Trial Outcomes & Findings for An Extension Study of Safety and Tolerability of SEP-363856 in Adult Subjects With Schizophrenia (NCT NCT02970929)

NCT ID: NCT02970929

Last Updated: 2024-07-05

Results Overview

Number of Participants with overall Adverse Events (AEs), Serious Adverse Events (SAEs), and Adverse Events (AEs) leading to discontinuation

Recruitment status

COMPLETED

Study phase

PHASE2

Target enrollment

157 participants

Primary outcome timeframe

From first dose of study drug to last study visit (27 weeks)

Results posted on

2024-07-05

Participant Flow

Subjects received open-label SEP-363856 50 mg/day from Day 1 through Day 3, and then received flexible dosing of SEP-363856 (25, 50, or 75 mg/day) for the rest of the trial.

Participant milestones

Participant milestones
Measure
SEP-363856
SEP-363856 capsule (25 mg, 50 mg, or 75 mg) once daily
Overall Study
STARTED
157
Overall Study
Subjects Who Received Study Medication
156
Overall Study
COMPLETED
105
Overall Study
NOT COMPLETED
52

Reasons for withdrawal

Reasons for withdrawal
Measure
SEP-363856
SEP-363856 capsule (25 mg, 50 mg, or 75 mg) once daily
Overall Study
Adverse Event
18
Overall Study
Lack of Efficacy
8
Overall Study
NON-COMPLIANCE WITH STUDY DRUG
1
Overall Study
INVESTIGATOR CONSIDERS SUBJECT CLINICALLY UNSTABLE, NOT APPROPRIATE FOR DISCHARGE TO AN OUTPATIENT
1
Overall Study
SPONSOR REQUEST THAT SUBJECT BE WITHDRAWN DUE TO POSITIVE DRUG RESULTS AND FOR THE SUBJECT'S SAFETY
1
Overall Study
LOST TO FOLLOWUP
6
Overall Study
MOVED OUT OF STATE
1
Overall Study
Withdrawal by Subject
16

Baseline Characteristics

An Extension Study of Safety and Tolerability of SEP-363856 in Adult Subjects With Schizophrenia

