Trial Outcomes & Findings for 2-Year Extension Study of Azeliragon in Subjects With Alzheimer's Disease (STEADFAST Extension) (NCT NCT02916056)

NCT ID: NCT02916056

Last Updated: 2021-06-01

Results Overview

Recruitment status

TERMINATED

Study phase

PHASE3

Target enrollment

297 participants

Primary outcome timeframe

up to 18 months

Results posted on

2021-06-01

Participant Flow

Eligible participants who completed TTP488-301 were enrolled into the TTP488-303 Open label extension from December 2016 through April 2018 in the United States and Canada.

Participant milestones

Participant milestones
Measure
Azeliragon 5 mg
Azeliragon (TTP488) 5mg orally once daily
Overall Study
STARTED
297
Overall Study
COMPLETED
0
Overall Study
NOT COMPLETED
297

Reasons for withdrawal

Reasons for withdrawal
Measure
Azeliragon 5 mg
Azeliragon (TTP488) 5mg orally once daily
Overall Study
Adverse Event
6
Overall Study
Lost to Follow-up
1
Overall Study
Other
12
Overall Study
Protocol Violation
1
Overall Study
Withdrawal by Subject
8
Overall Study
Study Terminated by Sponsor
269

Baseline Characteristics

2-Year Extension Study of Azeliragon in Subjects With Alzheimer's Disease (STEADFAST Extension)

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Azeliragon 5 mg
n=297 Participants
Azeliragon (TTP488) 5mg orally once daily
Age, Continuous
74.9 years
STANDARD_DEVIATION 8.43 • n=5 Participants
Sex: Female, Male
Female
144 Participants
n=5 Participants
Sex: Female, Male
Male
153 Participants
n=5 Participants
Ethnicity (NIH/OMB)
Hispanic or Latino
31 Participants
n=5 Participants
Ethnicity (NIH/OMB)
Not Hispanic or Latino
266 Participants
n=5 Participants
Ethnicity (NIH/OMB)
Unknown or Not Reported
0 Participants
n=5 Participants
Race (NIH/OMB)
American Indian or Alaska Native
0 Participants
n=5 Participants
Race (NIH/OMB)
Asian
6 Participants
n=5 Participants
Race (NIH/OMB)
Native Hawaiian or Other Pacific Islander
1 Participants
n=5 Participants
Race (NIH/OMB)
Black or African American
9 Participants
n=5 Participants
Race (NIH/OMB)
White
280 Participants
n=5 Participants
Race (NIH/OMB)
More than one race
1 Participants
n=5 Participants
Race (NIH/OMB)
Unknown or Not Reported
0 Participants
n=5 Participants

PRIMARY outcome

Timeframe: up to 18 months

Population: Safety Analysis Set

Outcome measures

Outcome measures
Measure
Azeliragon 5 mg
n=297 Participants
Azeliragon (TTP488) 5mg orally once daily
Number of Subjects With at Least One Treatment-Emergent Adverse Event
193 Participants

