Pembrolizumab (MK-3475) Plus Epacadostat vs Standard of Care in mRCC (KEYNOTE-679/ECHO-302)

NCT ID: NCT03260894

Last Updated: 2025-07-29

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

129 participants

Study Classification

INTERVENTIONAL

Study Start Date

2017-12-07

Study Completion Date

2025-06-04

Brief Summary

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The purpose of this study was to evaluate the efficacy and safety of pembrolizumab plus epacadostat compared to sunitinib or pazopanib in participants with locally advanced/metastatic renal cell carcinoma (mRCC) with a clear cell component who have not received prior systemic therapy for their mRCC.

Detailed Description

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Conditions

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Renal Cell Carcinoma (RCC)

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Pembrolizumab + Epacadostat

Group Type EXPERIMENTAL

Pembrolizumab

Intervention Type DRUG

Pembrolizumab 200 mg administered intravenously every 3 weeks.

Epacadostat

Intervention Type DRUG

Epacadostat 100 mg administered orally twice daily.

SoC (Sunitinib or Pazopanib)

Standard of care (SoC) (sunitinib or pazopanib monotherapy).

Group Type ACTIVE_COMPARATOR

Sunitinib

Intervention Type DRUG

Sunitinib 50 mg administered orally once daily; 4 weeks on, 2 weeks off for 6-wk cycle.

Pazopanib

Intervention Type DRUG

Pazopanib 800 mg administered orally once daily.

Interventions

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Pembrolizumab

Pembrolizumab 200 mg administered intravenously every 3 weeks.

Intervention Type DRUG

Epacadostat

Epacadostat 100 mg administered orally twice daily.

Intervention Type DRUG

Sunitinib

Sunitinib 50 mg administered orally once daily; 4 weeks on, 2 weeks off for 6-wk cycle.

Intervention Type DRUG

Pazopanib

Pazopanib 800 mg administered orally once daily.

Intervention Type DRUG

Other Intervention Names

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MK-3475 INCB024360 Sutent SU11248 Votrient

Eligibility Criteria

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Inclusion Criteria

* Histologic confirmation of locally advanced or metastatic RCC with a clear-cell component with or without sarcomatoid features.
* Must not have received any prior systemic therapy for their mRCC.
* Measurable disease based on RECIST v1.1.
* Archival tumor tissue sample or newly obtained core or excisional biopsy of a tumor lesion as required.
* Karnofsky performance status ≥ 70%.
* Adequate organ function per protocol-defined criteria.

Exclusion Criteria

* Use of protocol-defined prior/concomitant therapy.
* Currently receiving or has received an investigational treatment as part of a study of an investigational agent or has used an investigational device within 4 weeks before randomization.
* History of severe hypersensitivity reaction to study treatments or their excipients.
* Active autoimmune disease that has required systemic treatment in past 2 years.
* Known additional malignancy that has progressed or has required active treatment in the last 3 years.
* Known active central nervous system metastases and/or carcinomatous meningitis.
* History of (noninfectious) pneumonitis that required steroids or current pneumonitis.
* History or presence of an abnormal electrocardiogram that, in the investigator's opinion, is clinically meaningful.
* Significant cardiac event within 12 months before Cycle 1 Day 1.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Merck Sharp & Dohme LLC

INDUSTRY

Sponsor Role collaborator

Incyte Corporation

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Mark Jones, MD

Role: STUDY_DIRECTOR

Incyte Corporation

Locations

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Pinnacle Oncology Hematology

Scottsdale, Arizona, United States

Site Status

Scottsdale Healthcare

Scottsdale, Arizona, United States

Site Status

Arizona Oncology Associates PC- HOPE

Tucson, Arizona, United States

Site Status

Cedars-Sinai Medical Center

Los Angeles, California, United States

Site Status

UC Irvine Comprehensive Cancer Center/Chao Family Comprehensive Cancer Center

Orange, California, United States

Site Status

UC Davis Comprehensive Cancer Center

Sacramento, California, United States

Site Status

Woodlands Medical Specialists, PA

Pensacola, Florida, United States

Site Status

Northside Hospital

Atlanta, Georgia, United States

Site Status

Atlanta Cancer Care - Conyers

Conyers, Georgia, United States

Site Status

Northwest Georgia Oncology Centers Pc

Marietta, Georgia, United States

Site Status

Rush University Medical Center

Chicago, Illinois, United States

Site Status

Massachusetts General Hospital

Boston, Massachusetts, United States

Site Status

Dana Farber Cancer Institute

Boston, Massachusetts, United States

Site Status

Southeast Nebraska Hematology & Oncology Consultants, P.C.

