Health Economic Analysis of Islet Cell Transplantation for the Stabilization of the Severe Forms of Type 1 Diabetes

NCT ID: NCT02854696

Last Updated: 2022-06-24

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

UNKNOWN

Clinical Phase

PHASE3

Total Enrollment

42 participants

Study Classification

INTERVENTIONAL

Study Start Date

2016-07-07

Study Completion Date

2023-12-31

Brief Summary

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The main goal is to perform a cost-utility analysis to compare islet cell transplantation versus best medical treatment (defined as Sensor augmented pump therapy) for patients with brittle type1 diabetes.

Detailed Description

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The main goal is to perform a cost-utility analysis to compare islet cell transplantation versus best medical treatment (defined as Sensor augmented insulin pump therapy) for patients with brittle type1 diabetes.

Conditions

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Type 1 Diabetes

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Islet graft

Patients who receive islet graft Intervention : Procedure/Surgery

Group Type EXPERIMENTAL

Islet graft

Intervention Type PROCEDURE

Patients will be transplanted with pancreatic islet cells

Best medical care

Patients who continue their optimal medical treatment (insulin pump therapy coupled with real time continuous glucose monitoring) Intervention : insulin treatment

Group Type ACTIVE_COMPARATOR

best medical care

Intervention Type DRUG

Patients will continue their insulin treatment

Interventions

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Islet graft

Patients will be transplanted with pancreatic islet cells

Intervention Type PROCEDURE

best medical care

Patients will continue their insulin treatment

Intervention Type DRUG

Other Intervention Names

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islet cell transplantation insulin treatment

Eligibility Criteria

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Inclusion Criteria

* Suffering from diabetes since more than 5 years
* Patient with brittle type 1 diabetes despite an optimized insulin treatment and educational training will be included. A patient will be considered as experiencing a brittle type 1 diabetes if at least two criteria are present among: persistence of severe hypoglycemia, occurrence of ketoacidosis events without obvious etiology, diagnosis of unaware hypoglycemic episodes \< 3 mmol/l based on CGM or self-monitoring blood glucose data, a mean blood glucose standard deviation\>50%, MAGE index (Mean amplitude of glucose excursions)\>60 mg/dl, LBGI index (low blood glucose index)\>5, Clarke score≥4 or HYPOSCORE\>800.
* Insulin needs \< 0,85 U/kg/day
* HbA1c \< 12% ;
* No residual insulin secretion (plasmatic basal and stimulated C-peptide \< 0.3 ng/ml)
* Social Security membership or benefit from Social Security
* Patients who signed the consent form

Exclusion Criteria

* Hemostatic disorders, pre-existing liver disease (PAL, Gamma-GT, ASAT-ALAT \>2N) or vesicular lithiasis.


* Evolutive proliferative retinopathy, evolutive nephropathy (Glomerular filtration rate \<30 ml/min/1.73m2 and/or proteinuria \>0.5g/day), evolutive cardiopathy or obliterative arteriopathy with trophic cutaneous lesions.


* Hemoglobin \< 110mg/dL in women and \< 120 mg/dL in men, leuconeutropenia, thrombopenia, systemic infection including chronic hepatitis B, C and VIH, neoplasia disease and hypertension\>160/100 mmHg.
* Corticoid treatment (except for patient that benefited from a kidney graft with maintenance steroid therapy)
* Presence of anti-HLA antibody directed against the donor
* Positive B or T cells crossmatch
Minimum Eligible Age

18 Years

Maximum Eligible Age

65 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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University Hospital, Grenoble

OTHER

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Pierre-Yves BENHAMOU, MD, PhD

Role: PRINCIPAL_INVESTIGATOR

University Hospital, Grenoble

Locations

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University Hospital of Besançon

Besançon, , France

Site Status

university hospital of Clermont Ferrand

Clermont-Ferrand, , France

Site Status

Grenoble University Hospital

Grenoble, , France

Site Status

University hospital of Lille

Lille, , France

Site Status

University Hospital of Lyon

Lyon, , France

Site Status

University Hospital of Montpellier

Montpellier, , France

Site Status

University hospital of Nancy

Nancy, , France

Site Status

university hospital of Nantes

Nantes, , France

Site Status

APHP

Paris, , France

Site Status

University hospital of Strasbourg

Strasbourg, , France

Site Status

University Hospital of Geneva

Geneva, , Switzerland

Site Status

Countries

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France Switzerland

References

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Barton FB, Rickels MR, Alejandro R, Hering BJ, Wease S, Naziruddin B, Oberholzer J, Odorico JS, Garfinkel MR, Levy M, Pattou F, Berney T, Secchi A, Messinger S, Senior PA, Maffi P, Posselt A, Stock PG, Kaufman DB, Luo X, Kandeel F, Cagliero E, Turgeon NA, Witkowski P, Naji A, O'Connell PJ, Greenbaum C, Kudva YC, Brayman KL, Aull MJ, Larsen C, Kay TW, Fernandez LA, Vantyghem MC, Bellin M, Shapiro AM. Improvement in outcomes of clinical islet transplantation: 1999-2010. Diabetes Care. 2012 Jul;35(7):1436-45. doi: 10.2337/dc12-0063.

Reference Type BACKGROUND
PMID: 22723582 (View on PubMed)

Beckwith J, Nyman JA, Flanagan B, Schrover R, Schuurman HJ. A health economic analysis of clinical islet transplantation. Clin Transplant. 2012 Jan-Feb;26(1):23-33. doi: 10.1111/j.1399-0012.2011.01411.x. Epub 2011 Feb 16.

Reference Type BACKGROUND
PMID: 21323736 (View on PubMed)

Bellin MD, Kandaswamy R, Parkey J, Zhang HJ, Liu B, Ihm SH, Ansite JD, Witson J, Bansal-Pakala P, Balamurugan AN, Papas KK, Sutherland DE, Moran A, Hering BJ. Prolonged insulin independence after islet allotransplants in recipients with type 1 diabetes. Am J Transplant. 2008 Nov;8(11):2463-70. doi: 10.1111/j.1600-6143.2008.02404.x. Epub 2008 Sep 19.

Reference Type BACKGROUND
PMID: 18808408 (View on PubMed)

Badet L, Benhamou PY, Wojtusciszyn A, Baertschiger R, Milliat-Guittard L, Kessler L, Penfornis A, Thivolet C, Renard E, Bosco D, Morel P, Morelon E, Bayle F, Colin C, Berney T; GRAGIL Group. Expectations and strategies regarding islet transplantation: metabolic data from the GRAGIL 2 trial. Transplantation. 2007 Jul 15;84(1):89-96. doi: 10.1097/01.tp.0000268511.64428.d8.

Reference Type BACKGROUND
PMID: 17627243 (View on PubMed)

Lablanche S, David-Tchouda S, Margier J, Schir E, Wojtusciszyn A, Borot S, Kessler L, Morelon E, Thivolet C, Pattou F, Vantyghem MC, Berney T, Benhamou PY. Randomised, prospective, medico-economic nationwide French study of islet transplantation in patients with severely unstable type 1 diabetes: the STABILOT study protocol. BMJ Open. 2017 Feb 20;7(2):e013434. doi: 10.1136/bmjopen-2016-013434.

Reference Type DERIVED
PMID: 28219959 (View on PubMed)

Other Identifiers

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38RC14.453

Identifier Type: -

Identifier Source: org_study_id

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