Study to Assess Safety and Efficacy of Filgotinib, Lanraplenib and Tirabrutinib in Adults With Active Sjogren's Syndrome

NCT ID: NCT03100942

Last Updated: 2020-10-23

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

152 participants

Study Classification

INTERVENTIONAL

Study Start Date

2017-05-01

Study Completion Date

2019-10-02

Brief Summary

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The primary objective of this study is to assess the efficacy of filgotinib, lanraplenib, and tirabrutinib in adults with active Sjogren's Syndrome (SjS).

Detailed Description

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Conditions

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Sjogren's Syndrome

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Investigators

Study Groups

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Lanraplenib

Lanraplenib + filgotinib placebo + tirabrutinib placebo for up to 49.4 weeks.

Group Type EXPERIMENTAL

Lanraplenib

Intervention Type DRUG

1 x 30 mg tablet administered orally once daily

Filgotinib placebo

Intervention Type DRUG

1 x tablet administered orally once daily

Tirabrutinib placebo

Intervention Type DRUG

1 x tablet administered orally once daily

Filgotinib

Filgotinib + lanraplenib placebo + tirabrutinib placebo for up to 50.4 weeks.

Group Type EXPERIMENTAL

Filgotinib

Intervention Type DRUG

1 x 200 mg tablet administered orally once daily

Lanraplenib placebo

Intervention Type DRUG

1 x tablet administered orally once daily

Tirabrutinib placebo

Intervention Type DRUG

1 x tablet administered orally once daily

Tirabrutinib

Tirabrutinib + filgotinib placebo + lanraplenib placebo for up to 50.3 weeks.

Group Type EXPERIMENTAL

Tirabrutinib

Intervention Type DRUG

1 x 40 mg tablet administered orally once daily

Lanraplenib placebo

Intervention Type DRUG

1 x tablet administered orally once daily

Filgotinib placebo

Intervention Type DRUG

1 x tablet administered orally once daily

Placebo, then active treatment

Filgotinib placebo + lanraplenib placebo + tirabrutinib placebo for 24 weeks. Following completion of the Week 24 assessments and procedures, participants will be rerandomized 1:1:1, in a blinded fashion and receive either of the following study drugs through Week 48:

* filgotinib + lanraplenib placebo + tirabrutinib placebo
* lanraplenib + filgotinib placebo + tirabrutinib placebo
* tirabrutinib + filgotinib placebo + lanraplenib placebo

Group Type PLACEBO_COMPARATOR

Lanraplenib

Intervention Type DRUG

1 x 30 mg tablet administered orally once daily

Filgotinib

Intervention Type DRUG

1 x 200 mg tablet administered orally once daily

Tirabrutinib

Intervention Type DRUG

1 x 40 mg tablet administered orally once daily

Lanraplenib placebo

Intervention Type DRUG

1 x tablet administered orally once daily

Filgotinib placebo

Intervention Type DRUG

1 x tablet administered orally once daily

Tirabrutinib placebo

Intervention Type DRUG

1 x tablet administered orally once daily

Interventions

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Lanraplenib

1 x 30 mg tablet administered orally once daily

Intervention Type DRUG

Filgotinib

1 x 200 mg tablet administered orally once daily

Intervention Type DRUG

Tirabrutinib

1 x 40 mg tablet administered orally once daily

Intervention Type DRUG

Lanraplenib placebo

1 x tablet administered orally once daily

Intervention Type DRUG

Filgotinib placebo

1 x tablet administered orally once daily

Intervention Type DRUG

Tirabrutinib placebo

1 x tablet administered orally once daily

Intervention Type DRUG

Other Intervention Names

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GS-9876 GS-6034 GS-4059

Eligibility Criteria

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Inclusion Criteria

* Diagnosed with primary or secondary SjS according to the 2002 American European Consensus Group (AECG) classification
* Active SjS as defined by an European League Against Rheumatism (EULAR) Sjogren's syndrome disease activity index (ESSDAI) ≥ 5
* Seropositivity for antibodies to SjS-associated antigens A and/or B (anti-SSA or anti-SSB)

Exclusion Criteria

* Concurrent treatment with any biologic disease modifying antirheumatic drug (bDMARD) (prior bDMARD treatment allowed with appropriate washout as per study protocol)
Minimum Eligible Age

18 Years

Maximum Eligible Age

75 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Galapagos NV

INDUSTRY

Sponsor Role collaborator

Ono Pharmaceutical Co. Ltd

INDUSTRY

Sponsor Role collaborator

Gilead Sciences

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Gilead Study Director

Role: STUDY_DIRECTOR

Gilead Sciences

Locations

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AARR Arizona Arthritis & Rheumatology Research

Mesa, Arizona, United States

Site Status

AARR Arizona Arthritis & Rheumatology Research

Phoenix, Arizona, United States

Site Status

Medvin Clinical Research

Covina, California, United States

Site Status

Inland Rheumatology Clinical Trials, Inc.

