Trial Outcomes & Findings for A Trial to Assess Brexpiprazole Versus Placebo for the Treatment of Acute Manic Episodes, Associated With Bipolar I Disorder (NCT NCT03257865)

NCT ID: NCT03257865

Last Updated: 2020-02-11

Results Overview

The YMRS was utilized to assess a participant's level of manic symptoms. It consists of 11 items: 1) elevated mood, 2) increased motor activity-energy, 3) sexual interest, 4) sleep, 5) irritability, 6) speech (rate and amount), 7) language-thought disorder, 8) content, 9) disruptive-aggressive behavior, 10) appearance, and 11) insight. Seven items are rated on a 0- to 4-scale, while four items (Items 5, 6, 8, and 9) are rated on a 0- to 8-scale with 0, 2, 4, 6, and 8 being the possible scores (twice the weight of the other items). For all items, 0 is the "best" rating and the highest score (4 or 8) is the 'worst' rating. The YMRS total score is the sum of ratings for all 11 items; therefore, possible total scores range from 0 to 60, with higher scores signifying more severe manic symptoms. Comparison between treatment groups was carried out using mixed-effect model repeated measure (MRMM).

Recruitment status

COMPLETED

Study phase

PHASE3

Target enrollment

333 participants

Primary outcome timeframe

Baseline, Week 3

Results posted on

2020-02-11

Participant Flow

The trial population consisted of adult participants (18 to 65 years) diagnosed with bipolar I disorder displaying an acute manic episode with or without mixed features requiring hospitalization. One participant randomized to brexpiprazole was not treated and excluded from the safety analysis set.

Participant milestones

Participant milestones
Measure
Brexpiprazole
Brexpiprazole was administered orally with flexible dosing from 2 to 4 milligram (mg)/day; titrated to a maximum of 4 mg/day.
Placebo
Matching placebo was administered orally in the same way as brexpiprazole to maintain the blind.
Overall Study
STARTED
163
170
Overall Study
Received at Least 1 Dose of Study Drug
162
170
Overall Study
COMPLETED
128
135
Overall Study
NOT COMPLETED
35
35

Reasons for withdrawal

Reasons for withdrawal
Measure
Brexpiprazole
Brexpiprazole was administered orally with flexible dosing from 2 to 4 milligram (mg)/day; titrated to a maximum of 4 mg/day.
Placebo
Matching placebo was administered orally in the same way as brexpiprazole to maintain the blind.
Overall Study
Adverse Event
4
8
Overall Study
Lack of Efficacy
1
2
Overall Study
Non-compliance with Study Drug
0
2
Overall Study
Withdrawal by Subject
23
17
Overall Study
Physician Decision
3
1
Overall Study
Other
0
1
Overall Study
Lost to Follow-up
4
4

Baseline Characteristics

A Trial to Assess Brexpiprazole Versus Placebo for the Treatment of Acute Manic Episodes, Associated With Bipolar I Disorder

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Brexpiprazole
n=163 Participants
Brexpiprazole was administered orally with flexible dosing from 2 to 4 milligram (mg)/day; titrated to a maximum of 4 mg/day.
Placebo
n=170 Participants
Matching placebo was administered orally in the same way as brexpiprazole to maintain the blind.
Total
n=333 Participants
Total of all reporting groups
Age, Continuous
44.6 Years
STANDARD_DEVIATION 10.7 • n=5 Participants
44.3 Years
STANDARD_DEVIATION 12.0 • n=7 Participants
44.5 Years
STANDARD_DEVIATION 11.4 • n=5 Participants
Sex: Female, Male
Female
85 Participants
n=5 Participants
82 Participants
n=7 Participants
167 Participants
n=5 Participants
Sex: Female, Male
Male
78 Participants
n=5 Participants
88 Participants
n=7 Participants
166 Participants
n=5 Participants
Race/Ethnicity, Customized
White
90 Participants
n=5 Participants
102 Participants
n=7 Participants
192 Participants
n=5 Participants
Race/Ethnicity, Customized
Black or African American
70 Participants
n=5 Participants
67 Participants
n=7 Participants
137 Participants
n=5 Participants
Race/Ethnicity, Customized
American Indian or Alaska Native
1 Participants
n=5 Participants
0 Participants
n=7 Participants
1 Participants
n=5 Participants
Race/Ethnicity, Customized
Asian
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Race/Ethnicity, Customized
Native Hawaiian or Other Pacific Islander
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Race/Ethnicity, Customized
Other Race
2 Participants
n=5 Participants
1 Participants
n=7 Participants
3 Participants
n=5 Participants
Race/Ethnicity, Customized
Hispanic or Latino
22 Participants
n=5 Participants
17 Participants
n=7 Participants
39 Participants
n=5 Participants
Race/Ethnicity, Customized
Not Hispanic or Latino
140 Participants
n=5 Participants
153 Participants
n=7 Participants
293 Participants
n=5 Participants
Race/Ethnicity, Customized
Other Ethnicity
1 Participants
n=5 Participants
0 Participants
n=7 Participants
1 Participants
n=5 Participants

