Standard Chemotherapy vs Immunotherapie in 2nd Line Treatment of MSI Colorectal Mestastatic Cancer

NCT ID: NCT03186326

Last Updated: 2025-06-29

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

132 participants

Study Classification

INTERVENTIONAL

Study Start Date

2018-04-24

Study Completion Date

2025-03-01

Brief Summary

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Immune chekpoints (ICI) are evaluated in many digestive cancers. Certain types of cancer appear to be rather refractory to ICI such as colorectal cancers (CRC). However, the MSI CRC representing approximately 15% of the CRCs exhibits a high mutational load which generates many potentially immunogenic neoantigens. In addition, strong expression of PD-L1 was found in the MSI CRCs relative to the CRC (MSS) stages. Localized MSI CRCs have a better prognosis than MSS CRCs, probably due to immunogenic neoantigens associated with a CD8 + T-specific immune response. On the oher hand, in metastatic CRC (mCRC) things are different because i) the MSI frequency is only 4 to 7% and ii) the good prognosis conferred by the MSI status is controversial.

Preliminary results suggest that patients with MSI mCRC are highly sensitive to ICI even chemoresistant tumors receiving several lines of chemotherapy. Recently, another anti-PD1 alone or in combination with an anti-CTLA4 (antigen associated with cytotoxic T-lymphocyte 4) was tested in the MSI CRCs and a selection of interesting results in heavily pretreated patients with a disease control rate of 56% for monotherapy and 81% for combinated therapy.

Anti-PD1s now have marketing authorization for patients with melanoma and metastatic pulmonary carcinoma , Which are known to have a high level of mutations . ICIs appear to be as promising in MSI CRCs as in other tumors and therefore face the same major challenges.

Avalumab is an anti-PD-L1 antibody recently tested in several different types of tumors with promising results and is currently being studied in phase III in gastric cancer. There is no data on the effectiveness of this ICI in the MSI mCRCs. In addition, only anti-PD1 was used in the MSI-mCRC and not the anti-PD-L1, and only in chemoresistance (3rd line or more). The main objective of the SAMCO study is to test the efficacy and tolerance of avelumab in the 2nd line of treatment in patients with a MSI mCRC progression after standard 1st line chemotherapy +/- targeted therapy.

Detailed Description

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Conditions

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Metastatic Colorectal Cancer MSI

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Arm A Chemotherapy (standard treatment)

FOLFOX or FOLFIRI +/- targeted therapy

Group Type ACTIVE_COMPARATOR

FOLFOX regimen

Intervention Type DRUG

A course of treatment every 14 days

Oxaliplatin: 85 mg/m² IV over 2 hours Folinic acid: 400 mg/m² (or 200 mg/m² if Elvorine) IV over 2 hours 5FU bolus: 400 mg/m² IV bolus over 10 minutes in 100 ml 0.9% NaCl 5FU continuous: 2,400 mg/m² in NaCl 0.9% in IV over 46 hours

FOLFIRI Protocol

Intervention Type DRUG

A course of treatment every 14 days

Irinotecan: 180 mg/m² IV over 1H30 Folinic acid: 400 mg/m² (or 200 mg/m² if Elvorine) IV over 2 hours 5FU bolus: 400 mg/m² IV bolus over 10 minutes in 100 ml 0.9% NaCl 5FU continuous: 2,400 mg/m² in NaCl 0.9% in IV over 46 hours

Panitumumab

Intervention Type DRUG

Administered at 6 mg/Kg

Cetuximab

Intervention Type DRUG

Administered at 500 mg/m²

Bevacizumab

Intervention Type DRUG

Administered at 5 mg/Kg

Aflibercept

Intervention Type DRUG

Administered at 4 mg/Kg

Arm B - Immunotherapy (experimental arm)

Avelumab

Group Type EXPERIMENTAL

Avelumab

Intervention Type DRUG

A course of treatment every 14 days. Premedication obligatory with antihistamines and paracetamol (example: 25-50 mg diphenhydramine and 500-650 mg paracetamol) IV, approximately 30 to 60 minutes before each dose of avelumab.

