Trial Outcomes & Findings for Transarterial Chemoembolization Compared With Stereotactic Body Radiation Therapy or Stereotactic Ablative Radiation Therapy in Treating Patients With Residual or Recurrent Liver Cancer Undergone Initial Transarterial Chemoembolization (NCT NCT02762266)

NCT ID: NCT02762266

Last Updated: 2024-03-12

Results Overview

Local progression event: occurring in the treated hepatic lesion.

Recruitment status

TERMINATED

Study phase

PHASE3

Target enrollment

13 participants

Primary outcome timeframe

Up to 12 months

Results posted on

2024-03-12

Participant Flow

13 participants signed informed consent, 12 were randomized to a study arm.

Participant milestones

Participant milestones
Measure
Transarterial Chemoembolization (TACE)
Patients undergo TACE using an embolic agent (gelatin sponge \[gelfoam\], polyvinyl alcohol particles, or embolic beads).
Stereotactic Body Radiation Therapy (SBRT)
Patients undergo image-guided SBRT (3 fractions within 1 week or 5 fractions within 2 weeks).
Overall Study
STARTED
6
6
Overall Study
Received Treatment
4
6
Overall Study
COMPLETED
4
6
Overall Study
NOT COMPLETED
2
0

Reasons for withdrawal

Reasons for withdrawal
Measure
Transarterial Chemoembolization (TACE)
Patients undergo TACE using an embolic agent (gelatin sponge \[gelfoam\], polyvinyl alcohol particles, or embolic beads).
Stereotactic Body Radiation Therapy (SBRT)
Patients undergo image-guided SBRT (3 fractions within 1 week or 5 fractions within 2 weeks).
Overall Study
Physician Decision
2
0

Baseline Characteristics

Participants with AFP data

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Transarterial Chemoembolization (TACE)
n=4 Participants
Patients undergo TACE using an embolic agent.
Stereotactic Body Radiation Therapy (SBRT)
n=6 Participants
Patients undergo image-guided SBRT.
Total
n=10 Participants
Total of all reporting groups
Age, Continuous
69.9 years
STANDARD_DEVIATION 6.25 • n=4 Participants
67.7 years
STANDARD_DEVIATION 7.15 • n=6 Participants
68.6 years
STANDARD_DEVIATION 6.54 • n=10 Participants
Sex: Female, Male
Female
0 Participants
n=4 Participants
4 Participants
n=6 Participants
4 Participants
n=10 Participants
Sex: Female, Male
Male
4 Participants
n=4 Participants
2 Participants
n=6 Participants
6 Participants
n=10 Participants
Ethnicity (NIH/OMB)
Hispanic or Latino
0 Participants
n=4 Participants
5 Participants
n=6 Participants
5 Participants
n=10 Participants
Ethnicity (NIH/OMB)
Not Hispanic or Latino
4 Participants
n=4 Participants
1 Participants
n=6 Participants
5 Participants
n=10 Participants
Ethnicity (NIH/OMB)
Unknown or Not Reported
0 Participants
n=4 Participants
0 Participants
n=6 Participants
0 Participants
n=10 Participants
Race (NIH/OMB)
American Indian or Alaska Native
0 Participants
n=4 Participants
1 Participants
n=6 Participants
1 Participants
n=10 Participants
Race (NIH/OMB)
Asian
2 Participants
n=4 Participants
0 Participants
n=6 Participants
2 Participants
n=10 Participants
Race (NIH/OMB)
Native Hawaiian or Other Pacific Islander
0 Participants
n=4 Participants
2 Participants
n=6 Participants
2 Participants
n=10 Participants
Race (NIH/OMB)
Black or African American
0 Participants
n=4 Participants
0 Participants
n=6 Participants
0 Participants
n=10 Participants
Race (NIH/OMB)
White
1 Participants
n=4 Participants
1 Participants
n=6 Participants
2 Participants
n=10 Participants
Race (NIH/OMB)
More than one race
0 Participants
n=4 Participants
0 Participants
n=6 Participants
0 Participants
n=10 Participants
Race (NIH/OMB)
Unknown or Not Reported
1 Participants
n=4 Participants
2 Participants
n=6 Participants
3 Participants
n=10 Participants
Region of Enrollment
United States
3 Participants
n=4 Participants
6 Participants
n=6 Participants
9 Participants
n=10 Participants
Region of Enrollment
Japan
1 Participants
n=4 Participants
0 Participants
n=6 Participants
1 Participants
n=10 Participants
Elevated Serum Alpha-Fetoprotein (AFP)
0 Participants
n=3 Participants • Participants with AFP data
3 Participants
n=6 Participants • Participants with AFP data
3 Participants
n=9 Participants • Participants with AFP data

PRIMARY outcome

Timeframe: Up to 12 months

Population: Participants who received treatment

Local progression event: occurring in the treated hepatic lesion.

