Matching Patients With Hematologic Malignancy to Adequate Clinical Trials

NCT ID: NCT02758080

Last Updated: 2017-10-26

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

UNKNOWN

Clinical Phase

NA

Total Enrollment

90 participants

Study Classification

INTERVENTIONAL

Study Start Date

2016-01-31

Study Completion Date

2019-06-30

Brief Summary

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A molecular profile of a patient with hematologic malignancy, for whom standard-of-care had failed, is identified using next generation sequencing. Patients are assigned to early clinical trials of targeted agent based on the molecular profiling or physician's choice. The improvement of outcomes in the intention-to-treat population is investigated.

Detailed Description

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Most of hematologic malignancy patient becomes incurable with standard treatment during their disease course. Although these patients are recommended to participate in an early phase clinical trials, the response rate have reported be only 4 to 6 percent. Over several decades, a lot of cancer driving mutations has been identified, and targeted agents directed at the mutations are continuously developed and studied in many clinical trials. Most of the clinical trials recruited participants regardless of mutational status of them. Recently, however, participants has been recruited in recent clinical trials according to the presence of specific mutations. The response rate of these recent clinical trials is 12-75%.

In this pragmatic clinical trial, cancer driving mutations in hematologic malignancy patients is identified using next generation sequencing, and assign patients to an appropriate clinical trial which is anticipated to exhibit the best response. The improvement of outcome of this biomarker-driven assignment is investigated.

Conditions

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Hematologic Malignancies

Keywords

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Personalized medicine Next generation sequencing

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Matched

A molecular profile is identified using next generation sequencing. A participant in this arm is assigned to early clinical trial studying targeted agent, which is anticipated to have the best response rate.

Group Type EXPERIMENTAL

Matching on the basis of molecular analysis

Intervention Type OTHER

Not matched

A participants in this arm is assigned to a clinical trial at physician's choice.

Group Type OTHER

Matching on the basis of physician's choice

Intervention Type OTHER

Interventions

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Matching on the basis of molecular analysis

Intervention Type OTHER

Matching on the basis of physician's choice

Intervention Type OTHER

Eligibility Criteria

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Inclusion Criteria

* adults with \> 18 years old
* incurable hematologic malignancy patients who failed to respond to standard treatment
* patients who agreed to this protocol with informed consent
* Eastern Cooperative Oncology Group performance status ≤ 3
* Tolerable major organ function determined by laboratory examination

Exclusion Criteria

* Expected survival \< 3 months
* patients with poor compliance
* patients who can not give an informed consent
* patients who are participating another clinical trials
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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The Korea Health Technology R&D Project through the Korea Health Industry Development Institute

UNKNOWN

Sponsor Role collaborator

Ministry of Health, Republic of Korea

OTHER_GOV

Sponsor Role collaborator

Seoul National University Hospital

OTHER

Sponsor Role lead

Responsible Party

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Youngil Koh

Assistant professor

Responsibility Role PRINCIPAL_INVESTIGATOR

Principal Investigators

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Youngil Koh, MD

Role: PRINCIPAL_INVESTIGATOR

Seoul National University Hospital

Locations

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Seoul National University Hospital

Seoul, , South Korea

Site Status RECRUITING

Countries

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South Korea

Central Contacts

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Ryul Kim, MD

Role: CONTACT

Phone: +82 10 9412 6108

Email: [email protected]

Facility Contacts

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Ryul Kim, MD

Role: primary

References

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Other Identifiers

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2015-1690

Identifier Type: -

Identifier Source: org_study_id