Bezlotoxumab (MK-6072) Versus Placebo in Children With Clostridium Difficile Infection (CDI) (MK-6072-001)

NCT ID: NCT03182907

Last Updated: 2023-07-27

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

148 participants

Study Classification

INTERVENTIONAL

Study Start Date

2018-03-27

Study Completion Date

2022-05-12

Brief Summary

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The primary objectives of this study are to evaluate the pharmacokinetics (PK), safety, and tolerability of bezlotoxumab (MK-6072) in children aged 1 to \<18 years of age with a confirmed diagnosis of Clostridium difficile infection (CDI) who are receiving antibacterial drug treatment. The primary hypothesis is that the area under the concentration-time curve from 0 to infinity (AUC0-inf) of bezlotoxumab after treatment of pediatric participants with bezlotoxumab is similar when compared to the AUC0-inf of bezlotoxumab after treatment of adults with bezlotoxumab.

Detailed Description

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Historical adult pharmacokinetic data is from NCT01241552 and NCT01513239.

Conditions

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Clostridium Difficile Infection

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

PREVENTION

Blinding Strategy

TRIPLE

Participants Caregivers Investigators

Study Groups

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Bezlotoxumab

Participants receive 10 mg of bezlotoxumab per kg body weight via a single 60-minute (±10 minutes) intravenous (IV) infusion on Day 1. Additionally, participants receive background antibacterial drug treatment (ABD) for 10-21 days per institutional guidelines, at the investigator's discretion. Dose may then be changed based on results from initial 12 participants.

Group Type EXPERIMENTAL

Bezlotoxumab

Intervention Type BIOLOGICAL

A single intravenous (IV) infusion of 10 mg of bezlotoxumab per kg body weight. Dose may then be changed based on results from initial 12 participants.

Antibacterial drug treatment (ABD)

Intervention Type DRUG

ABD will be administered for 10-21 days including the duration of ABD prior to the screening visit, during the screening period, and after the infusion of study treatment, per institutional guidelines, at the investigator's discretion. ABD is defined as the receipt of oral metronidazole, oral vancomycin, intravenous (IV) metronidazole concurrent with oral vancomycin, oral fidaxomicin, or oral fidaxomicin concurrent with IV metronidazole.

Placebo

Participants receive placebo for bezlotoxumab consisting of either 0.9% sodium chloride or 5% dextrose via a single 60-minute (±10 minutes) IV infusion on Day 1. Additionally, participants receive background ABD for 10-21 days per institutional guidelines, at the investigator's discretion.

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

A single IV infusion of placebo for bezlotoxumab consisting of either 0.9% sodium chloride or 5% dextrose.

Antibacterial drug treatment (ABD)

Intervention Type DRUG

ABD will be administered for 10-21 days including the duration of ABD prior to the screening visit, during the screening period, and after the infusion of study treatment, per institutional guidelines, at the investigator's discretion. ABD is defined as the receipt of oral metronidazole, oral vancomycin, intravenous (IV) metronidazole concurrent with oral vancomycin, oral fidaxomicin, or oral fidaxomicin concurrent with IV metronidazole.

Interventions

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Bezlotoxumab

A single intravenous (IV) infusion of 10 mg of bezlotoxumab per kg body weight. Dose may then be changed based on results from initial 12 participants.

Intervention Type BIOLOGICAL

Placebo

A single IV infusion of placebo for bezlotoxumab consisting of either 0.9% sodium chloride or 5% dextrose.

Intervention Type DRUG

Antibacterial drug treatment (ABD)

ABD will be administered for 10-21 days including the duration of ABD prior to the screening visit, during the screening period, and after the infusion of study treatment, per institutional guidelines, at the investigator's discretion. ABD is defined as the receipt of oral metronidazole, oral vancomycin, intravenous (IV) metronidazole concurrent with oral vancomycin, oral fidaxomicin, or oral fidaxomicin concurrent with IV metronidazole.