PRIMARY outcome

Timeframe: Baseline, Week 3

Population: Full Analysis Set: all participants who received at least 1 dose of study drug and had a baseline value and at least 1 valid post-randomization efficacy evaluation for YMRS Total Score in the double-blind treatment phase at the specified timepoint.

The YMRS was utilized to assess a participant's level of manic symptoms. It consists of 11 items: 1) elevated mood, 2) increased motor activity-energy, 3) sexual interest, 4) sleep, 5) irritability, 6) speech (rate and amount), 7) language-thought disorder, 8) content, 9) disruptive-aggressive behavior, 10) appearance, and 11) insight. Seven items are rated on a 0- to 4-scale, while four items (Items 5, 6, 8, and 9) are rated on a 0- to 8-scale with 0, 2, 4, 6, and 8 being the possible scores (twice the weight of the other items). For all items, 0 is the "best" rating and the highest score (4 or 8) is the 'worst' rating. The YMRS total score is the sum of ratings for all 11 items; therefore, possible total scores range from 0 to 60, with higher scores signifying more severe manic symptoms. Comparison between treatment groups was carried out using mixed-effect model repeated measure (MRMM).

Outcome measures

Outcome measures
Measure
Brexpiprazole
n=128 Participants
Brexpiprazole was administered orally with flexible dosing from 2 to 4 milligram (mg)/day; titrated to a maximum of 4 mg/day.
Placebo
n=133 Participants
Matching placebo was administered orally in the same way as brexpiprazole to maintain the blind.
Change From Baseline In Young-Mania Rating Scale (YMRS) Score At Week 3
-12.3 units on a scale
Standard Error 0.73
-10.7 units on a scale
Standard Error 0.71

SECONDARY outcome

Timeframe: Baseline, Week 3

Population: Full Analysis Set: all participants who received at least 1 dose of study drug and had a baseline value and at least 1 valid post-randomization efficacy evaluation for YMRS Total Score in the double-blind treatment phase at the specified timepoint.

The CGI-BP scale refers to the global impression of the participant with respect to bipolar disorder. The scale rates the participant's severity of illness (CGI-BP severity of illness: mania, depression, and overall bipolar illness) based on a 7-point scale: 1 = normal, not at all ill, 2 = minimally ill, 3 = mildly ill, 4 = moderately ill, 5 = markedly ill, 6 = severely ill, 7 = very severely ill.

Outcome measures

Outcome measures
Measure
Brexpiprazole
n=128 Participants
Brexpiprazole was administered orally with flexible dosing from 2 to 4 milligram (mg)/day; titrated to a maximum of 4 mg/day.
Placebo
n=133 Participants
Matching placebo was administered orally in the same way as brexpiprazole to maintain the blind.
Change From Baseline In Clinical Global Impression-Bipolar (CGI-BP) Severity Score In Mania At Week 3
-1.31 units on a scale
Standard Deviation 1.22
-1.06 units on a scale
Standard Deviation 1.09