Then:

Avelumab: 10 mg/kg IV in 1 hour diluted with 0.9% saline solution; alternatively a 0.45% saline solution can be used if needed

Interventions

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FOLFOX regimen

A course of treatment every 14 days

Oxaliplatin: 85 mg/m² IV over 2 hours Folinic acid: 400 mg/m² (or 200 mg/m² if Elvorine) IV over 2 hours 5FU bolus: 400 mg/m² IV bolus over 10 minutes in 100 ml 0.9% NaCl 5FU continuous: 2,400 mg/m² in NaCl 0.9% in IV over 46 hours

Intervention Type DRUG

FOLFIRI Protocol

A course of treatment every 14 days

Irinotecan: 180 mg/m² IV over 1H30 Folinic acid: 400 mg/m² (or 200 mg/m² if Elvorine) IV over 2 hours 5FU bolus: 400 mg/m² IV bolus over 10 minutes in 100 ml 0.9% NaCl 5FU continuous: 2,400 mg/m² in NaCl 0.9% in IV over 46 hours

Intervention Type DRUG

Avelumab

A course of treatment every 14 days. Premedication obligatory with antihistamines and paracetamol (example: 25-50 mg diphenhydramine and 500-650 mg paracetamol) IV, approximately 30 to 60 minutes before each dose of avelumab.

Then:

Avelumab: 10 mg/kg IV in 1 hour diluted with 0.9% saline solution; alternatively a 0.45% saline solution can be used if needed

Intervention Type DRUG

Panitumumab

Administered at 6 mg/Kg

Intervention Type DRUG

Cetuximab

Administered at 500 mg/m²

Intervention Type DRUG

Bevacizumab

Administered at 5 mg/Kg

Intervention Type DRUG

Aflibercept

Administered at 4 mg/Kg

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Histologically proven colorectal adenocarcinoma with metastasis(es) non-resectable
* MSI-H determined by immunohistochemistry (loss of expression of MLH1, MSH2, MSH6 and/or PMS2) or by molecular biology
* At least one measurable target (primary tumor or metastasis) according to RECIST v1.1
* Mutational status RAS and BRAF
* Age ≥ 18
* OMS ≤ 2
* Life expectancy \< 3 months
* Patient failure (progression or unacceptable toxicity) of chemotherapy containing fluoropyrimidine (capecitabine or 5FU) +/- irinotecan +/- oxaliplatin with or without cetuximab, bevacizumab and panitumumab (patients in progression during or within 3 months after discontinuation of adjuvant chemotherapy are eligible)
* PNN \> 1500/mm3, platelets \> 100 000/mm3, Hb \> 9 g/dL
* Total bilirubin \< 25 µmol/L, ASAT \< 5x LSN, ALAT \< 5 x LSN, PT \> 60%, , PAL\<2.5 x LSN ( \< 5 x LSN in case of hepatic metastasis)
* Creatinine clearance \> 50 ml/min according to MDRD formula (≥ 30 ml/min according to the Cockcroft-Gault formula)
* Patient belonging to a social security scheme
* Patient information and signature of the informed consent

Exclusion Criteria

* Patient immediately eligible for a curative therapy (surgical and/or percutaneous) after discussion in CPR
* Patient treated with FOLFIRINOX or FOLFOXIRI in 1st line
* Cerebral metastasis
* Previous treatment with anti-PD1 or anti-PDL1
* Autoimmune disease that might be aggravated during treatment with an immuno-stimulating agent (patients with type I diabetes, vitiligo, psoriasis, hypo- or hyperthyroid disease not requiring immunosuppressive treatment are eligible)
* Immunosuppressive long-term treatment (patients necessitating a corticotherapy are eligible if they are administered in doses \< or = to the equivalent of 10 mg of prednisone daily, administration of steroids by a route resulting in minimal systemic exposure (local, intra-anal, intraocular or inhalation) are eligible).
* Transplant patients (including stem cell transplants), HIV positive or other immune deficiency syndromes
* Active infection by HBV or HCV
* Known severe hypersensitivity to monoclonal antibodies or history of anaphylactic shock, or uncontrolled asthma
* Any known specific contraindication or allergy to the treatments used in the study
* Persistence of toxicities related to 1st line chemotherapy grade \> 2 (NCI-CTC v4.0) (except alopecia and neuropathy sequelae of oxaliplatin)
* Vaccination during the 4 weeks preceding the start of treatment
* Known deficit in DPD
* QT/QTc interval \> 450 msec for men and \> 470 msec for women
* K+ \< LIN, Mg2+ \< LIN, Ca2+ \< LIN
* Following alterations in the 6 months prior to inclusion: myocardial infarction, angina, severe/unstable angina, coronary artery bypass surgery, congestive heart failure NYHA class II, III or IV, stroke or transient ischemic attack
* Any progressive pathology not stabilised over the past 6 months: hepatic failure, renal failure, respiratory failure
* Patient with interstitial pneumonitis or pulmonary fibrosis
* History of chronic diarrhea or inflammatory disease of the colon or rectum, or unresolved occlusion or sub-occlusion in symptomatic treatment
* History of malignant pathologies during the past 5 years except basocellular skin carcinoma or in situ cervical carcinoma, properly treated
* Patient already included in another clinical trial during treatment with an experimental molecule for L2
* Lack of effective contraception in patients (men and/or women) of childbearing age, pregnant or breastfeeding women, women of childbearing age not having had a pregnancy test
* Persons deprived of liberty or under supervision
* Impossibility of undergoing medical monitoring during the trial for geographic, social or psychological reasons
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Federation Francophone de Cancerologie Digestive