Intervention Type DRUG

Other Intervention Names

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MK-6072

Eligibility Criteria

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Inclusion Criteria

* At screening has suspected or confirmed Clostridium difficile infection (CDI), and is receiving or is planning to receive a 10- to 21-day course of antibacterial drug treatment for CDI
* At study infusion has a diagnosis of CDI confirmed by a diagnostic assay which detects the presence of C. difficile toxin in stool, and is still receiving antibacterial drug treatment for CDI
* Female is not pregnant, and not breastfeeding; but if of childbearing potential agrees to follow contraceptive guidance during the treatment period and for at least 12 weeks after the last dose of study treatment
* Participant and/or parent or caregiver must be able to read, understand, and complete the daily diary

Exclusion Criteria

* Has an uncontrolled chronic diarrheal illness
* Has a known hypersensitivity to bezlotoxumab, its active substance and/or any of its excipients
* At randomization, their planned course of antibacterial drug treatment for CDI is longer than 21 days
* At screening has received any listed prohibited prior and concomitant treatments and procedures
* Has previously participated in this study, has previously received bezlotoxumab, has received an experimental monoclonal antibody against C. difficile toxin B, or has received a vaccine directed against C. difficile or its toxins.
* Has received an investigational study agent within the previous 30 days, or is currently participating in or scheduled to participate in any other clinical study with an investigational agent during the 12-week study period
Minimum Eligible Age

1 Year

Maximum Eligible Age

17 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Merck Sharp & Dohme LLC

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Medical Director

Role: STUDY_DIRECTOR

Merck Sharp & Dohme LLC

Locations

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Children's Hospital - Los Angeles ( Site 0021)

Los Angeles, California, United States

Site Status

UCSF Medical Center ( Site 0049)

San Francisco, California, United States

Site Status

Children's Hospital - Colorado ( Site 0013)

Aurora, Colorado, United States

Site Status

Children's Center for Digestive Healthcare ( Site 0052)

Atlanta, Georgia, United States

Site Status

University of Chicago ( Site 0019)

Chicago, Illinois, United States

Site Status

Our Lady of the Lake Hospital ( Site 0007)

Baton Rouge, Louisiana, United States

Site Status

The Johns Hopkins Rubenstein Child Health Building ( Site 0034)

Baltimore, Maryland, United States

Site Status

Tufts Medical Center-Floating Hospital for Children ( Site 0046)

Boston, Massachusetts, United States

Site Status

Mayo Clinic - Rochester ( Site 0004)

Rochester, Minnesota, United States

Site Status

Washington University ( Site 0037)

St Louis, Missouri, United States

Site Status

Columbia University Medical Center/ MSCHONY ( Site 0042)

New York, New York, United States

Site Status

SUNY Upstate Medical Center, University Hospital ( Site 0027)

Syracuse, New York, United States

Site Status

Montefiore Einstein Center ( Site 0041)

The Bronx, New York, United States

Site Status

Duke University Health System ( Site 0025)

Durham, North Carolina, United States

Site Status

Cincinnati Children's Hospital Medical Center ( Site 0024)

Cincinnati, Ohio, United States

Site Status

University Hospitals Cleveland Medical Center ( Site 0029)

Cleveland, Ohio, United States

Site Status

St. Jude Children's Research Hospital ( Site 0050)

Memphis, Tennessee, United States

Site Status

Vanderbilt University Medical Center ( Site 0022)

Nashville, Tennessee, United States

Site Status

The Children's Hospital of San Antonio ( Site 0009)

San Antonio, Texas, United States

Site Status

Primary Children's Hospital ( Site 0001)

Salt Lake City, Utah, United States

Site Status

Seattle Childrens Hospital ( Site 0028)

Seattle, Washington, United States

Site Status

Hospital Italiano de Buenos Aires. ( Site 2103)

Caba, Buenos Aires, Argentina

Site Status

Hospital Privado de Cordoba ( Site 2102)

