Intranasal Oxytocin for Frontotemporal Dementia

NCT ID: NCT03260920

Last Updated: 2023-12-15

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

ACTIVE_NOT_RECRUITING

Clinical Phase

PHASE2

Total Enrollment

112 participants

Study Classification

INTERVENTIONAL

Study Start Date

2018-01-31

Study Completion Date

2024-12-31

Brief Summary

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The purpose of this study is to assess the safety, tolerability and effects on behaviour of Syntocinon given intranasally (by a spray into the nostrils) compared to placebo (an inactive saline substance that contains no medication) in participants with frontotemporal dementia/Pick's disease. This study will take place in approximately 15 centres across Canada and the United States. Approximately 112 patients in total will be enrolled in this study. In the first phase we will examine which of three different dosing schedules of oxytocin may be more effective. In the second phase of the study, patients entering the study will be randomized to the oxytocin dosing schedule that appeared most effective in the first phase.

Detailed Description

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Conditions

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Frontotemporal Dementia

Keywords

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oxytocin frontotemporal dementia apathy empathy

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

CROSSOVER

A Proof-of-Concept Double Blind Randomized Controlled, Cross-Over Adaptive Design Trial
Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors
Double Blind

Study Groups

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Low Dose

Group Type EXPERIMENTAL

Syntocinon

Intervention Type DRUG

Intranasal Oxytocin

Medium Dose

Group Type EXPERIMENTAL

Syntocinon

Intervention Type DRUG

Intranasal Oxytocin

High Dose

Group Type EXPERIMENTAL

Syntocinon

Intervention Type DRUG

Intranasal Oxytocin

Interventions

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Syntocinon

Intranasal Oxytocin

Intervention Type DRUG

Other Intervention Names

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Intranasal Oxytocin

Eligibility Criteria

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Inclusion Criteria

* Diagnosis of probable FTD (behavioural variant FTD, FTD-semantic subtype or FTD-Progressive Nonfluent Aphasia) with supportive brain imaging (centrally rated frontotemporal atrophy score of 2 or greater on brain MRI or CT) or known FTD causing genetic mutation.68
* Current symptoms of social apathy/indifference as measured by NPI apathy/indifference severity subscale score \>= 2 indicating the presence of moderate to marked levels of apathy/indifference.
* Study partner who consents to study participation and who cares for/visits the patient daily for at least 3 hours/day and who can administer all trial medications.
* FTLD-CDR score 0-2.
* MMSE \>10.
* Stable baseline medications related to cognition or behaviour for \>=30 days such as acetylcholinesterase inhibitors, memantine, anti-depressants, antipsychotic agents, other mood stabilizers, benzodiazepines.
* Written informed consent must be obtained and documented (from the patient or, where jurisdictions allow it, from their substitute decision maker).

Exclusion Criteria

* History of stroke, other neurologic or psychiatric disorder other than FTD that is considered to better account for behavioural symptoms.
* History of a myocardial infarction within the last two years or congestive heart failure.
* Current uncontrolled hypertension
* Current bradycardia (rate \< 50 beats per minute/bpm) or tachycardia (rate \> 100 bpm)
* Current hyponatremia (Na \<135 mEq/L)
* Current use of topical prostaglandin medications applied to the cervix.
* Females who are pregnant or breastfeeding, or planning to conceive within the study period.
* Use of any investigational or experimental drug or device within the last 60 days prior to screening or within 5 half-lives of the experimental drug, whichever is longer.
* Participant has speech difficulties that in the opinion of the investigator would be incompatible with neuropsychology and safety assessments
* History of cancer except:

* If considered to be cured
* If not being actively treated with anti-cancer therapy or radiotherapy and, in the opinion of the investigator, not likely to require treatment in the ensuing 5 years
* For prostate cancer or basal cell carcinoma, no significant progression over the previous 2 years
* Any clinically significant hematological, endocrine, cardiovascular, renal, hepatic, gastrointestinal or neurological disease. If the condition has been stable for at least the past year and is judged by the investigator not to interfere with the patient's participation in the study, the patient may be included.
* For the CSF sub-study, current use of anticoagulant medications (warfarin, rivaroxaban, etc.).
* Plan for FTD patient to be placed into long-term care or plan for hospital admission for any kind of treatment within study period or if caregiver plans for holidays/respite care \> 3 days during study period.
Minimum Eligible Age

30 Years

Maximum Eligible Age

80 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Weston Brain Institute

OTHER

Sponsor Role collaborator

Canadian Institutes of Health Research (CIHR)

OTHER_GOV

Sponsor Role collaborator

Berry Consultants

OTHER

Sponsor Role collaborator

London Health Sciences Centre Research Institute OR Lawson Research Institute of St. Joseph's

OTHER

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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UCLA

Los Angeles, California, United States

Site Status

University of California, San Francisco

San Francisco, California, United States

Site Status

Johns Hopkins Bayview Medical Center

Baltimore, Maryland, United States

Site Status

Columbia University Medical Center

New York, New York, United States

Site Status

University of Washington

Seattle, Washington, United States

Site Status

University of British Columbia

Vancouver, British Columbia, Canada

Site Status

Parkwood Institute

London, Ontario, Canada

Site Status

Sunnybrook Health Sciences Centre

Toronto, Ontario, Canada

Site Status

University Health Network

Toronto, Ontario, Canada

Site Status

Montreal Neurological Institute and Hospital

Montreal, Quebec, Canada

Site Status

Laval University

Québec, , Canada

Site Status

Countries

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United States Canada

References

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Coleman KKL, Berry S, Cummings J, Hsiung GR, Laforce R, Huey E, Ducharme S, Tartaglia MC, Mendez MF, Onyike C, Domoto-Reilly K, Masellis M, Herrmann N, Porsteinsson A, Detry MA, Stewart C, Bosse AL, McGlothlin A, Dias B, Pandey S, Mayich M, Pasternak SH, Ruiz Garcia R, Restrepo-Martinez M, Feldman H, Boxer AL, Finger EC. Intranasal oxytocin for apathy in people with frontotemporal dementia (FOXY): a multicentre, randomised, double-blind, placebo-controlled, adaptive, crossover, phase 2a/2b superiority trial. Lancet Neurol. 2025 Feb;24(2):128-139. doi: 10.1016/S1474-4422(24)00456-3.

Reference Type DERIVED
PMID: 39862881 (View on PubMed)

Finger E, Berry S, Cummings J, Coleman K, Hsiung R, Feldman HH, Boxer A. Adaptive crossover designs for assessment of symptomatic treatments targeting behaviour in neurodegenerative disease: a phase 2 clinical trial of intranasal oxytocin for frontotemporal dementia (FOXY). Alzheimers Res Ther. 2018 Sep 27;10(1):102. doi: 10.1186/s13195-018-0427-2.

Reference Type DERIVED
PMID: 30261917 (View on PubMed)

Provided Documents

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Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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FTDOXY17EF

Identifier Type: -

Identifier Source: org_study_id