OTHER

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Julien Taieb, Pr

Role: PRINCIPAL_INVESTIGATOR

HOPITAL EUROPEEN G. POMPIDOU

Locations

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Ch - Centre Hospitalier D'Abbeville

Abbeville, , France

Site Status

Ch - Centre Hospitalier Du Pays D'Aix

Aix-en-Provence, , France

Site Status

Chu - Hôpital Sud - Service D'Hge

Amiens, , France

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Privé - Clinique de L'Europe

Amiens, , France

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Cac - Ico Site Paul Papin

Angers, , France

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CHU - Hôtel Dieu

Angers, , France

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Privé - Hopital Privé D'Antony

Antony, , France

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Ch - Hôpital Victor Dupouy

Argenteuil, , France

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Ch - Centre Hospitalier Ardeche Meridionale

Aubenas, , France

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Ch - Ght Unyon Auxerre

Auxerre, , France

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Ch - Hôpital Henri Duffaut

Avignon, , France

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Privé - Institut Sainte Catherine

Avignon, , France

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Ch - Centre Hôspitalier Côte Basque

Bayonne, , France

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Ch - Centre Hospitalier de Beauvais

Beauvais, , France

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Chu - Jean Minjoz

Besançon, , France

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Privé - Centre de Radiotherapie Pierre Curie

Beuvry, , France

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Privé - Polyclinique Bordeaux Nord

Bordeaux, , France

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Privé - Cac Institut Bergionié

Bordeaux, , France

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Privé - Polyclinique Saint-Privat

Boujan-sur-Libron, , France

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Ch - Hôpital Duchenne

Boulogne-sur-Mer, , France

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Privé - Clinique Pasteur Lanroze Cfro

Brest, , France

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Privé - Centre Maurice Tubiana

Caen, , France

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Privé - Cac Centre Francois Baclesse

Caen, , France

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Privé - Infirmerie Protestante de Lyon

Caluire-et-Cuire, , France

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Ch - Centre Hospitalier de Carcassonne

Carcassonne, , France

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Chi - Centre Hospitalier de Castres Mazamet

Castres, , France

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Ch - Centre Hospitalier William Morey

Chalon-sur-Saône, , France

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Privé - Hopital Prive Sainte Marie

Chalon-sur-Saône, , France

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Ch - Centre Hospitalier Metropole Savoie

Chambéry, , France

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Ch - Centre Hospitalier de Charleville Mezieres

Charleville, , France

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Ch - Centre Hospitalier General

Châlons-en-Champagne, , France

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Ch - Centre Hospitalier de Châteauroux

Châteauroux, , France

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Ch - Centre Hospitalier de Cholet

Cholet, , France

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Ch - Hopitaux Civils de Colmar

Colmar, , France

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Privé - Clinique Saint Come

Compiègne, , France

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Ch - Centre Hospitalier Sud Francilien