Córdoba, , Argentina

Site Status

Santa Casa de Misericordia de Belo Horizonte ( Site 0208)

Belo Horizonte, Minas Gerais, Brazil

Site Status

Hospital de Clinicas da Universidade Federal do Parana ( Site 0203)

Curitiba, Paraná, Brazil

Site Status

Hospital Pequeno Principe ( Site 0200)

Curitiba, Paraná, Brazil

Site Status

Hospital Universitario da Universidade Federal de Santa Maria ( Site 0209)

Santa Maria, Rio Grande do Sul, Brazil

Site Status

Instituto de Oncologia Pediatrica - GRAACC - Unifesp ( Site 0205)

São Paulo, , Brazil

Site Status

Hospital Pablo Tobon Uribe-Infectology pediatric ( Site 2166)

Medellín, Antioquia, Colombia

Site Status

Fundacion Santa Fe de Bogota ( Site 2167)

Bogotá, Bogota D.C., Colombia

Site Status

Fundacion Cardioinfantil Instituto de Cardiologia ( Site 2163)

Bogotá, Bogota D.C., Colombia

Site Status

Fundacion Valle del Lili ( Site 2161)

Cali, Valle del Cauca Department, Colombia

Site Status

Centro Medico Imbanaco ( Site 2160)

Cali, Valle del Cauca Department, Colombia

Site Status

Fakultni Nemocnice Brno Bohunice ( Site 2000)

Brno, Brno-mesto, Czechia

Site Status

Fakultni nemocnice Plzen ( Site 2001)

Plzen Lochotin, Plzeň Region, Czechia

Site Status

2. LF UK a FN Motol ( Site 2003)

Prague, , Czechia

Site Status

Universitaetsklinikum Muenster ( Site 1400)

Münster, North Rhine-Westphalia, Germany

Site Status

Universitaetsklinikum Hamburg Eppendorf ( Site 1402)

Hamburg, , Germany

Site Status

SZTE Szent-Gyorgyi Albert Klinikai Kozpont ( Site 2200)

Szeged, Csongrád megye, Hungary

Site Status

Semmelweis University-II.sz. Gyermekgyógyászati Klinika ( Site 2201)

Budapest, , Hungary

Site Status

Del-pesti Centrumkorhaz Orszagos Hematologiai es Infektologiai Intezet ( Site 2202)

Budapest, , Hungary

Site Status

Sabah Womens & Childrens Hospital ( Site 3101)

Kota Kinabalu, Sabah, Malaysia

Site Status

Hospital Kuala Lumpur ( Site 3100)

Kuala Lumpur, , Malaysia

Site Status

Hospital Universitario "Dr. Jose Eleuterio Gonzalez" ( Site 0508)

Monterrey, Nuevo León, Mexico

Site Status

Instituto Tecnologico y de Estudios Superiores de Monterrey ( Site 0502)

Monterrey, Nuevo León, Mexico

Site Status

Instituto Nacional de Pediatria ( Site 0503)

Mexico City, , Mexico

Site Status

Hospital Infantil de Mexico Federico Gomez ( Site 0501)

Mexico City, , Mexico

Site Status

Haukeland universitetssykehus ( Site 1501)

Bergen, Vestfold, Norway

Site Status

Oslo universitetssykehus ( Site 1500)

Oslo, , Norway

Site Status

Wojewodzki Szpital Obserwacyjno Zakazny ( Site 2404)

Bydgoszcz, Kuyavian-Pomeranian Voivodeship, Poland

Site Status

Instytut Pomnik Centrum Zdrowia Dziecka ( Site 2406)

Warsaw, Masovian Voivodeship, Poland

Site Status

SPZOZ im. Dzieci Warszawy w Dziekanowie Lesnym ( Site 2405)

Łomianki, Masovian Voivodeship, Poland

Site Status

Wojewodzki Specjalistyczny Szpital Dzieciecy ( Site 2410)

