2nd day of the treatment
High Fecal Microbiota Dose
n=8 Participants
receiving healthy microbiota (PRIM-DJ2727) collected from 100g stool for 2 consecutive days High fecal microbiota dose: receiving healthy microbiota (PRIM-DJ2727) collected from 100g stool for 2 consecutive days
Safety as Assessed by Number of Participants With Nausea
0 Participants
2 Participants
1 Participants

PRIMARY outcome

Timeframe: 180 days

Outcome measures

Outcome measures
Measure
Low Fecal Microbiota Dose
n=4 Participants
receiving healthy microbiota (PRIM-DJ2727) collected from 50g stool for 2 consecutive days Low fecal microbiota dose: receiving healthy microbiota (PRIM-DJ2727) collected from 50g stool for 2 consecutive days
Mid Fecal Microbiota Dose
n=3 Participants
receiving healthy microbiota (PRIM-DJ2727) collected from 100g stool on the 1st day of treatment and from 50g stool on the 2nd day of the treatment Mid fecal microbiota dose: receiving healthy microbiota (PRIM-DJ2727) collected from 100g stool on the 1st day of treatment and from 50g stool on the 2nd day of the treatment
High Fecal Microbiota Dose
n=8 Participants
receiving healthy microbiota (PRIM-DJ2727) collected from 100g stool for 2 consecutive days High fecal microbiota dose: receiving healthy microbiota (PRIM-DJ2727) collected from 100g stool for 2 consecutive days
Safety as Assessed by Number of Participants With Vomiting
0 Participants
1 Participants
0 Participants

PRIMARY outcome

Timeframe: 180 days

Outcome measures

Outcome measures
Measure
Low Fecal Microbiota Dose
n=4 Participants
receiving healthy microbiota (PRIM-DJ2727) collected from 50g stool for 2 consecutive days Low fecal microbiota dose: receiving healthy microbiota (PRIM-DJ2727) collected from 50g stool for 2 consecutive days
Mid Fecal Microbiota Dose
n=3 Participants
receiving healthy microbiota (PRIM-DJ2727) collected from 100g stool on the 1st day of treatment and from 50g stool on the 2nd day of the treatment Mid fecal microbiota dose: receiving healthy microbiota (PRIM-DJ2727) collected from 100g stool on the 1st day of treatment and from 50g stool on the 2nd day of the treatment
High Fecal Microbiota Dose
n=8 Participants
receiving healthy microbiota (PRIM-DJ2727) collected from 100g stool for 2 consecutive days High fecal microbiota dose: receiving healthy microbiota (PRIM-DJ2727) collected from 100g stool for 2 consecutive days
Safety as Assessed by Number of Participants With Diarrhea
1 Participants
0 Participants
2 Participants

PRIMARY outcome

Timeframe: 180 days

Outcome measures

Outcome measures
Measure
Low Fecal Microbiota Dose
n=4 Participants
receiving healthy microbiota (PRIM-DJ2727) collected from 50g stool for 2 consecutive days Low fecal microbiota dose: receiving healthy microbiota (PRIM-DJ2727) collected from 50g stool for 2 consecutive days
Mid Fecal Microbiota Dose
n=3 Participants
receiving healthy microbiota (PRIM-DJ2727) collected from 100g stool on the 1st day of treatment and from 50g stool on the 2nd day of the treatment Mid fecal microbiota dose: receiving healthy microbiota (PRIM-DJ2727) collected from 100g stool on the 1st day of treatment and from 50g stool on the 2nd day of the treatment
High Fecal Microbiota Dose
n=8 Participants
receiving healthy microbiota (PRIM-DJ2727) collected from 100g stool for 2 consecutive days High fecal microbiota dose: receiving healthy microbiota (PRIM-DJ2727) collected from 100g stool for 2 consecutive days
Safety as Assessed by Number of Participants With Bloating
0 Participants
0 Participants
2 Participants

PRIMARY outcome

Timeframe: 180 days

Outcome measures

Outcome measures
Measure
Low Fecal Microbiota Dose
n=4 Participants
receiving healthy microbiota (PRIM-DJ2727) collected from 50g stool for 2 consecutive days Low fecal microbiota dose: receiving healthy microbiota (PRIM-DJ2727) collected from 50g stool for 2 consecutive days
Mid Fecal Microbiota Dose
n=3 Participants
receiving healthy microbiota (PRIM-DJ2727) collected from 100g stool on the 1st day of treatment and from 50g stool on the 2nd day of the treatment Mid fecal microbiota dose: receiving healthy microbiota (PRIM-DJ2727) collected from 100g stool on the 1st day of treatment and from 50g stool on the 2nd day of the treatment
High Fecal Microbiota Dose
n=8 Participants
receiving healthy microbiota (PRIM-DJ2727) collected from 100g stool for 2 consecutive days High fecal microbiota dose: receiving healthy microbiota (PRIM-DJ2727) collected from 100g stool for 2 consecutive days
Safety as Assessed by Number of Participants With Constipation
0 Participants
0 Participants
1 Participants