Outcome measures

Outcome measures
Measure
Transarterial Chemoembolization (TACE)
n=4 Participants
Patients undergo TACE using an embolic agent.
Stereotactic Body Radiation Therapy (SBRT)
n=6 Participants
Patients undergo image-guided SBRT.
Number of Participants With a Local Progression Event
0 Participants
0 Participants

SECONDARY outcome

Timeframe: Up to 16 weeks

Population: Participants who received treatment

The time to freedom from extra hepatic progression will be estimated by competing risk models with death as a competing risk. Risk factors such as tumor size and institution will be tested in a multivariate Cox regression model adjusting for the competing risks.

Outcome measures

Outcome measures
Measure
Transarterial Chemoembolization (TACE)
n=4 Participants
Patients undergo TACE using an embolic agent.
Stereotactic Body Radiation Therapy (SBRT)
n=6 Participants
Patients undergo image-guided SBRT.
Comparison of Median Freedom From Extra Hepatic Progression
NA months
Not calculable due to an insufficient number of events
NA months
Not calculable due to an insufficient number of events

SECONDARY outcome

Timeframe: At 18 months

Population: Participants who received treatment

Extra hepatic PFS within each subgroup will be summarized by cumulative incidence function estimators adjusted for the competing risk of death or regional or distant progression.

Outcome measures

Outcome measures
Measure
Transarterial Chemoembolization (TACE)
n=4 Participants
Patients undergo TACE using an embolic agent.
Stereotactic Body Radiation Therapy (SBRT)
n=6 Participants
Patients undergo image-guided SBRT.
Median Extra Hepatic PFS for Patients With Tumors Smaller Than 3 cm and Greater Than 3 cm Per Treatment Group
NA months
Not calculable due to an insufficient number of events
NA months
Not calculable due to an insufficient number of events

SECONDARY outcome

Timeframe: At 18 months

Population: Participants who received treatment

FFLP within each subgroup will be summarized by cumulative incidence function estimators adjusted for the competing risk of death or regional or distant progression.

Outcome measures

Outcome measures
Measure
Transarterial Chemoembolization (TACE)
n=4 Participants
Patients undergo TACE using an embolic agent.
Stereotactic Body Radiation Therapy (SBRT)
n=6 Participants
Patients undergo image-guided SBRT.
Median FFLP for Patients With Tumors Smaller Than 3 cm and With Tumors Greater Than 3 cm Per Treatment Group
NA months
Not calculable due to an insufficient number of events
NA months
Not calculable due to an insufficient number of events

SECONDARY outcome

Timeframe: Time from randomization until death from any cause, assessed up to 3 years

Population: Participants who received treatment

Overall survival will be summarized using Kaplan-Meier curves and medians with 95% confidence intervals calculated using Greenwood's formula. Log rank tests will be used to compare treatment groups. Cox proportional hazard models will be used to estimate hazard ratios between treatment groups and to assess other risk factors, in particular the effect of tumor size and the impact of the different institutions.

Outcome measures

Outcome measures
Measure
Transarterial Chemoembolization (TACE)
n=4 Participants
Patients undergo TACE using an embolic agent.
Stereotactic Body Radiation Therapy (SBRT)
n=6 Participants
Patients undergo image-guided SBRT.
Median OS
NA months
Not calculable due to an insufficient number of events
NA months
Not calculable due to an insufficient number of events

SECONDARY outcome

Timeframe: At 18 months

Population: Participants who received treatment

Within each subgroup OS will be summarized using Kaplan-Meier curves and medians with 95% confidence intervals calculated using Greenwood's formula.

Outcome measures

Outcome measures
Measure
Transarterial Chemoembolization (TACE)
n=4 Participants
Patients undergo TACE using an embolic agent.
Stereotactic Body Radiation Therapy (SBRT)
n=6 Participants
Patients undergo image-guided SBRT.
Median OS for Patients With Tumors Smaller Than 3 cm and Greater Than 3 cm Per Treatment Group
NA months
Not calculable due to an insufficient number of events
NA months
Not calculable due to an insufficient number of events

SECONDARY outcome

Timeframe: Randomization through 3 years

Population: Participants who received treatment

Including local, regional, or distant progression events, or death. Local progression event: occurring in the treated tumor. Regional progression event: occurring in the same part of the body as the treated tumor. Distant progression event: occurring outside the region of the body where the treated tumor is located.