Corbeil-Essonnes, , France

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Privé - Clinique Des Cèdres

Cornebarrieu, , France

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Privé - Clinique de Flandre

Coudekerque-Branche, , France

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Ch - Ghpso Site de Creil

Creil, , France

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Ch - Chic de Créteil

Créteil, , France

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Chu - Aphp - Hopital Henri Mondor

Créteil, , France

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Privé - Institut de Cancerologie de Bourgogne Grrecc

Dijon, , France

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Chu - Hopital Francois Mitterrand

Dijon, , France

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Privé - Cac- Centre Georges-Francois Leclerc

Dijon, , France

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Privé - Ghm Institut Daniel Hollard

Grenoble, , France

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Chu - Grenoble Alpes

Grenoble, , France

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Privé - Clinique Sainte Marguerite

Hyères, , France

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Ch - Centre Hospitalier Marne La Vallee-Jossigny

Jossigny, , France

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Chd - Centre Hospitalier Vendee

La Roche-sur-Yon, , France

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Privé - Clinique Du Cap D'Or

La Seyne-sur-Mer, , France

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Ch - Hopital Andre Mignot

Le Chesnay, , France

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Ch - Hopital Louis Pasteur - Oncologie Hematologie

Le Coudray, , France

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Privé - Cmc Les Ormeaux

Le Havre, , France

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Chu - Aphp - Hôpital de Bicêtre

Le Kremlin-Bicêtre, , France

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Ch - Centre Hospitalier Du Mans

Le Mans, , France

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Ch - Centre Hospitalier Docteur Schaffner

Lens, , France

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Ch - Hôpital Franco Britannique

Levallois-Perret, , France

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Privé - Cac - Centre Oscar Lambret

Lille, , France

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Chu - Dupuytren

Limoges, , France

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Ch - Gh Nord Essone

Longjumeau, , France

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Chu - Hôpital de La Croix Rousse

Lyon, , France

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Privé - Cac Centre Léon Berard

Lyon, , France

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Chu - Hôpital Edouard Herriot

Lyon, , France

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Privé - Cac Institut Paoli Calmettes

Marseille, , France

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Ch - Hôpital Saint Joseph

Marseille, , France

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Privé - Hôpital Européen Marseille

Marseille, , France

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Chu - La Timone

Marseille, , France

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Ch - Ghi de L'Est Francilien Site de Meaux

Meaux, , France

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Ch - Hôpital Belle Isle

Metz, , France

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Privé - Clinique Claude Bernard

Metz, , France

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Ch - Hôpital Layné

Mont-de-Marsan, , France

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Ch - Centre Hospitalier de Montceau Les Mines

Montceau-les-Mines, , France

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Ch - Centre Hospitalier de Montélimar

Montélimar, , France

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Ch - Groupe Hospitalier Intercommunal Le Raincy

Montfermeil, , France

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Privé - Centre de Cancérologie Du Grand Montpellier

Montpellier, , France

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Privé - Hôpital Prive Du Confluent Sas

Nantes, , France

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Privé - Cac - Centre Antoine Lacassagne

Nice, , France

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Chu - Hôpital Caremeau

Nîmes, , France

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Chr - Centre Hospitalier Régional de La Source

Orléans, , France

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Privé - Cac - Institut Curie

Paris, , France

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Chu - Hôpital Cochin

Paris, , France

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Chu - Hôpital Europeen Georges Pompidou

Paris, , France

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Chu - Aphp - Hôpital Saint Louis

Paris, , France

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Chu - Hôpital Saint Antoine

Paris, , France

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Chu - Aphp - Gh La Pitié Salpêtrière

Paris, , France

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Ch - Centre Hospitalier de Pau

Pau, , France

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Ch - Hôpital Saint Jean

Perpignan, , France

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Chu - Hôpital Haut Lévêque

Pessac, , France

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Privé - Polyclinique Francheville

Périgueux, , France

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Ch - Hôpital Lyon Sud

Pierre-Bénite, , France

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Privé - Centre Cario - Hcpa

Plérin, , France

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Chu - Hôpital de La Miletrie

Poitiers, , France

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Ch - Hôpital Rene Dubos

Pontoise, , France

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Ch - Hôpital Annecy Genevois

Pringy, , France

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Ch - Chic - Centre Hospitalier de Cornouaille

Quimper, , France

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Chu - Hôpital Robert Debre

Reims, , France

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Chu - Centre Hospitalier Universitaire Pontchaillou

