Study of Nivolumab in Combination With Ipilimumab Compared to the Standard of Care (Extreme Regimen) as First Line Treatment in Patients With Recurrent or Metastatic Squamous Cell Carcinoma of the Head and Neck

NCT ID: NCT02741570

Last Updated: 2023-09-21

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

947 participants

Study Classification

INTERVENTIONAL

Study Start Date

2016-10-05

Study Completion Date

2022-09-22

Brief Summary

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The main purpose of this study is to compare nivolumab and ipilimumab with the extreme regimen as first line treatment in patients with recurrent or metastatic squamous cell of the head and neck cancer

Detailed Description

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Conditions

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Head and Neck Cancer

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Nivolumab and Ipilimumab

Specified dose on specified days

Group Type EXPERIMENTAL

Nivolumab

Intervention Type BIOLOGICAL

Ipilimumab

Intervention Type BIOLOGICAL

Extreme Regimen

Specified dose on specified days

Group Type ACTIVE_COMPARATOR

Cetuximab/Erbitux

Intervention Type DRUG

Cisplatin/Platinol

Intervention Type DRUG

Carboplatin/Paraplatin

Intervention Type DRUG

Fluorouracil/Adrucil

Intervention Type DRUG

Interventions

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Nivolumab

Intervention Type BIOLOGICAL

Ipilimumab

Intervention Type BIOLOGICAL

Cetuximab/Erbitux

Intervention Type DRUG

Cisplatin/Platinol

Intervention Type DRUG

Carboplatin/Paraplatin

Intervention Type DRUG

Fluorouracil/Adrucil

Intervention Type DRUG

Other Intervention Names

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BMS-936558 Opdivo BMS-734016 Yervoy

Eligibility Criteria

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Inclusion Criteria

* Histologically confirmed metastatic or recurrent squamous cell carcinoma of the head and neck (oral cavity, oropharynx, hypopharynx \& larynx) that is not amenable to curative therapy.
* No prior systemic cancer therapy for recurrent or metastatic disease (except if chemotherapy was part of multimodal treatment completed 6 months prior to enrolment).
* Measurable disease detected by imaging exam (CT or MRI).
* Have tumor tissue for PD L1 expression testing, and for oropharyngeal cancer have results from testing of HPV p16 status.

Exclusion Criteria

* Metastatic or recurrent carcinoma of the nasopharynx, squamous cell carcinoma of unknown primary, squamous cell carcinoma originating from skin and salivary glands or non squamous histologies (eg. mucosal melanoma).
* No prior treatment with anti PD1, anti PD L1, anti CTLA 4 antibody or any other antibody or drugs targeting T cell costimulation or checkpoint pathways, or cetuximab or EGFR inhibitors in any treatment setting.
* Participants with certain diseases such as active autoimmune disease, type I diabetes, hypothyroidism that needs hormone replacement, active infection, psychiatric disorder.
* Inadequate hematologic, renal or hepatic function.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Ono Pharmaceutical Co. Ltd

INDUSTRY

Sponsor Role collaborator

Bristol-Myers Squibb

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Bristol-Myers Squibb

Role: STUDY_DIRECTOR

Bristol-Myers Squibb

Locations

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Local Institution - 0134

Tucson, Arizona, United States

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Duarte, California, United States

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Stanford, California, United States

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Jacksonville, Florida, United States

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Tampa, Florida, United States

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Atlanta, Georgia, United States

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Chicago, Illinois, United States

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Boston, Massachusetts, United States

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Boston, Massachusetts, United States

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Boston, Massachusetts, United States

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Ann Arbor, Michigan, United States

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Charlotte, North Carolina, United States

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Columbus, Ohio, United States

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Langhorne, Pennsylvania, United States

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Philadelphia, Pennsylvania, United States

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Pittsburgh, Pennsylvania, United States

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Local Institution - 0139

Dallas, Texas, United States

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Houston, Texas, United States

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Houston, Texas, United States

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Charlottesville, Virginia, United States

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Fairfax, Virginia, United States

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Morgantown, West Virginia, United States

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Local Institution - 0142

Blacktown, New South Wales, Australia

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Local Institution - 0127

Darlinghurst, New South Wales, Australia

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Local Institution - 0128

Gosford, New South Wales, Australia

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St Leonards, New South Wales, Australia

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Brisbane, Queensland, Australia

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Douglas, Queensland, Australia

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Elizabeth Vale, South Australia, Australia

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Clayton, Victoria, Australia

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Local Institution - 0131

Melbourne, Victoria, Australia

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Nedlands, Western Australia, Australia

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Local Institution - 0075

Linz, , Austria

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Local Institution - 0071

Vienna, , Austria

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Local Institution - 0148

Belo Horizonte, Minas Gerais, Brazil

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Local Institution - 0121

Ijuí, Rio Grande do Sul, Brazil

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Porto Alegre, Rio Grande do Sul, Brazil

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Local Institution - 0120

Porto Alegre, Rio Grande do Sul, Brazil

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Barretos, São Paulo, Brazil

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Sao Jose de Rio Preto, São Paulo, Brazil

