A Study to Evaluate the Efficacy and Safety of Pemigatinib (INCB054828) in Subjects With Myeloid/Lymphoid Neoplasms With FGFR1 Rearrangement - (FIGHT-203)

NCT ID: NCT03011372

Last Updated: 2025-11-18

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

47 participants

Study Classification

INTERVENTIONAL

Study Start Date

2017-04-25

Study Completion Date

2024-10-30

Brief Summary

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The purpose of this study is to evaluate the efficacy and safety of pemigatinib (INCB054828) in subjects with myeloid/lymphoid neoplasms with fibroblast growth factor receptor (FGFR) 1 rearrangement.

Detailed Description

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Conditions

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MPN (Myeloproliferative Neoplasms)

Study Design

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Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Pemigatinib

Group Type EXPERIMENTAL

Pemigatinib

Intervention Type DRUG

Pemigatinib once a day by mouth for 2 consecutive weeks and 1 week off therapy.

Participants will receive either the intermittent dose (as written) or continuous dosing.

Interventions

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Pemigatinib

Pemigatinib once a day by mouth for 2 consecutive weeks and 1 week off therapy.

Participants will receive either the intermittent dose (as written) or continuous dosing.

Intervention Type DRUG

Other Intervention Names

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INCB054828

Eligibility Criteria

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Inclusion Criteria

* Documented lymphoid or myeloid neoplasm with 8p11 rearrangement known to lead to FGFR1 activation, based on standard diagnostic cytogenetic evaluation performed locally, before signing informed consent for this study.
* Eligible subjects must:

* Have relapsed after stem cell transplantation or after other disease modifying therapy, OR
* Not be current candidates for stem cell transplantation or other disease modifying therapies.
* Note: All relapsed/refractory subjects must have evidence of either cytogenetic or hematological disease and have no evidence of residual toxicity (eg, graft-versus-host disease requiring treatment).
* Life expectancy ≥ 12 weeks.
* Eastern Cooperative Oncology Group (ECOG) performance status 0 to 2.

Exclusion Criteria

* Prior receipt of a selective FGFR inhibitor.
* History and/or current evidence of ectopic mineralization/calcification, including but not limited to soft tissue, kidneys, intestine, myocardia, or lung, except calcified lymph nodes and asymptomatic arterial or cartilage/tendon calcifications.
* Current evidence of corneal disorder/keratopathy, including but not limited to bullous/band keratopathy, corneal abrasion, inflammation/ulceration, and keratoconjunctivitis, as confirmed by ophthalmologic examination.
* Use of any potent cytochrome P450 3A4 inhibitors or inducers within 14 days or 5 half-lives (whichever is shorter) before the first dose of study drug.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Incyte Corporation

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Philomena Collucci, MD

Role: STUDY_DIRECTOR

Incyte Corporation

Locations

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Mayo Clinic Arizona

Phoenix, Arizona, United States

Site Status

City of Hope National Medical Center

Duarte, California, United States

Site Status

Stanford Cancer Institute

Stanford, California, United States

Site Status

Emory University - Winship Cancer Institute

Atlanta, Georgia, United States

Site Status

Franciscan St. Francis Health

Indianapolis, Indiana, United States

Site Status

Washington University School of Medicine

St Louis, Missouri, United States

Site Status

Weill Cornell Medical Centers

New York, New York, United States

Site Status

Md Anderson Cancer Center

Houston, Texas, United States

Site Status

University of Utah

Salt Lake City, Utah, United States

Site Status

Ordensklinikum Krankenhaus Der Barmherzigen Schwestern Linz

Linz, , Austria

Site Status

Medical University of Vienna

Vienna, , Austria

Site Status

Iii Med. Abteilung For Hematologie and Onkologie Hanuscfhkrankenhaus

Vienna, , Austria

Site Status

Universitair Ziekenhuis (Uz) Leuven

Leuven, , Belgium

Site Status

Princess Margaret Cancer Center

Toronto, Ontario, Canada

Site Status

Centre Leon Berard

Lyon, , France

Site Status

Chu de Nice - Hospital L Archet

Nice, , France

Site Status

Hospital Saint Louis

Paris, , France

Site Status

Universitaire Du Cancer de Toulouse Institut Claudius Regaud Iuct-Oncopole

Toulouse, , France

Site Status

University Medical Center Rwth Aachen

Aachen, , Germany

Site Status

Universitatsklinikum Halle (Saale)

Halle, , Germany

Site Status

Universitatsklinikum Jena

Jena, , Germany

Site Status

Universitatsklinikum Leipzig

Leipzig, , Germany

Site Status

University Hospital Mannheim

Mannheim, , Germany

Site Status

Johannes Wesling Klinikum Minden

Minden, , Germany

Site Status

Ospedale Papa Giovanni Xxiii

Bergamo, , Italy

Site Status

Azienda Ospedaliero-Universitaria Careggi (Aouc)

Florence, , Italy

Site Status

Kindai University Hospital

Osaka, , Japan

Site Status

Ntt Medical Center Tokyo

Tokyo, , Japan

Site Status

Hospital Clinico Universitario de Valencia

Valencia, , Spain

Site Status

Inselspital - Universitaetsspital Bern

Bern, , Switzerland

Site Status

Universitatsspital Zurich

Zurich, , Switzerland

Site Status

Guys and St Thomas Nhs Foundation Trust

London, , United Kingdom

Site Status

Oxford University Hospitals Nhs Foundation Trust

Oxford, , United Kingdom

Site Status

Countries

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United States Austria Belgium Canada France Germany Italy Japan Spain Switzerland United Kingdom

References

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Al-Bazaz M, Forstreuter A, Hammada I, Hille J, Wagner JN, Reinert J, Wehrhahn J, Bokemeyer C, Fiedler W. Acute Lymphoblastic Leukemia Characterized by Rare BCR::FGFR1 Translocation: A Case Report With Literature Review. Case Rep Hematol. 2025 Oct 23;2025:8892036. doi: 10.1155/crh/8892036. eCollection 2025.

Reference Type DERIVED
PMID: 41180818 (View on PubMed)

Verstovsek S, Kiladjian JJ, Vannucchi AM, Patel JL, Rambaldi A, Shomali WE, Oh ST, Usuki K, Harrison CN, Ritchie EK, Akard LP, Hernandez-Boluda JC, Huguet F, Colucci P, Zhen H, Oliveira N, Gilmartin A, Langford C, George TI, Reiter A, Gotlib J. Pemigatinib for Myeloid/Lymphoid Neoplasms with FGFR1 Rearrangement. NEJM Evid. 2025 Sep;4(9):EVIDoa2500017. doi: 10.1056/EVIDoa2500017. Epub 2025 Aug 26.

Reference Type DERIVED
PMID: 40856555 (View on PubMed)

Subbiah V, Burris HA 3rd, Kurzrock R. Revolutionizing cancer drug development: Harnessing the potential of basket trials. Cancer. 2024 Jan;130(2):186-200. doi: 10.1002/cncr.35085. Epub 2023 Nov 7.

Reference Type DERIVED
PMID: 37934000 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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2016-002596-10

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

INCB 54828-203

Identifier Type: -

Identifier Source: org_study_id

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