A Study to Evaluate the Safety and Efficacy of Ruxolitinib Phosphate Cream Applied Topically to Adults With Atopic Dermatitis

NCT ID: NCT03011892

Last Updated: 2021-04-09

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

307 participants

Study Classification

INTERVENTIONAL

Study Start Date

2017-01-09

Study Completion Date

2018-03-12

Brief Summary

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The purpose of this study is to establish the efficacy of each strength of ruxolitinib cream once daily (QD) or twice daily (BID) in participants with atopic dermatitis as compared with vehicle cream BID.

Detailed Description

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Conditions

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Atopic Dermatitis

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

TRIPLE

Participants Investigators Outcome Assessors

Study Groups

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Double Blind (DB): Vehicle BID

Participants applied vehicle cream twice daily (BID) for 8 weeks DB period.

Group Type PLACEBO_COMPARATOR

Vehicle Cream BID

Intervention Type DRUG

Vehicle cream BID

DB: Triamcinolone (TAC) 0.1% BID/Vehicle Cream BID

Participants applied triamcinolone 0.1% cream BID for 4 weeks followed by vehicle cream for 4 weeks in DB period.

Group Type ACTIVE_COMPARATOR

Triamcinolone 0.1% Cream BID

Intervention Type DRUG

Triamcinolone 0.1% cream BID

Vehicle Cream BID

Intervention Type DRUG

Vehicle cream BID

DB: Ruxolitinib 0.15% Once Daily (QD)

Participants applied ruxolitinib 0.15% cream QD for 8 weeks in DB period.

Group Type EXPERIMENTAL

Ruxolitinib 0.15% Cream QD

Intervention Type DRUG

Ruxolitinib 0.15% cream QD

DB: Ruxolitinib 0.5% QD

Participants applied ruxolitinib 0.5% cream QD for 8 weeks in DB period.

Group Type EXPERIMENTAL

Ruxolitinib 0.5% Cream QD

Intervention Type DRUG

Ruxolitinib 0.5% cream QD

DB: Ruxolitinib 1.5% QD

Participants applied ruxolitinib 1.5% cream QD for 8 weeks in DB period.

Group Type EXPERIMENTAL

Ruxolitinib 1.5% Cream QD

Intervention Type DRUG

Ruxolitinib 1.5% cream QD

DB: Ruxolitinib 1.5% BID

Participants applied ruxolitinib 1.5% cream BID for 8 weeks in DB period.

Group Type EXPERIMENTAL

Ruxolitinib 1.5% Cream BID

Intervention Type DRUG

Ruxolitinib 1.5% cream BID

Open-Label (OL): Vehicle BID to Ruxolitinib 1.5% BID

Following DB Period, at Week 8, participants who met criteria (compliant with the protocol and no safety concerns) received open-label treatment with ruxolitinib 1.5% cream BID for 4 weeks.

Group Type PLACEBO_COMPARATOR

Ruxolitinib 1.5% Cream BID

Intervention Type DRUG

Ruxolitinib 1.5% cream BID

OL: TAC BID/Vehicle BID to Ruxolitinib 1.5% BID

Following DB Period, at Week 8, participants who met criteria (compliant with the protocol and no safety concerns) received open-label treatment with ruxolitinib 1.5% cream BID for 4 weeks.

Group Type ACTIVE_COMPARATOR

Ruxolitinib 1.5% Cream BID

Intervention Type DRUG

Ruxolitinib 1.5% cream BID

OL: Ruxolitinib 0.15% QD to Ruxolitinib 1.5% BID

Following DB Period, at Week 8, participants who met criteria (compliant with the protocol and no safety concerns) received open-label treatment with ruxolitinib 1.5% cream BID for 4 weeks.

Group Type EXPERIMENTAL

Ruxolitinib 1.5% Cream BID

Intervention Type DRUG

Ruxolitinib 1.5% cream BID

OL: Ruxolitinib 0.5% QD to Ruxolitinib 1.5% BID

Following DB Period, at Week 8, participants who met criteria (compliant with the protocol and no safety concerns) received open-label treatment with ruxolitinib 1.5% cream BID for 4 weeks.