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
SEP-363856
n=156 Participants
SEP-363856 capsule (25 mg, 50 mg, or 75 mg) once daily
Age, Categorical
<=18 years
2 Participants
n=93 Participants
Age, Categorical
Between 18 and 65 years
154 Participants
n=93 Participants
Age, Categorical
>=65 years
0 Participants
n=93 Participants
Age, Continuous
30.2 Years
STANDARD_DEVIATION 6.03 • n=93 Participants
Sex: Female, Male
Female
54 Participants
n=93 Participants
Sex: Female, Male
Male
102 Participants
n=93 Participants
Ethnicity (NIH/OMB)
Hispanic or Latino
5 Participants
n=93 Participants
Ethnicity (NIH/OMB)
Not Hispanic or Latino
151 Participants
n=93 Participants
Ethnicity (NIH/OMB)
Unknown or Not Reported
0 Participants
n=93 Participants
Race (NIH/OMB)
American Indian or Alaska Native
4 Participants
n=93 Participants
Race (NIH/OMB)
Asian
0 Participants
n=93 Participants
Race (NIH/OMB)
Native Hawaiian or Other Pacific Islander
0 Participants
n=93 Participants
Race (NIH/OMB)
Black or African American
15 Participants
n=93 Participants
Race (NIH/OMB)
White
136 Participants
n=93 Participants
Race (NIH/OMB)
More than one race
1 Participants
n=93 Participants
Race (NIH/OMB)
Unknown or Not Reported
0 Participants
n=93 Participants
Age, Customized
>=18 - <25 years
38 Participants
n=93 Participants
Age, Customized
>=25 - <=40 years
118 Participants
n=93 Participants
Country
Hungary
8 Participants
n=93 Participants
Country
Romania
6 Participants
n=93 Participants
Country
Russia
68 Participants
n=93 Participants
Country
Ukraine
54 Participants
n=93 Participants
Country
United States
20 Participants
n=93 Participants
Double-blind Baseline BMI (Body Mass Index) Group
<18.5 kg/m^2
2 Participants
n=93 Participants
Double-blind Baseline BMI (Body Mass Index) Group
>=18.5 - <25.0 kg/m^2
80 Participants
n=93 Participants
Double-blind Baseline BMI (Body Mass Index) Group
>=25.0 - <30.0 kg/m^2
55 Participants
n=93 Participants
Double-blind Baseline BMI (Body Mass Index) Group
>=30.0 kg/m^2
19 Participants
n=93 Participants
Open-label Baseline BMI (Body Mass Index) Group
<18.5 kg/m^2
3 Participants
n=93 Participants
Open-label Baseline BMI (Body Mass Index) Group
>=18.5 - <25.0 kg/m^2
82 Participants
n=93 Participants
Open-label Baseline BMI (Body Mass Index) Group
>=25.0 - <30.0 kg/m^2
53 Participants
n=93 Participants
Open-label Baseline BMI (Body Mass Index) Group
>=30.0 kg/m^2
18 Participants
n=93 Participants
Open-label Baseline Waist Circumference (cm)
85.20 cm
STANDARD_DEVIATION 13.467 • n=93 Participants
Open-label Baseline BMI (Body Mass Index) (kg/m^2)
25.05 kg/m^2
STANDARD_DEVIATION 3.890 • n=93 Participants
Open-label Baseline Weight (kg)
75.32 kg
STANDARD_DEVIATION 13.987 • n=93 Participants
Open-label Baseline Height (cm)
173.1 cm
STANDARD_DEVIATION 7.73 • n=93 Participants
Double-blind Baseline Waist Circumference (cm)
85.36 cm
STANDARD_DEVIATION 13.508 • n=93 Participants
Double-blind Baseline BMI (Body Mass Index) (kg/m^2)
25.07 kg/m^2
STANDARD_DEVIATION 3.863 • n=93 Participants
Double-blind Baseline Weight (kg)
75.38 kg
STANDARD_DEVIATION 13.873 • n=93 Participants
Double-blind Baseline Height (cm)
173.1 cm
STANDARD_DEVIATION 7.73 • n=93 Participants

PRIMARY outcome

Timeframe: From first dose of study drug to last study visit (27 weeks)

Number of Participants with overall Adverse Events (AEs), Serious Adverse Events (SAEs), and Adverse Events (AEs) leading to discontinuation

Outcome measures

Outcome measures
Measure
SEP-363856
n=156 Participants
SEP-363856 capsule (25 mg, 50 mg, or 75 mg) once daily
SEP-SEP
Subjects who received SEP-363856 in study SEP361-201 and SEP-363856 in study SEP361-202
The Incidence of Overall Adverse Events (AEs), Serious Adverse Events (SAEs), and Adverse Events (AEs) Leading to Discontinuation
Overall Adverse Events (AEs)
88 Participants
The Incidence of Overall Adverse Events (AEs), Serious Adverse Events (SAEs), and Adverse Events (AEs) Leading to Discontinuation
Serious Adverse Events (SAEs)
15 Participants
The Incidence of Overall Adverse Events (AEs), Serious Adverse Events (SAEs), and Adverse Events (AEs) Leading to Discontinuation
Adverse Events leading to discontinuation from study
18 Participants
The Incidence of Overall Adverse Events (AEs), Serious Adverse Events (SAEs), and Adverse Events (AEs) Leading to Discontinuation
Adverse Events leading to discontinuation of study drug
18 Participants

SECONDARY outcome

Timeframe: Overall post Open-label Baseline treatment period (26 weeks)

Number of participants with suicidal ideation (SI) and suicidal behavior (SB) using the Columbia - Suicide Severity Rating Scale (C-SSRS). The C-SSRS is a tool designed to systematically assess and track suicidal behavior and suicidal ideation for life time, one month prior to the screening visit for suicidal ideation and 6 months prior to the screening visit for suicidal behavior, and throughout the study. The strength of this suicide classification system is in its ability to comprehensively identify suicidal events while limiting the over-identification of suicidal behavior.