Adverse Events

Brexpiprazole

Serious events: 0 serious events
Other events: 32 other events
Deaths: 0 deaths

Placebo

Serious events: 3 serious events
Other events: 28 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
Brexpiprazole
n=162 participants at risk
Brexpiprazole was administered orally with flexible dosing from 2 to 4 milligram (mg)/day; titrated to a maximum of 4 mg/day.
Placebo
n=170 participants at risk
Matching placebo was administered orally in the same way as brexpiprazole to maintain the blind.
Nervous system disorders
Epilepsy
0.00%
0/162 • From Day 1 (after dosing) through 6 weeks (3 weeks treatment, 3 weeks safety follow-up).
0.59%
1/170 • Number of events 1 • From Day 1 (after dosing) through 6 weeks (3 weeks treatment, 3 weeks safety follow-up).
Psychiatric disorders
Mania
0.00%
0/162 • From Day 1 (after dosing) through 6 weeks (3 weeks treatment, 3 weeks safety follow-up).
1.2%
2/170 • Number of events 2 • From Day 1 (after dosing) through 6 weeks (3 weeks treatment, 3 weeks safety follow-up).

Other adverse events

Other adverse events
Measure
Brexpiprazole
n=162 participants at risk
Brexpiprazole was administered orally with flexible dosing from 2 to 4 milligram (mg)/day; titrated to a maximum of 4 mg/day.
Placebo
n=170 participants at risk
Matching placebo was administered orally in the same way as brexpiprazole to maintain the blind.
Gastrointestinal disorders
Constipation
3.7%
6/162 • Number of events 6 • From Day 1 (after dosing) through 6 weeks (3 weeks treatment, 3 weeks safety follow-up).
2.9%
5/170 • Number of events 5 • From Day 1 (after dosing) through 6 weeks (3 weeks treatment, 3 weeks safety follow-up).
Gastrointestinal disorders
Nausea
1.2%
2/162 • Number of events 2 • From Day 1 (after dosing) through 6 weeks (3 weeks treatment, 3 weeks safety follow-up).
4.1%
7/170 • Number of events 8 • From Day 1 (after dosing) through 6 weeks (3 weeks treatment, 3 weeks safety follow-up).
Nervous system disorders
Akathisia
8.0%
13/162 • Number of events 14 • From Day 1 (after dosing) through 6 weeks (3 weeks treatment, 3 weeks safety follow-up).
2.4%
4/170 • Number of events 4 • From Day 1 (after dosing) through 6 weeks (3 weeks treatment, 3 weeks safety follow-up).
Nervous system disorders
Dizziness
3.1%
5/162 • Number of events 5 • From Day 1 (after dosing) through 6 weeks (3 weeks treatment, 3 weeks safety follow-up).
0.59%
1/170 • Number of events 1 • From Day 1 (after dosing) through 6 weeks (3 weeks treatment, 3 weeks safety follow-up).
Nervous system disorders
Headache
6.2%
10/162 • Number of events 12 • From Day 1 (after dosing) through 6 weeks (3 weeks treatment, 3 weeks safety follow-up).
10.6%
18/170 • Number of events 19 • From Day 1 (after dosing) through 6 weeks (3 weeks treatment, 3 weeks safety follow-up).
Psychiatric disorders
Insomnia
3.1%
5/162 • Number of events 6 • From Day 1 (after dosing) through 6 weeks (3 weeks treatment, 3 weeks safety follow-up).
1.2%
2/170 • Number of events 2 • From Day 1 (after dosing) through 6 weeks (3 weeks treatment, 3 weeks safety follow-up).

Additional Information

Global Clinical Development

Otsuka Pharmaceutical Development & Commercialization, Inc.

Phone: 1-609-524-6788

Results disclosure agreements

  • Principal investigator is a sponsor employee Sponsor reserves the right to review results publications prior to public release and can delay such publications for a period greater than 60 days but no more than 120 days from the date that the publication is submitted to the Sponsor for review. Sponsor can require changes to the publication to protect Sponsor's intellectual property rights and/or confidential information and reserves the right to limit publication timing and scope of data published based on the number of study locations.
  • Publication restrictions are in place

Restriction type: OTHER