Group Type EXPERIMENTAL

Ruxolitinib 1.5% Cream BID

Intervention Type DRUG

Ruxolitinib 1.5% cream BID

OL: Ruxolitinib 1.5% QD to Ruxolitinib 1.5% BID

Following DB Period, at Week 8, participants who met criteria (compliant with the protocol and no safety concerns) received open-label treatment with ruxolitinib 1.5% cream BID for 4 weeks.

Group Type EXPERIMENTAL

Ruxolitinib 1.5% Cream BID

Intervention Type DRUG

Ruxolitinib 1.5% cream BID

OL: Ruxolitinib 1.5% BID to Ruxolitinib 1.5% BID

Following DB Period, at Week 8, participants who met criteria (compliant with the protocol and no safety concerns) received open-label treatment with ruxolitinib 1.5% cream BID for 4 weeks.

Group Type EXPERIMENTAL

Ruxolitinib 1.5% Cream BID

Intervention Type DRUG

Ruxolitinib 1.5% cream BID

Interventions

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Ruxolitinib 0.15% Cream QD

Ruxolitinib 0.15% cream QD

Intervention Type DRUG

Ruxolitinib 0.5% Cream QD

Ruxolitinib 0.5% cream QD

Intervention Type DRUG

Ruxolitinib 1.5% Cream QD

Ruxolitinib 1.5% cream QD

Intervention Type DRUG

Ruxolitinib 1.5% Cream BID

Ruxolitinib 1.5% cream BID

Intervention Type DRUG

Triamcinolone 0.1% Cream BID

Triamcinolone 0.1% cream BID

Intervention Type DRUG

Vehicle Cream BID

Vehicle cream BID

Intervention Type DRUG

Other Intervention Names

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INCB018424 INCB018424 INCB018424 INCB018424

Eligibility Criteria

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Inclusion Criteria

* Participants diagnosed with atopic dermatitis (AD) as defined by the Hanifin and Rajka criteria.
* Participants with a history of AD for at least 2 years.
* Participants with an Investigator's Global Assessment (IGA) score of 2 to 3 at screening and baseline.
* Participants with body surface area (BSA) of AD involvement, excluding the face and intertriginous areas, of 3% to 20% at screening and baseline.
* Participants who agree to discontinue all agents used to treat AD from screening through the final follow-up visit.

Exclusion Criteria

* Participants with evidence of active acute or chronic infections.
* Use of topical treatments for AD (other than bland emollients) within 2 weeks of baseline.
* Systemic immunosuppressive or immunomodulating drugs (eg, oral or injectable corticosteroids, methotrexate, cyclosporine, mycophenolate mofetil, azathioprine) within 4 weeks or 5 half-lives of baseline (whichever is longer).
* Participants with other dermatologic disease besides AD whose presence or treatments could complicate the assessment of disease (eg, psoriasis).
* Participants with a history of other diseases besides dermatologic disorders (eg, other autoimmune diseases) taking treatments that could complicate assessments.
* Participants with cytopenias at screening, defined as:

* Leukocytes \< 3.0 × 10\^9/L.
* Neutrophils \< lower limit of normal.
* Hemoglobin \< 10 g/dL.
* Lymphocytes \< 0.8 × 10\^9/L
* Platelets \< 100 × 10\^9/L.
* Participants with severely impaired liver function (Child-Pugh Class C) or end-stage renal disease (ESRD) on dialysis or at least 1 of the following:

* Serum creatinine \> 1.5 mg/dL.
* Alanine aminotransferase (ALT) or aspartate aminotransferase (AST) ≥ 1.5 × upper limit of normal.
* Participants taking potent systemic cytochrome P450 3A4 inhibitors or fluconazole within 2 weeks or 5 half-lives, whichever is longer, before the baseline visit (topical agents with limited systemic availability are permitted).
* Participants who have previously received Janus kinase (JAK) inhibitors, systemic or topical (e.g., ruxolitinib, tofacitinib, baricitinib, filgotinib, lestaurtinib, pacritinib).
Minimum Eligible Age

