Safety, Efficacy and Pharmacokinetics of CF-301 vs. Placebo in Addition to Antibacterial Therapy for Treatment of S. Aureus Bacteremia

NCT ID: NCT03163446

Last Updated: 2021-10-08

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

121 participants

Study Classification

INTERVENTIONAL

Study Start Date

2017-05-23

Study Completion Date

2019-03-07

Brief Summary

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The purpose of this study is to evaluate the safety, tolerability, efficacy and pharmacokinetics (PK) of CF-301 in addition to background standard of care (SOC) antibacterial therapy for the treatment of Staphylococcus aureus (S. aureus) bloodstream infections (bacteremia), including endocarditis in adults. Patients will be randomized to receive a single intravenous dose of CF-301 or placebo in addition to SOC antibacterial therapy. Patients will be prescribed standard of care antibiotics selected by the investigators based on their professional experience, practice guidelines and local antibiotic susceptibility information for the treatment of S. aureus bacteremia.

CF-301 is a lysin and member of a new class of targeted protein-based antimicrobials that has demonstrated activity against S. aureus in laboratory (in vitro) and animal studies, alone and in addition to conventional antibiotics.

Detailed Description

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Conditions

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Staphylococcus Aureus Bacteremia Staphylococcus Aureus Endocarditis

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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CF-301

Patients will receive a single IV infusion of CF-301 in addition to standard of care (SOC) antibacterial therapy selected by the investigator.

Group Type EXPERIMENTAL

CF-301

Intervention Type BIOLOGICAL

CF-301, 0.25 mg/kg, given as a single 2 hour iv infusion

Placebo

Patients will receive a single IV infusion of placebo in addition to standard of care (SOC) antibacterial therapy selected by the investigator.

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Placebo, given as a single 2 hour iv infusion

Interventions

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CF-301

CF-301, 0.25 mg/kg, given as a single 2 hour iv infusion

Intervention Type BIOLOGICAL

Placebo

Placebo, given as a single 2 hour iv infusion

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* male or female, 18 years or older
* blood culture positive for S. aureus
* at least one sign or symptom attributable to S. aureus bacteremia
* known or suspected complicated S. aureus BSI and/or endocarditis by Modified Duke Criteria
* patient is not pregnant or breastfeeding and is not of reproductive potential or agrees to use contraception if of reproductive potential.

Exclusion Criteria

* patient previously received CF-301.
* treatment with any potentially effective (anti-staphylococcal) systemic antibiotic for more than 72 hours within 7 days before randomization.
* presence of any removable infection source that will not be removed or debrided within 72 hours after randomization.
* brain abscess or meningitis.
* community acquired pneumonia or known polymicrobial bacteremia
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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ContraFect

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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CF-301-102 Study Site

