Muscle Function and Its Biological and Physiological Determinants in Sickle Cell Disease

NCT ID: NCT03243812

Last Updated: 2025-12-19

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

NA

Total Enrollment

77 participants

Study Classification

INTERVENTIONAL

Study Start Date

2017-09-15

Study Completion Date

2019-12-13

Brief Summary

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Background : Sickle cell patients have profound remodeling of their muscle microcirculation networks with signs of amyotrophy. However, the consequences of these muscle alterations on the functional status of muscles are unknown. In addition, whether the poor physical fitness of sickle cell patients can be attributed, at least partly, to an hypothetical muscle dysfunction has never been tested.

Purpose : this study will compare the muscle function of legs between sickle cell patients (SS and SC genotypes) and healthy individuals (AA genotype) before, during and after a short localized muscle endurance exercise.

Abstract : Very recently, a study reported large differences between the muscle microcirculation networks of sickle cell patients compared to healthy individuals with decreased capillary density and higher proportion of large capillaries in the former population. In addition, the same study showed signs of amyotrophy in sickle cell patients. However, the muscle function of sickle cell patients has not been investigated and one may suggest that muscle dysfunction could participate in the decrease of physical fitness, in association with the hematological and hemorheological disorders, already reported in this population. The hypothesis is that muscle fatigue during a short localized muscle endurance exercise should be higher in sickle cell patients compared to healthy individuals, due to a greater recruitment of glycolytic fibers and a faster decrease of muscle oxygenation during exercise.

Detailed Description

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Conditions

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Sickle Cell Disease

Keywords

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Sickle Cell Disease Muscle function Hemorheological disorders

Study Design

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Allocation Method

NON_RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

BASIC_SCIENCE

Blinding Strategy

NONE

Study Groups

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SS genotype group

Sickle cell patients with SS genotype. Each subject will undergo the following :

1. Blood sample
2. Maximum Voluntary Contraction (MVC) test force before and after a localized muscle endurance test
3. Localized muscle endurance test: 4 series of 20 submaximal dynamic contractions at 50% of the MVC interspaced with 1 min recovery.
4. Self-paced six-minute walk test will be conducted according to the guidelines of the American Thoracic Society

Group Type ACTIVE_COMPARATOR

Blood sampling

Intervention Type BIOLOGICAL

Blood sampling will be performed to assess hematological and hemorheological parameters

Maximum Voluntary Contraction (MVC) test force

Intervention Type OTHER

Maximum Voluntary Contraction (MVC) test force will be performed before and after a localized muscle endurance test

Localized muscle endurance test

Intervention Type OTHER

Subject will perform 4 series of 20 submaximal dynamic contractions at 50% of the MVC interspaced with 1 min recovery.

Self-paced six-minute walk test

Intervention Type OTHER

Self-paced six-minute walk test will be conducted according to the guidelines of the American Thoracic Society

SC genotype group

Sickle cell patients with SC genotype. Each subject will undergo the following :

1. Blood sample
2. Maximum Voluntary Contraction (MVC) test force before and after a localized muscle endurance test
3. Localized muscle endurance test: 4 series of 20 submaximal dynamic contractions at 50% of the MVC interspaced with 1 min recovery.
4. Self-paced six-minute walk test will be conducted according to the guidelines of the American Thoracic Society

Group Type ACTIVE_COMPARATOR

Blood sampling

Intervention Type BIOLOGICAL

Blood sampling will be performed to assess hematological and hemorheological parameters

Maximum Voluntary Contraction (MVC) test force

Intervention Type OTHER

Maximum Voluntary Contraction (MVC) test force will be performed before and after a localized muscle endurance test

Localized muscle endurance test

Intervention Type OTHER

Subject will perform 4 series of 20 submaximal dynamic contractions at 50% of the MVC interspaced with 1 min recovery.

Self-paced six-minute walk test

Intervention Type OTHER

Self-paced six-minute walk test will be conducted according to the guidelines of the American Thoracic Society

control group

Healthy subjects. Each subject will undergo the following :

1. Blood sample
2. Maximum Voluntary Contraction (MVC) test force before and after a localized muscle endurance test
3. Localized muscle endurance test: 4 series of 20 submaximal dynamic contractions at 50% of the MVC interspaced with 1 min recovery.
4. Self-paced six-minute walk test will be conducted according to the guidelines of the American Thoracic Society

Group Type ACTIVE_COMPARATOR

Blood sampling

Intervention Type BIOLOGICAL

Blood sampling will be performed to assess hematological and hemorheological parameters

Maximum Voluntary Contraction (MVC) test force

Intervention Type OTHER

Maximum Voluntary Contraction (MVC) test force will be performed before and after a localized muscle endurance test

Localized muscle endurance test

Intervention Type OTHER

Subject will perform 4 series of 20 submaximal dynamic contractions at 50% of the MVC interspaced with 1 min recovery.

Self-paced six-minute walk test

Intervention Type OTHER

Self-paced six-minute walk test will be conducted according to the guidelines of the American Thoracic Society

Interventions

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Blood sampling

Blood sampling will be performed to assess hematological and hemorheological parameters

Intervention Type BIOLOGICAL

Maximum Voluntary Contraction (MVC) test force

Maximum Voluntary Contraction (MVC) test force will be performed before and after a localized muscle endurance test

Intervention Type OTHER

Localized muscle endurance test

Subject will perform 4 series of 20 submaximal dynamic contractions at 50% of the MVC interspaced with 1 min recovery.

Intervention Type OTHER

Self-paced six-minute walk test

Self-paced six-minute walk test will be conducted according to the guidelines of the American Thoracic Society

Intervention Type OTHER

Eligibility Criteria

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Inclusion Criteria

For Sickle cell patients :

* age ≥ 15 and \< 60 years old,
* SS homozygote or SC heterozygote
* in clinical steady state (i.e. without vaso-occlusive crisis or recent blood transfusion)
* identified by systematic neonatal screening programs,
* registered in the French medical social security national program

For Healthy and non sickle cell subjects:

* age ≥ 18 and \< 60 years old
* without cardiovascular/respiratory/muscle disease,
* registered in the French medical social security national program.

Exclusion Criteria

* other hemoglobinopathies,
* stroke or vasculopathy history,
* presence of leg ulcers or osteonecrosis,
* recent infectious episode (less than 1 month),
* chronic transfusion therapy programs,
* recent blood transfusion or phlebotomies (less than 3 months),
* patients not at steady state,
* pregnancy or breast feeding
Minimum Eligible Age

15 Years

Maximum Eligible Age

60 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

Yes

Sponsors

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Hospices Civils de Lyon

OTHER

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Giovanna CANNAS, MD

Role: PRINCIPAL_INVESTIGATOR

Hospices Civils de Lyon

Locations

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Hôpital Edouard Herriot

Lyon, , France

Site Status

Countries

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France

References

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Gouraud E, Connes P, Gauthier-Vasserot A, Faes C, Merazga S, Poutrel S, Renoux C, Boisson C, Joly P, Bertrand Y, Hot A, Cannas G, Hautier C. Is Skeletal Muscle Dysfunction a Limiting Factor of Exercise Functional Capacity in Patients with Sickle Cell Disease? J Clin Med. 2021 May 22;10(11):2250. doi: 10.3390/jcm10112250.

Reference Type RESULT
PMID: 34067352 (View on PubMed)

Other Identifiers

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69HCL17_0313

Identifier Type: -

Identifier Source: org_study_id