Study of Nivolumab in Combination With Ipilimumab or Standard of Care Chemotherapy Compared to the Standard of Care Chemotherapy Alone in Treatment of Participants With Untreated Inoperable or Metastatic Urothelial Cancer

NCT ID: NCT03036098

Last Updated: 2025-10-24

Study Results

Results available

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Basic Information

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Recruitment Status

ACTIVE_NOT_RECRUITING

Clinical Phase

PHASE3

Total Enrollment

1314 participants

Study Classification

INTERVENTIONAL

Study Start Date

2017-03-24

Study Completion Date

2026-02-19

Brief Summary

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The purpose of this study is to determine whether an investigational immunotherapy nivolumab in combination with ipilimumab or in combination with standard of care chemotherapy is more effective than standard of care chemotherapy alone in treating participants with previously untreated inoperable or metastatic urothelial cancer.

Detailed Description

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Conditions

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Urothelial Cancer

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Arm A: Investigational immunotherapy

Group Type EXPERIMENTAL

Nivolumab

Intervention Type BIOLOGICAL

Specified Dose on Specified Days

Ipilimumab

Intervention Type BIOLOGICAL

Specified Dose on Specified Days

Arm B: Standard of care chemotherapy

Group Type ACTIVE_COMPARATOR

Gemcitabine

Intervention Type DRUG

Specified Dose on Specified Days

Cisplatin

Intervention Type DRUG

Specified Dose on Specified Days

Carboplatin

Intervention Type DRUG

Specified Dose on Specified Days

Arm C: Investigational immunotherapy

Group Type EXPERIMENTAL

Nivolumab

Intervention Type BIOLOGICAL

Specified Dose on Specified Days

Gemcitabine

Intervention Type DRUG

Specified Dose on Specified Days

Cisplatin

Intervention Type DRUG

Specified Dose on Specified Days

Arm D: Standard of care chemotherapy

Group Type ACTIVE_COMPARATOR

Gemcitabine

Intervention Type DRUG

Specified Dose on Specified Days

Cisplatin

Intervention Type DRUG

Specified Dose on Specified Days

Interventions

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Nivolumab

Specified Dose on Specified Days

Intervention Type BIOLOGICAL

Ipilimumab

Specified Dose on Specified Days

Intervention Type BIOLOGICAL

Gemcitabine

Specified Dose on Specified Days

Intervention Type DRUG

Cisplatin

Specified Dose on Specified Days

Intervention Type DRUG

Carboplatin

Specified Dose on Specified Days

Intervention Type DRUG

Other Intervention Names

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BMS-936558 Opdivo BMS-734016 Yervoy

Eligibility Criteria

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Inclusion Criteria

* Histological or cytological evidence of metastatic or surgically inoperable transitional cell cancer (TCC) of the urothelium involving the renal pelvis, ureter, bladder or urethra
* No prior systemic chemotherapy for metastatic or surgically inoperable urothelial cancer (UC)
* Eastern Cooperative Oncology Group (ECOG) performance status (PS) 0 or 1
* Women and men must agree to follow specific methods of contraception, if applicable

Exclusion Criteria

* Disease that is suitable for local therapy administered with curative intent
* Any serious or uncontrolled medical disorder in the opinion of the investigator that may increase the risk associated with study participation or study drug administration or interfere with the interpretation of study results
* Prior treatment with an anti-PD-1, anti-PD-L1, anti-PD-L2, anti-CD137, or anti-CTLA-4 antibody, or any other antibody or drug specifically targeting T-cell co-stimulation or checkpoint pathways
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Ono Pharmaceutical Co. Ltd

