Trial Outcomes & Findings for Safety and Efficacy Study in Infant With SBS (NCT NCT02865122)

NCT ID: NCT02865122

Last Updated: 2021-10-12

Results Overview

Percent change in %PN/IV from baseline based on caloric intake

Recruitment status

TERMINATED

Study phase

PHASE2/PHASE3

Target enrollment

2 participants

Primary outcome timeframe

baseline and end of treatment or 24 weeks, whichever occurs first

Results posted on

2021-10-12

Participant Flow

Participant milestones

Participant milestones
Measure
NTRA-9620-A
NTRA-9620 Dose 1: 2 IU/kg To be dosed orally for 24 weeks, 4 times/day NTRA-9620: Oral daily dose
NTRA-9620-B
NTRA-9620 Dose 2 - 1 IU/kg To be dosed orally for 24 weeks, 4 times/day NTRA-9620: Oral daily dose
Placebo
Placebo To be dosed orally for 24 weeks, 4 times/day Placebo: Oral daily dose
Overall Study
STARTED
1
1
0
Overall Study
COMPLETED
0
1
0
Overall Study
NOT COMPLETED
1
0
0

Reasons for withdrawal

Reasons for withdrawal
Measure
NTRA-9620-A
NTRA-9620 Dose 1: 2 IU/kg To be dosed orally for 24 weeks, 4 times/day NTRA-9620: Oral daily dose
NTRA-9620-B
NTRA-9620 Dose 2 - 1 IU/kg To be dosed orally for 24 weeks, 4 times/day NTRA-9620: Oral daily dose
Placebo
Placebo To be dosed orally for 24 weeks, 4 times/day Placebo: Oral daily dose
Overall Study
Adverse Event
1
0
0

Baseline Characteristics

Safety and Efficacy Study in Infant With SBS

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
NTRA-9620-A
n=1 Participants
NTRA-9620 Dose 1 To be dosed orally for 24 weeks, 4 times/day NTRA-9620: Oral daily dose
NTRA-9620-B
n=1 Participants
NTRA-9620 Dose 2 To be dosed orally for 24 weeks, 4 times/day NTRA-9620: Oral daily dose
Placebo
Placebo To be dosed orally for 24 weeks, 4 times/day Placebo: Oral daily dose
Total
n=2 Participants
Total of all reporting groups
Age, Categorical
<=18 years
1 Participants
n=5 Participants
1 Participants
n=7 Participants
2 Participants
n=4 Participants
Age, Categorical
Between 18 and 65 years
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=4 Participants
Age, Categorical
>=65 years
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=4 Participants
Sex: Female, Male
Female
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
0 Participants
n=4 Participants
Sex: Female, Male
Male
1 Participants
n=5 Participants
1 Participants
n=7 Participants
0 Participants
n=5 Participants
2 Participants
n=4 Participants
Race (NIH/OMB)
American Indian or Alaska Native
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=4 Participants
Race (NIH/OMB)
Asian
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=4 Participants
Race (NIH/OMB)
Native Hawaiian or Other Pacific Islander
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=4 Participants
Race (NIH/OMB)
Black or African American
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=4 Participants
Race (NIH/OMB)
White
1 Participants
n=5 Participants
0 Participants
n=7 Participants
1 Participants
n=4 Participants
Race (NIH/OMB)
More than one race
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=4 Participants
Race (NIH/OMB)
Unknown or Not Reported
0 Participants
n=5 Participants
1 Participants
n=7 Participants
1 Participants
n=4 Participants
Region of Enrollment
United States
1 participants
n=5 Participants
1 participants
n=7 Participants
2 participants
n=4 Participants

PRIMARY outcome

Timeframe: baseline and end of treatment or 24 weeks, whichever occurs first

Population: During the course of the study only two (2) subjects were enrolled prior to discontinuation. Thus, no conclusions regarding the efficacy or safety (risk/benefit) of NTRA-9620 in the short bowel syndrome (SBS) population can be determined from this study.

Percent change in %PN/IV from baseline based on caloric intake

Outcome measures

Outcome data not reported

Adverse Events

NTRA-9620-A

Serious events: 1 serious events
Other events: 0 other events
Deaths: 0 deaths

NTRA-9620-B

Serious events: 0 serious events
Other events: 0 other events
Deaths: 0 deaths

Placebo

Serious events: 0 serious events
Other events: 0 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
NTRA-9620-A
n=1 participants at risk
NTRA-9620 Dose 1 To be dosed orally for 24 weeks, 4 times/day NTRA-9620: Oral daily dose
NTRA-9620-B
n=1 participants at risk
NTRA-9620 Dose 2 To be dosed orally for 24 weeks, 4 times/day NTRA-9620: Oral daily dose
Placebo
Placebo To be dosed orally for 24 weeks, 4 times/day Placebo: Oral daily dose
Respiratory, thoracic and mediastinal disorders
Apparent life threatening event
100.0%
1/1 • Number of events 5 • 6 months
Only one patient experienced Serious Adverse Events. There were no deaths in the study. There were no "Other" Adverse Events experienced in the study.
0.00%
0/1 • 6 months
Only one patient experienced Serious Adverse Events. There were no deaths in the study. There were no "Other" Adverse Events experienced in the study.
0/0 • 6 months
Only one patient experienced Serious Adverse Events. There were no deaths in the study. There were no "Other" Adverse Events experienced in the study.

Other adverse events

Adverse event data not reported

Additional Information

Miki Olshansky, Chief Executive Officer

Elgan Pharma Ltd.

Phone: 972-4-6098600

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place