Outcome measures

Outcome measures
Measure
Transarterial Chemoembolization (TACE)
n=4 Participants
Patients undergo TACE using an embolic agent.
Stereotactic Body Radiation Therapy (SBRT)
n=6 Participants
Patients undergo image-guided SBRT.
Number of Participants With Disease Progression or Death
1 Participants
3 Participants

SECONDARY outcome

Timeframe: Randomization through 18 months

Population: Participants who receive treatment

Including local, regional, or distant progression events, or death. Local progression event: occurring in the treated tumor. Regional progression event: occurring in the same part of the body as the treated tumor. Distant progression event: occurring outside the region of the body where the treated tumor is located.

Outcome measures

Outcome measures
Measure
Transarterial Chemoembolization (TACE)
n=4 Participants
Patients undergo TACE using an embolic agent.
Stereotactic Body Radiation Therapy (SBRT)
n=6 Participants
Patients undergo image-guided SBRT.
Number of Participants With Disease Progression or Death by Tumor Size (<= 3 cm and > 3 cm) Per Treatment Group
<= 3 cm
1 Participants
2 Participants
Number of Participants With Disease Progression or Death by Tumor Size (<= 3 cm and > 3 cm) Per Treatment Group
> 3 cm
1 Participants

SECONDARY outcome

Timeframe: Up to 18 months

Population: Participants who received treatment

The impact of elevated AFP level on time to event endpoints will be evaluated both in terms of the initial AFP level and on-study levels in a Cox proportional hazards model.

Outcome measures

Outcome measures
Measure
Transarterial Chemoembolization (TACE)
n=4 Participants
Patients undergo TACE using an embolic agent.
Stereotactic Body Radiation Therapy (SBRT)
n=6 Participants
Patients undergo image-guided SBRT.
The Impact of Elevated Serum Alpha-Fetoprotein Level (AFP) on Freedom From Local Progression (FFLP)
NA months
Not calculable due to an insufficient number of events
NA months
Not calculable due to an insufficient number of events

SECONDARY outcome

Timeframe: Up to 18 months

Population: Participants who received treatment

The impact of elevated AFP level on time to event endpoints will be evaluated both in terms of the initial AFP level and on-study levels in a Cox proportional hazards model.

Outcome measures

Outcome measures
Measure
Transarterial Chemoembolization (TACE)
n=4 Participants
Patients undergo TACE using an embolic agent.
Stereotactic Body Radiation Therapy (SBRT)
n=6 Participants
Patients undergo image-guided SBRT.
The Impact of Elevated Serum Alpha-Fetoprotein Level (AFP) on Progression-free Survival (PFS)
NA months
Not calculable due to an insufficient number of events
NA months
Not calculable due to an insufficient number of events

SECONDARY outcome

Timeframe: Up to 18 months

Population: Participants who received treatment

The impact of elevated AFP level on time to event endpoints: FFLP, PFS, extra hepatic PFS and OS will be evaluated both in terms of the initial AFP level and on-study levels in a Cox proportional hazards model.

Outcome measures

Outcome measures
Measure
Transarterial Chemoembolization (TACE)
n=4 Participants
Patients undergo TACE using an embolic agent.
Stereotactic Body Radiation Therapy (SBRT)
n=6 Participants
Patients undergo image-guided SBRT.
The Impact of Elevated Serum Alpha-Fetoprotein Level (AFP) on Extra Hepatic PFS
NA months
Not calculable due to an insufficient number of events
NA months
Not calculable due to an insufficient number of events

SECONDARY outcome

Timeframe: Up to 18 months

Population: Participants who received treatment

The impact of elevated AFP level on time to event endpoints will be evaluated both in terms of the initial AFP level and on-study levels in a Cox proportional hazards model.

Outcome measures

Outcome measures
Measure
Transarterial Chemoembolization (TACE)
n=4 Participants
Patients undergo TACE using an embolic agent.
Stereotactic Body Radiation Therapy (SBRT)
n=6 Participants
Patients undergo image-guided SBRT.
The Impact of Elevated Serum Alpha-Fetoprotein Level (AFP) on Overall Survival (OS)
NA months
Not calculable due to an insufficient number of events
NA months
Not calculable due to an insufficient number of events

Adverse Events

Transarterial Chemoembolization (TACE)

Serious events: 0 serious events
Other events: 6 other events
Deaths: 0 deaths

Stereotactic Body Radiation Therapy (SBRT)

