MT-8554 for Reduction of Vasomotor Symptoms in Postmenopausal Women

NCT ID: NCT03291067

Last Updated: 2025-12-30

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

375 participants

Study Classification

INTERVENTIONAL

Study Start Date

2017-10-09

Study Completion Date

2018-11-09

Brief Summary

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The purpose of this study is to assess the efficacy and safety of MT-8554 for treatment of vasomotor symptoms (VMS) associated with menopause.

Detailed Description

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This is a Phase II randomized, double-blind, placebo-controlled study for dose selection in postmenopausal women with moderate to severe VMS, defined as follows:

* Moderate: sensation of heat with sweating, able to continue activity
* Severe: sensation of heat with sweating, causing cessation of activity This study is comprised of a screening period, a run-in period and a 12-week double-blind treatment period.

Conditions

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Menopause Hot Flashes

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

TRIPLE

Participants Investigators Outcome Assessors

Study Groups

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MT-8554 1mg

Group Type EXPERIMENTAL

MT-8554 1mg

Intervention Type DRUG

MT-8554 1mg QD, oral, 12 weeks

MT-8554 5mg

Group Type EXPERIMENTAL

MT-8554 5mg

Intervention Type DRUG

MT-8554 5mg QD, oral, 12 weeks

MT-8554 10mg

Group Type EXPERIMENTAL

MT-8554 10mg

Intervention Type DRUG

MT-8554 10mg QD, oral, 12 weeks

Placebo

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Placebo QD, oral, 12 weeks

Interventions

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MT-8554 1mg

MT-8554 1mg QD, oral, 12 weeks

Intervention Type DRUG

MT-8554 5mg

MT-8554 5mg QD, oral, 12 weeks

Intervention Type DRUG

MT-8554 10mg

MT-8554 10mg QD, oral, 12 weeks

Intervention Type DRUG

Placebo

Placebo QD, oral, 12 weeks

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

Additional screening criteria check may apply for qualification:

* Provide written informed consent to participate in this study
* Spontaneous amenorrhea for ≥12 months; or spontaneous amenorrhea for at least 6 months and with follicle stimulating hormone (FSH) levels \>40 mIU/mL; or documented bilateral salpingo oophorectomy ≥6 weeks, with or without hysterectomy
* 7 or more moderate to severe VMS per day, or 50 or more moderate to severe VMS per week
* Have a consistent bedtime on at least 5 nights per week
* Mean VMS frequency during the Placebo Run in period does not drop by more than 50% from the mean level reported for 2 weeks during the Screening period
* VMS diary compliance \>50%
* In the Investigator's opinion, subject is able to understand the nature of the study and any risk involved in participation, and is willing to cooperate and comply with the protocol restrictions and requirements

Exclusion Criteria

Additional screening criteria check may apply for qualification:

* History of any cancer within 5 years except for basal cell carcinoma
* History of undiagnosed abnormal vaginal bleeding
* History of Hepatitis B, Hepatitis C or HIV
* History of psychiatric illness, excessive alcohol intake or use of recreational drugs who are unsuitable for study enrollment and compliance
* Presence or history of severe adverse reaction or allergy to any drug
* Peripheral vascular disease or disorders with associated vasculopathies
* Clinically significant conditions which could interfere with the objectives of the study or the safety of the subject, as judged by the Investigator
* Endometrial thickness of \>=5 mm as measured by transvaginal ultrasound
* Abnormal result from baseline endometrial biopsy (i.e., endometrial hyperplasia or endometrial cancer)
* Aspartate aminotransferase (AST), alanine aminotransferase (ALT), or total bilirubin ≥2.0 × upper limit of normal (ULN) above the reference range
* Subjects of childbearing potential
Minimum Eligible Age

18 Years

Eligible Sex

FEMALE

Accepts Healthy Volunteers

No

Sponsors

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Tanabe Pharma America, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Head of Medical Science

Role: STUDY_DIRECTOR

Tanabe Pharma America, Inc.

Locations

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Birmingham, Alabama, United States

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Dothan, Alabama, United States

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Phoenix, Arizona, United States

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Norwalk, California, United States

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Sacramento, California, United States

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San Diego, California, United States

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Denver, Colorado, United States

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New London, Connecticut, United States

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New London, Connecticut, United States

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Aventura, Florida, United States

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Clearwater, Florida, United States

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Crystal River, Florida, United States

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Fort Myers, Florida, United States

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Hialeah, Florida, United States

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Hialeah, Florida, United States

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Jacksonville, Florida, United States

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Jacksonville, Florida, United States

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Jupiter, Florida, United States

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Miami, Florida, United States

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Miami, Florida, United States

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Miami, Florida, United States

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Orlando, Florida, United States

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Orlando, Florida, United States

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Ponte Vedra, Florida, United States

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Port Saint Lucie, Florida, United States

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Sarasota, Florida, United States

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Sarasota, Florida, United States

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Wellington, Florida, United States

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West Palm Beach, Florida, United States

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Sandy Springs, Georgia, United States

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Idaho Falls, Idaho, United States

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Ankeny, Iowa, United States

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Wichita, Kansas, United States

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Marrero, Louisiana, United States

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Metairie, Louisiana, United States

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Baltimore, Maryland, United States

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Kalamazoo, Michigan, United States

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Saginaw, Michigan, United States

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Saginaw, Michigan, United States

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Kansas City, Missouri, United States

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Missoula, Montana, United States

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Las Vegas, Nevada, United States

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Las Vegas, Nevada, United States

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Lawrenceville, New Jersey, United States

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Morehead City, North Carolina, United States

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Winston-Salem, North Carolina, United States

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Cleveland, Ohio, United States

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Columbus, Ohio, United States

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Columbus, Ohio, United States

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Englewood, Ohio, United States

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Philadelphia, Pennsylvania, United States

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Bristol, Tennessee, United States

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Jackson, Tennessee, United States

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Knoxville, Tennessee, United States

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Memphis, Tennessee, United States

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Fort Worth, Texas, United States

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Schertz, Texas, United States

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Draper, Utah, United States

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Ogden, Utah, United States

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Salt Lake City, Utah, United States

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Norfolk, Virginia, United States

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Covington, Washington, United States

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Seattle, Washington, United States

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Countries

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United States

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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MT-8554-A01

Identifier Type: -

Identifier Source: org_study_id