Outcome measures

Outcome measures
Measure
SEP-363856
n=156 Participants
SEP-363856 capsule (25 mg, 50 mg, or 75 mg) once daily
SEP-SEP
Subjects who received SEP-363856 in study SEP361-201 and SEP-363856 in study SEP361-202
Frequency of Suicidal Ideation (SI) and Suicidal Behavior (SB) Using the Columbia - Suicide Severity Rating Scale (C-SSRS)
Any suicidal ideation
3 Participants
Frequency of Suicidal Ideation (SI) and Suicidal Behavior (SB) Using the Columbia - Suicide Severity Rating Scale (C-SSRS)
Any suicidal behavior
1 Participants
Frequency of Suicidal Ideation (SI) and Suicidal Behavior (SB) Using the Columbia - Suicide Severity Rating Scale (C-SSRS)
Any suicidality
3 Participants

SECONDARY outcome

Timeframe: Overall post Open-label Baseline treatment period (26 weeks)

The C-SSRS is a tool designed to systematically assess and track suicidal behavior and suicidal ideation for life time, one month prior to the screening visit for suicidal ideation and 6 months prior to the screening visit for suicidal behavior, and throughout the study. The strength of this suicide classification system is in its ability to comprehensively identify suicidal events while limiting the over-identification of suicidal behavior.

Outcome measures

Outcome measures
Measure
SEP-363856
n=156 Participants
SEP-363856 capsule (25 mg, 50 mg, or 75 mg) once daily
SEP-SEP
Subjects who received SEP-363856 in study SEP361-201 and SEP-363856 in study SEP361-202
Severity of Suicidal Ideation (SI) and Suicidal Behavior (SB) Using the Columbia - Suicide Severity Rating Scale (C-SSRS)
SI: Wish to be dead
2 Participants
Severity of Suicidal Ideation (SI) and Suicidal Behavior (SB) Using the Columbia - Suicide Severity Rating Scale (C-SSRS)
SI: Non-specific active suicidal thoughts
2 Participants
Severity of Suicidal Ideation (SI) and Suicidal Behavior (SB) Using the Columbia - Suicide Severity Rating Scale (C-SSRS)
SI: Any methods (not plan) without intent to act
0 Participants
Severity of Suicidal Ideation (SI) and Suicidal Behavior (SB) Using the Columbia - Suicide Severity Rating Scale (C-SSRS)
SI: Some intent to act, without specific plan
0 Participants
Severity of Suicidal Ideation (SI) and Suicidal Behavior (SB) Using the Columbia - Suicide Severity Rating Scale (C-SSRS)
SI: Specific plan and intent
0 Participants
Severity of Suicidal Ideation (SI) and Suicidal Behavior (SB) Using the Columbia - Suicide Severity Rating Scale (C-SSRS)
SB: Preparatory acts or behavior
0 Participants
Severity of Suicidal Ideation (SI) and Suicidal Behavior (SB) Using the Columbia - Suicide Severity Rating Scale (C-SSRS)
SB: Aborted attempt
1 Participants
Severity of Suicidal Ideation (SI) and Suicidal Behavior (SB) Using the Columbia - Suicide Severity Rating Scale (C-SSRS)
SB: Interrupted attempt
0 Participants
Severity of Suicidal Ideation (SI) and Suicidal Behavior (SB) Using the Columbia - Suicide Severity Rating Scale (C-SSRS)
SB: Actual attempt (non-fatal)
0 Participants
Severity of Suicidal Ideation (SI) and Suicidal Behavior (SB) Using the Columbia - Suicide Severity Rating Scale (C-SSRS)
SB: Completed suicide
0 Participants

SECONDARY outcome

Timeframe: From the time of clinical response to relapse or censor (one day after the last study drug dose)

Population: Relapse population, which includes subjects who received at least one dose of open-label treatment and demonstrated a clinical response to 4 weeks of treatment with SEP-363856. Clinical response is defined as meeting (1) a decrease in PANSS total score of ≥ 20% from double-blind Baseline, AND (2) a CGI-S score ≤ 4. For PBO-SEP subjects, clinical response was evaluated at Week 4 of study SEP361-201. For SEP-SEP subjects, clinical response was evaluated at Week 4 of study SEP361-202.

