Trial Outcomes & Findings for Vitamin B12 for Aromatase Inhibitors Musculoskeletal Symptoms (NCT NCT03069313)

NCT ID: NCT03069313

Last Updated: 2018-02-01

Results Overview

The Brief Pain Inventory - Short Form (BPI- SF) average pain score used. This item has a scale of 0 to 10 with 0 indicating "No pain" and 10 indicating "Pain as bad as you can imagine" We expect at least 20% improvement in BPI-SF pain scores. Participants were asked to rate worst pain an average pain within the last 24 hours.

Recruitment status

COMPLETED

Study phase

NA

Target enrollment

41 participants

Primary outcome timeframe

Baseline and 90 days (+/- 10 days)

Results posted on

2018-02-01

Participant Flow

we needed at least a total of 30 patients to achieve more than 85% power to detect the differences in BPI-SF pain scores relative to baseline using a two tailed paired t-test with 5% level of significance. After accounting for 15% dropouts, we estimated to include at least 35 patients in the study.

IRB approved recruitment of 50 participants

Participant milestones

Participant milestones
Measure
Arm I
Oral Vitamin B12 Vitamin B12: Vitamin B12 2500 micrograms sublingually per day over the course of 90 days (+/- 10 days)
Overall Study
STARTED
41
Overall Study
COMPLETED
36
Overall Study
NOT COMPLETED
5

Reasons for withdrawal

Reasons for withdrawal
Measure
Arm I
Oral Vitamin B12 Vitamin B12: Vitamin B12 2500 micrograms sublingually per day over the course of 90 days (+/- 10 days)
Overall Study
Adverse Event
5

Baseline Characteristics

Vitamin B12 for Aromatase Inhibitors Musculoskeletal Symptoms

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Arm I
n=41 Participants
Oral Vitamin B12 Vitamin B12: Vitamin B12 2500 micrograms sublingually per day over the course of 90 days (+/- 10 days)
Age, Categorical
<=18 years
0 Participants
n=5 Participants
Age, Categorical
Between 18 and 65 years
41 Participants
n=5 Participants
Age, Categorical
>=65 years
0 Participants
n=5 Participants
Sex: Female, Male
Female
41 Participants
n=5 Participants
Sex: Female, Male
Male
0 Participants
n=5 Participants
Race (NIH/OMB)
American Indian or Alaska Native
0 Participants
n=5 Participants
Race (NIH/OMB)
Asian
0 Participants
n=5 Participants
Race (NIH/OMB)
Native Hawaiian or Other Pacific Islander
0 Participants
n=5 Participants
Race (NIH/OMB)
Black or African American
0 Participants
n=5 Participants
Race (NIH/OMB)
White
41 Participants
n=5 Participants
Race (NIH/OMB)
More than one race
0 Participants
n=5 Participants
Race (NIH/OMB)
Unknown or Not Reported
0 Participants
n=5 Participants
Region of Enrollment
United States
41 participants
n=5 Participants

PRIMARY outcome

Timeframe: Baseline and 90 days (+/- 10 days)

Population: A total of forty-one patients were enrolled, five patients withdrew, leaving thirty-six patients to complete the study.

The Brief Pain Inventory - Short Form (BPI- SF) average pain score used. This item has a scale of 0 to 10 with 0 indicating "No pain" and 10 indicating "Pain as bad as you can imagine" We expect at least 20% improvement in BPI-SF pain scores. Participants were asked to rate worst pain an average pain within the last 24 hours.

Outcome measures

Outcome measures
Measure
Arm I
n=36 Participants
Oral Vitamin B12 Vitamin B12: Vitamin B12 2500 micrograms sublingually per day over the course of 90 days (+/- 10 days)
Percentage Change in Average Joint Pain in Women With Aromatase Inhibitor-associated Musculoskeletal Symptoms (AIMSS) Compared to Baseline as Measured by the Brief Pain Inventory Short Form (BPI-SF).
-33.8 Percentage change
Standard Deviation 34.1

SECONDARY outcome

Timeframe: Baseline and 90 days (+/- 10 days)

Population: Postmenopausal women with ER+ breast cancer, stages I-III on aromatase inhibitors and musculoskeletal pain (average pain level \> or=4 using BPI-SF)

Analysis of the data collected at baseline and at the end of treatment in the BPI-SF questionnaire. The Brief Pain Inventory - Short Form (BPI- SF) worst pain score used. This item has a scale of 0 to 10 with 0 indicating "No pain" and 10 indicating "Pain as bad as you can imagine". Participants were asked to rate worst pain an average pain within the last 24 hours.

