Assessment of INS1007 in Participants With Non-Cystic Fibrosis Bronchiectasis

NCT ID: NCT03218917

Last Updated: 2023-03-27

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

256 participants

Study Classification

INTERVENTIONAL

Study Start Date

2017-10-31

Study Completion Date

2019-12-12

Brief Summary

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The purpose of the study is to evaluate if INS1007 can reduce pulmonary exacerbations over a 24-week treatment period in participants with non-cystic fibrosis bronchiectasis.

Detailed Description

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Phase 2 randomized, double-blind, placebo-controlled, parallel-group, multicenter, multi-national study to assess the efficacy, safety and tolerability, and pharmacokinetics (PK) of INS1007 administered once daily for 24 weeks in participants with non-cystic fibrosis bronchiectasis (NCFBE).

Conditions

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Non-Cystic Fibrosis Bronchiectasis

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Brensocatib 10 mg

Participants received brensocatib 10 mg once daily (QD) before breakfast, for 24 weeks.

Group Type EXPERIMENTAL

Brensocatib 10 mg

Intervention Type DRUG

Administered once per day for 24 weeks

Brensocatib 25 mg

Participants received brensocatib 25 mg QD before breakfast, for 24 weeks.

Group Type EXPERIMENTAL

Brensocatib 25 mg

Intervention Type DRUG

Administered once per day for 24 weeks

Placebo

Participants received the matching placebo QD before breakfast, for 24 weeks.

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Administered once per day for 24 weeks

Interventions

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Brensocatib 10 mg

Administered once per day for 24 weeks

Intervention Type DRUG

Brensocatib 25 mg

Administered once per day for 24 weeks

Intervention Type DRUG

Placebo

Administered once per day for 24 weeks

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

1. Clinical history consistent with NCFBE (cough, chronic sputum production and/or recurrent respiratory infections)
2. Are current sputum producers with a history of chronic expectoration and able to provide a sputum sample during Screening
3. Have at least 2 documented pulmonary exacerbations in the past 12 months before Screening

Exclusion Criteria

1. Have a primary diagnosis of chronic obstructive pulmonary disease (COPD) or asthma
2. Have bronchiectasis due to cystic fibrosis (CF), hypogammaglobulinemia, common variable immunodeficiency, or alpha1-antitrypsin deficiency
3. Are current smokers
4. Are currently being treated for a nontuberculous mycobacterial lung infection, allergic bronchopulmonary aspergillosis, or tuberculosis
5. Have any acute infections, (including respiratory infections)
Minimum Eligible Age

18 Years

Maximum Eligible Age

85 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Insmed Incorporated

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Carlos Fernandez, MD

Role: STUDY_DIRECTOR

Insmed Incorporated

Locations

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University of Alabama at Birmingham

Birmingham, Alabama, United States

Site Status

Phoenix Medical Group

Peoria, Arizona, United States

Site Status

NewportNativeMD

Newport Beach, California, United States

Site Status

Palmtree Clinical Research

Palm Springs, California, United States

Site Status

UC Davis Medical Center

Sacramento, California, United States

Site Status

Stanford University Medical Center

Stanford, California, United States

Site Status

National Jewish Heath

Denver, Colorado, United States

Site Status

UConn Health Center

Farmington, Connecticut, United States

Site Status

MedStar Georgetown University Hospital

Washington D.C., District of Columbia, United States

Site Status

Clinical Research Specialists, LLC

Celebration, Florida, United States

Site Status

St. Francis Medical Institute

Clearwater, Florida, United States

Site Status

University of Florida

Gainesville, Florida, United States

Site Status

University of Miami Miller School of Medicine

Miami, Florida, United States

Site Status

San Marcus Research Clinic, Inc.