Relapse is defined as the earliest occurrence of any of the following: - An increase in PANSS total score by ≥ 30% from the PANSS total score at clinical response and a CGI-S score ≥ 3; - Re-hospitalization for worsening of psychosis; - Emergence of suicidality, homicidality, and/or risk of harm to self or others.

Outcome measures

Outcome measures
Measure
SEP-363856
n=59 Participants
SEP-363856 capsule (25 mg, 50 mg, or 75 mg) once daily
SEP-SEP
n=51 Participants
Subjects who received SEP-363856 in study SEP361-201 and SEP-363856 in study SEP361-202
Time to Relapse During the 26-week Open-label Treatment Period for Subjects Who Demonstrated a Clinical Response to 4 Weeks of Treatment With SEP-363856
NA Days
insufficient number of participants with events
NA Days
insufficient number of participants with events

SECONDARY outcome

Timeframe: From the time of clinical response to relapse or censor (one day after the last study drug dose)

Population: Relapse population, which includes subjects who received at least one dose of open-label treatment and demonstrated a clinical response to 4 weeks of treatment with SEP-363856. Clinical response is defined as meeting (1) a decrease in PANSS total score of ≥ 20% from double-blind Baseline, AND (2) a CGI-S score ≤ 4. For PBO-SEP subjects, clinical response was evaluated at Week 4 of study SEP361-201. For SEP-SEP subjects, clinical response was evaluated at Week 4 of study SEP361-202.

Relapse is defined as the earliest occurrence of any of the following: - An increase in PANSS total score by ≥ 30% from the PANSS total score at clinical response and a CGI-S score ≥ 3; - Re-hospitalization for worsening of psychosis; - Emergence of suicidality, homicidality, and/or risk of harm to self or others.

Outcome measures

Outcome measures
Measure
SEP-363856
n=59 Participants
SEP-363856 capsule (25 mg, 50 mg, or 75 mg) once daily
SEP-SEP
n=51 Participants
Subjects who received SEP-363856 in study SEP361-201 and SEP-363856 in study SEP361-202
Rate of Relapse During the 26-week Open-label Treatment Period for Subjects Who Demonstrated a Clinical Response to 4 Weeks of Treatment With SEP-363856
12 Participants
11 Participants

SECONDARY outcome

Timeframe: Double-blind Baseline (DB BLN), Open-label Baseline (OL BLN), Week 26 (Wk 26)

Population: Subjects with PANSS data missing at a particular time point did not contribute to the summary for that time point.

PANSS is comprised of 30 items and 3 subscales (Positive, Negative, General Psychopathology). An anchored Likert scale from 1 - 7, where values of 2 and above indicate the presence of progressively more severe symptoms, is used to score each item. Individual items are then summed to determine scores for the 3 subscales, as well as a total score. PANSS Positive subscale score range: 7-49. PANSS Negative subscale score range: 7-49. PANSS General Psychopathology subscale score range: 16-112. PANSS total score range: 30-210.