SECONDARY outcome

Timeframe: 6 months

Outcome measures

Outcome measures
Measure
Low Fecal Microbiota Dose
n=4 Participants
receiving healthy microbiota (PRIM-DJ2727) collected from 50g stool for 2 consecutive days Low fecal microbiota dose: receiving healthy microbiota (PRIM-DJ2727) collected from 50g stool for 2 consecutive days
Mid Fecal Microbiota Dose
n=3 Participants
receiving healthy microbiota (PRIM-DJ2727) collected from 100g stool on the 1st day of treatment and from 50g stool on the 2nd day of the treatment Mid fecal microbiota dose: receiving healthy microbiota (PRIM-DJ2727) collected from 100g stool on the 1st day of treatment and from 50g stool on the 2nd day of the treatment
High Fecal Microbiota Dose
n=8 Participants
receiving healthy microbiota (PRIM-DJ2727) collected from 100g stool for 2 consecutive days High fecal microbiota dose: receiving healthy microbiota (PRIM-DJ2727) collected from 100g stool for 2 consecutive days
Number of Participants With Recurrent C. Difficile Infection
2 Participants
0 Participants
2 Participants

Adverse Events

Low Fecal Microbiota Dose

Serious events: 1 serious events
Other events: 1 other events
Deaths: 0 deaths

Mid Fecal Microbiota Dose

Serious events: 0 serious events
Other events: 3 other events
Deaths: 0 deaths

High Fecal Microbiota Dose

Serious events: 0 serious events
Other events: 6 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
Low Fecal Microbiota Dose
n=4 participants at risk
receiving healthy microbiota (PRIM-DJ2727) collected from 50g stool for 2 consecutive days Low fecal microbiota dose: receiving healthy microbiota (PRIM-DJ2727) collected from 50g stool for 2 consecutive days
Mid Fecal Microbiota Dose
n=3 participants at risk
receiving healthy microbiota (PRIM-DJ2727) collected from 100g stool on the 1st day of treatment and from 50g stool on the 2nd day of the treatment Mid fecal microbiota dose: receiving healthy microbiota (PRIM-DJ2727) collected from 100g stool on the 1st day of treatment and from 50g stool on the 2nd day of the treatment
High Fecal Microbiota Dose
n=8 participants at risk
receiving healthy microbiota (PRIM-DJ2727) collected from 100g stool for 2 consecutive days High fecal microbiota dose: receiving healthy microbiota (PRIM-DJ2727) collected from 100g stool for 2 consecutive days
Gastrointestinal disorders
Hospitalization
25.0%
1/4 • Number of events 1 • 6 months
0.00%
0/3 • 6 months
0.00%
0/8 • 6 months

Other adverse events

Other adverse events
Measure
Low Fecal Microbiota Dose
n=4 participants at risk
receiving healthy microbiota (PRIM-DJ2727) collected from 50g stool for 2 consecutive days Low fecal microbiota dose: receiving healthy microbiota (PRIM-DJ2727) collected from 50g stool for 2 consecutive days
Mid Fecal Microbiota Dose
n=3 participants at risk
receiving healthy microbiota (PRIM-DJ2727) collected from 100g stool on the 1st day of treatment and from 50g stool on the 2nd day of the treatment Mid fecal microbiota dose: receiving healthy microbiota (PRIM-DJ2727) collected from 100g stool on the 1st day of treatment and from 50g stool on the 2nd day of the treatment
High Fecal Microbiota Dose
n=8 participants at risk
receiving healthy microbiota (PRIM-DJ2727) collected from 100g stool for 2 consecutive days High fecal microbiota dose: receiving healthy microbiota (PRIM-DJ2727) collected from 100g stool for 2 consecutive days
Gastrointestinal disorders
diarrhea
25.0%
1/4 • Number of events 1 • 6 months
0.00%
0/3 • 6 months
25.0%
2/8 • Number of events 2 • 6 months
Gastrointestinal disorders
nausea
0.00%
0/4 • 6 months
66.7%
2/3 • Number of events 2 • 6 months
12.5%
1/8 • Number of events 1 • 6 months
Gastrointestinal disorders
vomiting
0.00%
0/4 • 6 months
33.3%
1/3 • Number of events 1 • 6 months
0.00%
0/8 • 6 months
Gastrointestinal disorders
bloating
0.00%
0/4 • 6 months
0.00%
0/3 • 6 months
25.0%
2/8 • Number of events 2 • 6 months
Gastrointestinal disorders
constipation
0.00%
0/4 • 6 months
0.00%
0/3 • 6 months
12.5%
1/8 • Number of events 1 • 6 months

Additional Information

Dr. Herbert DuPont

UTexas_Houston

Phone: 713-500-9366

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place