Lincoln, Nebraska, United States

Site Status

New York Oncology Hematology P.C

Albany, New York, United States

Site Status

Memorial Sloan Kettering Cancer Center

New York, New York, United States

Site Status

Levine Cancer Institute

Charlotte, North Carolina, United States

Site Status

Willamette Valley Cancer Institute and Research Center

Eugene, Oregon, United States

Site Status

University of Tennessee Erlanger Oncology & Hematology

Chattanooga, Tennessee, United States

Site Status

The West Clinic, P.C.

Germantown, Tennessee, United States

Site Status

US Oncology and Research

The Woodlands, Texas, United States

Site Status

Utah Cancer Specialists

Salt Lake City, Utah, United States

Site Status

Huntsman Cancer Institute

Salt Lake City, Utah, United States

Site Status

Oncology & Hematology Associates of Southwest Virginia, Inc., DBA Blue Ridge Cancer Care

Roanoke, Virginia, United States

Site Status

Shenandoah Oncology, P.C.

Winchester, Virginia, United States

Site Status

Canberra Hospital

Garran, Australian Capital Territory, Australia

Site Status

Calvary Mater Newcastle

Waratah, New South Wales, Australia

Site Status

Westmead Hospital

Westmead, New South Wales, Australia

Site Status

Cabrini Health

Malvern, Victoria, Australia

Site Status

Fiona Stanley Hospital

Murdoch, , Australia

Site Status

Centro de pesquisa Porto Alegre

Porto Alegre, Florianopolis, Brazil

Site Status

Fundacao Pio XII - Hospital de Cancer de Barretos

Barretos, São Paulo, Brazil

Site Status

Instituto do Cancer de Sao Paulo - ICESP

São Paulo, São Paulo, Brazil

Site Status

Hospital Sao Jose

São Paulo, São Paulo, Brazil

Site Status

Centro Avancado de Tratamento Oncologico - CENANTRON -

Belo Horizonte, , Brazil

Site Status

Hospital de Clinicas de Porto Alegre

Porto Alegre, , Brazil

Site Status

Tom Baker Cancer Centre

Calgary, Alberta, Canada

Site Status

Kingston Health Sciences Centre - KGH Site

Kingston, Ontario, Canada

Site Status

Sunnybrook Health Sciences, Odette Cancer Centre

Toronto, Ontario, Canada

Site Status

Jewish General Hospital

Montreal, Quebec, Canada

Site Status

CHU de Quebec-Universite Laval-Hotel Dieu de Quebec

Québec, Quebec, Canada

Site Status

CIUSSS de la Mauricie-et-du-Centre-du-Quebec

Trois-Rivières, Quebec, Canada

Site Status

Clinica Alemana de Osorno

Osorno, Los Lagos Region, Chile

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Fundacion Arturo Lopez Perez FALP

Santiago, , Chile

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Pontificia Universidad Catolica de Chile

Santiago, , Chile

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Hospital Clinico Vina del Mar

Viña del Mar, , Chile

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Centre Antoine Lacassagne

Nice, Cedex 2, France

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CHU Besancon - Hopital Jean Minjoz

Besançon, , France

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Hopital Saint Andre

Bordeaux, , France

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Centre Francois Baclesse

Caen, , France

Site Status

Hopital Prive Toulon Hyeres Sainte Marguerite

Hyères, , France

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Hopital Europeen Georges Pompidou

Paris, , France

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Hospices Civils de Lyon Centre Hospitalier Lyon Sud

Pierre-Bénite, , France

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Clinique Sainte Anne

Strasbourg, , France

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CHU de Strasbourg - Nouvel Hopital Civil

