Phase 1 Study to Evaluate the Safety, Pharmacokinetics and Pharmacodynamics of H3B-6527 in Participants With Advanced Hepatocellular Carcinoma

NCT ID: NCT02834780

Last Updated: 2023-11-13

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE1

Total Enrollment

128 participants

Study Classification

INTERVENTIONAL

Study Start Date

2016-12-28

Study Completion Date

2022-02-23

Brief Summary

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The purpose of this study is to determine the maximum tolerated dose (MTD) and recommended Phase 2 dose (RP2D) of H3B-6527, and to assess the safety, tolerability and pharmacokinetics of H3B-6527.

Detailed Description

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Conditions

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Advanced Hepatocellular Carcinoma Hepatocellular Carcinoma Liver Cancer Liver Neoplasms Hepatic Cancer Hepatic Carcinoma

Study Design

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Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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H3B-6527 (escalation and expansion)

Hepatocellular Carcinoma

Group Type EXPERIMENTAL

H3B-6527

Intervention Type DRUG

H3B-6527 by mouth once or twice daily at specified doses.

Interventions

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H3B-6527

H3B-6527 by mouth once or twice daily at specified doses.

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

1. Participants with hepatocellular carcinoma.
2. Must have had at least one prior standard-of-care therapy, unless contraindicated.
3. Eastern Cooperative Oncology Group (ECOG) Performance Status of 0 or 1.
4. Must be willing to undergo a biopsy up to 8 weeks before administration of H3B-6527 on Cycle 1 Day 1 for part 2 (dose expansion).
5. Adequate bone marrow and organ function.

Exclusion Criteria

1. Uncontrolled significant active infections, except hepatitis B virus (HBV) or hepatitis C virus (HCV).
2. Known human immunodeficiency virus infection.
3. Presence of gastric or esophageal varices requiring active treatment.
4. Previous treatment with a selective FGF19-FGFR4 targeted therapy.
5. Females of childbearing potential, or males who have not had a successful vasectomy, who are unable or unwilling to follow adequate contraceptive measures.
6. Hereditary problems of galactose intolerance, the Lapp lactase deficiency, or glucose-galactose malabsorption.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Eisai Inc.

INDUSTRY

Sponsor Role collaborator

H3 Biomedicine Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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USC/Norris Comprehensive Cancer Center

Los Angeles, California, United States

Site Status

Hoag Memorial Hospital Presbyterian

Newport Beach, California, United States

Site Status

UC Irvine Medical Center

Orange, California, United States

Site Status

UCLA Medical Center

Santa Monica, California, United States

Site Status

Georgetown Unversity Lombardi Comprehensive Cancer Center

Washington D.C., District of Columbia, United States

Site Status

Northwestern Unversity

Chicago, Illinois, United States

Site Status

Massachusetts General Hospital

Boston, Massachusetts, United States

Site Status

Barbara Ann Karmanos Cancer Institute

Detroit, Michigan, United States

Site Status

John theurer Cancer Center at Hackensack University Medical Center

Hackensack, New Jersey, United States

Site Status

Duke University Cancer Center

Durham, North Carolina, United States

Site Status

University of Cincinnati Cancer Institute

Cincinnati, Ohio, United States

Site Status

University of Pennsylsvania - Perelman Cancer Center for Advanced Medicine

Philadelphia, Pennsylvania, United States

Site Status

Simmons Comprehensive Cancer Center

Dallas, Texas, United States

Site Status

University of Texas Southwestern Medical Center

Dallas, Texas, United States

Site Status

McGuire VA Medical Center

Richmond, Virginia, United States

Site Status

UCL Cliniques universitaires Saint-Luc

Woluwe-Saint-Lambert, Brussels Capital, Belgium

Site Status

Universitair Ziekenhuis Gent

Ghent, , Belgium

Site Status

Cross Cancer Institute

Edmonton, Alberta, Canada

Site Status

Jurvanski Cancer Center

Hamilton, Ontario, Canada

Site Status

Institut Bergonié

Bordeaux, , France

Site Status

Centre Oscar Lambret

Lille, , France

Site Status

Hôpital Haut-Lévêque - CHU de Bordeaux

Pessac, , France

Site Status

Centre Eugène Marquis

Rennes, , France

Site Status

IRCCS Istituto Scientifico Romagnolo per lo studio e la cura dei tumori - U.O. di Oncologia Medica

Meldola, , Italy

Site Status

IRCCS Ospedale San Raffaele S.r.l. - PPDS

Milan, , Italy

Site Status

Azienda Ospedaliero Universitaria - Policlinico di Modena

Modena, , Italy

Site Status

Altay Regional Oncology Center

Barnaul, Altay, Re, Russia

Site Status

Russian Oncology Research Center n a N N Blokhin

Moscow, , Russia

Site Status

Omsk Regional Oncology Center

Omsk, , Russia

Site Status

Railway Clinical Hospital JSC RZhD

Saint Petersburg, , Russia

Site Status

City Clinical Oncology Dispensary

Saint Petersburg, , Russia

Site Status

National University Cancer Insitute

Singapore, , Singapore

Site Status

Asan Medical Center

Seoul, , South Korea

Site Status

Hospital Universitario Marques de Valdecilla

Santander, Cantabria, Spain

Site Status

Clínica Universidad de Navarra

Pamplona, Navarre, Spain

Site Status

Hospital Universitario de Badajoz

Badajoz, , Spain

Site Status

Hospital Universitario Vall d'Hebron

Barcelona, , Spain

Site Status

General Universitario Gregorio Maranon

Madrid, , Spain

Site Status

START Madrid FJD, Hospital Universitario Fundacion Jimenez Diaz

Madrid, , Spain

Site Status

Hospital Universitario HM Sanchinarro

Madrid, , Spain

Site Status

Hospital Universitario Virgen del Rocio

Seville, , Spain

Site Status

Taichung Veterans General Hospital

Taichung, , Taiwan

Site Status

National Cheng Kung University Hospital

Tainan City, , Taiwan

Site Status

Sarah Cannon Research Institute UK - SCRI - PPDS

London, , United Kingdom

Site Status

Countries

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United States Belgium Canada France Italy Russia Singapore South Korea Spain Taiwan United Kingdom

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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2016-001915-19

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

H3B-6527-G000-101

Identifier Type: -

Identifier Source: org_study_id

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