Intracerebral Transplantation of Neural Stem Cells for the Treatment of Ischemic Stroke

NCT ID: NCT03296618

Last Updated: 2017-10-05

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

UNKNOWN

Clinical Phase

PHASE1

Total Enrollment

18 participants

Study Classification

INTERVENTIONAL

Study Start Date

2012-06-30

Study Completion Date

2018-05-31

Brief Summary

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The study is to determine the safety of human neural stem cell transplantation for the treatment of paralysis and related symptoms due to chronic motor stroke and to determine the maximum tolerated dose.

Detailed Description

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This is a Phase I study of human neural stem cell transplantation for the treatment of chronic motor stroke. This single-site, Phase I, open-label study may enroll up to 18 patients across 5 cohorts of ascending doses of human neural stem cells to define maximal tolerated dose.

Conditions

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Ischemic Motor Stroke, Chronic

Study Design

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Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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NSI-566 neural stem cell implantation

Group Type EXPERIMENTAL

NSI-566

Intervention Type DRUG

Dosing will consist of a one-time stereotactic, intracranial injection of a hNSC line, NSI-566, ranging from 1.2×107 cells to 8×107 cells, as tolerated.

Interventions

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NSI-566

Dosing will consist of a one-time stereotactic, intracranial injection of a hNSC line, NSI-566, ranging from 1.2×107 cells to 8×107 cells, as tolerated.

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

1. Have the ability to understand the requirements of the study, provide written informed consent, understand and provide written authorization for the use and disclosure of Protected Health Information (PHI) \[per Health Insurance Portability and Accountability Act (HIPAA) Privacy Ruling\] and comply with the study procedures
2. Men and women 30-65 years old
3. Women must have a negative serum pregnancy test and practice an acceptable method of contraception or be of non-childbearing potential (post-menopausal for at least 2 years or who have undergone hysterectomy or oophorectomy or surgical sterilization)
4. At least 3 months but no more than 24 months from time of stroke, with a motor neurological deficit
5. Documented history of completed ischemic stroke in subcortical region of MCA or lenticulostriate artery with or without cortical involvement, with correlated findings by MRI
6. Modified Rankin Score of 2, 3 or 4
7. FMMS score of 55 or less;
8. Two evaluations at approximately 3 weeks apart prior to surgery with less than +/- 4 point change in the NIHSS
9. Able and willing to meet all follow-up requirements
10. Able and willing to undergo post-physical therapy/rehabilitation

Exclusion Criteria

1. Any disabling psychological or psychiatric disorders which may confound the study
2. History of more than one symptomatic stroke, TIAs allowed
3. History of another major neurological disease or injury
4. Cerebral infarct size \>8cm in any one measurement
5. Myocardial infarction within the prior 3 months
6. History of seizures or current use of antiepileptic medication
7. Receipt of any investigational drug or device within 30 days
8. Receipt of any cell infusion other than blood transfusion
9. Any concomitant medical disease or condition noted below:

1. Coagulopathy with INR \> 1.4 at the time of surgery
2. Panel Reactive Antibodies (PRA) \> 20% at initial screen
3. Active infection at the time of surgery
4. Active hypotension requiring vasopressor therapy
5. Skin breakdown over the site of surgery
6. Active or history of malignancy
7. Primary or secondary immune deficiency
8. Persistent MRI artifact that would prevent imaging pre and post-operation or unable to undergo MRI
9. Creatinine \>115μmol/L, liver function tests (SGOT/SGPT, Bilirubin, Alk Phos) \> 2x upper limit of normal, hematocrit/hemoglobin \< 30/10, total WBC \< 4000/mm3,platelet count \<100,000/mm3, uncontrolled hypertension (systolic \> 180mmHg or diastolic\> 100mmHg) or uncontrolled diabetes (defined as hemoglobin A1C\>8%), evidence of GI bleeding by hemoccult test,positive tuberculosis (TB test: PPD/Mantoux), hepatitis B or C, or human immunodeficiency virus (HIV)
10. Presence of any of the following conditions:

1. Current drug abuse or alcoholism
2. Unstable medical conditions
3. Unstable psychiatric illness including psychosis and untreated major depression
11. Any condition that the Investigator or primary physician feels may interfere with participation in the study or may endanger the subject
12. Any condition that the surgeon feels may pose complications for the surgery
13. Known hypersensitivity to tacrolimus or methylprednisolone
14. Unable or unwilling to participate in physical and/or occupational therapy or return to clinic for follow up examinations as scheduled
15. Inability to provide informed consent as determined by screening protocol.
16. Use of antiplatelet drugs less than 2 weeks before surgery
Minimum Eligible Age

30 Years

Maximum Eligible Age

65 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Suzhou Neuralstem Biopharmaceuticals

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Xu Ruxiang, M.D

Role: PRINCIPAL_INVESTIGATOR

BaYi Brain Hospital, Army General Hospital

Locations

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Ba Yi Brain Hospital

Beijing, , China

Site Status

Countries

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China

References

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Glass JD, Boulis NM, Johe K, Rutkove SB, Federici T, Polak M, Kelly C, Feldman EL. Lumbar intraspinal injection of neural stem cells in patients with amyotrophic lateral sclerosis: results of a phase I trial in 12 patients. Stem Cells. 2012 Jun;30(6):1144-51. doi: 10.1002/stem.1079.

Reference Type BACKGROUND
PMID: 22415942 (View on PubMed)

Boulis NM, Federici T, Glass JD, Lunn JS, Sakowski SA, Feldman EL. Translational stem cell therapy for amyotrophic lateral sclerosis. Nat Rev Neurol. 2011 Dec 13;8(3):172-6. doi: 10.1038/nrneurol.2011.191.

Reference Type BACKGROUND
PMID: 22158518 (View on PubMed)

Lunn JS, Sakowski SA, Hur J, Feldman EL. Stem cell technology for neurodegenerative diseases. Ann Neurol. 2011 Sep;70(3):353-61. doi: 10.1002/ana.22487.

Reference Type BACKGROUND
PMID: 21905078 (View on PubMed)

Lunn JS, Sakowski SA, Federici T, Glass JD, Boulis NM, Feldman EL. Stem cell technology for the study and treatment of motor neuron diseases. Regen Med. 2011 Mar;6(2):201-13. doi: 10.2217/rme.11.6.

Reference Type BACKGROUND
PMID: 21391854 (View on PubMed)

Other Identifiers

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NS2012-1

Identifier Type: -

Identifier Source: org_study_id