Study of Efficacy and Safety of QAW039 When Added to Standard-of-care Asthma Therapy in Patients With Uncontrolled Asthma

NCT ID: NCT03215758

Last Updated: 2026-01-13

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

675 participants

Study Classification

INTERVENTIONAL

Study Start Date

2017-11-01

Study Completion Date

2019-07-30

Brief Summary

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A randomized, multicenter, double-blind, placebo- controlled parallel-group study to determine the efficacy and safety of QAW039, compared with placebo, when added to standard-of-care (SoC) asthma therapy in adult and adolescent (≥ 12 years) patients with uncontrolled asthma with respect to change from baseline in forced expiratory volume in 1 second (FEV1) at the end of 12 weeks of treatment.

Detailed Description

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Conditions

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Asthma

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Investigators

Study Groups

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QAW039

QAW039 once daily

Group Type ACTIVE_COMPARATOR

QAW039

Intervention Type DRUG

QAW039 once daily

Placebo

Placebo once daily

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Placebo once daily

Interventions

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QAW039

QAW039 once daily

Intervention Type DRUG

Placebo

Placebo once daily

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* A diagnosis of asthma (according to GINA 2016) for a period of at least 6 months.
* Treated with medium dose inhaled corticosteroid (ICS), or high dose ICS, or low dose ICS plus long- acting beta agonist (LABA), or low dose ICS plus leukotriene receptor antagonist (LTRA), or medium dose ICS plus LABA for at least 3 months prior to Visit 1 and the doses have been stable for at least 4 weeks prior to Visit 1.
* FEV1 of ≤85% for patients aged ≥18 years. FEV1 of ≤90% for patients aged 12 to \<18 years.
* Daytime asthma symptom score (0 to 6 scale) of ≥1 per day during 4 of the last 7 days of the placebo run- in period.
* Total daily SABA use ≥1 puff per day during 4 of the last 7 days of the placebo run-in period.
* Demonstrated reversible airway obstruction.
* Asthma control questionnaire (ACQ) score ≥ 1.5.

Exclusion Criteria

* Use of other investigational drugs within 5 half-lives of enrollment, or within 30 days, whichever is longer.
* A resting QTcF (Fridericia) ≥450 msec (male) or

≥460 msec (female).
* Pregnant or nursing (lactating) women.
* Serious co-morbidities.
* Patients on \>20 mg of simvastatin, \> 40 mg of atorvastatin, \>40 mg of pravastatin, or \>2 mg of pitavastatin.
Minimum Eligible Age

12 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Novartis Pharmaceuticals

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Novartis Investigative Site

Flagstaff, Arizona, United States

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Phoenix, Arizona, United States

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Huntington Beach, California, United States

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Long Beach, California, United States

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Los Angeles, California, United States

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Mission Viejo, California, United States

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Mountain View, California, United States

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Orange, California, United States

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Roseville, California, United States

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Walnut Creek, California, United States

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Denver, Colorado, United States

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Tamarac, Florida, United States

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Winter Park, Florida, United States

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Albany, Georgia, United States

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Dacula, Georgia, United States

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Honolulu, Hawaii, United States

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Lihue, Hawaii, United States

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Overland Park, Kansas, United States

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Louisville, Kentucky, United States

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Columbia, Missouri, United States

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Rolla, Missouri, United States

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Missoula, Montana, United States

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Bellevue, Nebraska, United States

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La Vista, Nebraska, United States

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Skillman, New Jersey, United States

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Asheville, North Carolina, United States

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Gastonia, North Carolina, United States

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High Point, North Carolina, United States

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Cincinnati, Ohio, United States

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Edmond, Oklahoma, United States

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Eugene, Oregon, United States

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Medford, Oregon, United States

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Portland, Oregon, United States

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Portland, Oregon, United States

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Rapid City, South Dakota, United States

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Boerne, Texas, United States

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Dallas, Texas, United States

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El Paso, Texas, United States

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Fort Worth, Texas, United States

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McKinney, Texas, United States

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Seattle, Washington, United States

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Greenfield, Wisconsin, United States

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Berazategui, Buenos Aires, Argentina

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CABA, Buenos Aires, Argentina

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CABA, Buenos Aires, Argentina

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CABA, Buenos Aires, Argentina

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CABA, Buenos Aires, Argentina

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Lanús, Buenos Aires, Argentina

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Mar del Plata, Buenos Aires, Argentina

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Santa Rosa, La Pampa Province, Argentina

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Buenos Aires, Nueve De Julio, Argentina

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Santa Fe, Rosario, Argentina

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Rosario, Santa Fe Province, Argentina

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Rosario, Santa Fe Province, Argentina

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San Miguel de Tucumán, Tucumán Province, Argentina

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San Miguel de Tucumán, Tucumán Province, Argentina

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Buenos Aires, , Argentina

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Buenos Aires, , Argentina

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Córdoba, , Argentina

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Mendoza, , Argentina

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Mendoza, , Argentina

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Salta, , Argentina

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Peine, Lower Saxony, Germany

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Cottbus, Saxony, Germany

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Aschaffenburg, , Germany

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Bamberg, , Germany

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Berlin, , Germany

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Berlin, , Germany

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Fürstenwalde, , Germany

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Gauting, , Germany

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Leipzig, , Germany

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Lübeck, , Germany

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Prien A Chiemsee, , Germany

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Rudersdorf, , Germany

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Schleswig, , Germany

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Schwerin, , Germany

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Witten, , Germany

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Budaörs, HUN, Hungary

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Ajka, , Hungary

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Budapest, , Hungary

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Debrecen, , Hungary

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Gödöllő, , Hungary

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Szeged, , Hungary

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Culiacán, Sinaloa, Mexico

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Río de Janeiro, , Mexico

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Lipa City, Batangas, Philippines

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Quezon City, Manila, Philippines

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Iloilo City, , Philippines

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Manila, , Philippines

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Riyadh, SAU, Saudi Arabia

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Jeddah, , Saudi Arabia

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Bardejov, Slovak Republic, Slovakia

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Kežmarok, , Slovakia

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Michalovce, , Slovakia

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Poprad, , Slovakia

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Prešov, , Slovakia

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Spišská Nová Ves, , Slovakia

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Žilina, , Slovakia

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Tygerberg, Cape Town, South Africa

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Cape Town, , South Africa

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Chatsworth, , South Africa

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Durban, , South Africa

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Pretoria, , South Africa

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Istanbul, TUR, Turkey (Türkiye)

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Adana, , Turkey (Türkiye)

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Ankara, , Turkey (Türkiye)

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Istanbul, , Turkey (Türkiye)

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Mersin, , Turkey (Türkiye)

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Talas / Kayseri, , Turkey (Türkiye)

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Yenisehir/Izmir, , Turkey (Türkiye)

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Countries

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United States Argentina Germany Hungary Mexico Philippines Saudi Arabia Slovakia South Africa Turkey (Türkiye)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Related Links

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https://www.novctrd.com/ctrdweb/patientsummary/patientsummaries?patientSummaryId=593

A Plain Language Trial Summary is available on novartisclinicaltrials.com

https://www.novctrd.com/ctrdweb/ppatientsummary/ppatientsummaries?periodicPatientSummaryId=452

A Pediatric Plain Language Trial Summary is available on www.novctrd.com

Other Identifiers

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2017-001273-16

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

CQAW039A2316

Identifier Type: -

Identifier Source: org_study_id

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