Upland, California, United States

Site Status

Denver Arthritis Clinic

Denver, Colorado, United States

Site Status

Clinical Research of West Florida, Inc.

Clearwater, Florida, United States

Site Status

Omega Research Consultants LLC

DeBary, Florida, United States

Site Status

Center for Rheumatology Immunology and Arthritis

Fort Lauderdale, Florida, United States

Site Status

Suncoast Clinical Research, Inc.

New Port Richey, Florida, United States

Site Status

IRIS Research and Development, LLC

Plantation, Florida, United States

Site Status

North Georgia Rheumatology Group, PC

Lawrenceville, Georgia, United States

Site Status

Springfield Clinic

Springfield, Illinois, United States

Site Status

Center for Arthritis & Osteoporosis

Elizabethtown, Kentucky, United States

Site Status

June DO, PC

Lansing, Michigan, United States

Site Status

North Mississippi Medical Clinics, Inc. - Clinical Research

Tupelo, Mississippi, United States

Site Status

Clayton Medical Associates

St Louis, Missouri, United States

Site Status

Physician Research Collaboration, LLC

Lincoln, Nebraska, United States

Site Status

Albuquerque Clinical Trials

Albuquerque, New Mexico, United States

Site Status

Joint and Muscle Research Institute

Charlotte, North Carolina, United States

Site Status

Cape Fear Arthritis Care, PLLC

Leland, North Carolina, United States

Site Status

PMG Research of Salisbury

Salisbury, North Carolina, United States

Site Status

East Penn Rheumatology Associates, P.C.

Bethlehem, Pennsylvania, United States

Site Status

Altoona Center for Clinical Research

Duncansville, Pennsylvania, United States

Site Status

Clinical Research Center of Reading, LLC

Wyomissing, Pennsylvania, United States

Site Status

ClinSearch

Chattanooga, Tennessee, United States

Site Status

Ramesh C. Gupta, MD

Memphis, Tennessee, United States

Site Status

Diagnostic Group Integrated Healthcare System, Pllc

Beaumont, Texas, United States

Site Status

Accurate Clinical Research Inc.

Houston, Texas, United States

Site Status

Southwest Rheumatology Research

Mesquite, Texas, United States

Site Status

Trinity Universal Research Associates

Plano, Texas, United States

Site Status

Arthritis & Osteoporosis Clinic

Waco, Texas, United States

Site Status

Wasatch Peak Family Practice

Layton, Utah, United States

Site Status

The Center for Arthritis and Rheumatic Diseases, PC

Chesapeake, Virginia, United States

Site Status

Arthritis Northwest

Spokane, Washington, United States

Site Status

Centrum Kliniczno-Badawcze

Elblag, , Poland

Site Status

Intermedius

Kościan, , Poland

Site Status

Centrum Badan Klinicznych S.C

Poznan, , Poland

Site Status

Ai Centrum Medyczne

Poznan, , Poland

Site Status

Centrum Medyczne Amed Warszawa Targowek

Warsaw, , Poland

Site Status

Centrum Medyczne Oporow

Wroclaw, , Poland

Site Status

Hospital de la Santa Creu i Sant Pau

Barcelona, , Spain

Site Status

Hospital General Universitario De Elche

Elche, , Spain

Site Status

Hospital Universitario de Fuenlabrada

Fuenlabrada, , Spain

Site Status

Hospital Regional Universitario de Malaga

Málaga, , Spain

Site Status

Hospital De Merida

Mérida, , Spain

Site Status

Corporacio Sanitaria Parc Taulí de Sabadell

Sabadell, , Spain

Site Status

Hospital Clinico Universitario de Salamanca

San Vicente, , Spain

Site Status

Hospital Quironsalud Infanta Luisa

Seville, , Spain

Site Status

Doncaster Royal Infirmary

Doncaster, , United Kingdom

Site Status

Western General Hospital

Edinburgh, , United Kingdom

Site Status

Princess Alexandra Hospital

Harlow, , United Kingdom

Site Status

Great Western Hospital

Swindon, , United Kingdom

Site Status

Warrington Hospital

Warrington, , United Kingdom

Site Status

Countries

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United States Poland Spain United Kingdom

References

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Price E, Bombardieri M, Kivitz A, Matzkies F, Gurtovaya O, Pechonkina A, Jiang W, Downie B, Mathur A, Mozaffarian A, Mozaffarian N, Gottenberg JE. Safety and efficacy of filgotinib, lanraplenib and tirabrutinib in Sjogren's syndrome: a randomized, phase 2, double-blind, placebo-controlled study. Rheumatology (Oxford). 2022 Nov 28;61(12):4797-4808. doi: 10.1093/rheumatology/keac167.

Reference Type DERIVED
PMID: 35377447 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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2016-003558-34

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

GS-US-445-4189

Identifier Type: -

Identifier Source: org_study_id

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