Study of Cemiplimab in Adults With Cervical Cancer

NCT ID: NCT03257267

Last Updated: 2025-04-08

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

608 participants

Study Classification

INTERVENTIONAL

Study Start Date

2017-09-05

Study Completion Date

2023-04-20

Brief Summary

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The primary objective is to compare overall survival (OS) for patients with recurrent or metastatic cervical cancer who have histology of squamous cell carcinoma (SCC) and who have any eligible histology treated with either cemiplimab or investigator's choice (IC) chemotherapy.

The secondary objectives performed among SCC patients and among all eligible histologies (SCC and adenocarcinoma/adenosquamous carcinoma (AC) are:

* To compare progression-free survival (PFS) of cemiplimab versus IC chemotherapy
* To compare objective response rate (ORR) (partial response \[PR\] + complete response \[CR\]) of cemiplimab versus IC chemotherapy per Response Evaluation Criteria in Solid Tumors (RECIST) 1.1
* To compare the duration of response (DOR) of cemiplimab versus IC chemotherapy
* To compare the safety profiles of cemiplimab versus IC chemotherapy by describing adverse events (AE)
* To compare quality of life (QOL) for patients treated with cemiplimab versus IC chemotherapy using the European Organization for Research and Treatment of Cancer Quality of Life Questionnaire-Core 30 (EORTC QLQ-C30)

Detailed Description

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Conditions

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Squamous Cell Carcinoma (SCC) Recurrent or Metastatic, Platinum-refractory Cervical Cancer

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Experimental Therapy

Cemiplimab

Group Type EXPERIMENTAL

Cemiplimab

Intervention Type DRUG

Intravenous (IV) administration every 3 weeks (Q3W)

Control Therapy

Investigator choice (IC) chemotherapy

Group Type ACTIVE_COMPARATOR

Investigator Choice (IC) Chemotherapy

Intervention Type DRUG

IC chemotherapy options include:

1. Antifolate: Pemetrexed
2. Topoisomerase 1 inhibitor: Topotecan or Irinotecan
3. Nucleoside analogue: Gemcitabine
4. Vinca alkaloid: Vinorelbine

The only chemotherapy treatments allowed in the control arm are any of the 5 drugs that are listed as IC options above.

Interventions

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Cemiplimab

Intravenous (IV) administration every 3 weeks (Q3W)

Intervention Type DRUG

Investigator Choice (IC) Chemotherapy

IC chemotherapy options include:

1. Antifolate: Pemetrexed
2. Topoisomerase 1 inhibitor: Topotecan or Irinotecan
3. Nucleoside analogue: Gemcitabine
4. Vinca alkaloid: Vinorelbine

The only chemotherapy treatments allowed in the control arm are any of the 5 drugs that are listed as IC options above.

Intervention Type DRUG

Other Intervention Names

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REGN2810 Libtayo

Eligibility Criteria

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Inclusion Criteria

1. Recurrent, persistent, and/or metastatic cervical cancer with squamous cell histology, for which there is not a curative-intent option (surgery or radiation therapy with or without chemotherapy).

* Acceptable histologies (squamous carcinoma, adenocarcinoma, and adenosquamous carcinoma) as defined in the protocol
2. Tumor progression or recurrence after treatment with platinum therapy (must have been used to treat metastatic, persistent, or recurrent cervical cancer)
3. Patient must have measurable disease as defined by RECIST 1.1.
4. Eastern Cooperative Oncology Group (ECOG) performance status ≤1
5. ≥18 years old
6. Adequate organ or bone marrow function
7. Received prior bevacizumab therapy or had clinically documented reason why not administered
8. Received prior paclitaxel therapy or had clinically documented reason why not administered

Exclusion Criteria

1. Ongoing or recent (within 5 years) evidence of significant autoimmune disease that required treatment with systemic immunosuppressive treatments
2. Prior treatment with an agent that blocks the PD-1/PD-L1 pathway
3. Prior treatment with other systemic immune-modulating agents that was