Serious events: 1 serious events
Other events: 6 other events
Deaths: 3 deaths

Serious adverse events

Serious adverse events
Measure
Transarterial Chemoembolization (TACE)
n=6 participants at risk
Patients undergo TACE using an embolic agent.
Stereotactic Body Radiation Therapy (SBRT)
n=6 participants at risk
Patients undergo image-guided SBRT.
Hepatobiliary disorders
Cholecystitis
0.00%
0/6 • Up to 3 years
16.7%
1/6 • Up to 3 years

Other adverse events

Other adverse events
Measure
Transarterial Chemoembolization (TACE)
n=6 participants at risk
Patients undergo TACE using an embolic agent.
Stereotactic Body Radiation Therapy (SBRT)
n=6 participants at risk
Patients undergo image-guided SBRT.
Blood and lymphatic system disorders
Anemia
0.00%
0/6 • Up to 3 years
66.7%
4/6 • Up to 3 years
Gastrointestinal disorders
Abdominal Pain
16.7%
1/6 • Up to 3 years
33.3%
2/6 • Up to 3 years
Gastrointestinal disorders
Ascites
16.7%
1/6 • Up to 3 years
33.3%
2/6 • Up to 3 years
Gastrointestinal disorders
Bloating
0.00%
0/6 • Up to 3 years
16.7%
1/6 • Up to 3 years
Gastrointestinal disorders
Constipation
16.7%
1/6 • Up to 3 years
16.7%
1/6 • Up to 3 years
Gastrointestinal disorders
GI disorder other
0.00%
0/6 • Up to 3 years
16.7%
1/6 • Up to 3 years
Gastrointestinal disorders
Nausea
16.7%
1/6 • Up to 3 years
16.7%
1/6 • Up to 3 years
General disorders
Fatigue
50.0%
3/6 • Up to 3 years
50.0%
3/6 • Up to 3 years
Hepatobiliary disorders
Bile duct stenosis
16.7%
1/6 • Up to 3 years
0.00%
0/6 • Up to 3 years
Hepatobiliary disorders
Hepatic Pain
16.7%
1/6 • Up to 3 years
0.00%
0/6 • Up to 3 years
Hepatobiliary disorders
Portal Hypertension
0.00%
0/6 • Up to 3 years
16.7%
1/6 • Up to 3 years
Investigations
Alkaline phosphatase increased
16.7%
1/6 • Up to 3 years
33.3%
2/6 • Up to 3 years
Investigations
Alkaline Phosphatase increased
0.00%
0/6 • Up to 3 years
33.3%
2/6 • Up to 3 years
Investigations
ALT
16.7%
1/6 • Up to 3 years
16.7%
1/6 • Up to 3 years
Investigations
AST increased
33.3%
2/6 • Up to 3 years
66.7%
4/6 • Up to 3 years
Investigations
Blood Bilirubin increased
16.7%
1/6 • Up to 3 years
66.7%
4/6 • Up to 3 years
Investigations
Creatinine increased
0.00%
0/6 • Up to 3 years
16.7%
1/6 • Up to 3 years
Investigations
INR increased
16.7%
1/6 • Up to 3 years
0.00%
0/6 • Up to 3 years
Investigations
Lymphocyte count decreased
0.00%
0/6 • Up to 3 years
33.3%
2/6 • Up to 3 years
Investigations
Neutrophil count decreased
0.00%
0/6 • Up to 3 years
33.3%
2/6 • Up to 3 years
Investigations
Platelet count decreased
16.7%
1/6 • Up to 3 years
100.0%
6/6 • Up to 3 years
Investigations
WBC decreased
0.00%
0/6 • Up to 3 years
33.3%
2/6 • Up to 3 years
Investigations
0.00%
0/6 • Up to 3 years
16.7%
1/6 • Up to 3 years
Metabolism and nutrition disorders
Anorexia
16.7%
1/6 • Up to 3 years
0.00%
0/6 • Up to 3 years
Metabolism and nutrition disorders
Hypoalbuminemia
0.00%
0/6 • Up to 3 years
16.7%
1/6 • Up to 3 years
Metabolism and nutrition disorders
Hypocalcemia
0.00%
0/6 • Up to 3 years
33.3%
2/6 • Up to 3 years
Metabolism and nutrition disorders
Hypokalemia
0.00%
0/6 • Up to 3 years
16.7%
1/6 • Up to 3 years
Metabolism and nutrition disorders
Hyponatremia
0.00%
0/6 • Up to 3 years
16.7%
1/6 • Up to 3 years
Vascular disorders
Hypertension
0.00%
0/6 • Up to 3 years
16.7%
1/6 • Up to 3 years

Additional Information

Erqi Pollom, MD

Stanford University

Phone: (650) 498-0484

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place