Miami Lakes, Florida, United States

Site Status

Sarasota Memorial Hospital Clinical Research Center

Sarasota, Florida, United States

Site Status

The Emory Clinic, Pulmonology

Atlanta, Georgia, United States

Site Status

University of Chicago

Chicago, Illinois, United States

Site Status

University of Iowa

Iowa City, Iowa, United States

Site Status

LSU Health Sciences Center

New Orleans, Louisiana, United States

Site Status

Johns Hopkins University, Division of Pulmonary and Critical Care Medicine

Baltimore, Maryland, United States

Site Status

Pulmonary and Critical Care Associates of Baltimore

Towson, Maryland, United States

Site Status

Mid Atlantic Pulmonary & Research Center

Westminster, Maryland, United States

Site Status

Michigan Medicine

Ann Arbor, Michigan, United States

Site Status

NYU Pulmonary & Critical Care Associates

New York, New York, United States

Site Status

Columbia University Medical Center/ New York Presbyterian Hospital

New York, New York, United States

Site Status

The University of North Carolina at Chapel Hill

Chapel Hill, North Carolina, United States

Site Status

Novant Health Pulmonary Medicine South

Charlotte, North Carolina, United States

Site Status

Southeastern Research Center

Winston-Salem, North Carolina, United States

Site Status

University Hospitals Cleveland Medical Center

Cleveland, Ohio, United States

Site Status

Cleveland Clinic

Cleveland, Ohio, United States

Site Status

Oregon Health & Science University

Portland, Oregon, United States

Site Status

University of Pennsylvania

Philadelphia, Pennsylvania, United States

Site Status

Temple University Hospital

Philadelphia, Pennsylvania, United States

Site Status

SMS Clinical Research, LLC

Mesquite, Texas, United States

Site Status

The University of Texas Health Science at Tyler

Tyler, Texas, United States

Site Status

MultiCare Institute for Research & Innovation

Tacoma, Washington, United States

Site Status

Concord Repatriation General Hospital

Concord, New South Wales, Australia

Site Status

Mater Misericordia Medical Centre

Brisbane, Queensland, Australia

Site Status

Gallipoli Medical Research Foundation

Brisbane, Queensland, Australia

Site Status

Metro North Hospital and Health Service (The Prince Charles Hospital)

Chermside, Queensland, Australia

Site Status

Respiratory Clinical Trials Unit, Royal Adelaide Hospital

Adelaide, South Australia, Australia

Site Status

Respiratory Clinical Trials PTY LTD

Kent Town, South Australia, Australia

Site Status

Box Hill Hospital, Eastern Clinical Research Unit

Box Hill, Victoria, Australia

Site Status

Alfred Hospital

Melbourne, Victoria, Australia

Site Status

Institute for Respiratory Health

Nedlands, Western Australia, Australia

Site Status

UZ Leuven

Leuven, Vlaams Brabant, Belgium

Site Status

Medical Center ReSpiro Ltd (Kiselov)

Razgrad, Momina, Bulgaria

Site Status

Medical Center UNIMED

Plovdiv, , Bulgaria

Site Status

MHAT "Dr IvanSeliminski"-Sliven

Sliven, , Bulgaria

Site Status

Cardioart Medical Center

Stara Zagora, , Bulgaria

Site Status

Hvidovre Hospital

Hvidovre, Capital Region, Denmark

Site Status

Aarhus University Hospital

Aarhus, , Denmark

Site Status

Sjællands Universitetshospital, Roskilde

Roskilde, , Denmark

Site Status

Krankenhaus Donaustauf

Donaustauf, Bavaria, Germany

Site Status

Klinikum der Universität München Medizinische Klinik V Pneumologie / Mukoviszidose-Zentrum für Erwachsene

Munich, Bavaria, Germany

Site Status

Klinikum Nuernberg

Nuremberg, Bavaria, Germany

Site Status

Universitätsklinikum Frankfurt

Frankfurt am Main, Hesse, Germany

Site Status

IKF Pneumologie Frankfurt

Frankfurt am Main, Hesse, Germany

Site Status

Ruhrlandklinik Essen, University Essen

Essen, North Rhine-Westphalia, Germany

Site Status

Forschungszentrum Borstel

Borstel, Schleswig-Holstein, Germany

Site Status

Universitätsklinikum Jena

Jena, Thuringia, Germany

Site Status

Research Center for Medical Studies (RCMS)

Berlin, , Germany

Site Status

Städt. Klinikum München GmbH, Bogenhausen

München, , Germany

Site Status

University of Milan, IRCCS Fondazione Ca' Granda Ospedale Maggiore Policlinico

Milan, Lombardy, Italy

Site Status

Ospedale San Gerardo

Monza, Monza E Brianza, Italy

Site Status

University Hospital of Pisa

Pisa, Via Paradisa 2, Italy

Site Status

Fondazione IRCCS Policlinico San Matteo

Pavia, , Italy

Site Status

ICS Maugeri spa SB, IRCSS Telese

Telese Terme, , Italy

Site Status

Noordwest Ziekenhuis Group

Alkmaar, , Netherlands

Site Status

Amphia Longresearch Astma/COPD Uni 52/5e etage

Breda, , Netherlands

Site Status

RadboudUMC, location Dekkerswald

Nijmegen, , Netherlands

Site Status

Zuyderland MC

Sittard, , Netherlands

Site Status

P3 Research

Tauranga, BOP, New Zealand

Site Status

P3 Research (Hawke's Bay)

Hastings, Hawkes Bay, New Zealand

Site Status

Southern District health Board/Dunedin Hospital

Dunedin, Otago, New Zealand

Site Status

Waikato District Health Board

Hamilton, Waikato Region, New Zealand

Site Status

Auckland District Health Board, Greenlane clinical Centre

Auckland, , New Zealand

Site Status

Centrum Badan Klinicznych, Piotr Napora Lekarze i Spolka Partnerska, Osrodek Badan Wczesnej Fazy

