Trial Outcomes & Findings for Safety and Efficacy of KPI-121 in Subjects With Postsurgical Inflammation and Pain (NCT NCT02793817)

NCT ID: NCT02793817

Last Updated: 2020-12-16

Results Overview

Number and percentage of subjects with complete resolution of AC cells in the surgical eye (study eye) at Day 8 maintained through Day 15, without receiving rescue medication prior to Day 15, for KPI-121 1% dosed twice daily (BID) compared with vehicle dosed BID. Investigators were asked to grade AC cell based on the following scale wherein higher scores indicate a higher degree of cells present and a decrease across time indicates the condition is getting better. Anterior Chamber Cells 0 = No cells seen 1. = 1 - 5 cells 2. = 6 - 15 cells 3. = 16 - 30 cells 4. = greater than 30 cells

Recruitment status

COMPLETED

Study phase

PHASE3

Target enrollment

520 participants

Primary outcome timeframe

Visit 5 (Day 8) maintained through Visit 6 (Day 15)

Results posted on

2020-12-16

Participant Flow

Participant milestones

Participant milestones
Measure
KPI-121 1.0% Ophthalmic Suspension
dosed BID KPI-121 1% Ophthalmic Suspension dosed BID
Vehicle of KPI-121 Ophthalmic Suspension
dosed BID Vehicle of KPI-121 Ophthalmic Suspension dosed BID
Overall Study
STARTED
261
259
Overall Study
COMPLETED
258
254
Overall Study
NOT COMPLETED
3
5

Reasons for withdrawal

Withdrawal data not reported

Baseline Characteristics

Safety and Efficacy of KPI-121 in Subjects With Postsurgical Inflammation and Pain

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
KPI-121 1.0% Ophthalmic Suspension
n=261 Participants
dosed BID KPI-121 1% Ophthalmic Suspension dosed BID
Vehicle of KPI-121 Ophthalmic Suspension
n=259 Participants
dosed BID Vehicle of KPI-121 Ophthalmic Suspension dosed BID
Total
n=520 Participants
Total of all reporting groups
Age, Continuous
67.5 years
n=5 Participants
69.3 years
n=7 Participants
68.4 years
n=5 Participants
Sex: Female, Male
Female
144 Participants
n=5 Participants
144 Participants
n=7 Participants
288 Participants
n=5 Participants
Sex: Female, Male
Male
117 Participants
n=5 Participants
115 Participants
n=7 Participants
232 Participants
n=5 Participants
Ethnicity (NIH/OMB)
Hispanic or Latino
38 Participants
n=5 Participants
36 Participants
n=7 Participants
74 Participants
n=5 Participants
Ethnicity (NIH/OMB)
Not Hispanic or Latino
223 Participants
n=5 Participants
223 Participants
n=7 Participants
446 Participants
n=5 Participants
Ethnicity (NIH/OMB)
Unknown or Not Reported
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Race (NIH/OMB)
American Indian or Alaska Native
1 Participants
n=5 Participants
1 Participants
n=7 Participants
2 Participants
n=5 Participants
Race (NIH/OMB)
Asian
17 Participants
n=5 Participants
19 Participants
n=7 Participants
36 Participants
n=5 Participants
Race (NIH/OMB)
Native Hawaiian or Other Pacific Islander
2 Participants
n=5 Participants
2 Participants
n=7 Participants
4 Participants
n=5 Participants
Race (NIH/OMB)
Black or African American
27 Participants
n=5 Participants
24 Participants
n=7 Participants
51 Participants
n=5 Participants
Race (NIH/OMB)
White
206 Participants
n=5 Participants
207 Participants
n=7 Participants
413 Participants
n=5 Participants
Race (NIH/OMB)
More than one race
2 Participants
n=5 Participants
0 Participants
n=7 Participants
2 Participants
n=5 Participants
Race (NIH/OMB)
Unknown or Not Reported
6 Participants
n=5 Participants
6 Participants
n=7 Participants
12 Participants
n=5 Participants
Region of Enrollment
United States
261 participants
n=5 Participants
259 participants
n=7 Participants
520 participants
n=5 Participants

PRIMARY outcome

Timeframe: Visit 5 (Day 8) maintained through Visit 6 (Day 15)