Birmingham, Alabama, United States

Site Status

CF-301-102 Study Site

Sacramento, California, United States

Site Status

CF301-102 Study Site

Sylmar, California, United States

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CF-301-102 Study Site

New Haven, Connecticut, United States

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CF-301-102 Study Site

Newark, Delaware, United States

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CF-301-102 Study Site

Atlanta, Georgia, United States

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CF-301-102 Study Site

Augusta, Georgia, United States

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CF0301-102 Study Site

Decatur, Georgia, United States

Site Status

CF-301 Study Site

Idaho Falls, Idaho, United States

Site Status

CF301-102 Study Site

Chicago, Illinois, United States

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CF301-102 Study Site

Burlington, Massachusetts, United States

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CF-301-102 Study Site

Detroit, Michigan, United States

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CF301-102 Study Site

Royal Oak, Michigan, United States

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CF301-102 Study Site

St Louis, Missouri, United States

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CF301-102 Study site

Butte, Montana, United States

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CF301-102 Study Site

Omaha, Nebraska, United States

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CF-301-102 Study Site

Omaha, Nebraska, United States

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CF-301-102 Study Site

Englewood, New Jersey, United States

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CF301-102 Study Site

Paterson, New Jersey, United States

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CF-301-102 Study Site

New York, New York, United States

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CF-301-102 Study Site

New York, New York, United States

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CF-301-102 Study Site

Valhalla, New York, United States

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CF-301-102 Study Site

Cleveland, Ohio, United States

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CF301-102 Study Site

Columbus, Ohio, United States

Site Status

Cf-301-102

Columbus, Ohio, United States

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CF-301 Study Site

Toledo, Ohio, United States

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CF-301-102 Study Site

Bethlehem, Pennsylvania, United States

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Cf-301-102

Richmond, Virginia, United States

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CF-301-102 Study Site

Roanoke, Virginia, United States

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CF-301-102 Study Site

Seattle, Washington, United States

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CF-301-102 Study Site

Milwaukee, Wisconsin, United States

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CF-301-102 Study Site #2

Brussels, , Belgium

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CF301-102 Study Site

Brussels, , Belgium

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CF301-102 Study Site

Edegem, , Belgium

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CF301-102 Study Site

Ghent, , Belgium

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Leuven, , Belgium

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Rousse, , Bulgaria

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Sofia, , Bulgaria

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CF-301-102 Study Site

Santiago, , Chile

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CF-301-102 Study Site

Viña del Mar, , Chile

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CF301-102 Study Site

Brno, , Czechia

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CF301-102 Study Site #2

Prague, , Czechia

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CF301-102 Study Site

Prague, , Czechia

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CF301-102 Study Site

Limoges, , France

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CF301-102 Study Site

Lyon, , France

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CF301-102 Study Site

Paris, , France

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CF301-102 Study Site

Toulon, , France

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CF-301-102 Study Site #2

Berlin, , Germany

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CF-301-102 Study Site

Berlin, , Germany

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CF-301-102 Study Site

Cologne, , Germany

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CF-301-102 Study Site

Freiburg im Breisgau, , Germany

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CF301-102 Study Site #3

Athens, , Greece

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CF301-102 Study Site

Athens, , Greece

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Study Site #2

Athens, , Greece

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CF301-102 Study Site

Larissa, , Greece

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CF-301-102 Study Site

Guatemala City, , Guatemala

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CF-301-102 Study Site

Santa Rosita, , Guatemala

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CF301-102 Study Site

Beersheba, , Israel

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CF301-102 Study Site

Nazareth, , Israel

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CF301-102 Study Site

Safed, , Israel

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CF301-102 Study Site

Tel Litwinsky, , Israel

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CF301-102 Study Site

Bergamo, , Italy

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CF-301-102 Study Site

Busto Arsizio, , Italy

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CF-301-102 Study Site

Genoa, , Italy

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CF-301-102 Study Site

Krasnodar, , Russia

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CF-301-102 Study Site

Moscow, , Russia

Site Status

CF-301-102 Study Site

Saint Pertersburg, , Russia

Site Status

CF-301-102 Study Site #2

Saint Petersburg, , Russia

Site Status

CF-301-102 Study Site #2

Barcelona, , Spain

Site Status

Cf301-102

Barcelona, , Spain

Site Status

CF301-102 Study Site

Córdoba, , Spain

Site Status

CF301-102 Study Site

Seville, , Spain

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CF301-102 Study Site

Terrassa, , Spain

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CF301-102 Study Site

Chelmsford, , United Kingdom

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CF301-102 Study Site

Liverpool, , United Kingdom

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CF-301-102 Study Site

London, , United Kingdom

Site Status

CF301-102 Study Site #2

London, , United Kingdom

Site Status

CF301-102 Study Site

Oxford, , United Kingdom

Site Status

Countries

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United States Belgium Bulgaria Chile Czechia France Germany Greece Guatemala Israel Italy Russia Spain United Kingdom

References

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Fowler VG Jr, Das AF, Lipka-Diamond J, Schuch R, Pomerantz R, Jauregui-Peredo L, Bressler A, Evans D, Moran GJ, Rupp ME, Wise R, Corey GR, Zervos M, Douglas PS, Cassino C. Exebacase for patients with Staphylococcus aureus bloodstream infection and endocarditis. J Clin Invest. 2020 Jul 1;130(7):3750-3760. doi: 10.1172/JCI136577.

Reference Type DERIVED
PMID: 32271718 (View on PubMed)

Provided Documents

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Document Type: Study Protocol and Statistical Analysis Plan

View Document

Other Identifiers

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CF-301-102

Identifier Type: -

Identifier Source: org_study_id

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