INDUSTRY

Sponsor Role collaborator

Bristol-Myers Squibb

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Bristol-Myers Squibb

Role: STUDY_DIRECTOR

Bristol-Myers Squibb

Locations

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Local Institution - 0001

Anchorage, Alaska, United States

Site Status

Local Institution - 0115

Fresno, California, United States

Site Status

St Joseph Heritage Healthcare

Santa Rosa, California, United States

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Local Institution - 0051

Boca Raton, Florida, United States

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Local Institution - 0087

Fort Lauderdale, Florida, United States

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Local Institution - 0062

Jacksonville, Florida, United States

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Local Institution - 0004

Athens, Georgia, United States

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Local Institution - 0033

Thomasville, Georgia, United States

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Local Institution - 0046

Chicago, Illinois, United States

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Local Institution - 0117

New Orleans, Louisiana, United States

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Local Institution - 0056

Boston, Massachusetts, United States

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Local Institution - 0073

Boston, Massachusetts, United States

Site Status

Local Institution - 0208

Boston, Massachusetts, United States

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Local Institution - 0207

Milford, Massachusetts, United States

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Local Institution - 0063

Ann Arbor, Michigan, United States

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Local Institution - 0002

Burnsville, Minnesota, United States

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Hattiesburg Clinic

Hattiesburg, Mississippi, United States

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Local Institution - 0032

Kansas City, Missouri, United States

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Local Institution - 0095

St Louis, Missouri, United States

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Local Institution - 0057

Manchester, New Hampshire, United States

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Local Institution - 0084

Albuquerque, New Mexico, United States

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Local Institution - 0083

Buffalo, New York, United States

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Local Institution - 0014

Mineola, New York, United States

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Local Institution - 0072

New York, New York, United States

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Local Institution - 0116

Durham, North Carolina, United States

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Local Institution - 0082

Columbus, Ohio, United States

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Local Institution - 0104

Portland, Oregon, United States

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Local Institution - 0013

Pittsburgh, Pennsylvania, United States

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Local Institution - 0086

Kirkland, Washington, United States

Site Status

Local Institution - 0005

Capital Federal, Buenos Aires, Argentina

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Local Institution - 0007

Mar del Plata, Buenos Aires, Argentina

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Local Institution - 0009

Buenos Aires, , Argentina

Site Status

Local Institution - 0134

Córdoba, , Argentina

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Local Institution - 0006

Córdoba, , Argentina

Site Status

Local Institution - 0008

Viedma, , Argentina

Site Status

Local Institution - 0096

Waratah, New South Wales, Australia

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Local Institution - 0099

Westmead, New South Wales, Australia

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Local Institution - 0188

South Brisbane, Queensland, Australia

Site Status

Local Institution - 0120

Tugun, Queensland, Australia

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Local Institution - 0101

Heidelberg, Victoria, Australia

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Local Institution - 0100

Doubleview, Western Australia, Australia

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Local Institution - 0017

Brasília, Federal District, Brazil

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Local Institution - 0021

Ijuí, Rio Grande do Sul, Brazil

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Local Institution - 0119

Passo Fundo, Rio Grande do Sul, Brazil

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Local Institution - 0020

Porto Alegre, Rio Grande do Sul, Brazil

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Local Institution - 0016

Florianópolis, Santa Catarina, Brazil

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Local Institution - 0018

Barretos, São Paulo, Brazil

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Local Institution - 0019

São José do Rio Preto, São Paulo, Brazil

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Local Institution - 0053

Halifax, Nova Scotia, Canada

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Local Institution - 0064

London, Ontario, Canada

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Local Institution - 0054

Québec, Quebec, Canada

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Local Institution - 0052

Sherbrooke, Quebec, Canada

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Local Institution - 0012

Viña del Mar, Región de Valparaíso, Chile

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Local Institution - 0010

Santiago, Santiago Metropolitan, Chile

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Local Institution - 0106

Vitacura, , Chile

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Local Institution - 0171

Beijing, Beijing Municipality, China

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Local Institution - 0169

Beijing, Beijing Municipality, China

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Local Institution - 0182

