A Study to Evaluate the Efficacy and Safety of Semorinemab in Patients With Prodromal to Mild Alzheimer's Disease

NCT ID: NCT03289143

Last Updated: 2022-03-16

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

View full results

Basic Information

Get a concise snapshot of the trial, including recruitment status, study phase, enrollment targets, and key timeline milestones.

Recruitment Status

TERMINATED

Clinical Phase

PHASE2

Total Enrollment

457 participants

Study Classification

INTERVENTIONAL

Study Start Date

2017-10-04

Study Completion Date

2021-01-15

Brief Summary

Review the sponsor-provided synopsis that highlights what the study is about and why it is being conducted.

This was a phase II, randomized, placebo-controlled, double-blind study to evaluate the efficacy and safety of Semorinemab in participants with prodromal to mild Alzheimer's disease. An optional 96-week open-label extension period was available to participants who completed the double-blind treatment period and who, in the judgment of the investigator, would potentially benefit from open-label Semorinemab treatment.

Detailed Description

Dive into the extended narrative that explains the scientific background, objectives, and procedures in greater depth.

Conditions

See the medical conditions and disease areas that this research is targeting or investigating.

Alzheimer's Disease

Study Design

Understand how the trial is structured, including allocation methods, masking strategies, primary purpose, and other design elements.

Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

TRIPLE

Participants Investigators Outcome Assessors
Additional blinded personnel will include study site personnel who will evaluate participant status, contract research organization (CRO) personnel who will review case report forms (CRFs), and other sponsor agents (with the exception of the interactive voice or web-based response system \[IxRS\] vendor).

Study Groups

Review each arm or cohort in the study, along with the interventions and objectives associated with them.

Dose 1 Semorinemab

Group Type EXPERIMENTAL

Semorinemab

Intervention Type DRUG

Participants will receive Semorinemab intravenously (IV).

[18F]GTP1

Intervention Type DRUG

\[18F\]GTP1 will be administered as a solution for intravenous (IV) use, as part of positron emission tomography (PET) imaging.

Dose 2 Semorinemab

Group Type EXPERIMENTAL

Semorinemab

Intervention Type DRUG

Participants will receive Semorinemab intravenously (IV).

[18F]GTP1

Intervention Type DRUG

\[18F\]GTP1 will be administered as a solution for intravenous (IV) use, as part of positron emission tomography (PET) imaging.

Dose 3 Semorinemab

Group Type EXPERIMENTAL

Semorinemab

Intervention Type DRUG

Participants will receive Semorinemab intravenously (IV).

[18F]GTP1

Intervention Type DRUG

\[18F\]GTP1 will be administered as a solution for intravenous (IV) use, as part of positron emission tomography (PET) imaging.

Placebo

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Matching placebo doses of Semorinemab given intravenously (IV).

[18F]GTP1

Intervention Type DRUG

\[18F\]GTP1 will be administered as a solution for intravenous (IV) use, as part of positron emission tomography (PET) imaging.

Interventions

Learn about the drugs, procedures, or behavioral strategies being tested and how they are applied within this trial.

Semorinemab

Participants will receive Semorinemab intravenously (IV).

Intervention Type DRUG

Placebo

Matching placebo doses of Semorinemab given intravenously (IV).

Intervention Type DRUG

[18F]GTP1

\[18F\]GTP1 will be administered as a solution for intravenous (IV) use, as part of positron emission tomography (PET) imaging.

Intervention Type DRUG

Other Intervention Names

Discover alternative or legacy names that may be used to describe the listed interventions across different sources.

RG6100 MTAU9937A RO7105705 RO6880276

Eligibility Criteria

Check the participation requirements, including inclusion and exclusion rules, age limits, and whether healthy volunteers are accepted.

Inclusion Criteria

* Age between 50 and 80 years
* National Institute on Aging/Alzheimer's Association core clinical criteria for probable Alzheimer's disease (AD) dementia or mild cognitive impairment (prodromal AD)
* Evidence of the AD pathological process, by a positive amyloid assessment either on cerebrospinal fluid Aβ1-42 OR amyloid positron emission tomography (PET) scan. Historical amyloid PET scans may be accepted in some cases
* Mild AD symptomatology, as defined by a screening Mini-Mental State Examination score of \>= 20 points and Clinical Dementia Rating (CDR) -Global Score of 0.5 or 1
* Abnormal memory function at screening
* Availability of a person with sufficient contact with the participant to be able to provide accurate information on the participant's cognitive and functional ability