1. within fewer than 4 weeks (28 days) of the enrollment date, or
2. associated with irAEs of any grade within 90 days prior to enrollment, or
3. associated with toxicity that resulted in discontinuation of the immune modulating agent
4. Active or untreated brain metastases
5. Immunosuppressive corticosteroid doses (\>10 mg prednisone daily or equivalent) within 4 weeks prior to the first dose of study drug cemiplimab or IC chemo)
6. Active infection requiring therapy
7. History of pneumonitis within the last 5 years
8. History of documented allergic reactions or acute hypersensitivity reaction attributed to antibody treatments
9. Concurrent malignancy other than cervical cancer and/or history of malignancy other than cervical cancer within 3 years of date of first planned dose of study drug cemiplimab or IC chemo), except for tumors with negligible risk of metastasis or death, such as adequately treated cutaneous squamous cell carcinoma or basal cell carcinoma of the skin or ductal carcinoma in situ of the breast. Patients with hematologic malignancies (eg, chronic lymphocytic leukemia) are excluded.

Note: Other protocol defined Inclusion/Exclusion apply
Minimum Eligible Age

18 Years

Eligible Sex

FEMALE

Accepts Healthy Volunteers

No

Sponsors

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Sanofi

INDUSTRY

Sponsor Role collaborator

Regeneron Pharmaceuticals

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Clinical Trial Management

Role: STUDY_DIRECTOR

Regeneron Pharmaceuticals

Locations

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Arizona Oncology Associates

Phoenix, Arizona, United States

Site Status

Arizona Oncology Associates

Tucson, Arizona, United States

Site Status

University of California Irvine

Orange, California, United States

Site Status

Ochsner Clinic Foundation

New Orleans, Louisiana, United States

Site Status

Cancer Research for the Ozarks

Springfield, Missouri, United States

Site Status

New York Presbyterian Queens

Flushing, New York, United States

Site Status

Northwell Health

Lake Success, New York, United States

Site Status

Laura and Issac Perlmutter Cancer Center at NYU Langone

New York, New York, United States

Site Status

First Health of the Carolinas Outpatient Cancer Center

Pinehurst, North Carolina, United States

Site Status

Thomas Jefferson University Hospital

Philadelphia, Pennsylvania, United States

Site Status

Texas Oncology, P.A.

