Vadastuximab Talirine (SGN-CD33A; 33A) Combined With Azacitidine or Decitabine in Older Patients With Newly Diagnosed Acute Myeloid Leukemia

NCT ID: NCT02785900

Last Updated: 2018-12-12

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE3

Total Enrollment

240 participants

Study Classification

INTERVENTIONAL

Study Start Date

2016-05-31

Study Completion Date

2017-10-03

Brief Summary

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The purpose of this study in AML patients is to test whether vadastuximab talirine (SGN-CD33A; 33A) combined with either azacitidine or decitabine improves remission rates and extends overall survival as compared to placebo combined with either azacitidine or decitabine.

Detailed Description

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Hypomethylating agents (HMAs), such as decitabine or azacitidine, are considered a standard treatment for older patients with AML. The primary goals of this study are to test whether patients treated with an HMA (either decitabine or azacitidine) in combination with 33A will have better anti-tumor activity and/or survive longer than patients treated with an HMA in combination with placebo.

Patients who meet eligibility criteria will be randomly assigned to one of two treatment groups: 1) 33A plus HMA (Experimental Arm); or 2) placebo plus HMA (Comparator Arm). In addition to evaluating survival and remission rates, the minimal residual disease (MRD)-negative remission rate, duration of remission, event free- and leukemia-free survival, and safety and tolerability will be compared between arms.

Conditions

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Acute Myeloid Leukemia

Keywords

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Antibodies, monoclonal Antibody drug conjugate Antigens, cluster of differentiation 33 (CD33) Drug therapy Immunotherapy

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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33A + HMA

33A plus azacitidine or decitabine

Group Type EXPERIMENTAL

33A

Intervention Type DRUG

33A, 10 mcg/kg, every 4 weeks via intravenous (IV) push

azacitidine

Intervention Type DRUG

75 mg/m2 given subcutaneously (SC) or IV x 7 days, every 4 weeks

decitabine

Intervention Type DRUG

20 mg/m2 given IV x 5 days, every 4 weeks

placebo + HMA

placebo plus azacitidine or decitabine

Group Type ACTIVE_COMPARATOR

placebo

Intervention Type DRUG

Volume equivalent to 10 mcg/kg, every 4 weeks via IV push

azacitidine

Intervention Type DRUG

75 mg/m2 given subcutaneously (SC) or IV x 7 days, every 4 weeks

decitabine

Intervention Type DRUG

20 mg/m2 given IV x 5 days, every 4 weeks

Interventions

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33A

33A, 10 mcg/kg, every 4 weeks via intravenous (IV) push

Intervention Type DRUG

placebo

Volume equivalent to 10 mcg/kg, every 4 weeks via IV push

Intervention Type DRUG

azacitidine

75 mg/m2 given subcutaneously (SC) or IV x 7 days, every 4 weeks

Intervention Type DRUG

decitabine

20 mg/m2 given IV x 5 days, every 4 weeks

Intervention Type DRUG

Other Intervention Names

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vadastuximab talirine, SGN-CD33A

Eligibility Criteria

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Inclusion Criteria

* Newly diagnosed, previously untreated, cytologically/histologically confirmed de novo or secondary AML according to World Health Organization (WHO) classification (except for acute promyelocytic leukemia (APL))
* Intermediate or adverse cytogenetic risk
* Eligible for therapy with either decitabine or azacitidine
* Acceptable hematologic and organ function

Exclusion Criteria

* AML associated with favorable risk karyotypes including inv(16), t(8;21), t(16;16), or t(15;17)
* Patients who are candidates for allogeneic stem cell transplant at the time of enrollment
* Patients with a history of one of the following myeloproliferative neoplasms: essential thrombocythemia, polycythemia vera, and primary myelofibrosis
* Received prior treatment with HMA or chemotherapy for antecedent myelodysplastic syndrome (MDS)
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Seagen Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Phoenix Ho, MD

Role: STUDY_DIRECTOR

Seagen Inc.

Locations

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University of Arkansas for Medical Sciences