Exclusion Criteria

* Pregnant or breastfeeding
* Inability to tolerate magnetic resonance imaging (MRI) procedures or contraindication to MRI
* Contraindications to both PET imaging and lumbar dural puncture (must be able to undergo at least one of these procedures to be eligible)
* Residence in a skilled nursing facility
* Any serious medical condition or abnormality in clinical laboratory tests that remains abnormal on retest and, in the investigator's judgment, precludes the patient's safe participation in and completion of the study, or bias the assessment of the clinical or mental status of the participant to a significant degree
* Any evidence of a condition other than AD that may affect cognition
* Alcohol or substance abuse within the past 2 years
* Use of any experimental therapy within 90 days or 5 half-lives prior to screening, whichever is greater and any passive immunotherapy (immunoglobulin) against tau, except use of RO7105705 in Genentech Study GN39058, as long as the last dose was at least 90 days prior to screening
* Use of any passive immunotherapy (immunoglobulin) against Aβ, unless the last dose was at least 1 year prior to screening and any active immunotherapy (vaccine) that is under evaluation to prevent or postpone cognitive decline
* Any previous treatment with medications specifically intended to treat Parkinsonian symptoms or any other neurodegenerative disorder within 1 year of screening
* Systemic immunosuppressive therapy within 12 months of screening through the entire study period
* Typical antipsychotic or neuroleptic medication within 6 months of screening
* Daily treatment with any of the following classes of medication, except for intermittent short-term use, which is permitted except within 2 days or 5 half-lives (whichever is longer) prior to any COA: atypical antipsychotics, opiates or opioids, benzodiazepines, barbiturates, hypnotics, or any medication with clinically significant centrally-acting antihistamine or anticholinergic activity
* Stimulant medications, unless the dose has been stable within the 6 months prior to screening and is expected to be stable throughout the study
Minimum Eligible Age

50 Years

Maximum Eligible Age

80 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

Meet the organizations funding or collaborating on the study and learn about their roles.

Genentech, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

Identify the individual or organization who holds primary responsibility for the study information submitted to regulators.

Responsibility Role SPONSOR

Principal Investigators

Learn about the lead researchers overseeing the trial and their institutional affiliations.

Clinical Trials

Role: STUDY_DIRECTOR

Genentech, Inc.

Locations

Explore where the study is taking place and check the recruitment status at each participating site.

University of Alabama at Birmingham

Birmingham, Alabama, United States

Site Status

California Clinical Trials

Glendale, California, United States

Site Status

University of California Irvine

Irvine, California, United States

Site Status

Pharmacology Research Inst

Newport Beach, California, United States

Site Status

Stanford Neuroscience Health Center (SNHC)

Palo Alto, California, United States

Site Status

Pacific Research Network - PRN

San Diego, California, United States

Site Status

Neurological Research Inst

Santa Monica, California, United States

Site Status

Collaborative Neuroscience Network Inc.

Torrance, California, United States

Site Status

Invicro, a Konica Minolta company

New Haven, Connecticut, United States

Site Status

Yale University

New Haven, Connecticut, United States

Site Status

KI Health Partners, LLC; New England Institute for Clinical Research

Stamford, Connecticut, United States

Site Status

Georgetown University Hospital

Washington D.C., District of Columbia, United States

Site Status

JEM Research LLC

Atlantis, Florida, United States

Site Status

Bradenton Research Center

Bradenton, Florida, United States

Site Status

Brain Matters Research, Inc.

Delray Beach, Florida, United States

Site Status

Neuropsychiatric Research; Center of Southwest Florida

Fort Myers, Florida, United States

Site Status

Miami Jewish Health Systems

Miami, Florida, United States

Site Status

Collier Neurologic Specialists

Naples, Florida, United States

Site Status

Compass Research East, LLC

Orlando, Florida, United States

Site Status

Stedman Clinical Trials, LLC

Tampa, Florida, United States

Site Status

Alzheimer's Research and Treatment Center

Wellington, Florida, United States

Site Status

Premiere Research Institute

West Palm Beach, Florida, United States

Site Status

Emory University; Global Health

Atlanta, Georgia, United States

Site Status

Rush Alzheimer's Disease Cntr.