Rennes, , France

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Privé - Centre de Radiotherapie Et D'Oncologie Médicale de L'Essone

Ris-Orangis, , France

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Privé - Clinique Pasteur

Ris-Orangis, , France

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Ch - Hôpitaux Drome Nord

Romans-sur-Isère, , France

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Chu - Hôpital Charles Nicolle

Rouen, , France

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Privé - Hôpital Privé Saint Gregoire

Saint-Grégoire, , France

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Privé - Clinique de L'Union

Saint-Jean, , France

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Privé - Cmco Côte D'Opale

Saint-Martin-Boulogne, , France

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Privé - Clinique Mutualiste de L'Estuaire - Cite Sanitaire

Saint-Nazaire, , France

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Chu - Hôpital Nord - Saint-Étienne

Saint-Priest-en-Jarez, , France

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Privé - Clinique Trenel

Sainte-Colombe, , France

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Ch - Centre Hospitalier de Soisson

Soissons, , France

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Ch - Centre Hospitalier de Saint-Malo

St-Malo, , France

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Privé - Cac - Institut de Cancérologie de Strasbourg Europe

Strasbourg, , France

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Privé - Clinique Sainte Anne

Strasbourg, , France

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Ch - Hopitaux Du Leman

Thonon-les-Bains, , France

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Ch - Hôpital Sainte Musse

Toulon, , France

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Chu - Hôpital Rangueil

Toulouse, , France

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Chu - Hôpital Trousseau

Tours, , France

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Chu - Hôpital Nancy-Brabois

Vandœuvre-lès-Nancy, , France

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Privé - Institut de Cancerologie de Lorraine

Vandœuvre-lès-Nancy, , France

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Chu - Aphp - Hôpital Paul Brousse

Villejuif, , France

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Privé - Cac - Gustave Roussy

Villejuif, , France

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Ch - Centre Hospitalier Intercommunal

Villeneuve-Saint-Georges, , France

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Countries

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France

References

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Taieb J, Andre T, El Hajbi F, Barbier E, Toullec C, Kim S, Bouche O, Di Fiore F, Chauvenet M, Perrier H, Evesque L, Laurent-Puig P, Emile JF, Bez J, Lepage C, Tougeron D. Avelumab versus standard second line treatment chemotherapy in metastatic colorectal cancer patients with microsatellite instability: The SAMCO-PRODIGE 54 randomised phase II trial. Dig Liver Dis. 2021 Mar;53(3):318-323. doi: 10.1016/j.dld.2020.11.031. Epub 2020 Dec 25.

Reference Type BACKGROUND
PMID: 33359404 (View on PubMed)

Taieb J, Sullo FG, Lecanu A, Bourreau C, Barbier E, Gandini A, Bez J, Mulot C, Di Fiore F, Elhajbi F, Borg C, Bouche O, Aparicio T, Zaanan A, Andre T, Tougeron D, Taly V, Laurent-Puig P. Early ctDNA and Survival in Metastatic Colorectal Cancer Treated With Immune Checkpoint Inhibitors: A Secondary Analysis of the SAMCO-PRODIGE 54 Randomized Clinical Trial. JAMA Oncol. 2025 Aug 1;11(8):874-882. doi: 10.1001/jamaoncol.2025.1646.

Reference Type DERIVED
PMID: 40531517 (View on PubMed)

Taieb J, Bouche O, Andre T, Le Malicot K, Laurent-Puig P, Bez J, Toullec C, Borg C, Randrian V, Evesque L, Corbinais S, Perrier H, Buecher B, Di Fiore F, Gallois C, Emile JF, Lepage C, Elhajbi F, Tougeron D; SAMCO-PRODIGE 54 Investigators. Avelumab vs Standard Second-Line Chemotherapy in Patients With Metastatic Colorectal Cancer and Microsatellite Instability: A Randomized Clinical Trial. JAMA Oncol. 2023 Oct 1;9(10):1356-1363. doi: 10.1001/jamaoncol.2023.2761.

Reference Type DERIVED
PMID: 37535388 (View on PubMed)

Other Identifiers

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PRODIGE 54 - FFCD 1603

Identifier Type: -

Identifier Source: org_study_id

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