Outcome measures

Outcome measures
Measure
SEP-363856
n=156 Participants
SEP-363856 capsule (25 mg, 50 mg, or 75 mg) once daily
SEP-SEP
Subjects who received SEP-363856 in study SEP361-201 and SEP-363856 in study SEP361-202
Changes From Double-blind Baseline of Study SEP361-201 and Open-label Baseline of Study SEP361-202 in Positive and Negative Syndrome Scale (PANSS) Total Score and Subscale Scores (Positive, Negative, and General Psychopathology)
Total Score: DB BLN Observed
101.5 Units on a scale
Standard Deviation 7.99
Changes From Double-blind Baseline of Study SEP361-201 and Open-label Baseline of Study SEP361-202 in Positive and Negative Syndrome Scale (PANSS) Total Score and Subscale Scores (Positive, Negative, and General Psychopathology)
Total Score: OL BLN Observed
83.1 Units on a scale
Standard Deviation 15.03
Changes From Double-blind Baseline of Study SEP361-201 and Open-label Baseline of Study SEP361-202 in Positive and Negative Syndrome Scale (PANSS) Total Score and Subscale Scores (Positive, Negative, and General Psychopathology)
Total Score: Wk 26 Observed
59.3 Units on a scale
Standard Deviation 12.45
Changes From Double-blind Baseline of Study SEP361-201 and Open-label Baseline of Study SEP361-202 in Positive and Negative Syndrome Scale (PANSS) Total Score and Subscale Scores (Positive, Negative, and General Psychopathology)
Total Score: Chg from DB BLN at Wk 26
-41.8 Units on a scale
Standard Deviation 13.98
Changes From Double-blind Baseline of Study SEP361-201 and Open-label Baseline of Study SEP361-202 in Positive and Negative Syndrome Scale (PANSS) Total Score and Subscale Scores (Positive, Negative, and General Psychopathology)
Total Score: Chg from OL BLN at Wk 26
-22.6 Units on a scale
Standard Deviation 15.48
Changes From Double-blind Baseline of Study SEP361-201 and Open-label Baseline of Study SEP361-202 in Positive and Negative Syndrome Scale (PANSS) Total Score and Subscale Scores (Positive, Negative, and General Psychopathology)
Positive SS: DB BLN Observed
25.7 Units on a scale
Standard Deviation 3.22
Changes From Double-blind Baseline of Study SEP361-201 and Open-label Baseline of Study SEP361-202 in Positive and Negative Syndrome Scale (PANSS) Total Score and Subscale Scores (Positive, Negative, and General Psychopathology)
Positive SS: OL BLN Observed
19.8 Units on a scale
Standard Deviation 4.96
Changes From Double-blind Baseline of Study SEP361-201 and Open-label Baseline of Study SEP361-202 in Positive and Negative Syndrome Scale (PANSS) Total Score and Subscale Scores (Positive, Negative, and General Psychopathology)
Positive SS: Wk 26 Observed
12.2 Units on a scale
Standard Deviation 3.72
Changes From Double-blind Baseline of Study SEP361-201 and Open-label Baseline of Study SEP361-202 in Positive and Negative Syndrome Scale (PANSS) Total Score and Subscale Scores (Positive, Negative, and General Psychopathology)
Positive SS: Chg from DB BLN at Wk 26
-13.5 Units on a scale
Standard Deviation 4.75
Changes From Double-blind Baseline of Study SEP361-201 and Open-label Baseline of Study SEP361-202 in Positive and Negative Syndrome Scale (PANSS) Total Score and Subscale Scores (Positive, Negative, and General Psychopathology)
Positive SS: Chg from OL BLN at Wk 26
-7.3 Units on a scale
Standard Deviation 5.37
Changes From Double-blind Baseline of Study SEP361-201 and Open-label Baseline of Study SEP361-202 in Positive and Negative Syndrome Scale (PANSS) Total Score and Subscale Scores (Positive, Negative, and General Psychopathology)
Negative SS: DB BLN Observed
25.4 Units on a scale
Standard Deviation 4.03
Changes From Double-blind Baseline of Study SEP361-201 and Open-label Baseline of Study SEP361-202 in Positive and Negative Syndrome Scale (PANSS) Total Score and Subscale Scores (Positive, Negative, and General Psychopathology)
Negative SS: OL BLN Observed
22.3 Units on a scale
Standard Deviation 4.38
Changes From Double-blind Baseline of Study SEP361-201 and Open-label Baseline of Study SEP361-202 in Positive and Negative Syndrome Scale (PANSS) Total Score and Subscale Scores (Positive, Negative, and General Psychopathology)
Negative SS: Wk 26 Observed
17.2 Units on a scale
Standard Deviation 4.10
Changes From Double-blind Baseline of Study SEP361-201 and Open-label Baseline of Study SEP361-202 in Positive and Negative Syndrome Scale (PANSS) Total Score and Subscale Scores (Positive, Negative, and General Psychopathology)
Negative SS: Chg from DB BLN at Wk 26
-8.4 Units on a scale
Standard Deviation 4.48
Changes From Double-blind Baseline of Study SEP361-201 and Open-label Baseline of Study SEP361-202 in Positive and Negative Syndrome Scale (PANSS) Total Score and Subscale Scores (Positive, Negative, and General Psychopathology)
Negative SS: Chg from OL BLN at Wk 26
-5.2 Units on a scale
Standard Deviation 4.20
Changes From Double-blind Baseline of Study SEP361-201 and Open-label Baseline of Study SEP361-202 in Positive and Negative Syndrome Scale (PANSS) Total Score and Subscale Scores (Positive, Negative, and General Psychopathology)
Gen-Psychopathology SS: DB BLN Observed
50.4 Units on a scale
Standard Deviation 5.01
Changes From Double-blind Baseline of Study SEP361-201 and Open-label Baseline of Study SEP361-202 in Positive and Negative Syndrome Scale (PANSS) Total Score and Subscale Scores (Positive, Negative, and General Psychopathology)
Gen-Psychopathology SS: OL BLN Observed
41.1 Units on a scale
Standard Deviation 7.93
Changes From Double-blind Baseline of Study SEP361-201 and Open-label Baseline of Study SEP361-202 in Positive and Negative Syndrome Scale (PANSS) Total Score and Subscale Scores (Positive, Negative, and General Psychopathology)
Gen-Psychopathology SS: Wk 26 Observed
30.0 Units on a scale
Standard Deviation 6.77
Changes From Double-blind Baseline of Study SEP361-201 and Open-label Baseline of Study SEP361-202 in Positive and Negative Syndrome Scale (PANSS) Total Score and Subscale Scores (Positive, Negative, and General Psychopathology)
Gen-Psychopathology SS: Chg from DB BLN at Wk 26
-19.9 Units on a scale
Standard Deviation 7.86
Changes From Double-blind Baseline of Study SEP361-201 and Open-label Baseline of Study SEP361-202 in Positive and Negative Syndrome Scale (PANSS) Total Score and Subscale Scores (Positive, Negative, and General Psychopathology)
Gen-Psychopathology SS: Chg from OL BLN at Wk 26
-10.2 Units on a scale
Standard Deviation 8.31