Population: Intent to Treat - All subjects randomized

Number and percentage of subjects with complete resolution of AC cells in the surgical eye (study eye) at Day 8 maintained through Day 15, without receiving rescue medication prior to Day 15, for KPI-121 1% dosed twice daily (BID) compared with vehicle dosed BID. Investigators were asked to grade AC cell based on the following scale wherein higher scores indicate a higher degree of cells present and a decrease across time indicates the condition is getting better. Anterior Chamber Cells 0 = No cells seen 1. = 1 - 5 cells 2. = 6 - 15 cells 3. = 16 - 30 cells 4. = greater than 30 cells

Outcome measures

Outcome measures
Measure
KPI-121 1% Ophthalmic Suspension
n=261 Participants
KPI-121 1% Ophthalmic Suspension dosed BID
Vehicle of KPI-121 1% Ophthalmic Suspension
n=259 Participants
Vehicle of KPI-121 1% Ophthalmic Suspension dosed BID
Complete Resolution of Anterior Chamber (AC) Cells at Day 8
54 Participants
32 Participants

PRIMARY outcome

Timeframe: Visit 5 (Day 8) maintained through Visit 6 (Day 15)

Population: Intent to Treat - All subjects randomized

Number and percentage of subjects with complete resolution of ocular pain in the surgical eye (study eye) at Day 8 maintained through Day 15, without receiving rescue medication prior to Day 15, for KPI-121 1% dosed twice daily (BID) compared with vehicle dosed BID. Subjects were given the Subject-Rated Ocular Pain Assessment to subjectively rate their pain at Days 1, 4, 8, 15, and the follow-up visit between Days 17 and 19. Higher scores were worse outcomes. The following scoring scale was used for ocular pain: 0 = None 1. = Minimal 2. = Mild 3. = Moderate 4. = Moderately Severe 5. = Severe

Outcome measures

Outcome measures
Measure
KPI-121 1% Ophthalmic Suspension
n=261 Participants
KPI-121 1% Ophthalmic Suspension dosed BID
Vehicle of KPI-121 1% Ophthalmic Suspension
n=259 Participants
Vehicle of KPI-121 1% Ophthalmic Suspension dosed BID
Complete Resolution of Ocular Pain at Day 8
149 Participants
96 Participants

SECONDARY outcome

Timeframe: Visit 4 (Day 4) maintained through Visit 6 (Day 15)

Population: Intent to Treat - All subjects randomized

Number and percentage of subjects with complete resolution of ocular pain in the surgical eye (study eye) at Day 4 maintained through Day 15, without receiving rescue medication prior to Day 15, for KPI-121 1% dosed twice daily (BID) compared with vehicle dosed BID. Subjects were given the Subject-Rated Ocular Pain Assessment to subjectively rate their pain at Days 1, 4, 8, 15, and the follow-up visit between Days 17 and 19. Higher scores were worse outcomes. The following scoring scale was used for ocular pain: 0 = None 1. = Minimal 2. = Mild 3. = Moderate 4. = Moderately Severe 5. = Severe

Outcome measures

Outcome measures
Measure
KPI-121 1% Ophthalmic Suspension
n=261 Participants
KPI-121 1% Ophthalmic Suspension dosed BID
Vehicle of KPI-121 1% Ophthalmic Suspension
n=259 Participants
Vehicle of KPI-121 1% Ophthalmic Suspension dosed BID
Complete Resolution of Ocular Pain at Day 4
109 Participants
64 Participants

SECONDARY outcome

Timeframe: Visit 4 (Day 4) maintained through Visit 6 (Day 15)

Population: Intent to Treat - All subjects randomized

Number and percentage of subjects with complete resolution of AC flare in the surgical eye (study eye) at Day 4 maintained through Day 15, without receiving rescue medication prior to Day 15, for KPI-121 1% dosed twice daily (BID) compared with vehicle dosed BID. Investigators were asked to grade AC flare based on the following scale wherein higher scores indicate a higher degree of flare present and a decrease across time indicates the condition is getting better. Anterior Chamber Flare 0 = None 1. = Mild (trace to clearly noticeable, visible) 2. = Moderate (without plastic aqueous humor) 3. = Marked (with plastic aqueous humor) 4. = Severe (with fibrin deposits and/or clots)

Outcome measures

Outcome measures
Measure
KPI-121 1% Ophthalmic Suspension
n=261 Participants
KPI-121 1% Ophthalmic Suspension dosed BID
Vehicle of KPI-121 1% Ophthalmic Suspension
n=259 Participants
Vehicle of KPI-121 1% Ophthalmic Suspension dosed BID
Complete Resolution of Anterior Chamber (AC) Flare at Day 4
113 Participants
63 Participants