18 Years

Maximum Eligible Age

70 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Incyte Corporation

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Michael Kuligowski, MD

Role: STUDY_DIRECTOR

Incyte Corporation

Locations

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UAB DERMATOLOGY, 2000 6th Avenue South

Birmingham, Alabama, United States

Site Status

BURKE PHARMACEUTICAL RESEARCH, 601 W. Commerce

Bryant, Arkansas, United States

Site Status

ENCINO RESEARCH CENTER, 16133 Ventura Blvd

Encino, California, United States

Site Status

DERMATOLOGY RESEARCH ASSOCIATES,8930 South Sepulveda Blvd

Los Angeles, California, United States

Site Status

DERMATOLOGY SPECIALISTS, INC, 3629 Vista Way

Oceanside, California, United States

Site Status

INTEGRATED RESEARCH GROUP, INC, 4646 Brockton Avenue

Riverside, California, United States

Site Status

SAN LUIS DERMATOLOGY AND LASER CLINIC, 15 Santa Rosa Street

San Luis Obispo, California, United States

Site Status

NEW ENGLAND RESEARCH ASSOCIATES LLC, 5520 Park Avenue

Trumbull, Connecticut, United States

Site Status

DS RESEARCH, 2241 Green Valley Road

New Albany, Indiana, United States

Site Status

THE INDIANA CLINICAL TRIALS CENTER, 824 Edwards Drive

Plainfield, Indiana, United States

Site Status

DERMRESEARCH, 1169 Eastern Parkway 2310

Louisville, Kentucky, United States

Site Status

DS RESEARCH, 3810 Springhurst Blvd

Louisville, Kentucky, United States

Site Status

ACTIVMED PRACTICES & RESEARCH, INC, 138 Conant Street

Beverly, Massachusetts, United States

Site Status

TUFTS MEDICAL CENTER, 800 Washington Street

Boston, Massachusetts, United States

Site Status

HENRY FORD HOSPITAL, 3031 West Grand Blvd

Detroit, Michigan, United States

Site Status

WASHINGTON UNIVERSITY - DERMATOLOGY, 4921 Parkview Place

St Louis, Missouri, United States

Site Status

WASHINGTON UNIVERSITY - DERMATOLOGY, 969 Mason Road

St Louis, Missouri, United States

Site Status

ACTIVMED PRACTICES AND RESEARCH, INC, 110 Corporate Drive

Portsmouth, New Hampshire, United States

Site Status

HASSMAN RESEARCH INSTITUTE, LLC, 175 Cross Keys Road

Berlin, New Jersey, United States

Site Status

DERMATOLOGY CONSULTING SERVICES, PLLC, 2444 North Main Street

High Point, North Carolina, United States

Site Status

WAKE RESEARCH ASSOCIATES LLC, 3100 Duraleigh Road

Raleigh, North Carolina, United States

Site Status

DERMATOLOGISTS OF GREATER COLUMBUS, 2359 East Main Street

Bexley, Ohio, United States

Site Status

RAPID MEDICAL RESEARCH, INC, 3619 Park East Drive

Cleveland, Ohio, United States

Site Status

CENTRAL SOONER RESEARCH, 900 North Porter

Norman, Oklahoma, United States

Site Status

PARISH DERMATOLOGY, INC, 1845 Walnut Street

Philadelphia, Pennsylvania, United States

Site Status

PEAK RESEARCH LLC, 2589 Washington Rd

Upper Saint Clair, Pennsylvania, United States

Site Status

ARLINGTON RESEARCH CENTER, INC, 711 East Lamar Blvd

Arlington, Texas, United States

Site Status

DERMRESEARCH INC., 8140 North Mopac Expressway

Austin, Texas, United States

Site Status

J&S STUDIES, INC, 1710 Crescent Pointe Pkwy

College Station, Texas, United States

Site Status

CENTER FOR CLINICAL STUDIES (CCS), 1401 Binz