SECONDARY outcome

Timeframe: Double-blind (DB) Baseline, Open-label (OL) Baseline, Week 26

Population: Subjects with CGI-S score data missing at a particular time point did not contribute to the summary for that time point.

The CGI-S is a single-item clinician-rated assessment of the subject's current illness state on a 7-point scale (score range: 1-7), where a higher score is associated with greater illness severity.

Outcome measures

Outcome measures
Measure
SEP-363856
n=156 Participants
SEP-363856 capsule (25 mg, 50 mg, or 75 mg) once daily
SEP-SEP
Subjects who received SEP-363856 in study SEP361-201 and SEP-363856 in study SEP361-202
Change From Double-blind Baseline of Study SEP361-201 and Open-label Baseline of Study SEP361-202 in Clinical Global Impression - Severity (CGI-S) Score
CGI-S Score: DB Baseline Observed
5.0 Units on a scale
Standard Deviation 0.42
Change From Double-blind Baseline of Study SEP361-201 and Open-label Baseline of Study SEP361-202 in Clinical Global Impression - Severity (CGI-S) Score
CGI-S Score: OL Baseline Observed
4.0 Units on a scale
Standard Deviation 0.84
Change From Double-blind Baseline of Study SEP361-201 and Open-label Baseline of Study SEP361-202 in Clinical Global Impression - Severity (CGI-S) Score
CGI-S Score: Week 26 Observed
3.0 Units on a scale
Standard Deviation 0.74
Change From Double-blind Baseline of Study SEP361-201 and Open-label Baseline of Study SEP361-202 in Clinical Global Impression - Severity (CGI-S) Score
CGI-S Score: Change from DB Baseline at Week 26
-2.0 Units on a scale
Standard Deviation 0.82
Change From Double-blind Baseline of Study SEP361-201 and Open-label Baseline of Study SEP361-202 in Clinical Global Impression - Severity (CGI-S) Score
CGI-S Score: Change from OL Baseline at Week 26
-1.0 Units on a scale
Standard Deviation 0.91

SECONDARY outcome

Timeframe: Double-blind (DB) Baseline, Open-label (OL) Baseline, Week 26

Population: Subjects with BNSS total score data missing at a particular time point did not contribute to the summary for that time point.