SECONDARY outcome

Timeframe: Visit 1 (Baseline) and Visit 4 (Day 4)

Population: Intent to Treat - All subjects randomized

The difference in mean changes from BL in AC cell count grade at Day 4 for KPI-121 1% dosed twice daily (BID) compared with vehicle dosed BID. Investigators were asked to grade AC cell based on the following scale wherein higher scores indicate a higher degree of cells present and a decrease across time indicates the condition is getting better. Anterior Chamber Cells 0 = No cells seen 1. = 1 - 5 cells 2. = 6 - 15 cells 3. = 16 - 30 cells 4. = greater than 30 cells

Outcome measures

Outcome measures
Measure
KPI-121 1% Ophthalmic Suspension
n=258 Participants
KPI-121 1% Ophthalmic Suspension dosed BID
Vehicle of KPI-121 1% Ophthalmic Suspension
n=257 Participants
Vehicle of KPI-121 1% Ophthalmic Suspension dosed BID
Change From Baseline (BL) Anterior Chamber (AC) Cells at Day 4
-0.7 score on a scale
Standard Deviation 0.84
-0.5 score on a scale
Standard Deviation 0.91

POST_HOC outcome

Timeframe: Visit 1 (Baseline) and Visit 5 (Day 8)

Population: Intent to Treat - All subjects randomized

The difference in mean changes from BL in AC cell count grade at Day 8 for KPI-121 1% dosed twice daily (BID) compared with vehicle dosed BID. Investigators were asked to grade AC cell based on the following scale wherein higher scores indicate a higher degree of cells present and a decrease across time indicates the condition is getting better. Anterior Chamber Cells 0 = No cells seen 1. = 1 - 5 cells 2. = 6 - 15 cells 3. = 16 - 30 cells 4. = greater than 30 cells

Outcome measures

Outcome measures
Measure
KPI-121 1% Ophthalmic Suspension
n=258 Participants
KPI-121 1% Ophthalmic Suspension dosed BID
Vehicle of KPI-121 1% Ophthalmic Suspension
n=257 Participants
Vehicle of KPI-121 1% Ophthalmic Suspension dosed BID
Change From Baseline (BL) Anterior Chamber (AC) Cells at Day 8
-1.3 score on a scale
Standard Deviation 0.90
-1.0 score on a scale
Standard Deviation 0.94

POST_HOC outcome

Timeframe: Visit 1 (Baseline) and Visit 6 (Day 15)

Population: Intent to Treat - All subjects randomized

The difference in mean changes from BL in AC cell count grade at Day 15 for KPI-121 1% dosed twice daily (BID) compared with vehicle dosed BID. Investigators were asked to grade AC cell based on the following scale wherein higher scores indicate a higher degree of cells present and a decrease across time indicates the condition is getting better. Anterior Chamber Cells 0 = No cells seen 1. = 1 - 5 cells 2. = 6 - 15 cells 3. = 16 - 30 cells 4. = greater than 30 cells

Outcome measures

Outcome measures
Measure
KPI-121 1% Ophthalmic Suspension
n=257 Participants
KPI-121 1% Ophthalmic Suspension dosed BID
Vehicle of KPI-121 1% Ophthalmic Suspension
n=254 Participants
Vehicle of KPI-121 1% Ophthalmic Suspension dosed BID
Change From Baseline (BL) Anterior Chamber (AC) Cells at Day 15
-1.8 score on a scale
Standard Deviation 0.84
-1.6 score on a scale
Standard Deviation 0.87