Adverse Events

Azeliragon 5 mg

Serious events: 25 serious events
Other events: 137 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
Azeliragon 5 mg
n=297 participants at risk
Azeliragon (TTP488) 5mg orally once daily
Nervous system disorders
Transient ischaemic attack
1.0%
3/297 • Adverse events were collected from consent through end of study participation. Duration of study participation was up to 456 days.
Nervous system disorders
Ataxia
0.34%
1/297 • Adverse events were collected from consent through end of study participation. Duration of study participation was up to 456 days.
Nervous system disorders
Cerebral infarction
0.34%
1/297 • Adverse events were collected from consent through end of study participation. Duration of study participation was up to 456 days.
Nervous system disorders
Complex partial seizures
0.34%
1/297 • Adverse events were collected from consent through end of study participation. Duration of study participation was up to 456 days.
Nervous system disorders
Convulsion
0.34%
1/297 • Adverse events were collected from consent through end of study participation. Duration of study participation was up to 456 days.
Nervous system disorders
Dysarthria
0.34%
1/297 • Adverse events were collected from consent through end of study participation. Duration of study participation was up to 456 days.
Nervous system disorders
Haemorrhagic stroke
0.34%
1/297 • Adverse events were collected from consent through end of study participation. Duration of study participation was up to 456 days.
Nervous system disorders
Ischaemic cerebral infarction
0.34%
1/297 • Adverse events were collected from consent through end of study participation. Duration of study participation was up to 456 days.
Nervous system disorders
Syncope
0.34%
1/297 • Adverse events were collected from consent through end of study participation. Duration of study participation was up to 456 days.
Injury, poisoning and procedural complications
Fall
0.67%
2/297 • Adverse events were collected from consent through end of study participation. Duration of study participation was up to 456 days.
Injury, poisoning and procedural complications
Pelvic fracture
0.67%
2/297 • Adverse events were collected from consent through end of study participation. Duration of study participation was up to 456 days.
Injury, poisoning and procedural complications
Femoral neck fracture
0.34%
1/297 • Adverse events were collected from consent through end of study participation. Duration of study participation was up to 456 days.
Injury, poisoning and procedural complications
Hip fracture
0.34%
1/297 • Adverse events were collected from consent through end of study participation. Duration of study participation was up to 456 days.
Injury, poisoning and procedural complications
Lumbar vertebral fracture
0.34%
1/297 • Adverse events were collected from consent through end of study participation. Duration of study participation was up to 456 days.
Injury, poisoning and procedural complications
Subdural haematoma
0.34%
1/297 • Adverse events were collected from consent through end of study participation. Duration of study participation was up to 456 days.
Infections and infestations
Bacterial prostatitis
0.34%
1/297 • Adverse events were collected from consent through end of study participation. Duration of study participation was up to 456 days.
Infections and infestations
Cellulitis
0.34%
1/297 • Adverse events were collected from consent through end of study participation. Duration of study participation was up to 456 days.
Infections and infestations
Enterocolitis infectious
0.34%
1/297 • Adverse events were collected from consent through end of study participation. Duration of study participation was up to 456 days.
Infections and infestations
Pneumonia
0.34%
1/297 • Adverse events were collected from consent through end of study participation. Duration of study participation was up to 456 days.
Infections and infestations
Pyelonephritis
0.34%
1/297 • Adverse events were collected from consent through end of study participation. Duration of study participation was up to 456 days.
Vascular disorders
Orthostatic hypotension
0.67%
2/297 • Adverse events were collected from consent through end of study participation. Duration of study participation was up to 456 days.
Vascular disorders
Aortic stenosis
0.34%
1/297 • Adverse events were collected from consent through end of study participation. Duration of study participation was up to 456 days.
Cardiac disorders
Aortic valve stenosis
0.34%
1/297 • Adverse events were collected from consent through end of study participation. Duration of study participation was up to 456 days.
Cardiac disorders
Atrial fibrillation
0.34%
1/297 • Adverse events were collected from consent through end of study participation. Duration of study participation was up to 456 days.
Cardiac disorders
Bradycardia
0.34%
1/297 • Adverse events were collected from consent through end of study participation. Duration of study participation was up to 456 days.
Ear and labyrinth disorders
Vertigo
0.34%
1/297 • Adverse events were collected from consent through end of study participation. Duration of study participation was up to 456 days.
Musculoskeletal and connective tissue disorders
Back pain
0.34%
1/297 • Adverse events were collected from consent through end of study participation. Duration of study participation was up to 456 days.
Renal and urinary disorders
Renal failure acute
0.34%
1/297 • Adverse events were collected from consent through end of study participation. Duration of study participation was up to 456 days.
Respiratory, thoracic and mediastinal disorders
Chronic obstructive pulmonary disease
0.34%
1/297 • Adverse events were collected from consent through end of study participation. Duration of study participation was up to 456 days.

Other adverse events

Other adverse events
Measure
Azeliragon 5 mg
n=297 participants at risk
Azeliragon (TTP488) 5mg orally once daily
Nervous system disorders
Dizziness
4.0%
12/297 • Adverse events were collected from consent through end of study participation. Duration of study participation was up to 456 days.
Nervous system disorders
Headache
2.4%
7/297 • Adverse events were collected from consent through end of study participation. Duration of study participation was up to 456 days.
Infections and infestations
Upper respiratory tract infection
3.0%
9/297 • Adverse events were collected from consent through end of study participation. Duration of study participation was up to 456 days.
Infections and infestations
Urinary tract infection
3.0%
9/297 • Adverse events were collected from consent through end of study participation. Duration of study participation was up to 456 days.
Psychiatric disorders
Depression
4.4%
13/297 • Adverse events were collected from consent through end of study participation. Duration of study participation was up to 456 days.
Psychiatric disorders
Insomnia
2.7%
8/297 • Adverse events were collected from consent through end of study participation. Duration of study participation was up to 456 days.
Injury, poisoning and procedural complications
Fall
9.8%
29/297 • Adverse events were collected from consent through end of study participation. Duration of study participation was up to 456 days.
Injury, poisoning and procedural complications
Laceration
2.0%
6/297 • Adverse events were collected from consent through end of study participation. Duration of study participation was up to 456 days.
Musculoskeletal and connective tissue disorders
Arthralgia
2.7%
8/297 • Adverse events were collected from consent through end of study participation. Duration of study participation was up to 456 days.
Respiratory, thoracic and mediastinal disorders
Cough
2.4%
7/297 • Adverse events were collected from consent through end of study participation. Duration of study participation was up to 456 days.
General disorders
Fatigue
2.4%
7/297 • Adverse events were collected from consent through end of study participation. Duration of study participation was up to 456 days.
General disorders
Gait disturbance
2.4%
7/297 • Adverse events were collected from consent through end of study participation. Duration of study participation was up to 456 days.
Investigations
Weight decreased
3.0%
9/297 • Adverse events were collected from consent through end of study participation. Duration of study participation was up to 456 days.
Vascular disorders
Hypertension
2.0%
6/297 • Adverse events were collected from consent through end of study participation. Duration of study participation was up to 456 days.

Additional Information

Ann Gooch PhD, VP Clinical Development & Regulatory Operations

vTv Therapeutics

Phone: 336-841-0300

Results disclosure agreements

  • Principal investigator is a sponsor employee Where PI requires the use of the Study Results for publication, the PI shall seek the Sponsor's written approval which shall not be unreasonably withheld; provided, however, that (i) Sponsor may require removal of any Confidential Information of Sponsor or may delay publication for a reasonable period of time in order to secure protection any IP Rights; and, (ii) as the Study is designed as a multi-center Study, no publication shall be made until after the first multi-center publication.
  • Publication restrictions are in place

Restriction type: OTHER