Chongqing, Chongqing Municipality, China

Site Status

Local Institution - 0217

Guiyang, Guizhou, China

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Local Institution - 0219

Harbin, Heilongjiang, China

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Local Institution - 0180

Wuhan, Hubei, China

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Local Institution - 0175

Nanjing, Jiangsu, China

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Local Institution - 0177

Nanjing, Jiangsu, China

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Local Institution - 0176

Nanjing, Jiangsu, China

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Local Institution - 0186

Changchun, Jilin, China

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Local Institution - 0220

Taiyuan, Shan1xi, China

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Local Institution - 0216

Yantai, Shandong, China

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Local Institution - 0167

Shanghai, Shanghai Municipality, China

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Local Institution - 0162

Shanghai, Shanghai Municipality, China

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Local Institution - 0163

Shanghai, Shanghai Municipality, China

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Local Institution - 0184

Chengdu, Sichuan, China

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Local Institution - 0173

Hangzhou, Zhejiang, China

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Local Institution - 0174

Hangzhou, Zhejiang, China

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Local Institution - 0172

Hangzhou, Zhejiang, China

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Local Institution - 0170

Beijing, , China

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Local Institution - 0164

Shanghai, , China

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Local Institution - 0160

Brno, , Czechia

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Local Institution - 0152

Hradec Králové, , Czechia

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Local Institution - 0190

Aalborg, , Denmark

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Local Institution - 0196

Herlev, , Denmark

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Local Institution - 0060

Helsinki, , Finland

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Local Institution - 0091

Nîmes, Gard, France

Site Status

Local Institution - 0089

Lille, , France

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Local Institution - 0088

Marseille, , France

Site Status

Local Institution - 0090

Saint-Priest-en-Jarez, , France

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Local Institution - 0092

Suresnes, , France

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Local Institution - 0093

Tours, , France

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Local Institution - 0094

Villejuif, , France

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Local Institution - 0036

Dresden, , Germany

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Local Institution - 0048

Essen, , Germany

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Local Institution - 0047

Freiburg im Breisgau, , Germany

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Local Institution - 0049

Hamburg, , Germany

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Local Institution - 0037

Hanover, , Germany

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Local Institution - 0041

Jena, , Germany

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Local Institution - 0213

Mannheim, , Germany

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Local Institution - 0038

Nuremberg, , Germany

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Local Institution - 0040

Tübingen, , Germany

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Local Institution - 0114

Weiden, , Germany

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Local Institution - 0039

Würzburg, , Germany

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Local Institution - 0102

Athens, , Greece

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Local Institution - 0103

Ioannina, Ípeiros, Greece

Site Status

Local Institution - 0199

Kfar Saba, , Israel

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Local Institution - 0198

Ramat Gan, , Israel

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Local Institution - 0108

Arezzo, , Italy

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Local Institution - 0197

Faenza, , Italy

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Local Institution - 0111

Forlì, , Italy

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Local Institution - 0109

Grosseto, , Italy

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Local Institution - 0107

Milan, , Italy

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Local Institution - 0110

Napoli, , Italy

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Local Institution - 0136

Hirosaki, Aomori, Japan

Site Status

Local Institution - 0135

Chiba, Chiba, Japan

Site Status

Local Institution - 0147

Matsuyama, Ehime, Japan

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Local Institution - 0140

Fukuoka, Fukuoka, Japan

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Local Institution - 0146

Sapporo, Hokkaido, Japan

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Local Institution - 0150

Tsukuba, Ibaraki, Japan

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Local Institution - 0214

Morioka, Iwate, Japan

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Local Institution - 0137

Kita-Gun, Kagawa-ken, Japan

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Local Institution - 0141

Niigata, Niigata, Japan

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Local Institution - 0143

Okayama, Okayama-ken, Japan

Site Status

Local Institution - 0144

Osaka, Osaka, Japan

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Local Institution - 0139

Sayama, Osaka, Japan

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Local Institution - 0145

Takatsuki-shi, Osaka, Japan

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Local Institution - 0201

Hamamatasu, Shizuoka, Japan

