Pirfenidone for Progressive Fibrotic Sarcoidosis

NCT ID: NCT03260556

Last Updated: 2017-09-28

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

UNKNOWN

Clinical Phase

PHASE4

Total Enrollment

60 participants

Study Classification

INTERVENTIONAL

Study Start Date

2017-09-27

Study Completion Date

2020-03-30

Brief Summary

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Study comparing pirfenidone versus placebo for patients with advanced fibrotic sarcoidosis

Detailed Description

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Patients who meet the inclusion and exclusion criteria will be randomized to be treated with either placebo or pirfenidone at the current approved dosage for idiopathic pulmonary fibrosis at a 2:1 pirfenidone to placebo ratio. Patients treated with pirfenidone will be titrated using the following schedule:

One 267 mg capsules three times a day for two weeks. Two 267 mg capsules three times a day for two weeks Three 267 mg capsules three times a day thereafter Patients will be instructed to take all doses of medication with food. Dosage will be titrated on an individual basis depending on patient tolerance of medication.

Those randomized to placebo will receive the same schedule using placebo tablets.

Block randomization will be done at each site. Liver function tests will be evaluated as listed above. If the patient has an abnormal liver function test, then the dose will be adjusted per the company's protocol for commercial drug.

Conditions

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Sarcoidosis, Pulmonary

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Double blind placebo controlled trial
Primary Study Purpose

TREATMENT

Blinding Strategy

TRIPLE

Participants Caregivers Investigators
Placebo controlled

Study Groups

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Pirfenidone

Pirfenidone titrated to three 267 mg tablets three times a day

Group Type ACTIVE_COMPARATOR

Pirfenidone

Intervention Type DRUG

Increasing doses

Placebos

Placebo titrated to three tablets three times a day

Group Type PLACEBO_COMPARATOR

Placebos

Intervention Type DRUG

Increasing doses

Interventions

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Pirfenidone

Increasing doses

Intervention Type DRUG

Placebos

Increasing doses

Intervention Type DRUG

Other Intervention Names

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esbriet placebo

Eligibility Criteria

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Inclusion Criteria

* Diagnosis of sarcoidosis
* Pulmonary function testing with a Composite Physiologic Index (CPI) score of greater than 40
* Patient must have evidence of \>20% fibrosis on high resolution cat scan
* Patients must be on a stable prednisone therapy for sarcoidosis for at least two months and no change in other immunosuppressives in the two months prior to entry into study
* Age greater than 18 and less than 90.
* Able to provide written informed consent for participation in the study

Exclusion Criteria

* Patients receiving therapy for precapillary pulmonary hypertension.
* Patients with liver disease Childs class 3 or 4
* Patients with a left ventricular ejection fraction of less than 40%
* Patients receiving more than 20 mg prednisone daily or its equivalent
* Patients with massive hemoptysis within prior three months. Patients with mycetomas are eligible as long as no massive hemoptysis in prior three months.
* Patients with clinically important co-existing disease which in the opinion of the investigator is likely to affect patient's chance for survival during the course of the study
* Patient who is pregnant, lactating, intending to become pregnant during the study, or child bearing capacity who is not willing to use appropriate birth control methods approved by investigator
Minimum Eligible Age

18 Years

Maximum Eligible Age

90 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Royal Brompton & Harefield NHS Foundation Trust

OTHER

Sponsor Role collaborator

University of Cincinnati

OTHER

Sponsor Role lead

Responsible Party

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Robert P Baughman

Professor

Responsibility Role PRINCIPAL_INVESTIGATOR

Principal Investigators

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Robert P Baughman, MD

Role: PRINCIPAL_INVESTIGATOR

University of Cincinnati

Locations

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University of Cincinnati

Cincinnati, Ohio, United States

Site Status RECRUITING

Countries

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United States

Central Contacts

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Robert P Baughman, MD

Role: CONTACT

513-584-5225

Rebecca Reeves

Role: CONTACT

513-584-5226

Facility Contacts

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Robert P Baughman, MD

Role: primary

513-584-5225

Elyse E Lower

Role: backup

513-584-3829

Other Identifiers

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2016-5706

Identifier Type: -

Identifier Source: org_study_id