Cytokine Induced Memory-like NK Cell Adoptive Therapy After Haploidentical Donor Hematopoietic Cell Transplantation

NCT ID: NCT02782546

Last Updated: 2025-12-24

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

ACTIVE_NOT_RECRUITING

Clinical Phase

PHASE2

Total Enrollment

60 participants

Study Classification

INTERVENTIONAL

Study Start Date

2017-01-30

Study Completion Date

2028-02-13

Brief Summary

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This is a standard phase 2 study powered to demonstrate improvement in the 100 day leukemia free survival to 30% from \<10% expected with the use of reduced intensity haplo-HCT in this extremely high-risk patient cohort (based on the institutional experience using non-myeloablative / reduced intensity conditioning in a similar patient cohort).

A formal safety evaluation will be done after every 6th patient enrolled and the trial will be stopped if noted to have unusually higher engraftment failure (acute GVHD rates (\>60% any grades or \>30% grade III/IV or ≥ 50% severe cGVHD) or engraftment failure rates (≥15%).

Detailed Description

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Conditions

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Acute Myeloid Leukemia

Study Design

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Allocation Method

NON_RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Recipient

* Standard of care reduced conditioning regimen on Day -1
* Graft cell infusion on Day 0
* Post-transplant cyclophosphamide on Days +3 and +4
* GvHD prophylaxis with tacrolimus and mycophenolate mofetil (MMF) will start on Day +5. MMF will continue till Day +35 and tacrolimus till Day +180 in the absence of GvHD
* G-CSF will start on Day +7 and will continue until neutrophil engraftment as per institutional guidelines
* The cytokine-induced memory like natural killer (CIML NK) cells will be infused on Day +7 without a filter or pump, slowly by gravity over at least 15 minutes.
* ALT-803 will start approximately 4 hours after the CIML NK cell infusion. ALT-803 will be administered subcutaneously at a dose of 10 mcg/kg subcutaneously beginning Day +7 (on the day of CIML NK cell infusion) and then every 21 days for a total of 4 doses

Group Type EXPERIMENTAL

Graft cell infusion

Intervention Type PROCEDURE

-Day 0

Tacrolimus

Intervention Type DRUG

-GVHD prophylaxis

Mycophenolate mofetil

Intervention Type DRUG

-GVHD prophylaxis

G-CSF

Intervention Type DRUG

-Continue until neutrophil engraftment as per institutional guidelines

CIML NK cell infusion

Intervention Type PROCEDURE

-Day +7

ALT-803

Intervention Type DRUG

-Start approximately 4 hours after CIML NK cell infusion

Donor

* Donors will receive subcutaneous G-CSF from Day -4 till Day 0 and undergo 20L apheresis per institutional guidelines.
* Two consecutive days for collection are allowed in case of the target CD34+ cell dose being less than the target 4 x106/kg-bw from the first day of collection.
* On Day +6 (one day before the planned CIML NK cell infusion), peripheral blood mononuclear cells will be collected by a single standard 20-L apheresis over 4-5 hours from the same haploidentical related donor that provided the HCT graft.

Group Type EXPERIMENTAL

Leukapheresis

Intervention Type PROCEDURE

-Day +6

Interventions

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Graft cell infusion

-Day 0

Intervention Type PROCEDURE

Tacrolimus

-GVHD prophylaxis

Intervention Type DRUG

Mycophenolate mofetil

-GVHD prophylaxis

Intervention Type DRUG

G-CSF

-Continue until neutrophil engraftment as per institutional guidelines

Intervention Type DRUG

CIML NK cell infusion

-Day +7

Intervention Type PROCEDURE

ALT-803

-Start approximately 4 hours after CIML NK cell infusion

Intervention Type DRUG

Leukapheresis

-Day +6

Intervention Type PROCEDURE

Other Intervention Names

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HCT Prograf CellCept Myfortic Granulocyte-colony stimulating factor

Eligibility Criteria

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Inclusion Criteria

* Refractory AML without complete remission (CR) after 2 or more cycles of induction therapy (primary induction failure), or AML relapsed after obtaining a CR and failed one or more cycles of re-induction therapy. Standard dose 10-day decitabine (20 mg/m2 daily IV x 10 days) or 7-day azacitidine (75-100 mg/m2 daily SC/IV x 7 days) will be considered as one cycle of induction therapy.
* At least 18 years of age
* Available HLA-haploidentical donor that meets the criteria in the protocol
* Patients with known CNS involvement with AML are eligible provided that they have been treated and CSF is clear for at least 2 weeks prior to enrollment into the study. CNS therapy (chemotherapy or radiation) should continue as medically indicated during the study treatment.
* Karnofsky performance status \> 60 %
* Adequate organ function as defined below:

* Total bilirubin \< 2 mg/dl
* AST(SGOT)/ALT(SGPT) \< 3.0 x IULN
* Creatinine within normal institutional limits OR creatinine clearance \> 60 mL/min/1.73 m2 by Cockcroft-Gault Formula
* Oxygen saturation ≥90% on room air and adjusted DLCO of at least 40%
* Ejection fraction ≥40%
* Able to be off of corticosteroids (10 mg or less of prednisone or equivalent doses of other systemic steroids are allowed) and any other immune suppressive medications beginning on Day -3
* Women of childbearing potential must have a negative pregnancy test within 28 days prior to study registration. Female and male patients (along with their female partners) must agree to use two forms of acceptable contraception, including one barrier method, during participation in the study and throughout the DLT evaluation period.
* Ability to understand and willingness to sign an IRB approved written informed consent document (or that of legally authorized representative, if applicable).


* Related donor (sibling, offspring, or offspring of sibling)
* At least 18 years of age
* HLA-haploidentical donor/recipient match by at least Class I serologic typing at the A\&B locus.
* In general good health, and medically able to tolerate leukapheresis required for harvesting the NK cells for this study.
* Ability to understand and willingness to sign an IRB approved written informed consent document

Exclusion Criteria

* Relapsed after allogeneic transplantation.
* Circulating blast count \>30,000/uL by morphology or flow cytometry (cyto-reductive therapies including leukapheresis or hydroxyurea are allowed).
* Uncontrolled bacterial or viral infections, or known HIV, Hepatitis B or C infection.
* Presence of donor specific antibodies (DSA) with Mean Fluorescence Intensity (MFI) of \>5000 as assessed by the single antigen bead assay, \< 6 weeks prior to starting transplant conditioning
* Uncontrolled angina, severe uncontrolled ventricular arrhythmias, or EKG suggestive of acute ischemia or active conduction system abnormalities.
* New progressive pulmonary infiltrates on screening chest x-ray or chest CT scan that have not been evaluated with bronchoscopy. Infiltrates attributed to infection must be stable/ improving after 1 week of appropriate therapy (4 weeks for presumed or proven fungal infections)
* Known hypersensitivity to one or more of the study agents
* Received any investigational drugs within the 14 days prior to the first day of transplant conditioning
* Pregnant and/or breastfeeding


* Positive for hepatitis, HTLV, or HIV infection
* Pregnant and/or breastfeeding
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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National Institutes of Health (NIH)

NIH

Sponsor Role collaborator

The V Foundation for Cancer Research

OTHER

Sponsor Role collaborator

National Cancer Institute (NCI)

NIH

Sponsor Role collaborator

ImmunityBio, Inc.

INDUSTRY

Sponsor Role collaborator

Washington University School of Medicine

OTHER

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Amanda Cashen, M.D.

Role: PRINCIPAL_INVESTIGATOR

Washington University School of Medicine

Locations

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Washington University School of Medicine

St Louis, Missouri, United States

Site Status

Countries

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United States

References

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Berrien-Elliott MM, Foltz JA, Russler-Germain DA, Neal CC, Tran J, Gang M, Wong P, Fisk B, Cubitt CC, Marin ND, Zhou AY, Jacobs MT, Foster M, Schappe T, McClain E, Kersting-Schadek S, Desai S, Pence P, Becker-Hapak M, Eisele J, Mosior M, Marsala L, Griffith OL, Griffith M, Khan SM, Spencer DH, DiPersio JF, Romee R, Uy GL, Abboud CN, Ghobadi A, Westervelt P, Stockerl-Goldstein K, Schroeder MA, Wan F, Lie WR, Soon-Shiong P, Petti AA, Cashen AF, Fehniger TA. Hematopoietic cell transplantation donor-derived memory-like NK cells functionally persist after transfer into patients with leukemia. Sci Transl Med. 2022 Feb 23;14(633):eabm1375. doi: 10.1126/scitranslmed.abm1375. Epub 2022 Feb 23.

Reference Type DERIVED
PMID: 35196021 (View on PubMed)

Related Links

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http://siteman.wustl.edu

Alvin J. Siteman Cancer Center at Barnes-Jewish Hospital and Washington University School of Medicine

Other Identifiers

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1P50CA171963-01A1

Identifier Type: NIH

Identifier Source: secondary_id

View Link

2P50CA171963-06

Identifier Type: NIH

Identifier Source: secondary_id

View Link

201610088

Identifier Type: -

Identifier Source: org_study_id