A Study to Evaluate the Efficacy and Safety of Oxabact in Patients With Primary Hyperoxaluria

NCT ID: NCT03116685

Last Updated: 2021-12-10

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

25 participants

Study Classification

INTERVENTIONAL

Study Start Date

2018-01-09

Study Completion Date

2021-04-15

Brief Summary

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This study will evaluate the efficacy and safety of OC5 in patients with PH.

Detailed Description

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To evaluate the efficacy of Oxabact following 52 weeks treatment in subjects with maintained kidney function, but below the lower limit of the normal range (estimated glomerular filtration rate \[eGFR\] \< 90 ml/min/1.73 m2) and a total plasma oxalate (Pox) concentration ≥ 10 μmol/L. Parameters to be evaluated include the ability to stabilise/reduce Pox concentration, to stabilise/improve kidney function and to reduce oxalate deposits in primary hyperoxaluria (PH) subjects.

Conditions

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Primary Hyperoxaluria

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Oxabact OC5 capsules

Oxabact OC5 - Oxalobacter formigenes HC-1

Group Type EXPERIMENTAL

Oxabact OC5 - Oxalobacter formigenes HC-1

Intervention Type BIOLOGICAL

Active study drug

Placebo capsules

Placebo

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type OTHER

Placebo

Interventions

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Oxabact OC5 - Oxalobacter formigenes HC-1

Active study drug

Intervention Type BIOLOGICAL

Placebo

Placebo

Intervention Type OTHER

Eligibility Criteria

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Inclusion Criteria

1. Signed informed consent (as applicable for the age of the subject)
2. A diagnosis of PH (as determined by standard diagnostic methods).
3. eGFR \< 90 ml/min/1.73 m2. The Schwartz formula will be used to estimate GFR for children (age below 18), and CKD-EPI formula will be used for adults (age 18 or above).
4. Plasma oxalate concentration ≥10 μmol/L in total plasma oxalate.
5. Male or female patients ≥ 2 years of age.
6. Patients receiving vitamin B6 must be receiving a stable dose for at least 3 months prior to screening and must not change the dose during the study. Patients not receiving vitamin B6 at study entry must be willing to refrain from initiating pyridoxine during study participation.

Exclusion Criteria

1. Inability to swallow size 4 capsules.
2. Subjects that have undergone transplantation (solid organ or bone marrow).
3. Patients requiring dialysis or at immediate risk for kidney failure or expected to be in need of dialysis during the study period.
4. The existence of secondary hyperoxaluria, e.g. hyperoxaluria due to bariatric surgery or chronic gastrointestinal diseases such as cystic fibrosis, chronic inflammatory bowel disease and short-bowel syndrome.
5. Use of antibiotics to which O. formigenes is sensitive. (This includes current antibiotic use, or antibiotics use within 14 days of initiating study medication).
6. Current treatment with a separate ascorbic acid preparation.
7. Pregnant women (or women who are planning to become pregnant) or lactating women.
8. Women of childbearing potential who are not using adequate contraceptive precautions. Please see section 7.3 regarding requirements for contraception.
9. Presence of a medical condition that the Investigator considers likely to make the subject susceptible to adverse effect of study treatment or unable to follow study procedures or any condition that is likely to interfere with the study drug mechanism of action (such as abnormal GI function).
10. Participation in any interventional study of another investigational product, biologic, device, or other agent within 60 days prior to the first dose of OC5 or not willing to forego other forms of investigational treatment during this study.
Minimum Eligible Age

2 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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OxThera

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Gesa Schalk, MD

Role: PRINCIPAL_INVESTIGATOR

KindernierenZentrum, Bonn, Germany

Locations

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Vanderbilt University Hospital

Nashville, Tennessee, United States

Site Status

Centre Hospitalier Universitaire de Liège

Liège, , Belgium

Site Status

Hôpital Robert Debré

Paris, , France

Site Status

Kindernierenzentrum Bonn

Bonn, , Germany

Site Status

Hospital Vall d' Hebron

Barcelona, , Spain

Site Status

Hédi Chaker University Hospital

Sfax, , Tunisia

Site Status

Sahloul University Hospital

Sousse, , Tunisia

Site Status

Charles Nicolle University Hospital

Tunis, , Tunisia

Site Status

Royal Free Hospital

London, , United Kingdom

Site Status

Nottingham Children's Hospital

Nottingham, , United Kingdom

Site Status

Countries

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Netherlands United States Belgium France Germany Spain Tunisia United Kingdom

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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OC5-DB-02

Identifier Type: -

Identifier Source: org_study_id