Little Rock, Arkansas, United States

Site Status

City of Hope National Medical Center

Duarte, California, United States

Site Status

Pacific Hematology Oncology Associates

San Francisco, California, United States

Site Status

Colorado Blood Cancer Institute

Denver, Colorado, United States

Site Status

Florida Cancer Specialists - South Region

Fort Myers, Florida, United States

Site Status

Shands Cancer Center / University of Florida

Gainesville, Florida, United States

Site Status

Memorial Cancer Institute

Miami, Florida, United States

Site Status

Florida Center for Cellular Therapy / Blood and Marrow Transplant Center

Orlando, Florida, United States

Site Status

Florida Cancer Specialists - North Region

St. Petersburg, Florida, United States

Site Status

Northside Hospital

Atlanta, Georgia, United States

Site Status

OnCare Hawaii

Honolulu, Hawaii, United States

Site Status

Rush University Medical Center

Chicago, Illinois, United States

Site Status

University of Chicago

Chicago, Illinois, United States

Site Status

University of Kansas Cancer Center

Westwood, Kansas, United States

Site Status

Norton Cancer Institute

Louisville, Kentucky, United States

Site Status

LSU Health Sciences Center / Feist Weiller Cancer Center

Shreveport, Louisiana, United States

Site Status

Center for Cancer and Blood Disorders

Bethesda, Maryland, United States

Site Status

Tufts Medical Center

Boston, Massachusetts, United States

Site Status

Massachusetts General Hospital

Boston, Massachusetts, United States

Site Status

Beth Israel Deaconess Medical Center

Boston, Massachusetts, United States

Site Status

Dana Farber Cancer Institute

Boston, Massachusetts, United States

Site Status

University of Michigan Comprehensive Cancer Center

Ann Arbor, Michigan, United States

Site Status

Washington University School of Medicine

St Louis, Missouri, United States

Site Status

Hackensack University Medical Center

Hackensack, New Jersey, United States

Site Status

Roswell Park Cancer Institute

Buffalo, New York, United States

Site Status

James P. Wilmot Cancer Center / University of Rochester Medical Center

Rochester, New York, United States

Site Status

Duke University Medical Center

Durham, North Carolina, United States

Site Status

Providence Portland Medical Center

Portland, Oregon, United States

Site Status

University of Pennsylvania

Philadelphia, Pennsylvania, United States

Site Status

Rhode Island Hospital

Providence, Rhode Island, United States

Site Status

Medical University of South Carolina/Hollings Cancer Center

Charleston, South Carolina, United States

Site Status

Saint Francis Hospital / Bon Secours

Greenville, South Carolina, United States

Site Status

Sarah Cannon Research Institute

Nashville, Tennessee, United States

Site Status

MD Anderson Cancer Center / University of Texas

Houston, Texas, United States

Site Status

Brooke Army Medical Center

San Antonio, Texas, United States

Site Status

Texas Oncology - San Antonio Medical Center

San Antonio, Texas, United States

Site Status

Intermountain Blood and Marrow Transplant/Acute Leukemia Program

Salt Lake City, Utah, United States

Site Status

University of Virginia

Charlottesville, Virginia, United States

Site Status

Virginia Commonwealth University Medical Center

Richmond, Virginia, United States

Site Status

Swedish Cancer Institute

Seattle, Washington, United States

Site Status

Royal Adelaide Hospital

Adelaide, , Australia

Site Status

Monash Medical Centre

Clayton, , Australia

Site Status

St George Hospital

Kogarah, , Australia

Site Status

Royal Perth Hospital

Perth, , Australia

Site Status

Sunshine Hospital

St Albans, , Australia

Site Status

LKH Salzburg, Universitatsklinikum der PMU

Salzburg, , Austria

Site Status

Klinikum Wels-Grieskirchen GmbH

Wels, , Austria

Site Status

Ziekenhuis Netwerk Antwerpen Campus Stuivenberg

Antwerp, , Belgium

Site Status

Az Sint-Jane Brugge - Oostende Av - Campus Sint-Jan

Bruges, , Belgium

Site Status

Institut Jules Bordet

Brussels, , Belgium

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Cliniques Universitaires Saint Luc

Brussels, , Belgium

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Centre Hospitalier Universitaire Sart Tilman Liege

Liège, , Belgium

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AZ Delta - Campus Wilgenstraat

Roeselare, , Belgium

Site Status

Cliniques Universitaires UCL de Mont-Goddine

Yvoir, , Belgium

Site Status

Fakultni nemocnice Brno

Brno, , Czechia

Site Status

Fakultni nemocnice Hradec Kralove-oddeleni klinicke hematologie

Hradec Králové, , Czechia

Site Status

Fakultni Nemocnice Ostrava

Ostrava - Poruba, , Czechia

Site Status

Ustav hematologie a krevni transfuze

Prague, , Czechia

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CHU Amiens Picardie - Site Sud

Amiens, , France

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Center Hospitalier Universitaire d' Angers

Angers, , France

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Centre Hospitalier Victor Dupouy d'Argenteuil

Argenteuil, , France

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Centre Hospitalier Universitaire Hopital Avicenne

Bobigny, , France

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Hopital d'Instruction des Armees - Percy

Clamart, , France

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CHRU de Lille

Lille, , France

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Centre Hospitalier Universitaire (CHU) De Limoges - Hopital Dupuytren

Limoges, , France

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Hopital Emile Muller

Mulhouse, , France

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Centre Hospitalier Universitaire Nantes-Hotel Dieu

Nantes, , France

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CHU de Nice - Hopital l'Archet

Nice, , France

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Hopital Saint-Louis / Service d'Hematologie

Paris, , France

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CHU Bordeaux Hopital Haut-Levaque

Pessac, , France

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Centre Hospitalier Lyon Sud

Pierre-Bénite, , France

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Centre Hospitalier Universitaire de Poitiers

Poitiers, , France

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Centre Hospitalier Universitaire de Rennes, Hopital Pontchaillou

