Trial Outcomes & Findings for Treatment of Hyperprolactinemia With the Non-ergoline Dopamine Agonist Ropinirole (NCT NCT03038308)

NCT ID: NCT03038308

Last Updated: 2024-06-04

Results Overview

Serum prolactin concentrations (PRL levels) were measured in patients at baseline, 2 and 4 weeks after starting therapy and then once monthly thereafter for 24 weeks. Serum prolactin was measured in duplicate by two-site chemiluminescent enzyme immunometric assay using the Immulite 1000 Analyzer (Siemens Healthcare Diagnostics, Deerfield, IL). The reference range for serum prolactin is 1.9-25 ng/ml for adult females.

Recruitment status

COMPLETED

Study phase

PHASE1/PHASE2

Target enrollment

16 participants

Primary outcome timeframe

6-12 months

Results posted on

2024-06-04

Participant Flow

1 Subject was determined to be ineligible after consenting.

Participant milestones

Participant milestones
Measure
ROP Intervention
Patients with hyperprolactinemia were treated with long-term ROP therapy for 6 months in an open-label dose escalation study Ropinirole: 0.25mg/day - 6.0mg/day oral non-ergoline dopamine agonist ropinirole
Overall Study
STARTED
15
Overall Study
COMPLETED
11
Overall Study
NOT COMPLETED
4

Reasons for withdrawal

Reasons for withdrawal
Measure
ROP Intervention
Patients with hyperprolactinemia were treated with long-term ROP therapy for 6 months in an open-label dose escalation study Ropinirole: 0.25mg/day - 6.0mg/day oral non-ergoline dopamine agonist ropinirole
Overall Study
Surgical resection
1
Overall Study
Withdrawal by Subject
2
Overall Study
Lost to Follow-up
1

Baseline Characteristics

Treatment of Hyperprolactinemia With the Non-ergoline Dopamine Agonist Ropinirole

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
ROP Intervention
n=16 Participants
Patients with hyperprolactinemia were treated with long-term ROP therapy for 6 months in an open-label dose escalation study Ropinirole: 0.25mg/day - 6.0mg/day oral non-ergoline dopamine agonist ropinirole
Age, Categorical
<=18 years
0 Participants
n=93 Participants
Age, Categorical
Between 18 and 65 years
15 Participants
n=93 Participants
Age, Categorical
>=65 years
1 Participants
n=93 Participants
Sex: Female, Male
Female
16 Participants
n=93 Participants
Sex: Female, Male
Male
0 Participants
n=93 Participants
Ethnicity (NIH/OMB)
Hispanic or Latino
3 Participants
n=93 Participants
Ethnicity (NIH/OMB)
Not Hispanic or Latino
13 Participants
n=93 Participants
Ethnicity (NIH/OMB)
Unknown or Not Reported
0 Participants
n=93 Participants
Race (NIH/OMB)
American Indian or Alaska Native
0 Participants
n=93 Participants
Race (NIH/OMB)
Asian
0 Participants
n=93 Participants
Race (NIH/OMB)
Native Hawaiian or Other Pacific Islander
0 Participants
n=93 Participants
Race (NIH/OMB)
Black or African American
6 Participants
n=93 Participants
Race (NIH/OMB)
White
10 Participants
n=93 Participants
Race (NIH/OMB)
More than one race
0 Participants
n=93 Participants
Race (NIH/OMB)
Unknown or Not Reported
0 Participants
n=93 Participants
Region of Enrollment
United States
16 participants
n=93 Participants
Prolactin
126 ng/mL
STANDARD_DEVIATION 41.4 • n=93 Participants

PRIMARY outcome

Timeframe: 6-12 months

Population: Of the 16 subjects enrolled, 1 was deemed ineligible after completion of screening, 2 relocated out of state prior to taking first dose, 1 was withdrawn after week 1 following decision to pursue surgical resection of the prolactinoma. 12 participated longitudinally -- 1 was lost to follow-up after 16 weeks; 11 subjects completed 24 weeks and 5/11 subjects continued ropinirole therapy for one year with 2/11 remaining in protocol for 17 months due pandemic related delays in final visits.

Serum prolactin concentrations (PRL levels) were measured in patients at baseline, 2 and 4 weeks after starting therapy and then once monthly thereafter for 24 weeks. Serum prolactin was measured in duplicate by two-site chemiluminescent enzyme immunometric assay using the Immulite 1000 Analyzer (Siemens Healthcare Diagnostics, Deerfield, IL). The reference range for serum prolactin is 1.9-25 ng/ml for adult females.

Outcome measures

Outcome measures
Measure
ROP Intervention
n=12 Participants
Patients with hyperprolactinemia were treated with long-term ROP therapy for 6 months in an open-label dose escalation study Ropinirole: 0.25mg/day - 6.0mg/day oral non-ergoline dopamine agonist ropinirole
Percentage of Subjects That Achieved PRL Normalization as Defined by a Serum Prolactin Level Less Than 25ng/mL at Any Time Point During the Study Treatment Period.
6 Participants

SECONDARY outcome

Timeframe: 6 months

Population: Nine participants analyzed as only 9 participants had a followup MRI at 6 months.

Number of subjects with stable or decreased tumor size from baseline assessment to assessment after 6 months of treatment. Radiologic assessment of tumor size before and after treatment will be made by MRI.

Outcome measures

Outcome measures
Measure
ROP Intervention
n=9 Participants
Patients with hyperprolactinemia were treated with long-term ROP therapy for 6 months in an open-label dose escalation study Ropinirole: 0.25mg/day - 6.0mg/day oral non-ergoline dopamine agonist ropinirole
Number of Subjects With Stable or Decreased Tumor Size
7 participants

Adverse Events

ROP Intervention

Serious events: 0 serious events
Other events: 8 other events
Deaths: 0 deaths

Serious adverse events

Adverse event data not reported

Other adverse events

Other adverse events
Measure
ROP Intervention
n=10 participants at risk
Patients with hyperprolactinemia were treated with long-term ROP therapy for 6 months in an open-label dose escalation study Ropinirole: 0.25mg/day - 6.0mg/day oral non-ergoline dopamine agonist ropinirole
General disorders
Fatigue
60.0%
6/10 • 6 months
General disorders
Nausea
40.0%
4/10 • 6 months
General disorders
Headache
20.0%
2/10 • 6 months

Additional Information

Gabrielle Page-Wilson, MD

Columbia University

Phone: 212-305-3725

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place