The BNSS is a rating scale to measure the current level of severity of negative symptoms in schizophrenia and schizoaffective disorder. The measure is comprised of 13 individual items organized in 6 subscales. The 13 individual items provide a composite total score (ranging from 0 to 78). Each of the items are scored on a Likert-type 7-point scale from 0 - 6, where values of 0 indicates symptom is absent and a value of 6 means the symptom is a severe form.

Outcome measures

Outcome measures
Measure
SEP-363856
n=156 Participants
SEP-363856 capsule (25 mg, 50 mg, or 75 mg) once daily
SEP-SEP
Subjects who received SEP-363856 in study SEP361-201 and SEP-363856 in study SEP361-202
Change From Double-blind Baseline of Study SEP361-201 and Open-label Baseline of Study SEP361-202 in Brief Negative Symptom Scale (BNSS) Total Score
Total Score: DB Baseline Observed
38.4 Units on a scale
Standard Deviation 11.94
Change From Double-blind Baseline of Study SEP361-201 and Open-label Baseline of Study SEP361-202 in Brief Negative Symptom Scale (BNSS) Total Score
Total Score: OL Baseline Observed
33.0 Units on a scale
Standard Deviation 11.41
Change From Double-blind Baseline of Study SEP361-201 and Open-label Baseline of Study SEP361-202 in Brief Negative Symptom Scale (BNSS) Total Score
Total Score: Week 26 Observed
22.5 Units on a scale
Standard Deviation 11.83
Change From Double-blind Baseline of Study SEP361-201 and Open-label Baseline of Study SEP361-202 in Brief Negative Symptom Scale (BNSS) Total Score
Total Score: Change from DB Baseline at Week 26
-16.8 Units on a scale
Standard Deviation 12.42
Change From Double-blind Baseline of Study SEP361-201 and Open-label Baseline of Study SEP361-202 in Brief Negative Symptom Scale (BNSS) Total Score
Total Score: Change from OL Baseline at Week 26
-11.3 Units on a scale
Standard Deviation 9.69

SECONDARY outcome

Timeframe: Double-blind (DB) Baseline, Open-label (OL) Baseline, Week 26

Population: Subjects with MADRS total score data missing at a particular time point did not contribute to the summary for that time point.

The MADRS is a clinician-rated assessment of the subject's level of depression. The measure contains 10 items that measure apparent and reported sadness, inner tension, reduced sleep and appetite, difficulty concentrating, lassitude, inability to feel, and pessimistic and suicidal thoughts. Each item is scored in a range of 0 to 6 points, with higher scores indicating increased depressive symptoms. Total score will be equal to the sum of the 10 items (range between 0 and 60).

Outcome measures

Outcome measures
Measure
SEP-363856
n=156 Participants
SEP-363856 capsule (25 mg, 50 mg, or 75 mg) once daily
SEP-SEP
Subjects who received SEP-363856 in study SEP361-201 and SEP-363856 in study SEP361-202
Change From Double-blind Baseline of Study SEP361-201 and Open-label Baseline of Study SEP361-202 in Montgomery-Asberg Depression Rating Scale (MADRS) Total Score
Total Score: DB Baseline Observed
12.6 Units on a scale
Standard Deviation 7.25
Change From Double-blind Baseline of Study SEP361-201 and Open-label Baseline of Study SEP361-202 in Montgomery-Asberg Depression Rating Scale (MADRS) Total Score
Total Score: OL Baseline Observed
9.2 Units on a scale
Standard Deviation 6.33
Change From Double-blind Baseline of Study SEP361-201 and Open-label Baseline of Study SEP361-202 in Montgomery-Asberg Depression Rating Scale (MADRS) Total Score
Total Score: Week 26 Observed
4.4 Units on a scale
Standard Deviation 4.72
Change From Double-blind Baseline of Study SEP361-201 and Open-label Baseline of Study SEP361-202 in Montgomery-Asberg Depression Rating Scale (MADRS) Total Score
Total Score: Change from DB Baseline at Week 26
-8.1 Units on a scale
Standard Deviation 6.44
Change From Double-blind Baseline of Study SEP361-201 and Open-label Baseline of Study SEP361-202 in Montgomery-Asberg Depression Rating Scale (MADRS) Total Score
Total Score: Change from OL Baseline at Week 26
-4.5 Units on a scale
Standard Deviation 5.28