Strasbourg, , France

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Institut Gustave Roussy

Villejuif, , France

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Helios Klinikum Berlin Buch

Berlin, , Germany

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Universitaetsklinikum der Technischen Universitaet Dresden

Dresden, , Germany

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Universitaetsklinikum Essen

Essen, , Germany

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Universitaetsklinikum Frankfurt

Frankfurt am Main, , Germany

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Medizinische Hochschule Hannover

Hanover, , Germany

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Universitaetsklinikum Jena

Jena, , Germany

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Universitaetsklinikum Magdeburg. Klinik fuer Urologie

Magdeburg, , Germany

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Universitaetsklinikum Tuebingen

Tübingen, , Germany

Site Status

Orszagos Onkologiai Intezet

Budapest, Pest County, Hungary

Site Status

Zala Megyei Szent Rafael Korhaz

Zalaegerszeg, Pozva, Hungary

Site Status

Somogy Megyei Kaposi Mor Oktato Korhaz

Kaposvár, , Hungary

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Borsod-Abauj-Zemplen Megyei Korhaz es Egyetemi Oktato Korhaz

Miskolc, , Hungary

Site Status

Jasz Nagykun Szolnok Megyei Hetenyi Geza Korhaz Rendelointezet

Szolnok, , Hungary

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Markusovszky Egyetemi Oktatokorhaz

Szombathely, , Hungary

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Adelaide & Meath Hospital

Dublin, , Ireland

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University Hospital Waterford

Waterford, , Ireland

Site Status

Medical Oncology Ospedale San Donato

Arezzo, , Italy

Site Status

Azienda Ospedaliera-Spedali Civili

Brescia, , Italy

Site Status

Fondazione IRCCS Istituto Nazionale dei Tumori

Milan, , Italy

Site Status

A.O. Cardarelli

Napoli, , Italy

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Policlinico San Matteo

Pavia, , Italy

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Azienda Ospedaliera San Camillo Forlanini

Roma, , Italy

Site Status

Nagoya University Hospital

Nagoya, Aichi-ken, Japan

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National Cancer Center Hospital East

Kashiwa, Chiba, Japan

Site Status

Sapporo Medical University Hospital

Sapporo, Hokkaido, Japan

Site Status

Hokkaido University Hospital

Sapporo, Hokkaido, Japan

Site Status

Nara Medical University Hospital

Kashihara, Nara, Japan

Site Status

Kindai University Hospital

Sayama, Osaka, Japan

Site Status

Saitama Medical University International Medical Center

Hidaka, Saitama, Japan

Site Status

Yamaguchi University Hospital

Ube, Yamaguchi, Japan

Site Status

Akita University Hospital

Akita, , Japan

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Kyushu University Hospital

Fukuoka, , Japan

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Niigata University Medical & Dental Hospital

Niigata, , Japan

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Toranomon Hospital

Tokyo, , Japan

Site Status

Nippon Medical School Hospital

Tokyo, , Japan

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Keio University Hospital

Tokyo, , Japan

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Auckland City Hospital

Auckland, Grafton, New Zealand

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Helse Bergen HF Haukeland sykehus

Bergen, , Norway

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Sykehuset Oestfold

Grålum, , Norway

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Sorlandet sykehus HF

Kristiansand, , Norway

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Akershus University Hospital

Lørenskog, , Norway

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Oslo universitetssykehus

Oslo, , Norway

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Universitetssykehuset i Nord Norge. Kreftavdelingen

Tromsø, , Norway

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St Olavs Hospital

Trondheim, , Norway

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Leningrad Regional Oncology Dispensary

Saint Petersburg, Leningrad Region, Vsevolozhsky District, Russia

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Ivanovo regional oncology dispensary

Ivanovo, , Russia

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Russian Scientific Center of Roentgenoradiology

Moscow, , Russia

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Central Clinical Hospital with outpatient Clinic

Moscow, , Russia

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National Medical Research Radiology Centre

Moscow, , Russia

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Republican Clinical Oncology Dispensary of Republic of Bashkortostan

Ufa, , Russia

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Chonnam National University Hwasun Hospital

Hwasun, Jeollanam-do, South Korea

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Severance Hospital Yonsei University Health System