Chicago, Illinois, United States

Site Status

Alexian Brothers Neuroscience Institute

Elk Grove Village, Illinois, United States

Site Status

Southern Illinois University, School of Medicine

Springfield, Illinois, United States

Site Status

Eastern Maine Medical Center

Bangor, Maine, United States

Site Status

Brigham & Women's Hosp; TIMI Study Grp

Boston, Massachusetts, United States

Site Status

Alzheimers Disease Center

Quincy, Massachusetts, United States

Site Status

Health Partners Institute for Education and Research

Saint Paul, Minnesota, United States

Site Status

NeuroCognitive Institute

Mount Arlington, New Jersey, United States

Site Status

Advanced Memory Research Institute of NJ

Toms River, New Jersey, United States

Site Status

Albany Medical College; Neurology

Albany, New York, United States

Site Status

Empire Neurology PC; MS Center of Northeastern NY

Latham, New York, United States

Site Status

Columbia Univ Medical Center

New York, New York, United States

Site Status

University of Rochester; AD-CARE

Rochester, New York, United States

Site Status

Summit Research Network Inc.

Portland, Oregon, United States

Site Status

Abington Neurological Associates

Abington, Pennsylvania, United States

Site Status

Rhode Island Mood & Memory Research Institute

East Providence, Rhode Island, United States

Site Status

Butler Hospital

Providence, Rhode Island, United States

Site Status

Neurology Clinic PC

Cordova, Tennessee, United States

Site Status

New Orleans Center For Clinical Research

Knoxville, Tennessee, United States

Site Status

Clinical Neuroscience Research Associates, Inc.

