A Dose Finding Study to Assess the Effect of LIK066 Compared to Placebo or Empagliflozin in Patients With Type 2 Diabetes Mellitus and Heart Failure

NCT ID: NCT03152552

Last Updated: 2019-08-28

Study Results

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Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE2

Total Enrollment

125 participants

Study Classification

INTERVENTIONAL

Study Start Date

2017-07-25

Study Completion Date

2018-06-06

Brief Summary

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This was a dose-finding study to evaluate the efficacy, safety and tolerability of 3 different doses of LIK066 compared to placebo or empagliflozin in T2DM patients with heart failure

Detailed Description

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The study was prematurely discontinued on 04-May-2018 due to slow enrollment that would preclude obtaining study results in a timely manner.

Conditions

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Diabetes Mellitus and Heart Failure

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

TRIPLE

Participants Caregivers Investigators

Study Groups

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LIK066 2.5mg

Eligible participants randomized to this treatment arm received the LIK066 2.5mg dose regimen once daily for 36 weeks.

Group Type EXPERIMENTAL

LIK066

Intervention Type DRUG

LIK066 was supplied in different doses as tablets taken orally.

LIK066 10mg

Eligible participants randomized to this treatment arm received the LIK066 10mg dose regimen once daily for 36 weeks.

Group Type EXPERIMENTAL

LIK066

Intervention Type DRUG

LIK066 was supplied in different doses as tablets taken orally.

LIK066 50mg

Eligible participants randomized to this treatment arm received the LIK066 50mg dose regimen once daily for 36 weeks.

Group Type EXPERIMENTAL

LIK066

Intervention Type DRUG

LIK066 was supplied in different doses as tablets taken orally.

Empagliflozin

Participants randomized to this treatment arm received empagliflozin once daily for 36 weeks.

Group Type ACTIVE_COMPARATOR

Empagliflozin

Intervention Type DRUG

Empagliflozin was supplied as capsules taken orally.

Placebo

Participants randomized to this treatment arm received LIK066 matching placebo and empagliflozin matching placebo.

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Placebo was supplied as tablets and capsules taken orally.

Interventions

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LIK066

LIK066 was supplied in different doses as tablets taken orally.

Intervention Type DRUG

Placebo

Placebo was supplied as tablets and capsules taken orally.

Intervention Type DRUG

Empagliflozin

Empagliflozin was supplied as capsules taken orally.

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* BMI ≥ 22kg/m\^2
* Type 2 diabetes with HbA1c between 6.5% and 10.0%
* Documented symptomatic chronic heart failure (NYHA II-IV)
* Plasma NT-proBNP \> 300pg/ml
* eGFR ≥ 45ml/min/1.73m\^2 (calculated by MDRD)

Exclusion Criteria

* Pregnant or nursing (lactating) women
* Type 1 diabetes, monogenic diabetes, diabetes resulting from pancreatic injury, or secondary forms of diabetes
* History of ketoacidosis, lactic acidosis, or hyperosmolar coma
* Symptomatic genital infection or UTI within 4 weeks of screening
* Myocardial infarction, stroke, surgery for heart disease, percutaneous coronary intervention within 3 months of randomization
* Unstable angina within 3 months of screening
* Isolated right HF due to pulmonary disease
* Patients with a mean sitting systolic blood pressure ≤ 100mmHg, at randomization
* History of lower limb amputation
* Diabetic foot ulcer at screening
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Novartis Pharmaceuticals

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Novartis Pharmaceuticals

Role: STUDY_DIRECTOR

Novartis Pharmaceuticals

Locations

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Novartis Investigative Site

Bradenton, Florida, United States

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Huntsville, Alabama, United States

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Carmichael, California, United States

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Concord, California, United States

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Long Beach, California, United States

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Northridge, California, United States

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Stockton, California, United States

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Colorado Springs, Colorado, United States

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Clearwater, Florida, United States