Houston, Texas, United States

Site Status

SUZANNE BRUCE AND ASSOCIATES, PA, 1900 St. James Place

Houston, Texas, United States

Site Status

CLINICAL TRIALS OF TEXAS, INC, 7940 Floyd Curl Drive

San Antonio, Texas, United States

Site Status

DERMATOLOGY CLINICAL RESEARCH CENTER OF SAN ANTONIO, 7810 Louis Pasteur

San Antonio, Texas, United States

Site Status

CENTER FOR CLINICAL STUDIES, 451 North Texas Avenue

Webster, Texas, United States

Site Status

CHARLOTTESVILLE DERMATOLOGY, 600 Peter Jefferson Parkway

Charlottesville, Virginia, United States

Site Status

INSTITUTE FOR SKIN ADVANCEMENT, 4935 40th Avenue Nw

Calgary, Alberta, Canada

Site Status

DR. CHIH-HO HONG MEDICAL INC., 15300 105 Avenue

Surrey, British Columbia, Canada

Site Status

WISEMAN DERMATOLOGY RESEARCH INC, 6 - 1170 Taylor Avenue

Winnipeg, Manitoba, Canada

Site Status

CCA MEDICAL RESEARCH, 95 Bayly Street West

Ajax, Ontario, Canada

Site Status

SIMCODERM MEDICAL AND SURGICAL DERMATOLOGY CENTER, 5 Quarry Ridge Road

Barrie, Ontario, Canada

Site Status

LYNDERM RESEARCH INC, 25 Main Street Markham North

Markham, Ontario, Canada

Site Status

DERMEDGE RESEARCH INC., 333 Lakeshore Road West

Mississauga, Ontario, Canada

Site Status

NORTH BAY DERMATOLOGY CENTRE, 500 Cassells Street

North Bay, Ontario, Canada

Site Status

RESEARCH BY ICLS, 1344 Cornwall Road

Oakville, Ontario, Canada

Site Status

OFFICE OF DR. MICHAEL ROBERN, 1 Centrepointe Drive

Ottawa, Ontario, Canada

Site Status

SKIN CENTRE FOR DERMATOLOGY, 775 Monaghan Road

Peterborough, Ontario, Canada

Site Status

YORK DERMATOLOGY CENTER, 250 Harding Blvd West

Richmond Hill, Ontario, Canada

Site Status

RESEARCH TORONTO, 208 Bloor Street West

Toronto, Ontario, Canada

Site Status

K. PAPP CLINICAL RESEARCH, 135 Union Street East

Waterloo, Ontario, Canada

Site Status

XLR8 MEDICAL RESEARCH, 2425 Tecumseh Road East

Windsor, Ontario, Canada

Site Status

WINDSOR CLINICAL RESEARCH INC, 2224 Walker Road

Windsor, Ontario, Canada

Site Status

CLINIQUE DERMATOLOGIQUE DE SAINT-JEROME, 555 Boul. Saint-antoine

Saint-Jérôme, Quebec, Canada

Site Status

Countries

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United States Canada

References

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Gong X, Chen X, Kuligowski ME, Liu X, Liu X, Cimino E, McGee R, Yeleswaram S. Pharmacokinetics of Ruxolitinib in Patients with Atopic Dermatitis Treated With Ruxolitinib Cream: Data from Phase II and III Studies. Am J Clin Dermatol. 2021 Jul;22(4):555-566. doi: 10.1007/s40257-021-00610-x. Epub 2021 May 12.

Reference Type DERIVED
PMID: 33982267 (View on PubMed)

Kim BS, Howell MD, Sun K, Papp K, Nasir A, Kuligowski ME; INCB 18424-206 Study Investigators. Treatment of atopic dermatitis with ruxolitinib cream (JAK1/JAK2 inhibitor) or triamcinolone cream. J Allergy Clin Immunol. 2020 Feb;145(2):572-582. doi: 10.1016/j.jaci.2019.08.042. Epub 2019 Oct 17.

Reference Type DERIVED
PMID: 31629805 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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INCB 18424-206

Identifier Type: -

Identifier Source: org_study_id

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