Wroclaw, Lower Silesian Voivodeship, Poland

Site Status

Grażyna Jasieniak Pinis Niepubliczny Zakład Opieki Zdrowotnej Atopia

Krakow, , Poland

Site Status

NZOZ Krak-Medyk Sp. z o.o

Krakow, , Poland

Site Status

Medical University of Lodz Poland

Lodz, , Poland

Site Status

Gabinet Lekarski Pediatryczno-Alergologiczny Zenon Bukowczan

Sucha Beskidzka, , Poland

Site Status

Singapore General Hospital

Singapore, , Singapore

Site Status

Changi General Hospital

Singapore, , Singapore

Site Status

Inha University Hospital

Incheon, Jung-gu, South Korea

Site Status

Gachon University Gil Medical Center

Incheon, Namdong-gu, South Korea

Site Status

Chonnam National University Hospital

Gwangju, , South Korea

Site Status

The Catholic University of Korea Incheon St. Mary's Hospital

Incheon, , South Korea

Site Status

The Catholic University of Korea, St. Paul's Hospital

Seoul, , South Korea

Site Status

Seoul National University Hospital

Seoul, , South Korea

Site Status

Konkuk University Medical Center

Seoul, , South Korea

Site Status

Asan Medical Center

Seoul, , South Korea

Site Status

The Catholic University of Korea, Seoul St. Mary's Hospital

Seoul, , South Korea

Site Status

Hospital Clinic de Barcelona

Barcelona, , Spain

Site Status

Hospital de la Santa Creu i Sant Pau

Barcelona, , Spain

Site Status

Hospital Universitari de Bellvitge

Barcelona, , Spain

Site Status

Hospital Universitari de Girona Dr. Josep Trueta

Girona, , Spain

Site Status

Hospital Universiatrio y politecnico La Fe

Valencia, , Spain

Site Status

NHS Tayside

Dundee, Angus, United Kingdom

Site Status

Papworth Hospital NHS Foundation Trust

Cambridge, Cambridgeshire, United Kingdom

Site Status

Blackpool Teaching Hospitals NHS Foundation Trust

Blackpool, Lancashire, United Kingdom

Site Status

Liverpool Heart and Chest Hospital NHS Foundation Trust

Liverpool, Merseyside, United Kingdom

Site Status

NHS Lothian

Edinburgh, Scotland, United Kingdom

Site Status

Ashford and St Peter's Hospitals NHS Foundation Trust

Chertsey, Surrey, United Kingdom

Site Status

The Royal Wolverhampton NHS Trust

Wolverhampton, West Midlands, United Kingdom

Site Status

Royal Brompton & Harefield NHS Foundation Trust

London, , United Kingdom

Site Status

Pennine Acute Hospitals NHS Trust

Manchester, , United Kingdom

Site Status

University Hospital Southampton NHS Foundation Trust

Southampton, , United Kingdom

Site Status

Countries

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United States Australia Belgium Bulgaria Denmark Germany Italy Netherlands New Zealand Poland Singapore South Korea Spain United Kingdom

References

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Johnson ED, Long MB, Perea L, Shih VH, Fernandez C, Teper A, Cipolla D, McIntosh E, Galloway R, Eke Z, Shuttleworth M, Hull R, Spinou A, De Soyza A, Ringshausen FC, Goeminne P, Lorent N, Haworth C, Loebinger MR, Blasi F, Shteinberg M, Aliberti S, Polverino E, Sibila O, Shoemark A, Mange K, Huang JTJ, Stobo J, Chalmers JD. Broad Immunomodulatory Effects of the Dipeptidyl-peptidase-1 Inhibitor Brensocatib in Bronchiectasis: Data from the Phase 2, Double-Blind, Placebo-controlled WILLOW Trial. Am J Respir Crit Care Med. 2025 Feb 12. doi: 10.1164/rccm.202408-1545OC. Online ahead of print.

Reference Type DERIVED
PMID: 39938076 (View on PubMed)

Basso J, Chen KJ, Zhou Y, Mark L, LaSala D, Dorfman A, Atalla M, Chun D, Viramontes V, Chang C, Leifer F, McDonald PP, Cipolla DC. The pharmacokinetic profile of brensocatib and its effect on pharmacodynamic biomarkers including NE, PR3, and CatG in various rodent species. Front Pharmacol. 2023 Jul 19;14:1208780. doi: 10.3389/fphar.2023.1208780. eCollection 2023.

Reference Type DERIVED
PMID: 37538173 (View on PubMed)

Cipolla D, Zhang J, Korkmaz B, Chalmers JD, Basso J, Lasala D, Fernandez C, Teper A, Mange KC, Perkins WR, Sullivan EJ. Dipeptidyl peptidase-1 inhibition with brensocatib reduces the activity of all major neutrophil serine proteases in patients with bronchiectasis: results from the WILLOW trial. Respir Res. 2023 May 17;24(1):133. doi: 10.1186/s12931-023-02444-z.

Reference Type DERIVED
PMID: 37198686 (View on PubMed)

Chalmers JD, Haworth CS, Metersky ML, Loebinger MR, Blasi F, Sibila O, O'Donnell AE, Sullivan EJ, Mange KC, Fernandez C, Zou J, Daley CL; WILLOW Investigators. Phase 2 Trial of the DPP-1 Inhibitor Brensocatib in Bronchiectasis. N Engl J Med. 2020 Nov 26;383(22):2127-2137. doi: 10.1056/NEJMoa2021713. Epub 2020 Sep 7.

Reference Type DERIVED
PMID: 32897034 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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2017-002533-32

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

INS1007-201

Identifier Type: -

Identifier Source: org_study_id

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