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Delray Beach, Florida, United States

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Fort Lauderdale, Florida, United States

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Gurnee, Illinois, United States

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Bogalusa, Louisiana, United States

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Jackson, Mississippi, United States

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St Louis, Missouri, United States

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Omaha, Nebraska, United States

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Charleston, South Carolina, United States

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Columbia, South Carolina, United States

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San Antonio, Texas, United States

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Sugar Land, Texas, United States

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Tacoma, Washington, United States

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CABA, Buenos Aires, Argentina

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CABA, Buenos Aires, Argentina

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CABA, Buenos Aires F.D., Argentina

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Buenos Aires, , Argentina

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Graz, , Austria

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Vienna, , Austria

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Vienna, , Austria

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Lennik, Brussels Capital, Belgium

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Aalst, , Belgium

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Bonheiden, , Belgium

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Leuven, , Belgium

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Liège, , Belgium

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Sofia, , Bulgaria

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Sofia, , Bulgaria

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Sofia, , Bulgaria

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Sofia, , Bulgaria

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London, Ontario, Canada

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Toronto, Ontario, Canada

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Montreal, Quebec, Canada

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Québec, Quebec, Canada

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Saint-Jérôme, Quebec, Canada

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Sainte-Foy, Quebec, Canada

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Krapinske Toplice, , Croatia

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Rijeka, , Croatia

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Zagreb, , Croatia

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Brandýs nad Labem, Czech Republic, Czechia

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Svitavy, Czech Republic, Czechia

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Třebíč, Czech Republic, Czechia

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Fryštát, , Czechia

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Kolín, , Czechia

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Prague, , Czechia

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Prague, , Czechia

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Přerov, , Czechia

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Hellerup, , Denmark

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Svendborg, , Denmark

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Bad Oeynhausen, , Germany

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Berlin, , Germany

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Berlin, , Germany

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Berlin, , Germany

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Frankfurt, , Germany

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Halle, , Germany

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Hamburg, , Germany

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Stuttgart, , Germany

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Budapest, HUN, Hungary

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Budapest, , Hungary

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Szeged, , Hungary

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Szekszárd, , Hungary

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Wilton, Cork, Ireland

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County Limerick, , Ireland

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Dublin, , Ireland

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Bergamo, BG, Italy

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Milan, MI, Italy

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San Donato Milanese, MI, Italy

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Milan, , Italy

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Rimini, , Italy

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Durango, , Mexico

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Alkmaar, , Netherlands

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Groningen, , Netherlands

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Utrecht, , Netherlands

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Venlo, , Netherlands

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Loerenskog, , Norway

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Oslo, , Norway

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Trondheim, , Norway

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Warsaw, , Poland

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Wroclaw, , Poland

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Ponce, , Puerto Rico

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Singapore, , Singapore

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Bloemfontein, Free State, South Africa

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Paarl, Western Cape, South Africa

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Worcester, , South Africa

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Wŏnju, Gangwon-do, South Korea

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Bundang Gu, Gyeonggi-do, South Korea

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Cheongju-si, North Chungcheong, South Korea

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Seoul, , South Korea

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Seville, Andalusia, Spain

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Villamartín, Cadiz, Spain

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Cáceres, Extremadura, Spain

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Valencia, Valencia, Spain

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Changhua, , Taiwan

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Taichung, , Taiwan

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Taipei, , Taiwan

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Chelmsford, Essex, United Kingdom

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London, GBR, United Kingdom

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Sunderland, Tyne and Wear, United Kingdom

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Birmingham, , United Kingdom

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Countries

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United States Argentina Austria Belgium Bulgaria Canada Croatia Czechia Denmark Germany Hungary Ireland Italy Mexico Netherlands Norway Poland Puerto Rico Singapore South Africa South Korea Spain Taiwan United Kingdom

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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2016-003084-19

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

CLIK066B2204

Identifier Type: -

Identifier Source: org_study_id

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