Olsztyn, Warmian-Masurian Voivodeship, Poland

Site Status

Wojewodzki Specjalistyczny Szpital im. dr W. Bieganskiego w Lodzi ( Site 2400)

Lodz, Łódź Voivodeship, Poland

Site Status

Hospital de Braga ( Site 1600)

Braga, , Portugal

Site Status

Inst. Portugues de Oncologia de Lisboa Francisco Gentil EPE ( Site 1605)

Lisbon, , Portugal

Site Status

Centro Hospitalar de Lisboa Central EPE. Hospital D. Estefania ( Site 1601)

Lisbon, , Portugal

Site Status

Instituto Portugues de Oncologia Do Porto Francisco Gentil E.P.E. ( Site 1603)

Porto, , Portugal

Site Status

Spitalul Clinic de Boli Infectioase Cluj-Napoca ( Site 2502)

Cluj-Napoca, Cluj, Romania

Site Status

Institutul National de Boli Infectioase Prof. Dr. Matei Bals ( Site 2501)

Bucharest, , Romania

Site Status

Spitalul Clinic de Boli Infectioase si Tropicale Dr. Victor Babes ( Site 2500)

Bucharest, , Romania

Site Status

Spitalul Clinic de Boli Infectioase Constanta ( Site 2504)

Constanța, , Romania

Site Status

Phoenix Pharma Pty Ltd ( Site 2607)

Port Elizabeth, Eastern Cape, South Africa

Site Status

Johese Clinical Research ( Site 2605)

Centurion, Gauteng, South Africa

Site Status

Chris Hani Baragwanath Academic Hospital ( Site 2602)

Johannesburg, Gauteng, South Africa

Site Status

Molotlegi Street ( Site 2603)

Pretoria, Gauteng, South Africa

Site Status

Red Cross War Memorial Children's Hospital ( Site 2601)

Cape Town, Western Cape, South Africa

Site Status

Hospital Universitario Sant Joan de Deu ( Site 1704)

Esplugues de Llobregat, Barcelona, Spain

Site Status

Hospital Infantil Universitario Nino Jesus ( Site 1701)

Madrid, , Spain

Site Status

Hospital Universitario La Paz ( Site 1703)

Madrid, , Spain

Site Status

Hospital Universitario Virgen del Rocio ( Site 1705)

Seville, , Spain

Site Status

ITCC Barnokologen Astrid Lindgrens Barnsjukhus NKS ( Site 1800)

Stockholm, Stockholm County, Sweden

Site Status

Barncancercentrum ( Site 1801)

Gothenburg, Västra Götaland County, Sweden

Site Status

Southampton General Hospital ( Site 1900)

Southampton, Worcestershire, United Kingdom

Site Status

Leeds Teaching Hospitals NHS Trust ( Site 1901)

Leeds, , United Kingdom

Site Status

Countries

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United States Argentina Brazil Colombia Czechia Germany Hungary Malaysia Mexico Norway Poland Portugal Romania South Africa Spain Sweden United Kingdom

References

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Sferra TJ, Merta T, Neely M, Murta de Oliveira C, Lassaletta A, Fortuny Guasch C, Dorr MB, Winchell G, Su FH, Perko S, Fernsler D, Waskin H, Holden SR. Double-Blind, Placebo-Controlled Study of Bezlotoxumab in Children Receiving Antibacterial Treatment for Clostridioides difficile Infection (MODIFY III). J Pediatric Infect Dis Soc. 2023 Jun 30;12(6):334-341. doi: 10.1093/jpids/piad031.

Reference Type RESULT
PMID: 37389891 (View on PubMed)

Provided Documents

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Document Type: Study Protocol and Statistical Analysis Plan

View Document

Related Links

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https://merckclinicaltrials.com/

Merck Clinical Trial Information

Other Identifiers

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MK-6072-001

Identifier Type: OTHER

Identifier Source: secondary_id

2017-000070-11

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

6072-001

Identifier Type: -

Identifier Source: org_study_id

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