Bennington, Vermont, United States

Site Status

St Vincents Medical Centre

Darlinghurst, New South Wales, Australia

Site Status

Southern Neurology

Kogarah, New South Wales, Australia

Site Status

Queensland University of Technology

Mermaid Waters, Queensland, Australia

Site Status

Eastern Clinical Research Unit; Pharmacy

Box Hill, Victoria, Australia

Site Status

HammondCare Aged Psychiatry Clinical Trials

Malvern, Victoria, Australia

Site Status

The Alfred Hospital, Melbourne; Thrombosis and Haemostasis Unit

Melbourne, Victoria, Australia

Site Status

Neuro Trials Victoria

Noble Park, Victoria, Australia

Site Status

Royal Melbourne Hospital

Parkville, Victoria, Australia

Site Status

UZ Brussel

Brussels, , Belgium

Site Status

AZ Groeninge

Kortrijk, , Belgium

Site Status

UZ Leuven

Leuven, , Belgium

Site Status

AZ Delta Campus Westlaan

Roeselare, , Belgium

Site Status

JBN Medical Diagnostic Services; Clinical Trials Division

Burlington, Ontario, Canada

Site Status

Parkwood Institute, Mental Health Care Building

London, Ontario, Canada

Site Status

Elisabeth Bruyere Hospital

Ottawa, Ontario, Canada

Site Status

Toronto Memory Program

Toronto, Ontario, Canada

Site Status

Centre for Memory and Aging

Toronto, Ontario, Canada

Site Status

Toronto Sunnybrook Hospital

Toronto, Ontario, Canada

Site Status

Toronto Western Hospital

Toronto, Ontario, Canada

Site Status

Recherches Neuro-Hippocame

Gatineau, Quebec, Canada

Site Status

Center For Clinical and Basic Research (Ccbr); Site Management Organisation

Aalborg, , Denmark

Site Status

CCBR - Vejle - DK

Vejle, , Denmark

Site Status

Groupe Hospitalier Pellegrin; Service de Neurologie - 3ème étage

Bordeaux, , France

Site Status

Hopital Neurologique Pierre Wertheimer

Bron, , France

Site Status

Hopital Roger Salengro

Lille, , France

Site Status

CHU de la Timone - Hopital d Adultes; Service de Neurologie

Marseille, , France

Site Status

Hopital Gui de Chauliac; Neurologie

Montpellier, , France

Site Status

Hopital Fernand Widal Centre

Paris, , France

Site Status

Groupe Hospitalier Pitie-Salpetriere

Paris, , France

Site Status

CHU Rennes

Rennes, , France

Site Status

CHU Hautepierre; ACTR Association Recherche Clinique Rhumatologie

Strasbourg, , France

Site Status

CHU Strasbourg - Hôpital Hautepierre

Strasbourg, , France

Site Status

Hopital de La Grave

Toulouse, , France

Site Status

Hopital des Charpennes

Villeurbanne, , France

Site Status

Klinikum Bayreuth; Krankenhaus Hohe Warte

Bayreuth, , Germany

Site Status

Praxis Dr. med. Volker Shumann

Berlin, , Germany

Site Status

Studienambulanz emovis GmbH; St. Joseph Krankenhaus

Berlin, , Germany

Site Status

Charite Campus Benjamin Franklin

Berlin, , Germany

Site Status

Neurologisch-psychiatrische Praxis am Brosepark

Berlin, , Germany

Site Status

Bezirkskrankenhaus Günzburg

Günzburg, , Germany

Site Status

Klinische Forschung Hannover-Mitte GmbH

Hanover, , Germany

Site Status

Klinikum rechts der Isar der TU München; Klinik & Poliklinik für Neurologie

München, , Germany

Site Status

ZNS Siegen im MVZ Weidenau

Siegen, , Germany

Site Status

Universitätsklinik Tübingen; Psychiatrie und Psychotherapie

Tübingen, , Germany

Site Status

Universitätsklinikum Ulm; Klinik für Neurologie

Ulm, , Germany

Site Status

Az. Osp. C. Panico; Rep. Ematologia E Trapianto

Tricase - LE, Apulia, Italy

Site Status

Umberto I Policlinico di Roma-Università di Roma La Sapienza

Rome, Lazio, Italy

Site Status

Ospedale San Giovanni Calibita Fatebenefratell;Neurologia

Rome, Lazio, Italy

Site Status

Azienda Ospedaliero Universitaria San Martino; Dip. di Neuroscienze Oftalmologia e Genetica

Genoa, Liguria, Italy

Site Status

IRCCS Centro San Giovanni di Dio FBF

Brescia, Lombardy, Italy

Site Status

Fondazione IRCCS Istituto Neurologico Carlo Besta

Milan, Lombardy, Italy

Site Status

IRCCS Neuromed; Neurologia I-Centro studio e cura delle demenze e UVA

Pozzilli, Molise, Italy

Site Status

Jeroen Bosch Ziekenhuis

's-Hertogenbosch, , Netherlands

Site Status

Brain Research Center B.V

Amsterdam, , Netherlands

Site Status

Podlaskie Centrum Psychogeriatrii

Bialystok, , Poland

Site Status

PALLMED Sp. z o.o. prowadząca NZOZ DOM SUE RYDER

Bydgoszcz, , Poland

Site Status

M.A. - LEK A.M.Maciejowscy SC.

Katowice, , Poland

Site Status

Novo-Med Zielinski i wspolnicy Sp. j.

Katowice, , Poland

Site Status

Malopolskie Centrum Medyczne

Krakow, , Poland

Site Status

NEURO - KARD Ośrodek Badań Klinicznych

Poznan, , Poland

Site Status

NEURO-CARE Sp. z o.o. Sp. Komandytowa

Siemianowice Śląskie, , Poland

Site Status

Senior Sp. Z O.O. Poradnia Psychogeriatryczna

Sopot, , Poland

Site Status

EroMedis

Szczecin, , Poland

Site Status

AMED Medical Center

Warsaw, , Poland

Site Status

Centrum Medyczne NeuroProtect

Warsaw, , Poland

Site Status

NZOZ WCA

Wroclaw, , Poland

Site Status

Hospital Mutua de Terrassa

Terrassa, Barcelona, Spain

Site Status

Policlinica Guipuzcoa

Donostia / San Sebastian, Guipuzcoa, Spain

Site Status

Clinica Universitaria de Navarra; Servicio de Neurología

Pamplona, Navarre, Spain

Site Status

Hospital Virgen del Puerto

Plasencia, Palencia, Spain

Site Status

Hospital de Cruces; Servicio de Neurologia

Barakaldo, Vizcaya, Spain

Site Status

Hospital Perpetuo Socorro, Servicio de Geriatria

Albacete, , Spain

Site Status

Hospital de la Santa Creu i Sant Pau

Barcelona, , Spain

Site Status

Fundación ACE; Servicio de Neurología

Barcelona, , Spain

Site Status

Hospital Clinic i Provincial de Barcelona

Barcelona, , Spain

Site Status

Hospital Universitario Reina Sofia; Servicio de Neurologia

Córdoba, , Spain

Site Status

Hospital Universitario Ramon y Cajal

Madrid, , Spain

Site Status

Hospital de Cantoblanco; Servicio de Geriatria

Madrid, , Spain

Site Status

Hospital Universitario Virgen Macarena

Seville, , Spain

Site Status

Hospital Universitario Dr. Peset; Servicio de Neurologia

Valencia, , Spain

Site Status

Hospital Universitari i Politecnic La Fe de Valencia

Valencia, , Spain

Site Status

Länssjukhuset Ryhov

Jönköping, , Sweden

Site Status

Länssjukhuset Kalmar; Oncology

Kalmar, , Sweden

Site Status

Skane University Hospital Malmo/Lund, Dept.of Hematology and Coagulation Disorders

Malmo, , Sweden

Site Status

Sahlgrenska Univ Hospital Mölndal; Department of Nephrology

Mölndal, , Sweden

Site Status

Karolinska Universitetssjukhuset Huddinge

Stockholm, , Sweden

Site Status

Glasgow Memory Clinic

Glasgow, , United Kingdom

Site Status

RE:Cognition Health

London, , United Kingdom

Site Status

The National Hospital for Neurology & Neurosurgery

London, , United Kingdom

Site Status

Re:Cognition Health Guildford

Surrey, , United Kingdom

Site Status

Countries

Review the countries where the study has at least one active or historical site.

