Trial Outcomes & Findings for Neuromyelitis Optica (NMO) & Cetirizine (NCT NCT02865018)

NCT ID: NCT02865018

Last Updated: 2023-06-07

Results Overview

Relapses defined as "patient-reported symptoms or objectively observed signs typical of an acute inflammatory demyelinating event in the CNS, with duration of at least 24 hours, in the absence of fever or infection." The on study ARR was calculated as the number of relapses during the study divided by the length of time in the study.

Recruitment status

COMPLETED

Study phase

PHASE1/PHASE2

Target enrollment

16 participants

Primary outcome timeframe

Baseline and 1 year

Results posted on

2023-06-07

Participant Flow

Twenty-four potential participants were referred by treating physicians at the Corinne Goldsmith Dickinson Center for Multiple Sclerosis at Mount Sinai between April 2014 and February 2015. Sixteen were enrolled between Aprill 2014 and February 2016.

Participant milestones

Participant milestones
Measure
Cetirizine
10mg oral each day for 1 year
Overall Study
STARTED
16
Overall Study
COMPLETED
15
Overall Study
NOT COMPLETED
1

Reasons for withdrawal

Reasons for withdrawal
Measure
Cetirizine
10mg oral each day for 1 year
Overall Study
Withdrawal by Subject
1

Baseline Characteristics

Neuromyelitis Optica (NMO) & Cetirizine

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Cetirizine
n=16 Participants
10mg oral each day
Age, Continuous
36.5 years
n=93 Participants
Age, Customized
Age at Symptom onset
31.0 years
n=93 Participants
Sex: Female, Male
Female
15 Participants
n=93 Participants
Sex: Female, Male
Male
1 Participants
n=93 Participants
Positive NMO antibody in serum
13 Participants
n=93 Participants
Type of NMO Preventative Treatment at Enrollment
Rituximab
8 Participants
n=93 Participants
Type of NMO Preventative Treatment at Enrollment
Azathioprine
1 Participants
n=93 Participants
Type of NMO Preventative Treatment at Enrollment
Mycophenolate
7 Participants
n=93 Participants
Duration of Current Treatment
18.3 months
n=93 Participants
Number of Previous Preventative NMO treatment types
0
10 Participants
n=93 Participants
Number of Previous Preventative NMO treatment types
1
5 Participants
n=93 Participants
Number of Previous Preventative NMO treatment types
2
1 Participants
n=93 Participants
Oral Prednisone use at Enrollment
1 Participants
n=93 Participants
Total pre-study relapses
3.0 relapses
n=93 Participants
Total pre-study relapses while on current preventative treatment
0.0 relapses
n=93 Participants
Annualized Relapse Rate
0.0 relapses per treatment year
n=93 Participants

PRIMARY outcome

Timeframe: Baseline and 1 year

Relapses defined as "patient-reported symptoms or objectively observed signs typical of an acute inflammatory demyelinating event in the CNS, with duration of at least 24 hours, in the absence of fever or infection." The on study ARR was calculated as the number of relapses during the study divided by the length of time in the study.

Outcome measures

Outcome measures
Measure
Cetirizine
n=15 Participants
10mg oral each day for 1 year
Annualized Relapse Rate Before Cetirizine
Baseline
0.4 relapses per year
Standard Deviation 0.80
Annualized Relapse Rate Before Cetirizine
1 year
0.1 relapses per year
Standard Deviation 0.24

SECONDARY outcome

Timeframe: Baseline and 1 year

Sedation as measured by Epworth Sleepiness Scale. The test is a list of eight situations in which you rate your tendency to become sleepy on a scale of 0, no chance of dozing, to 3, high chance of dozing. Total score 0 to 24 from unlikelihood of abnormally sleep to excessively sleepy.

Outcome measures

Outcome measures
Measure
Cetirizine
n=15 Participants
10mg oral each day for 1 year
Epworth Sleepiness Scale
Baseline
6.5 units on a scale
Standard Deviation 5.33
Epworth Sleepiness Scale
1 year
6.9 units on a scale
Standard Deviation 4.50

SECONDARY outcome

Timeframe: Baseline and 1 year

Disability as measured by Expanded Disability Status Scale (EDSS). The EDSS provides a total score on a scale from 0 to 10, from normal function to lessening function with higher score, 10, being death due to MS.

Outcome measures

Outcome measures
Measure
Cetirizine
n=15 Participants
10mg oral each day for 1 year
Expanded Disability Status Scale (EDSS)
Baseline
3.9 units on a scale
Standard Deviation 2.18
Expanded Disability Status Scale (EDSS)
1 year
3.2 units on a scale
Standard Deviation 2.31

SECONDARY outcome

Timeframe: 6 months

Eotaxin - an eosinophil-specific chemoattractant in the blood. Immunological measures related to eosinophil activity. Eotaxin plasma levels.

Outcome measures

Outcome measures
Measure
Cetirizine
n=15 Participants
10mg oral each day for 1 year
Eotaxin Plasma Levels
19.25 pg/mL
Interval 1.44 to 27.75

Adverse Events

Cetirizine

Serious events: 0 serious events
Other events: 3 other events
Deaths: 0 deaths

Serious adverse events

Adverse event data not reported

Other adverse events

Other adverse events
Measure
Cetirizine
n=15 participants at risk
10mg oral each day for 1 year
Eye disorders
Unilateral eye pain with movement
6.7%
1/15
Eye disorders
Blurry vision with difficulty distinguishing colors
6.7%
1/15
Nervous system disorders
Neuro episode
13.3%
2/15

Additional Information

Ilana Katz Sand

Icahn School of Medicine at Mount Sinai, Corrine Goldsmith Dickinson Center for MS

Phone: 212-241-6854

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place