Stem Cell Therapy for Outer Retinal Degenerations

NCT ID: NCT02903576

Last Updated: 2020-07-22

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE1/PHASE2

Total Enrollment

15 participants

Study Classification

INTERVENTIONAL

Study Start Date

2015-08-31

Study Completion Date

2019-06-30

Brief Summary

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This study is a Phase I/II , open label,non randomized, prospective study to determine the safety of human embryonic stem cell derived Retinal pigmented epithelium (hESC RPE) sub retinal injections versus hESC RPE seeded on a polymeric substrate implanted in the sub retinal space,

Detailed Description

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To determine whether the surgical implantation of a human embryonic stem cell-derived retinal pigmented epithelium (hESC-RPE) monolayer seeded onto a polymeric versus hESC-RPE injections into the sub retinal space is a safe procedure.

6 Patients will receive hESC-RPE cell injections (100000 cells) in the sub retinal space (2 Dry Age-related macular degeneration (AMD), 2 Wet AMD with disciform scar and 2 with Stargardt's disease).

Also 5 patients Dry AMD, 5 patients with Wet AMD with disciform scar and 5 patients with Stargardt's disease with receive a subretinal implantation of the hESC-RPE seeded in a monolayer in a polymeric substrate.

Patients will be enrolled sequentially, and after the procedure the patients will be followed for 1 year.

Conditions

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Age Related Macular Degeneration Stargardt's Disease Exudative Age-related Macular Degeneration

Study Design

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Allocation Method

NON_RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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injection of hESC-RPE in suspension

6 patients will receive cell suspension injections on the sub retinal space prior to the surgeries, to access safety

Group Type ACTIVE_COMPARATOR

injection of hESC-RPE in suspension

Intervention Type PROCEDURE

The first six patients will receive a sub retinal injection of hESC-RPE in solution after a complete pars plana vitrectomy to access safety of the cell implant alone.

injection hESC-RPE seeded in a substrate

15 patients will receive a sub-retinal implantation of a polymeric scaffold seeded hesc- RPE in monolayer

Group Type ACTIVE_COMPARATOR

injection hESC-RPE seeded in a substrate

Intervention Type PROCEDURE

Fifteen patients will receive a sub-retinal implantation of embryonic stem cell derived retinal pigmented epithelium seeded in a polymeric substrate to access safety of substrate seeded with RPE

Interventions

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injection of hESC-RPE in suspension

The first six patients will receive a sub retinal injection of hESC-RPE in solution after a complete pars plana vitrectomy to access safety of the cell implant alone.

Intervention Type PROCEDURE

injection hESC-RPE seeded in a substrate

Fifteen patients will receive a sub-retinal implantation of embryonic stem cell derived retinal pigmented epithelium seeded in a polymeric substrate to access safety of substrate seeded with RPE

Intervention Type PROCEDURE

Other Intervention Names

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Human Embryonic Stem Cell - Retinal Pigmented Epithelium Human Embryonic Stem Cell seeded in a polymeric substrate

Eligibility Criteria

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Inclusion Criteria

* Patients with AMD ( Dry , Wet after failure of treatment, disciform scars)
* Patients with Stargardt's Disease BCVA on the selected eye: worse than 20/200

Exclusion Criteria

* Other ophthalmological diseases( Glaucoma, Diabetic Retinopathy, Previous retinal surgery, uveitis)
* Systemic diseases with contraindication for surgical procedures with local anaesthesia
Minimum Eligible Age

18 Years

Maximum Eligible Age

90 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Federal University of São Paulo

OTHER

Sponsor Role lead

Responsible Party

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Rubens Belfort Jr.

Full Professor of Ophthalmology

Responsibility Role PRINCIPAL_INVESTIGATOR

Principal Investigators

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Rubens Belfort, MD

Role: STUDY_CHAIR

Federal University of São Paulo UNIFESP

Locations

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Federal University of Sao Paulo

São Paulo, , Brazil

Site Status

Countries

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Brazil

Other Identifiers

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12018712.5.0000.5505

Identifier Type: -

Identifier Source: org_study_id

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