Austin, Texas, United States

Site Status

St. George Hospital

Kogarah, New South Wales, Australia

Site Status

Northern NSW Health District, The Tweed Hospital

Tweed Heads, New South Wales, Australia

Site Status

Royal Brisbane & Women's Hospital

Herston, Queensland, Australia

Site Status

Peter MacCallum Cancer Centre

Melbourne, Victoria, Australia

Site Status

Sir Charles Gairdner Hospital

Nedlands, Western Australia, Australia

Site Status

St. John of God Subiaco Hospital

Subiaco, Western Australia, Australia

Site Status

OLV ziekenhuis Aalst, Medische oncologie- Radiotherapie

Aalst, , Belgium

Site Status

Institut Bordet

Brussels, , Belgium

Site Status

Cliniques universitaires Saint-Luc

Brussels, , Belgium

Site Status

UZLeuven Gynaelologic Oncology

Leuven, , Belgium

Site Status

CHC Saint Joseph

Liège, , Belgium

Site Status

CHU Liège

Liège, , Belgium

Site Status

CHU UCL Namur site Sainte Elisabeth

Namur, , Belgium

Site Status

Liga Norte Riograndense Contra o Câncer

Natal, Rio Grande do Norte, Brazil

Site Status

Hosptial Sao Lucas da PUC de Porto Alegre

Porto Alegre, Rio Grande do Sul, Brazil

Site Status

Irmandade da Santa Casa de Misericórdia de Porto Alegre

Porto Alegre, Rio Grande do Sul, Brazil

Site Status

Centro de Novos Tratamentos Itajai

Itajaí, Santa Catarina, Brazil

Site Status

Fundação Pio XII - Hospital de Câncer de Barretos

Barretos, São Paulo, Brazil

Site Status

Instituto de Pesquisas Clinicas para Estudos Multicentricos - IPCEM

Caxias do Sul, , Brazil

Site Status

Instituto Nacional de Cancer - INCA

Rio de Janeiro, , Brazil

Site Status

Instituto COI de Pesquisa

Rio de Janeiro, , Brazil

Site Status

Tom Baker Cancer Center

Calgary, Alberta, Canada

Site Status

British Columbia Cancer Agency

Vancouver, British Columbia, Canada

Site Status

London Health Sciences Centre

London, Ontario, Canada

Site Status

Princess Margaret Cancer Centre

Toronto, Ontario, Canada

Site Status

Hospital Maisonneuve-Rosemont

Montreal, Quebec, Canada

Site Status

Hopital Notre-Dame du Centre Hospitalier de l'Universite de Montreal

Montreal, Quebec, Canada

Site Status

Jewish General Hospital

Montreal, Quebec, Canada

Site Status

General Hospital of Athens Alexandra

Athens, , Greece

Site Status

University Hospital of Ioannina

Ioannina, , Greece

Site Status

General Hospital of Patras

Pátrai, , Greece

Site Status

Euromedica General Clinic, B'Oncology Clinic

Thessaloniki, , Greece

Site Status

Azienda Ospedaliero Universitaria di Bologna

Bologna, , Italy

Site Status

U.O Oncologia Medica P.O Vito Fazzi

Lecce, , Italy

Site Status

Asst Lecco

Lecco, , Italy

Site Status

Irst Irccs

Meldola, , Italy

Site Status

Istituto Europeo di Oncologia

Milan, , Italy

Site Status

AUSL, IRCCS di Reggio Emilia

Reggio Emilia, , Italy

Site Status

Fondazione Policlinico Agostino Gemelli IRCCS di Roma

Roma, , Italy

Site Status

Regina Elena National Cancer Institute

Rome, , Italy

Site Status

Shikoku Cancer Center

Matsuyama, Ehime, Japan

Site Status

Ehime University Hospital

Tōon, Ehime, Japan

Site Status

Fukui University Hospital

Yoshida-gun, Fukui, Japan

Site Status

Kurume University Hospital

Kurume, Fukuoka, Japan

Site Status

Hokkaido University Hospital

Sapporo, Hokkaido, Japan

Site Status

St. Marianna University School of Medicine Hospital

Kawasaki, Kanagawa, Japan

Site Status

University of the Ryukyus Hospital

Nakagami-gun, Okinawa, Japan

Site Status

Saitama Medical University

Saitama, Saitama, Japan

Site Status

National Cancer Center Hospital

Chuo-ku, Tokyo, Japan

Site Status

The Cancer Institute Hospital of JFCR

Koto-Ku, Tokyo, Japan

Site Status

Kyorin University Hospital

Mitaka, Tokyo, Japan

Site Status

Saitama Cancer Center

Saitama, Tokyo, Japan

Site Status

National Kyushu Cancer Center

Fukuoka, , Japan

Site Status

Kagoshima City Hospital

Kagoshima, , Japan

Site Status

Bialostockie Centrum Onkologii

Bialystok, , Poland

Site Status

Szpitale Pomorskie

Gdynia, , Poland

Site Status

Center and Institute of Oncology Gliwice

Gliwice, , Poland

Site Status

Centrum Onkologii Ziemi Lubelskiej im sw. Jana z Dukli

Lublin, , Poland

Site Status

Greater Poland Cancer Center

Poznan, , Poland

Site Status

Regional Budgetary Institution of Healthcare Ivanovo Regional Oncology Dispensary

Ivanovo, Ivanovo Oblast, Russia

Site Status

State Budgetary Healthcare Institution "Oncology Dispensary" of Ministry of Healthcare of the Kabardino-Balkarian Republic

Nal'chik, Kabardino-Balkarian, Russia

Site Status

A. Tsyb Medical Radiological Research Center

Obninsk, Kaluga Oblast, Russia

Site Status

State Budgetary Institution of Healthcare, Clinical Oncology Dispensary #1 of Ministry of Health of Krasnodar Region

Krasnodar, Krasnodar Territory, Russia

Site Status

State Budgetary Healthcare Institution Leningrad Regional Oncological Dispensary (SBHI "LROD")

Vsevolozhsk, Leningradskaya Oblast', Russia

Site Status

State Autonomous Healthcare Institution ,Republican Clinical Oncological Dispensary of the Ministry of Healthcare of the Tatarstan Republic

Kazan', Tatarstan Republic, Russia

Site Status

Budgetary Institution of Healthcare of Omsk region Clinical Oncology Dispensary

Omsk, , Russia

Site Status

State Budgetary Institution of Healthcare "Orenburg Regional Clinical Oncology Dispensary"

Orenburg, , Russia

Site Status

Saint- Petersburg State Budgetary institution of Healthcare "City Clinical Oncological Dispensary"