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Local Institution - 0149

Adachi-ku, Tokyo, Japan

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Local Institution - 0148

Bunkyo-ku, Tokyo, Japan

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Local Institution - 0142

Bunkyo-ku, Tokyo, Japan

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Local Institution - 0138

Shinjuku-Ku, Tokyo, Japan

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Local Institution - 0215

Wakayama, Wakayama, Japan

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Local Institution - 0200

Ube, Yamaguchi, Japan

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Local Institution - 0129

Mexico City, Mexico City, Mexico

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Local Institution - 0154

Mexico City, Mexico City, Mexico

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Local Institution - 0130

Tlalpan, Mexico City, Mexico

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Local Institution - 0131

Monterrey, Nuevo León, Mexico

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Local Institution - 0022

Amsterdam, North Holland, Netherlands

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Local Institution - 0055

Enschede, , Netherlands

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Local Institution - 0024

Groningen, , Netherlands

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Local Institution - 0026

Leeuwarden, , Netherlands

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Local Institution - 0074

Bergen, , Norway

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Local Institution - 0081

Lorenskog, , Norway

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Local Institution - 0031

Lima, , Peru

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Local Institution - 0030

Lima, , Peru

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Local Institution - 0189

Bydgoszcz, , Poland

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Local Institution - 0205

Koszalin, , Poland

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Local Institution - 0202

Warsaw, , Poland

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Local Institution - 0191

Cluj-Napoca, Cluj, Romania

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Local Institution - 0187

Craiova, Dolj, Romania

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Moscow, , Russia

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Local Institution - 0192

Singapore, Central Singapore, Singapore

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Local Institution - 0125

Goyang-si, Gyeonggido, South Korea

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Local Institution - 0126

Seongnam-si, , South Korea

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Local Institution - 0124

Seoul, , South Korea

Site Status

Local Institution - 0151

Seoul, , South Korea

Site Status

Local Institution - 0128

Seoul, , South Korea

Site Status

Local Institution - 0127

Seoul, , South Korea

Site Status

Local Institution - 0070

A Coruña, , Spain

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Local Institution - 0068

Barcelona, , Spain

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Local Institution - 0065

Madrid, , Spain

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Local Institution - 0066

Madrid, , Spain

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Local Institution - 0209

Santander, , Spain

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Local Institution - 0067

Seville, , Spain

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Local Institution - 0069

Valencia, , Spain

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Local Institution - 0075

Jönköping, , Sweden

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Local Institution - 0059

Linköping, , Sweden

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Local Institution - 0058

Lund, , Sweden

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Local Institution - 0061

Baden, Canton of Aargau, Switzerland

Site Status

Local Institution - 0042

Chur, , Switzerland

Site Status

Local Institution - 0156

Kaohsiung City, , Taiwan

Site Status

Local Institution - 0159

Taichung, , Taiwan

Site Status

Local Institution - 0158

Taipei, , Taiwan

Site Status

Local Institution - 0155

Taipei, , Taiwan

Site Status

Local Institution - 0157

Taoyuan District, , Taiwan

Site Status

Local Institution - 0194

Ankara, , Turkey (Türkiye)

Site Status

Local Institution - 0204

Istanbul, , Turkey (Türkiye)

Site Status

Local Institution - 0193

Izmir, , Turkey (Türkiye)

Site Status

Countries

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United States Argentina Australia Brazil Canada Chile China Czechia Denmark Finland France Germany Greece Israel Italy Japan Mexico Netherlands Norway Peru Poland Romania Russia Singapore South Korea Spain Sweden Switzerland Taiwan Turkey (Türkiye)

References

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Tomita Y, Ye DW, Fujii A, Takeuchi N. Nivolumab plus gemcitabine-cisplatin for previously untreated unresectable or metastatic urothelial carcinoma: an Asian subgroup analysis from the global phase 3 CheckMate 901 trial. Urol Oncol. 2025 Sep 26:S1078-1439(25)00341-2. doi: 10.1016/j.urolonc.2025.08.022. Online ahead of print.

Reference Type DERIVED
PMID: 41015742 (View on PubMed)

van der Heijden MS, Sonpavde G, Powles T, Necchi A, Burotto M, Schenker M, Sade JP, Bamias A, Beuzeboc P, Bedke J, Oldenburg J, Chatta G, Urun Y, Ye D, He Z, Valderrama BP, Ku JH, Tomita Y, Filian J, Wang L, Purcea D, Patel MY, Nasroulah F, Galsky MD; CheckMate 901 Trial Investigators. Nivolumab plus Gemcitabine-Cisplatin in Advanced Urothelial Carcinoma. N Engl J Med. 2023 Nov 9;389(19):1778-1789. doi: 10.1056/NEJMoa2309863. Epub 2023 Oct 22.

Reference Type DERIVED
PMID: 37870949 (View on PubMed)

Provided Documents

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Document Type: Study Protocol and Statistical Analysis Plan

View Document

Related Links

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Other Identifiers

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2016-003881-14

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

CA209-901

Identifier Type: -

Identifier Source: org_study_id

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