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São Paulo, , Brazil

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Local Institution - 0124

São Paulo, , Brazil

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Local Institution - 0133

Amiens, Somme, France

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Bordeaux, , France

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La Tronche, , France

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Lille, , France

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Lyon, , France

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Lyon, , France

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Marseille, , France

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Nice, , France

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Paris, , France

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Paris, , France

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Paris, , France

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Strasbourg, , France

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Villejuif, , France

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Bonn, , Germany

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Freiburg im Breisgau, , Germany

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Hamburg, , Germany

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Hanover, , Germany

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Heidelberg, , Germany

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Leipzig, , Germany

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Mainz, , Germany

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München, , Germany

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Ulm, , Germany

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Würzburg, , Germany

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Athens, , Greece

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Nea Kifissia, , Greece

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Thessaloniki, , Greece

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Dublin, Dublin, Ireland

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Haifa, , Israel

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Jerusalem, , Israel

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Petah Tikva, , Israel

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Ramat Gan, , Israel

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Tel Aviv, , Israel

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Milan, MI, Italy

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Torino, TO, Italy

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Cuneo, , Italy

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IRST Meldola

Meldola (FC), , Italy

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Azienda Ospedaliera Universitaria Di Modena

Modena, , Italy

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Aorn Dei Colli

Napoli, , Italy

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Istituto Nazionale Tumori Fondazione Pascale

Napoli, , Italy

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Azienda Ospedaliera Di Perugia

Perugia, , Italy

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Fondazione Policlinico Universitario A. Gemelli

Roma, , Italy

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Local Institution - 0106

Nagoya, Aichi-ken, Japan

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Kashiwa, Chiba, Japan

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Fukuoka, Fukuoka, Japan

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Sapporo, Hokkaido, Japan

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Akashi-shi, Hyōgo, Japan

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Kobe, Hyōgo, Japan

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Isehara, Kanagawa, Japan

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Yokohama, Kanagawa, Japan

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Natori-shi, Miyagi, Japan

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Sendai, Miyagi, Japan

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Osakasayaha, Osaka, Japan

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Takatsuki-shi, Osaka, Japan

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Kitaadachi-gun, Saitama, Japan

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Sunto-gun, Shizuoka, Japan

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Shimotsuke-shi, Tochigi, Japan

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Bunkyo-ku, Tokyo, Japan

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Chuo-ku, Tokyo, Japan

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Koto-ku, Tokyo, Japan

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Kita-gun, , Japan

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León, Guanajuato, Mexico

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Mexico City, Mexico City, Mexico

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Mexico City, Mexico City, Mexico

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Morelia, Michoacán, Mexico

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Monterrey, Nuevo León, Mexico

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Oaxaca City, , Mexico

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Bydgoszcz, , Poland

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Gdansk, , Poland

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Gliwice, , Poland

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Krakow, , Poland

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Warsaw, , Poland

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Gangnam-gu, , South Korea

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Seoul, , South Korea

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Seoul, , South Korea

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Barcelona, , Spain

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L'Hospitalet Del Llobregat, , Spain

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Madrid, , Spain

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Madrid, , Spain

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Seville, , Spain

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Valencia, , Spain

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Basel, , Switzerland

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Zurich, , Switzerland

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Taichung, , Taiwan

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Taipei, , Taiwan

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Newcastle upon Tyne, Durham, United Kingdom

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London, Greater London, United Kingdom

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Manchester, Greater Manchester, United Kingdom

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Southampton, Hampshire, United Kingdom

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Sutton, Surrey, United Kingdom

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Birmingham, West Midlands, United Kingdom

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Sheffield, , United Kingdom

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Countries

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United States Australia Austria Brazil France Germany Greece Ireland Israel Italy Japan Mexico Poland South Korea Spain Switzerland Taiwan United Kingdom

References

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Haddad RI, Harrington K, Tahara M, Ferris RL, Gillison M, Fayette J, Daste A, Koralewski P, Zurawski B, Taberna M, Saba NF, Mak M, Kawecki A, Girotto G, Alvarez Avitia MA, Even C, Toledo JGR, Guminski A, Muller-Richter U, Kiyota N, Roberts M, Khan TA, Miller-Moslin K, Wei L, Argiris A. Nivolumab Plus Ipilimumab Versus EXTREME Regimen as First-Line Treatment for Recurrent/Metastatic Squamous Cell Carcinoma of the Head and Neck: The Final Results of CheckMate 651. J Clin Oncol. 2023 Apr 20;41(12):2166-2180. doi: 10.1200/JCO.22.00332. Epub 2022 Dec 6.

Reference Type DERIVED
PMID: 36473143 (View on PubMed)

Hwang M, Seiwert TY. Are taxanes the future for head and neck cancer? Pragmatism in the immunotherapy era. Lancet Oncol. 2021 Apr;22(4):413-415. doi: 10.1016/S1470-2045(21)00121-2. Epub 2021 Mar 5. No abstract available.

Reference Type DERIVED
PMID: 33684371 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Related Links

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Other Identifiers

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2016-000725-39

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

CA209-651

Identifier Type: -

Identifier Source: org_study_id

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