Adverse Events

KPI-121 1% Ophthalmic Suspension

Serious events: 1 serious events
Other events: 18 other events
Deaths: 0 deaths

Vehicle of KPI-121 1% Ophthalmic Suspension

Serious events: 2 serious events
Other events: 21 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
KPI-121 1% Ophthalmic Suspension
n=261 participants at risk
KPI-121 1% Ophthalmic Suspension dosed BID
Vehicle of KPI-121 1% Ophthalmic Suspension
n=259 participants at risk
Vehicle of KPI-121 1% Ophthalmic Suspension dosed BID
Hepatobiliary disorders
Cholecystitis
0.38%
1/261 • Number of events 1 • Adverse events were collected from the time a subjects signed the informed consent until they exited the study at the end of Visit 7 (up to 18 days).
0.00%
0/259 • Adverse events were collected from the time a subjects signed the informed consent until they exited the study at the end of Visit 7 (up to 18 days).
Cardiac disorders
Angina pectoris
0.00%
0/261 • Adverse events were collected from the time a subjects signed the informed consent until they exited the study at the end of Visit 7 (up to 18 days).
0.39%
1/259 • Number of events 1 • Adverse events were collected from the time a subjects signed the informed consent until they exited the study at the end of Visit 7 (up to 18 days).
Vascular disorders
Hypertensive emergency
0.00%
0/261 • Adverse events were collected from the time a subjects signed the informed consent until they exited the study at the end of Visit 7 (up to 18 days).
0.39%
1/259 • Number of events 1 • Adverse events were collected from the time a subjects signed the informed consent until they exited the study at the end of Visit 7 (up to 18 days).
Nervous system disorders
erebrovascular Accident
0.00%
0/261 • Adverse events were collected from the time a subjects signed the informed consent until they exited the study at the end of Visit 7 (up to 18 days).
0.39%
1/259 • Number of events 1 • Adverse events were collected from the time a subjects signed the informed consent until they exited the study at the end of Visit 7 (up to 18 days).

Other adverse events

Other adverse events
Measure
KPI-121 1% Ophthalmic Suspension
n=261 participants at risk
KPI-121 1% Ophthalmic Suspension dosed BID
Vehicle of KPI-121 1% Ophthalmic Suspension
n=259 participants at risk
Vehicle of KPI-121 1% Ophthalmic Suspension dosed BID
Eye disorders
Cystoid macular oedema
1.1%
3/261 • Number of events 3 • Adverse events were collected from the time a subjects signed the informed consent until they exited the study at the end of Visit 7 (up to 18 days).
1.2%
3/259 • Number of events 4 • Adverse events were collected from the time a subjects signed the informed consent until they exited the study at the end of Visit 7 (up to 18 days).
Eye disorders
Eye pain
1.1%
3/261 • Number of events 3 • Adverse events were collected from the time a subjects signed the informed consent until they exited the study at the end of Visit 7 (up to 18 days).
2.3%
6/259 • Number of events 6 • Adverse events were collected from the time a subjects signed the informed consent until they exited the study at the end of Visit 7 (up to 18 days).
Eye disorders
Posterior capsule opacification
1.1%
3/261 • Number of events 3 • Adverse events were collected from the time a subjects signed the informed consent until they exited the study at the end of Visit 7 (up to 18 days).
1.5%
4/259 • Number of events 4 • Adverse events were collected from the time a subjects signed the informed consent until they exited the study at the end of Visit 7 (up to 18 days).
General disorders
Instilation site pain
0.38%
1/261 • Number of events 2 • Adverse events were collected from the time a subjects signed the informed consent until they exited the study at the end of Visit 7 (up to 18 days).
1.2%
3/259 • Number of events 4 • Adverse events were collected from the time a subjects signed the informed consent until they exited the study at the end of Visit 7 (up to 18 days).
Infections and infestations
Nasopharyngitis
1.5%
4/261 • Number of events 4 • Adverse events were collected from the time a subjects signed the informed consent until they exited the study at the end of Visit 7 (up to 18 days).
0.39%
1/259 • Number of events 1 • Adverse events were collected from the time a subjects signed the informed consent until they exited the study at the end of Visit 7 (up to 18 days).
Nervous system disorders
Headache
1.5%
4/261 • Number of events 4 • Adverse events were collected from the time a subjects signed the informed consent until they exited the study at the end of Visit 7 (up to 18 days).
1.5%
4/259 • Number of events 4 • Adverse events were collected from the time a subjects signed the informed consent until they exited the study at the end of Visit 7 (up to 18 days).

Additional Information

Head, Clinical Operations

Kala Pharmaceuticals, Inc.

Phone: 781-996-5252

Results disclosure agreements

  • Principal investigator is a sponsor employee No submission for publication or public disclosure will be made by the PI until after the publication of the results of the multi-center clinical trial by the Sponsor. Thereafter, PI shall provide KALA with an advance copy of any proposed publication or public disclosure at least sixty (60) days prior to the planned date of submission or disclosure and KALA shall have forty-five (45) days from the date of its receipt to recommend changes.
  • Publication restrictions are in place

Restriction type: OTHER