United States Australia Belgium Canada Denmark France Germany Italy Netherlands Poland Spain Sweden United Kingdom

References

Explore related publications, articles, or registry entries linked to this study.

Chandler JM, Lansdall CJ, Ye W, McDougall F, Belger M, Toth B, Mi X, Sink KM, Atkins AS. The Alzheimer's Disease Cooperative Study - Activities of Daily Living dependence score: revision and validation of an algorithm evaluating patient dependence across the spectrum of AD severity. J Prev Alzheimers Dis. 2025 Sep;12(8):100261. doi: 10.1016/j.tjpad.2025.100261. Epub 2025 Jul 1.

Reference Type DERIVED
PMID: 40603145 (View on PubMed)

Schauer SP, Toth B, Lee J, Honigberg LA, Ramakrishnan V, Jiang J, Kollmorgen G, Bayfield A, Wild N, Hoffman J, Ceniceros R, Dolton M, Bohorquez SMS, Hoogenraad CC, Wildsmith KR, Teng E, Monteiro C, Anania V, Yeh FL. Pharmacodynamic effects of semorinemab on plasma and CSF biomarkers of Alzheimer's disease pathophysiology. Alzheimers Dement. 2024 Dec;20(12):8855-8866. doi: 10.1002/alz.14346. Epub 2024 Nov 8.

Reference Type DERIVED
PMID: 39513754 (View on PubMed)

Sanabria Bohorquez SM, Baker S, Manser PT, Tonietto M, Galli C, Wildsmith KR, Zou Y, Kerchner GA, Weimer R, Teng E. Evaluation of partial volume correction and analysis of longitudinal [18F]GTP1 tau PET imaging in Alzheimer's disease using linear mixed-effects models. Front Neuroimaging. 2024 Mar 28;3:1355402. doi: 10.3389/fnimg.2024.1355402. eCollection 2024.

Reference Type DERIVED
PMID: 38606196 (View on PubMed)

Teng E, Li Y, Manser PT, Pickthorn K, Butcher BD, Blendstrup M, Randolph C, Sikkes SAM. Cross-sectional and longitudinal assessments of function in prodromal-to-mild Alzheimer's disease: A comparison of the ADCS-ADL and A-IADL-Q scales. Alzheimers Dement (Amst). 2023 Jun 13;15(2):e12452. doi: 10.1002/dad2.12452. eCollection 2023 Apr-Jun.

Reference Type DERIVED
PMID: 37325545 (View on PubMed)

Teng E, Manser PT, Shah M, Pickthorn K, Hu N, Djakovic S, Swendsen H, Blendstrup M, Faccin G, Ostrowitzki S, Sink KM. The Use of Episodic Memory Tests for Screening in Clinical Trials for Early Alzheimer's Disease: A Comparison of the Free and Cued Selective Reminding Test (FCSRT) and the Repeatable Battery for the Assessment of Neuropsychological Status (RBANS). J Prev Alzheimers Dis. 2023;10(1):41-49. doi: 10.14283/jpad.2022.101.

Reference Type DERIVED
PMID: 36641609 (View on PubMed)

Teng E, Manser PT, Pickthorn K, Brunstein F, Blendstrup M, Sanabria Bohorquez S, Wildsmith KR, Toth B, Dolton M, Ramakrishnan V, Bobbala A, Sikkes SAM, Ward M, Fuji RN, Kerchner GA; Tauriel Investigators. Safety and Efficacy of Semorinemab in Individuals With Prodromal to Mild Alzheimer Disease: A Randomized Clinical Trial. JAMA Neurol. 2022 Aug 1;79(8):758-767. doi: 10.1001/jamaneurol.2022.1375.

Reference Type DERIVED
PMID: 35696185 (View on PubMed)

Provided Documents

Download supplemental materials such as informed consent forms, study protocols, or participant manuals.

Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

Review additional registry numbers or institutional identifiers associated with this trial.

2017-001800-31

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

GN39763

Identifier Type: -

Identifier Source: org_study_id

More Related Trials

Additional clinical trials that may be relevant based on similarity analysis.