Outcome measures

Outcome measures
Measure
Arm I
n=36 Participants
Oral Vitamin B12 Vitamin B12: Vitamin B12 2500 micrograms sublingually per day over the course of 90 days (+/- 10 days)
Percentage Change in Worst Pain at the End of Treatment .
-23.03 Percentage change
Standard Deviation 43.1

SECONDARY outcome

Timeframe: Baseline and 90 days (+/- 10 days)

Population: postemneopausal women with ER + , Stages I-III breast cancer

All of the items in this questionnaire have a 5 scale rating, from not at all (0) to very much (4). Outcomes were measured pre and post treatment. Version 4 of the FACT-ES contains 3 subscales with seven questions: Physical Well-Being (PWB) (score range 0-28), Functional Well-Being (FWB) (score range 0-28), and Social and Well-Being (SWB) (score range 0-28); Emotional Well-Being (EWB) (score range 0-24) with six questions, and the Endocrine Symptom Subscale (ESS) (score range 0-76) containing 19 questions. For all subscale a higher score represents better quality of life.

Outcome measures

Outcome measures
Measure
Arm I
n=36 Participants
Oral Vitamin B12 Vitamin B12: Vitamin B12 2500 micrograms sublingually per day over the course of 90 days (+/- 10 days)
Percentage Change in Functional Quality of Life as Measured by the Functional Assessment of Cancer Therapy-Endocrine Scale (FACT-ES)
SWB
10.02 Percentage change
Standard Deviation 27.7
Percentage Change in Functional Quality of Life as Measured by the Functional Assessment of Cancer Therapy-Endocrine Scale (FACT-ES)
EWB
10.8 Percentage change
Standard Deviation 38.6
Percentage Change in Functional Quality of Life as Measured by the Functional Assessment of Cancer Therapy-Endocrine Scale (FACT-ES)
PWB
46.3 Percentage change
Standard Deviation 62.5
Percentage Change in Functional Quality of Life as Measured by the Functional Assessment of Cancer Therapy-Endocrine Scale (FACT-ES)
FWB
18 Percentage change
Standard Deviation 45
Percentage Change in Functional Quality of Life as Measured by the Functional Assessment of Cancer Therapy-Endocrine Scale (FACT-ES)
ESS
15.6 Percentage change
Standard Deviation 19.6

SECONDARY outcome

Timeframe: Baseline and at 90 days (+/- 10 days)

Population: postmenopasual women receiving AI

Inflammatory markers were measured pre and post treatment.

Outcome measures

Outcome measures
Measure
Arm I
n=36 Participants
Oral Vitamin B12 Vitamin B12: Vitamin B12 2500 micrograms sublingually per day over the course of 90 days (+/- 10 days)
Percentage Change of Serum Levels of Vitamin B12, C-reactive Protein (CRP), Homoscyteine (HCys) and Methylmalonic Acid (MMA).
B12
209.8 Percentage change
Standard Deviation 191.3
Percentage Change of Serum Levels of Vitamin B12, C-reactive Protein (CRP), Homoscyteine (HCys) and Methylmalonic Acid (MMA).
CRP
64.2 Percentage change
Standard Deviation 298.5
Percentage Change of Serum Levels of Vitamin B12, C-reactive Protein (CRP), Homoscyteine (HCys) and Methylmalonic Acid (MMA).
HCys
-24.6 Percentage change
Standard Deviation 19.75
Percentage Change of Serum Levels of Vitamin B12, C-reactive Protein (CRP), Homoscyteine (HCys) and Methylmalonic Acid (MMA).
MMA
-7.1 Percentage change
Standard Deviation 81.65

Adverse Events

Arm I

Serious events: 0 serious events
Other events: 14 other events
Deaths: 0 deaths

Serious adverse events

Adverse event data not reported

Other adverse events

Other adverse events
Measure
Arm I
n=36 participants at risk
Oral Vitamin B12 Vitamin B12: Vitamin B12 2500 micrograms sublingually per day over the course of 90 days (+/- 10 days)
Gastrointestinal disorders
dry mouth and nausea
38.9%
14/36 • Number of events 19 • 90 Days (+/- 10 days)
Eye disorders
blurred vision
2.8%
1/36 • Number of events 1 • 90 Days (+/- 10 days)

Additional Information

Zeina Nahleh, MD (previoulsy PI at Texas Tech university HSC-EP)

Cleveland Clinic Florida

Phone: 9546595840

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place