SECONDARY outcome

Timeframe: Week 26

Population: Subjects who received at least one dose of open-label treatment and had PANSS total score data available at Double-blind Baseline and Week 26 are included in analysis.

PANSS is comprised of 30 items and 3 subscales (Positive, Negative, General Psychopathology). An anchored Likert scale from 1 - 7, where values of 2 and above indicate the presence of progressively more severe symptoms, is used to score each item. Individual items are then summed to determine scores for the 3 subscales, as well as a total score. PANSS Positive subscale score range: 7-49. PANSS Negative subscale score range: 7-49. PANSS General Psychopathology subscale score range: 16-112. PANSS total score range: 30-210.

Outcome measures

Outcome measures
Measure
SEP-363856
n=53 Participants
SEP-363856 capsule (25 mg, 50 mg, or 75 mg) once daily
SEP-SEP
n=51 Participants
Subjects who received SEP-363856 in study SEP361-201 and SEP-363856 in study SEP361-202
Proportion of Subjects Who Achieved a Response, Defined as a 20% or Greater Improvement in Positive and Negative Syndrome Scale (PANSS) Total Score From Double-blind Baseline of Study SEP361-201
52 Participants
49 Participants

Adverse Events

SEP-363856

Serious events: 15 serious events
Other events: 39 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
SEP-363856
n=156 participants at risk
SEP-363856 capsule (25 mg, 50 mg, or 75 mg) once daily
Psychiatric disorders
Acute psychosis
0.64%
1/156 • Number of events 1 • From first dose of study drug to last study visit (27 weeks)
Psychiatric disorders
Depression
0.64%
1/156 • Number of events 1 • From first dose of study drug to last study visit (27 weeks)
Psychiatric disorders
Psychotic disorder
0.64%
1/156 • Number of events 1 • From first dose of study drug to last study visit (27 weeks)
Psychiatric disorders
Schizophrenia
7.1%
11/156 • Number of events 11 • From first dose of study drug to last study visit (27 weeks)
Psychiatric disorders
Suicidal ideation
0.64%
1/156 • Number of events 1 • From first dose of study drug to last study visit (27 weeks)
Reproductive system and breast disorders
Uterine haemorrhage
0.64%
1/156 • Number of events 1 • From first dose of study drug to last study visit (27 weeks)

Other adverse events

Other adverse events
Measure
SEP-363856
n=156 participants at risk
SEP-363856 capsule (25 mg, 50 mg, or 75 mg) once daily
Nervous system disorders
Headache
11.5%
18/156 • Number of events 36 • From first dose of study drug to last study visit (27 weeks)
Psychiatric disorders
Anxiety
5.1%
8/156 • Number of events 36 • From first dose of study drug to last study visit (27 weeks)
Psychiatric disorders
Insomnia
8.3%
13/156 • Number of events 24 • From first dose of study drug to last study visit (27 weeks)
Psychiatric disorders
Schizophrenia
6.4%
10/156 • Number of events 12 • From first dose of study drug to last study visit (27 weeks)

Additional Information

CNS Medical Director

Sunovion Pharmaceuticals Inc.

Phone: 1 866-503-6351

Results disclosure agreements

  • Principal investigator is a sponsor employee In the event the Study is part of a multi-center study, the first publication of the results of the Study shall be made in conjunction with the results of other participating study sites as a multi-center publication; provided however, if a multi-center publication is not forthcoming within twenty-four (24) months following completion of the Study at all sites, Institution and Investigator shall be free to publish.
  • Publication restrictions are in place

Restriction type: OTHER