Saint Petersburg, , Russia

Site Status

National Cancer Center

Goyang-si, Gyeonggi-do, South Korea

Site Status

Keimyung University Dongsan Medical Center

Daegu, , South Korea

Site Status

Seoul National University Hospital

Seoul, , South Korea

Site Status

Asan Medical Center

Seoul, , South Korea

Site Status

Gangnam Severance Hospital

Seoul, , South Korea

Site Status

Korea University Guro Hospital

Seoul, , South Korea

Site Status

Hospital Universitario Son Espases

Palma de Mallorca, Balearic Islands, Spain

Site Status

Vall d´Hebron University Hospital

Barcelona, , Spain

Site Status

Hospital Reina Sofia

Córdoba, , Spain

Site Status

Instituto Catalan de Oncologia de Gerona

Girona, , Spain

Site Status

Hospital Ramon y Cajal

Madrid, , Spain

Site Status

Hospital Universitario HM Sanchinarro CIOCC

Madrid, , Spain

Site Status

Hospital Virgen de la Victoria

Málaga, , Spain

Site Status

Fundacion Instituto Valenciano de Oncologia

Valencia, , Spain

Site Status

Hospital Universitario La Fe

Valencia, , Spain

Site Status

Hospital Clinico Universitario Lozano Blesa

Zaragoza, , Spain

Site Status

Taichung Veterans General Hospital

Taichung, , Taiwan

Site Status

MacKay Memorial Hospital

Taipei, , Taiwan

Site Status

Koo-Foundation Sun Yat-Sen Cancer Center

Taipei, , Taiwan

Site Status

Taipei Veterans General Hospital

Taipei, , Taiwan

Site Status

Velindre Cancer Centre

Cardiff, , United Kingdom

Site Status

NHS Greater Glasgow and Clyde Beatson, West of Scotland Cancer care

Glasgow, , United Kingdom

Site Status

University College Hospital

London, , United Kingdom

Site Status

Royal Marsden NHS Foundation Trust, Chelsea

London, , United Kingdom

Site Status

Nottingham University Hospitals NHS Trust

Nottingham, , United Kingdom

Site Status

Royal Marsden NHS Foundation Trust, Sutton

Sutton, , United Kingdom

Site Status

Countries

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United States Australia Belgium Brazil Canada Greece Italy Japan Poland Russia South Korea Spain Taiwan United Kingdom

References

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Oaknin A, Monk BJ, Vergote I, Cristina de Melo A, Kim YM, Lisyanskaya AS, Samouelian V, Kim HS, Gotovkin EA, Damian F, Chang CL, Takahashi S, Li J, Mathias M, Fury MG, Ivanescu C, Reaney M, LaFontaine PR, Lowy I, Harnett J, Chen CI, Tewari KS. EMPOWER CERVICAL-1: Effects of cemiplimab versus chemotherapy on patient-reported quality of life, functioning and symptoms among women with recurrent cervical cancer. Eur J Cancer. 2022 Oct;174:299-309. doi: 10.1016/j.ejca.2022.03.016. Epub 2022 Jul 31.

Reference Type DERIVED
PMID: 35922251 (View on PubMed)

Tewari KS, Monk BJ, Vergote I, Miller A, de Melo AC, Kim HS, Kim YM, Lisyanskaya A, Samouelian V, Lorusso D, Damian F, Chang CL, Gotovkin EA, Takahashi S, Ramone D, Pikiel J, Mackowiak-Matejczyk B, Guerra Alia EM, Colombo N, Makarova Y, Rischin D, Lheureux S, Hasegawa K, Fujiwara K, Li J, Jamil S, Jankovic V, Chen CI, Seebach F, Weinreich DM, Yancopoulos GD, Lowy I, Mathias M, Fury MG, Oaknin A; Investigators for GOG Protocol 3016 and ENGOT Protocol En-Cx9. Survival with Cemiplimab in Recurrent Cervical Cancer. N Engl J Med. 2022 Feb 10;386(6):544-555. doi: 10.1056/NEJMoa2112187.

Reference Type DERIVED
PMID: 35139273 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Related Links

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https://www.trialsummaries.com/

A Plain Language Summary is available on TrialSummaries.com

Other Identifiers

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2017-000350-19

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

R2810-ONC-1676

Identifier Type: -

Identifier Source: org_study_id

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