Pharmacodynamic & Safety of Patiromer in Children & Adolescents (2-<18 Yrs) With Chronic Kidney Disease and Hyperkalemia

NCT ID: NCT03087058

Last Updated: 2022-10-19

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE2

Total Enrollment

23 participants

Study Classification

INTERVENTIONAL

Study Start Date

2017-07-07

Study Completion Date

2021-04-30

Brief Summary

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The purpose of this study is to evaluate the change in serum potassium levels from start of treatment to Day 14, when patiromer is administered at different doses, once daily, in children 2 - \< 18 years of age with chronic kidney disease (CKD) and hyperkalemia (too much potassium in the blood). Another purpose of the study is to evaluate the safety and tolerability of patiromer in children 2 - \< 18 years of age with CKD and hyperkalemia.

Detailed Description

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Up to 54 subjects, 2 - \< 18 years of age with CKD (estimated glomerular filtration rate \[eGFR\] \< 90 mL/min/1.73 m2 ) and hyperkalemia (two potassium measurements of 5.1 to \< 6.5 mEq/L performed on separate days) will be enrolled in this open-label, multiple-dose, Phase 2 study.

The study will include two treatment phases: Pharmacodynamic (PD; drug effect on potassium) / Dose Finding Phase consisting of the initial 14-day dose finding period followed by an up to 5.5-month Long-Term Treatment Phase for a total study participation duration for individual subjects of up to 6.5 months (includes a 2 week follow up period).

Conditions

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Hyperkalemia

Study Design

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Allocation Method

NON_RANDOMIZED

Intervention Model

SEQUENTIAL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Cohort 1

Patiromer for age 12 to \< 18 years

Group Type EXPERIMENTAL

Patiromer

Intervention Type DRUG

4.2 g/day, 8.4 g/day and 16.8 g/day

Cohort 2

Patiromer for age 6 to \< 12 years

Group Type EXPERIMENTAL

Patiromer

Intervention Type DRUG

2 g/day, 4 g/day and 8 g/day

Cohort 3

Patiromer for age 2 to \< 6 years

Group Type EXPERIMENTAL

Patiromer

Intervention Type DRUG

1 g/day, 2 g/day and 4 g/day

Interventions

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Patiromer

4.2 g/day, 8.4 g/day and 16.8 g/day

Intervention Type DRUG

Patiromer

2 g/day, 4 g/day and 8 g/day

Intervention Type DRUG

Patiromer

1 g/day, 2 g/day and 4 g/day

Intervention Type DRUG

Other Intervention Names

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Veltassa RLY5016 for Oral Suspension Veltassa RLY5016 for Oral Suspension Veltassa RLY5016 for Oral Suspension

Eligibility Criteria

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Inclusion Criteria

* Written assent (when applicable) and written informed consent by a legally authorized representative provided prior to participation in the study
* Age 2 - \<18 years old
* CKD defined by the estimated glomerular filtration rate (eGFR) \<90 mL/min/1.73m2, including renal transplant subjects, based on local creatinine measurement at screening
* Two potassium measurements of 5.1 to \< 6.5 mEq/L performed on separate days
* In the opinion of the study doctor, is expected to require treatment for hyperkalemia for at least 6 month
* If taking any renin-angiotensin-aldosterone system inhibitors (RAASi) beta blockers or diuretic medications, must be on a stable dose for at least 28 days prior to Screening
* Negative pregnancy test in females of child-bearing potential

Exclusion Criteria

* Pseudohyperkalemia due to hemolysis or to abnormally high numbers of platelets (\>500,000/mm3), leukocytes (\>70,000/mm3), or erythrocytes (hematocrit \>55%) at Screening based on results obtained locally
* Evidence of potassium-related electrocardiogram (ECG) changes at Screening
* Any of the following kidney conditions: maintenance hemodialysis or peritoneal dialysis, renal artery stenosis, and acute kidney injury or a history of acute renal insufficiency in the past 3 months
* Severe disorder of stomach or intestines including surgery that could affect gastrointestinal transit of the drug
* Increased liver enzymes (ALT, AST \> 3 times upper limit of normal) at Screening
* Active cancer, currently on cancer treatment or history of cancer in the past 2 years (except for non-melanoma skin cancer)
* Heart or liver transplant, or anticipated need for transplant during the study treatment period including a scheduled kidney transplant recipient. (Note: patients currently on a kidney transplant wait list are not excluded unless there is an identified donor).
* Alcohol abuse or substance use disorder within 1 year of Screening
* Subjects currently being treated with or having taken any one of the following medications (includes resins) in the 7 days prior to Screening: sodium or calcium polystyrene sulfonate, drospirenone
* Use of certain medications that can affect blood potassium levels if doses have not been stable for at least 14 days prior to Screening or if doses are anticipated to change during the 14-day PD / Dose Finding Phase
* Use of investigational product within 30 days of screening or within 5 half-lives, whichever is longer
* Known hypersensitivity to patiromer or its components
* In the opinion of the Investigator, any medical condition, uncontrolled systemic disease, or serious intercurrent illness that would significantly decrease study compliance or jeopardize the safety of the subject or potentially affect the quality of the data
Minimum Eligible Age

2 Years

Maximum Eligible Age

17 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Vifor Pharma, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Julian Platon, MD, PhD

Role: STUDY_DIRECTOR

Vifor Pharma, Inc.

Locations

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Investigator Site 1107

Palo Alto, California, United States

Site Status

Investigator Site 1101

Kansas City, Kansas, United States

Site Status

Investigator Site 1103

Baltimore, Maryland, United States

Site Status

Investigator Site 1102

The Bronx, New York, United States

Site Status

Investigator Site 1105

Cincinnati, Ohio, United States

Site Status

Investigator Site 1108

Pittsburgh, Pennsylvania, United States

Site Status

Investigator Site 1104

Amarillo, Texas, United States

Site Status

Investigator Site 1109

Dallas, Texas, United States

Site Status

Investigator Site 1113

Houston, Texas, United States

Site Status

Investigator Site 1106

Madison, Wisconsin, United States

Site Status

Investigator Site 1401

Sofia, , Bulgaria

Site Status

Investigator Site 1902

Vancouver, British Columbia, Canada

Site Status

Investigator Site 3915

Tbilisi, , Georgia

Site Status

Investigator Site 3913

Tbilisi, , Georgia

Site Status

Investigator Site 3911

Tbilisi, , Georgia

Site Status

Investigator Site 3912

Tbilisi, , Georgia

Site Status

Investigator Site 3914

Tbilisi, , Georgia

Site Status

Investiagor Site 4314

Cologne, , Germany

Site Status

Investigator Site 4312

Essen, , Germany

Site Status

Investigator Site 4313

Hanover, , Germany

Site Status

Investigator Site 4311

Heidelberg, , Germany

Site Status

Investigator Site 5401

Bialystok, , Poland

Site Status

Investigator Site 5404

Gdansk, , Poland

Site Status

Investigator Site 5406

Krakow, , Poland

Site Status

Investigator Site 5402

Lodz, , Poland

Site Status

Investigator Site 5403

Lublin, , Poland

Site Status

Investigator Site 5405

Warsaw, , Poland

Site Status

Investigator Site 7906

Dnipro, , Ukraine

Site Status

Investigator Site 7903

Kharkiv, , Ukraine

Site Status

Investigator Site 7904

Kyiv, , Ukraine

Site Status

Countries

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United States Bulgaria Canada Georgia Germany Poland Ukraine

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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2016-002785-31

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

RLY5016-206p

Identifier Type: -

Identifier Source: org_study_id

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