Rennes, , France

Site Status

Stadtisches Klinikum Braunschweig gGmbH

Braunschweig, , Germany

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Universitatsklinikum Koln

Cologne, , Germany

Site Status

Marien Hospital Dusseldorf GmbH

Düsseldorf, , Germany

Site Status

Universitatsklinik Freiburg

Freiburg im Breisgau, , Germany

Site Status

Universitatsklinikum Schleswig-Holstein

Kiel, , Germany

Site Status

Semmelweis Egyetem

Budapest, , Hungary

Site Status

Debreceni Egyetem Orvos és Egeszsegtudomanyi Centrum, III. sz. Belgyogyaszati Klinika

Debrecen, , Hungary

Site Status

Somogy Megyei Kaposi Mór Oktató Kórház

Kaposvár, , Hungary

Site Status

Bacs-Kiskun Megyei Korhaz Szegedi Tudomanyegyetem Altalanos Orvostudomanyi Kar Oktato Korhaza

Kecskemét, , Hungary

Site Status

Szegedi Tudomanyegyetem Szent-Gyorgyi Albert Klinikat Kozpont

Szeged, , Hungary

Site Status

Barzilai Medical Center

Ashkelon, , Israel

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Soroka Medical Center, Dept. of Oncology

Beersheba, , Israel

Site Status

Carmel Medical Center

Haifa, , Israel

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Edith Wolfson Medical Center

Holon, , Israel

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Shaare Zedek Medical Center

Jerusalem, , Israel

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Hadassah Medical Center

Jerusalem, , Israel

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Rabin Medical Center

Petah Tikva, , Israel

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Tel Aviv Sourasky Medical Center

Tel Aviv, , Israel

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Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico

Milan, , Italy

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IRCCS Ospedale San Raffaele

Milan, , Italy

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Azienda Ospedaliero-Univesitaria San Luigi Gonzaga

Orbassano, , Italy

Site Status

Azienda Ospedaliera Ospedali Riuniti Marche Nord

Pesaro, , Italy

Site Status

Università degli Studi di Roma "La Sapienza, Policlinico Umberto I

Roma, , Italy

Site Status

Centre Hospitalier Luxembourg - CHL Centre

Luxembourg, , Luxembourg

Site Status

SPZOZ Szpital Uniwersytecki w Krakowie

Krakow, , Poland

Site Status

Samodzielny Publiczny Centralny Szpital Kliniczny

Warsaw, , Poland

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Keimyung University Dongsan Medical Center

Daegu, , South Korea

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Yeungnam University Medical Center

Daegu, , South Korea

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Chungnam National University Hospital

Daejeon, , South Korea

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Chonnam National University Hwasun Hospital

Hwasun, , South Korea

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Chonbuk National University Hospital

Jeonju, , South Korea

Site Status

Seoul National University Hospital

Jongno-gu, , South Korea

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Severance Hospital, Yonsei University Health System

Seoul, , South Korea

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Samsung Medical Center

Seoul, , South Korea

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Seoul Saint Mary's Hospital

Seoul, , South Korea

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Korea University Guro Hospital

Seoul, , South Korea

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Hospital Universitari Germans Trias i Pujol

Badalona, , Spain

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Hospital de la Santa Creu i Sant Paul

Barcelona, , Spain

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Hospital Universitario Vall d'Hebron

Barcelona, , Spain

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Hospital San Pedro de Alcantara

Cáceres, , Spain

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Hospital Universitario de Girona Doctor Josep Trueta

Girona, , Spain

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Hospital Universitario Ramon y Cajal

Madrid, , Spain

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Hospital Universitario Virgen de la Victoria

Málaga, , Spain

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Hospital Universitaro de Salamanca

Salamanca, , Spain

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Hospital Universitari i Politecnic La Fe de Valencia

Valencia, , Spain

Site Status

Changhua Christian Hospital

Changhua, , Taiwan

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National Cheng-Kung University Hospital

Tainan City, , Taiwan

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National Taiwan University Hospital

Taipei, , Taiwan

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Taipei Veterans General Hospital

Taipei, , Taiwan

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County Durham and Darlington NHS Foundation Trust

Darlington, , United Kingdom

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Imperial College Healthcare NHS Trust

London, , United Kingdom

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North West London Hospitals NHS Trust

Middlesex, , United Kingdom

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The Newcastle upon Tyne Hospitals NHS Foundation Trust

Newcastle upon Tyne, , United Kingdom

Site Status

University Hospital Southampton NHS Foundation Trust

Southampton, , United Kingdom

Site Status

University Hospitals of North Midlands NHS Trust

Stoke-on-Trent, , United Kingdom

Site Status

Countries

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United States Australia Austria Belgium Czechia France Germany Hungary Israel Italy Luxembourg Poland South Korea Spain Taiwan United Kingdom

Provided Documents

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Document Type: Statistical Analysis Plan

View Document

Document Type: Study Protocol

View Document

Other Identifiers

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2015-003482-28

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

SGN33A-005

Identifier Type: -

Identifier Source: org_study_id