Study to Investigate the Safety and Efficacy of Sofosbuvir/Velpatasvir in Adolescents and Children With Chronic HCV Infection

NCT ID: NCT03022981

Last Updated: 2020-10-08

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

216 participants

Study Classification

INTERVENTIONAL

Study Start Date

2017-01-26

Study Completion Date

2020-02-26

Brief Summary

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This study will have 2 parts: Pharmacokinetics (PK) Lead-in Phase and the Treatment Phase.

The primary objective of the PK Lead-in Phase is to evaluate the steady state PK and confirm the dose of sofosbuvir/velpatasvir (SOF/VEL) fixed-dose combination (FDC) in pediatric participants with chronic hepatitis C virus (HCV) infection.

The primary objective of the Treatment Phase is to evaluate the safety and tolerability of SOF/VEL for 12 weeks in pediatric participants with chronic HCV.

Detailed Description

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Conditions

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Hepatitis C Virus Infection

Study Design

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Allocation Method

NON_RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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12 to < 18 Years Old

PK Lead-in Phase: Sofosbuvir/Velpatasvir (SOF/VEL) 400/100 mg once daily for 7 days. Participants who complete the PK lead-in phase, continue into the treatment phase with no interruption of study drug administration and additional participants will be enrolled into the treatment phase once the appropriateness of the dose is confirmed by PK results from the PK lead-in phase.

Treatment Phase: SOF/VEL 400/100 mg once daily for 12 weeks.

Group Type EXPERIMENTAL

SOF/VEL

Intervention Type DRUG

SOF/VEL fixed-dose combination (FDC) 400/100 mg tablets or SOF/VEL FDC 200/50 mg tablets (based on swallowability assessment)

6 to < 12 Years Old

PK Lead-in Phase: SOF/VEL 200/50 mg once daily for 7 days. Participants who complete the PK lead-in phase, continue into the treatment phase with no interruption of study drug administration and additional participants will be enrolled into the treatment phase once the appropriateness of the dose is confirmed by PK results from the PK lead-in phase.

Treatment Phase: SOF/VEL 200/50 mg once daily for 12 weeks.

Group Type EXPERIMENTAL

SOF/VEL

Intervention Type DRUG

SOF/VEL fixed-dose combination (FDC) 400/100 mg tablets or SOF/VEL FDC 200/50 mg tablets (based on swallowability assessment)

3 to < 6 Years Old

PK Lead-in Phase: SOF/VEL 200/50 mg once daily for 7 days for participants who weigh ≥ 17 kg. SOF/VEL 150/37.5 mg once daily for 7 days for participants who weigh \< 17 kg. Participants who complete the PK lead-in phase, continue into the treatment phase with no interruption of study drug administration and additional participants will be enrolled into the treatment phase once the appropriateness of the dose is confirmed by PK results from the PK lead-in phase.

Treatment Phase: SOF/VEL 200/50 mg once daily for 12 weeks for participants who weigh ≥ 17 kg. SOF/VEL 150/37.5 mg once daily for 12 weeks for participants who weigh \< 17 kg.

Group Type EXPERIMENTAL

SOF/VEL

Intervention Type DRUG

SOF/VEL FDC 200/50 mg oral granules

Interventions

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SOF/VEL

SOF/VEL fixed-dose combination (FDC) 400/100 mg tablets or SOF/VEL FDC 200/50 mg tablets (based on swallowability assessment)

Intervention Type DRUG

SOF/VEL

SOF/VEL FDC 200/50 mg oral granules

Intervention Type DRUG

Other Intervention Names

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Epclusa® GS-7977/GS-5816 Epclusa® GS-7977/GS-5816

Eligibility Criteria

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Inclusion Criteria

* Chronic HCV-infected, treatment-naive and treatment-experienced adolescent and pediatric individuals aged 3 to \< 18 as determined at Day 1.
Minimum Eligible Age

3 Years

Maximum Eligible Age

17 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Gilead Sciences

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Gilead Study Director

Role: STUDY_DIRECTOR

Gilead Sciences

Locations

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Children's Hospital Los Angeles

Los Angeles, California, United States

Site Status

University of California, San Francisco

San Francisco, California, United States

Site Status

Children's Hospital of Colorado

Aurora, Colorado, United States

Site Status

Children's National Medical Center

Washington D.C., District of Columbia, United States

Site Status

University of Florida Shands Medical

Gainesville, Florida, United States

Site Status

Florida Gastroenterology Care for Children

Orlando, Florida, United States

Site Status

Emory Children's Center

Atlanta, Georgia, United States

Site Status

Riley Hospital for Children

Indianapolis, Indiana, United States

Site Status

Kosair Charities Pediatric Clinical Research Unit

Louisville, Kentucky, United States

Site Status

Johns Hopkins University (JHU) - The Johns Hopkins Hospital (JHH)

Baltimore, Maryland, United States

Site Status

Boston Children's Hospital

Boston, Massachusetts, United States

Site Status

Children's Mercy Hospital

Kansas City, Missouri, United States

Site Status

Children's Hospital & Medical Center

Omaha, Nebraska, United States

Site Status

Mount Sinai Medical Center

New York, New York, United States

Site Status

Cincinnati Children's Hospital Medical Center

Cincinnati, Ohio, United States

Site Status

Nationwide Children's Hospital- The Ohio State University (OSU)

Columbus, Ohio, United States

Site Status

The Children's Hospital of Philadelphia

Philadelphia, Pennsylvania, United States

Site Status

Monroe Carell Jr. Children's Hospital at Vanderbilt

Nashville, Tennessee, United States

Site Status

Cook Children's Medical Center

Fort Worth, Texas, United States

Site Status

Baylor College of Medicine

Houston, Texas, United States

Site Status

Seattle Children's Hospital

Seattle, Washington, United States

Site Status

Cliniques Universitaires Saint Luc

Brussels, , Belgium

Site Status

Azienda Ospedaliero-Universitaria di Bologna - Policlinico S. Orsola - Malpighi

Bologna, , Italy

Site Status

Azienda Ospedaliera Universitaria Meyer

Florence, , Italy

Site Status

Ospedale Casa Sollievo della Sofferenza

San Giovanni Rotondo, , Italy

Site Status

The Leeds Teaching Hospitals NHS Trust

Leeds, England, United Kingdom

Site Status

King's College Hospital NHS Trust

London, England, United Kingdom

Site Status

Countries

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United States Belgium Italy United Kingdom

References

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Jonas MM, Romero R, Sokal EM, Rosenthal P, Verucchi G, Lin CH, et al. The Safety and Efficacy of Sofosbuvir/Velpatasvir in Pediatric Patients 6 to < 18 years old with Chronic Hepatitis C Infection [Abstract]. AASLD; 2019 08-12 November; Boston, Massachusetts.

Reference Type RESULT

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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2016-002446-23

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

GS-US-342-1143

Identifier Type: -

Identifier Source: org_study_id

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