Seoul, , South Korea

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Asan Medical Center

Seoul, , South Korea

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Samsung Medical Center

Seoul, , South Korea

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Hospital Parc Tauli

Sabadell, Barcelona, Spain

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Hospital del Mar

Barcelona, , Spain

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Hospital Germans Trias i Pujol

Barcelona, , Spain

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Hospital General Universitario Gregorio Maranon

Madrid, , Spain

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Hospital Universitario HM Sanchinarro

Madrid, , Spain

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Hospital Clinico Universitario de Santiago

Santiago de Compostela, , Spain

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Instituto Valenciano de Oncologia

Valencia, , Spain

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Chang Gung Med Foundation. Kaohsiung Branch

Kaohsiung City, , Taiwan

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China Medical University Hospital

Taichung, , Taiwan

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National Cheng Kung University Hospital

Tainan City, , Taiwan

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National Taiwan University Hospital

Taipei, , Taiwan

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Taipei Veterans General Hospital

Taipei, , Taiwan

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Baskent Universitesi Adana Dr. Turgut Noyan Uygulama ve Arastirma Merkezi

Adana, , Turkey (Türkiye)

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Ankara Numune Education and Research Hospital

Ankara, , Turkey (Türkiye)

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Hacettepe University Medical Faculty

Ankara, , Turkey (Türkiye)

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Istanbul Universitesi Onkoloji Enstitusu

Istanbul, , Turkey (Türkiye)

Site Status

Istanbul Medeniyet Universitesi Goztepe EAH

Istanbul, , Turkey (Türkiye)

Site Status

Ege Universitesi Tıp Fakultesi

Izmir, , Turkey (Türkiye)

Site Status

Namik Kemal Universitesi Tip Fakultesi

Tekirdağ, , Turkey (Türkiye)

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MI Kryviy Rih Center of Dnipropetrovsk Regional Council

Kryvyi Rih, Dnipropetrovsk Oblast, Ukraine

Site Status

Dnipropetrovsk Regional Hospital n.a. I.I. Mechnikov

Dnipro, , Ukraine

Site Status

Dnipropetrovsk City Multidiscipline Clinical Hosp. 4 of DRC

Dnipro, , Ukraine

Site Status

MI Precarpathian Clinical Oncology Center

Ivano-Frankivsk, , Ukraine

Site Status

RMI Sumy Regional Clinical Oncology Dispensary

Sumy, , Ukraine

Site Status

The Royal Marsden NHS Foundation Trust.

Sutton, Surrey, United Kingdom

Site Status

Western General Hospital

Edinburgh, , United Kingdom

Site Status

Beatson Institute of Cancer Research

Glasgow, , United Kingdom

Site Status

Barts Health NHS Trust - St Bartholomew s Hospital

London, , United Kingdom

Site Status

The Royal Marsden Foundation Trust

London, , United Kingdom

Site Status

The Christie NHS Foundation Trust

Manchester, , United Kingdom

Site Status

Countries

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United States Australia Brazil Canada Chile France Germany Hungary Ireland Italy Japan New Zealand Norway Russia South Korea Spain Taiwan Turkey (Türkiye) Ukraine United Kingdom

References

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Lara PN Jr, Villanueva L, Ibanez C, Erman M, Lee JL, Heinrich D, Lipatov ON, Gedye C, Gokmen E, Acevedo A, Semenov A, Park SH, Gafanov RA, Kose F, Jones M, Du X, Munteanu M, Perini R, Choueiri TK, Motzer RJ. A randomized, open-label, phase 3 trial of pembrolizumab plus epacadostat versus sunitinib or pazopanib as first-line treatment for metastatic renal cell carcinoma (KEYNOTE-679/ECHO-302). BMC Cancer. 2024 Jul 25;23(Suppl 1):1253. doi: 10.1186/s12885-023-10971-7.

Reference Type DERIVED
PMID: 39054430 (View on PubMed)

Provided Documents

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Document Type: Study Protocol and Statistical Analysis Plan

View Document

Other Identifiers

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2024-512016-22-00

Identifier Type: REGISTRY

Identifier Source: secondary_id

2017-002259-26

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

KEYNOTE-679/ECHO-302

Identifier Type: -

Identifier Source: org_study_id

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